1 00:00:04,993 --> 00:00:06,294 GOOD MORNING, I'M JENNIFER 2 00:00:06,294 --> 00:00:09,064 MORTON GRAY THE CHIEF OF THE 3 00:00:09,064 --> 00:00:12,367 COMMUNICATIONS AND OUTREACH 4 00:00:12,367 --> 00:00:14,669 BRANCH AT NIAMS AND IT'S MY 5 00:00:14,669 --> 00:00:16,371 ABSOLUTE PLEASURE TO SEE YOU ALL 6 00:00:16,371 --> 00:00:19,541 HERE TODAY AND WELCOME TO YOU 7 00:00:19,541 --> 00:00:21,142 THE 2023 NIAMS COALITION 8 00:00:21,142 --> 00:00:24,279 OUTREACH AND EDUCATION MEETING. 9 00:00:24,279 --> 00:00:25,480 THAT DESERVES A ROUND OF 10 00:00:25,480 --> 00:00:30,785 APPLAUSE. 11 00:00:30,785 --> 00:00:32,888 WE'RE DELIGHTED THAT ABOUT 55 OF 12 00:00:32,888 --> 00:00:34,589 OUR COLLEAGUES REPRESENTING MORE 13 00:00:34,589 --> 00:00:35,323 THAN 45 ORGANIZATIONS ARE HERE 14 00:00:35,323 --> 00:00:38,360 TODAY. 15 00:00:38,360 --> 00:00:40,128 AS YOU KNOW, THE NIAMS PORTFOLIO 16 00:00:40,128 --> 00:00:41,863 IS BROAD INCLUDING DISEASES THAT 17 00:00:41,863 --> 00:00:44,199 AFFECT THE BONES, JOINTS, 18 00:00:44,199 --> 00:00:46,635 MUSCLES AND SKIN. 19 00:00:46,635 --> 00:00:47,702 THESE DISEASES AFFECT ALMOST 20 00:00:47,702 --> 00:00:49,504 EVERY HOUSEHOLD IN AMERICA, 21 00:00:49,504 --> 00:00:52,307 PEOPLE OF ALL AGES, ALL RACIAL 22 00:00:52,307 --> 00:00:54,342 AND ETHNIC POPULATIONS AND EVERY 23 00:00:54,342 --> 00:00:55,043 ECONOMIC STRATA. 24 00:00:55,043 --> 00:00:56,411 AS WE WORK TO LEARN MORE ABOUT 25 00:00:56,411 --> 00:00:59,714 THESE DISEASES, THE NIAMS 26 00:00:59,714 --> 00:01:01,716 COALITION AND IT'S NEARLY 100 27 00:01:01,716 --> 00:01:03,685 MEMBER ORGANIZATION HAVE BEEN 28 00:01:03,685 --> 00:01:05,487 TREMENDOUS ALLIES OF NIAMS AND 29 00:01:05,487 --> 00:01:05,921 THE NIH. 30 00:01:05,921 --> 00:01:08,023 WE VALUE BRINGING THIS GROUP 31 00:01:08,023 --> 00:01:09,457 TOGETHER EVERY TWO YEARS FOR 32 00:01:09,457 --> 00:01:11,293 THIS MEETING AND LOOK FORWARD TO 33 00:01:11,293 --> 00:01:12,928 CONTINUING TO WORK WITH YOU TO 34 00:01:12,928 --> 00:01:15,764 BUILD ON OUR COMMON GOAL OF 35 00:01:15,764 --> 00:01:16,398 TURNING DISCOVERY INTO PUBLIC 36 00:01:16,398 --> 00:01:16,698 HEALTH. 37 00:01:16,698 --> 00:01:19,234 TODAY WE HAVE A GREAT PROGRAM IN 38 00:01:19,234 --> 00:01:19,434 STORE. 39 00:01:19,434 --> 00:01:21,069 YOU'LL HEAR FROM INFLUENTIAL 40 00:01:21,069 --> 00:01:23,838 LEADERS FROM ACROSS NIH PROGRAMS 41 00:01:23,838 --> 00:01:24,773 AND BEYOND AS WELL AS 42 00:01:24,773 --> 00:01:26,675 INFORMATIVE BREAKOUT SESSIONS 43 00:01:26,675 --> 00:01:28,577 LED BY NIAMS' PROGRAM DIRECTORS 44 00:01:28,577 --> 00:01:31,780 AND YOUR OWN COALITION 45 00:01:31,780 --> 00:01:32,147 COLLEAGUES. 46 00:01:32,147 --> 00:01:33,481 THIS MEETING IS INTERACTIVE. 47 00:01:33,481 --> 00:01:35,584 DUE TO THE AMOUNT OF NETWORKING 48 00:01:35,584 --> 00:01:36,885 ACTIVITIES AND SESSION WE BUILT 49 00:01:36,885 --> 00:01:38,720 IN THE AGENDA WE'LL BE MOVING TO 50 00:01:38,720 --> 00:01:40,121 VARIOUS ROOMS AND ORGANIZING 51 00:01:40,121 --> 00:01:43,692 INTO GROUPS THROUGHOUT THE DAY. 52 00:01:43,692 --> 00:01:44,659 THERE WILL ALSO BE OPPORTUNITIES 53 00:01:44,659 --> 00:01:45,727 TO NETWORK AND LEARN FROM ONE 54 00:01:45,727 --> 00:01:46,828 ANOTHER AT THE POSTER SESSION 55 00:01:46,828 --> 00:01:48,663 AND DURING BREAKS AND LUNCH. 56 00:01:48,663 --> 00:01:51,232 SO BEFORE WE BEGIN, I WOULD 57 00:01:51,232 --> 00:01:53,468 FIRST LIKE TO ACKNOWLEDGE THE 58 00:01:53,468 --> 00:01:54,603 NIAMS LEADERSHIP AND STAFF WHO 59 00:01:54,603 --> 00:01:55,570 ARE HERE TODAY. 60 00:01:55,570 --> 00:01:58,406 IT'S WONDERFUL TO SEE ALL OF 61 00:01:58,406 --> 00:01:59,040 YOU. 62 00:01:59,040 --> 00:02:01,309 WE WOULD ALSO LIKE TO 63 00:02:01,309 --> 00:02:03,778 ACKNOWLEDGE THE TIRELESS WORK OF 64 00:02:03,778 --> 00:02:05,380 THE COALITION PLANNING 65 00:02:05,380 --> 00:02:09,017 COMMITTEE, TRISHA, EVAN AND 66 00:02:09,017 --> 00:02:12,053 LAUREN WHO HELPED PLAN FOR THIS 67 00:02:12,053 --> 00:02:12,854 MEETING. 68 00:02:12,854 --> 00:02:14,856 I'D ALSO LIKE TO RECOGNIZE THE 69 00:02:14,856 --> 00:02:17,192 NIAMS STAFF WHO WORKS WITH THE 70 00:02:17,192 --> 00:02:18,693 LEADERSHIP TO PUT TOGETHER THE 71 00:02:18,693 --> 00:02:18,927 PROGRAM. 72 00:02:18,927 --> 00:02:21,096 IT'S WAS A COLLABORATIVE TEAM 73 00:02:21,096 --> 00:02:24,866 EFFORT BUT SPECIAL THANKS GO TO 74 00:02:24,866 --> 00:02:33,108 COLLEEN, SARA, LESLIE, BEATA AND 75 00:02:33,108 --> 00:02:34,242 COLLEEN WHO LED THE CHARGE. 76 00:02:34,242 --> 00:02:36,978 I WANT TO EXTEND OUR 77 00:02:36,978 --> 00:02:39,481 APPRECIATION OUR CONTRACT 78 00:02:39,481 --> 00:02:44,819 SUPPORT COLLEAGUES LED MY NATE 79 00:02:44,819 --> 00:02:45,453 ROBINSON INSTRUMENTAL IN THE 80 00:02:45,453 --> 00:02:49,424 SUCCESS AND MANY THANKS TO THE 81 00:02:49,424 --> 00:02:52,861 CORRELATION ORGANIZATIONS WHO 82 00:02:52,861 --> 00:02:55,830 PROVIDED BREAKFAST, LUNCH AND 83 00:02:55,830 --> 00:03:00,335 REFRESHMANMENTSS -- REFRESHMENS 84 00:03:00,335 --> 00:03:04,739 THROUGHOUT THE DAY AND NOW 85 00:03:04,739 --> 00:03:05,840 COLLEEN LENDA. 86 00:03:05,840 --> 00:03:07,075 >> GOOD MORNING, EVERYONE. 87 00:03:07,075 --> 00:03:09,044 IT'S SO WONDERFUL TO SEE SO MANY 88 00:03:09,044 --> 00:03:10,745 FAMILIAR FACES AND SO OF YOU WE 89 00:03:10,745 --> 00:03:12,647 HAVEN'T MET IN PERSON AND IT'S 90 00:03:12,647 --> 00:03:13,314 JUST SO NICE TO SEE EVERYONE IN 91 00:03:13,314 --> 00:03:14,683 PERSON. 92 00:03:14,683 --> 00:03:20,955 I'M GOING TO COVER A FEW 93 00:03:20,955 --> 00:03:21,790 HOUSEKEEPING ITEMS AND 94 00:03:21,790 --> 00:03:22,891 TRANSITION TO OUR PLENARY 95 00:03:22,891 --> 00:03:23,124 SESSION. 96 00:03:23,124 --> 00:03:24,459 A REMINDER THIS IS RECORD. 97 00:03:24,459 --> 00:03:26,761 IF YOU DIDN'T WANT YOUR PHOTO 98 00:03:26,761 --> 00:03:27,796 TAKEN OR ANY RECORDING YOU 99 00:03:27,796 --> 00:03:28,863 SHOULD HAVE RECEIVED SOMETHING 100 00:03:28,863 --> 00:03:30,498 ON YOUR BADGE WHEN YOU CAME IN 101 00:03:30,498 --> 00:03:34,369 SO STOP AT REGISTRATION IF NOT. 102 00:03:34,369 --> 00:03:35,904 ADDITIONALLY, IF YOU COULD JUST 103 00:03:35,904 --> 00:03:37,172 MAKE SURE YOU'RE PHONE IS ON 104 00:03:37,172 --> 00:03:40,108 SILENT FOR OUR SESSIONS, THAT 105 00:03:40,108 --> 00:03:40,842 WOULD BE TERRIFIC. 106 00:03:40,842 --> 00:03:43,845 THE BATHROOMS ARE ON THE RIGHT 107 00:03:43,845 --> 00:03:46,481 AND LEFT-HAND SIDE OF THE BACK 108 00:03:46,481 --> 00:03:49,217 OF THE MEETING SPACE. 109 00:03:49,217 --> 00:03:50,485 NEXT YOU'LL NOTICE TENT CARDS ON 110 00:03:50,485 --> 00:03:52,087 EACH OF THE TABLE. 111 00:03:52,087 --> 00:03:55,090 USE THE QR CODES TO CONNECT AND 112 00:03:55,090 --> 00:03:55,824 ENGAGE. 113 00:03:55,824 --> 00:03:57,392 WE'RE USING THE HASH TAG NIAMS 114 00:03:57,392 --> 00:03:58,460 COALITION DAY AND GO ON SOCIAL 115 00:03:58,460 --> 00:03:59,794 MEDIA AND SHARE ABOUT THE 116 00:03:59,794 --> 00:04:03,398 MEETING, TAKE PHOTOS WITH EACH 117 00:04:03,398 --> 00:04:04,365 OTHER AND SHARE AS MUCH AS YOU 118 00:04:04,365 --> 00:04:07,535 CAN AND WE'LL HAVE IN YOUR 119 00:04:07,535 --> 00:04:08,336 PACKET AN EVALUATION FORM WHICH 120 00:04:08,336 --> 00:04:11,005 IS GOING TO HELP US TO LEARN 121 00:04:11,005 --> 00:04:11,873 MORE ABOUT HOW YOU FEEL ABOUT 122 00:04:11,873 --> 00:04:13,641 EACH OF THE SESSIONS AND WE DO 123 00:04:13,641 --> 00:04:15,677 PAY ATTENTION TO THAT FEEDBACK 124 00:04:15,677 --> 00:04:16,978 SO PLEASE TAKE SOME TIME TO FILL 125 00:04:16,978 --> 00:04:18,580 THAT OUT AND YOU CAN RETURN IT 126 00:04:18,580 --> 00:04:19,547 TO THE REGISTRATION DESK AT THE 127 00:04:19,547 --> 00:04:21,116 ENDS OF THE DAY. 128 00:04:21,116 --> 00:04:22,917 -- END OF THE DAY. 129 00:04:22,917 --> 00:04:23,818 FOR Q&A THROUGHOUT THE DAY IN 130 00:04:23,818 --> 00:04:25,754 THIS ROOM IF YOU HAVE A QUESTION 131 00:04:25,754 --> 00:04:27,388 JUST RAISE YOUR HAND AND WE HAVE 132 00:04:27,388 --> 00:04:28,656 WONDERFUL STAFF ON THE SIDELINE 133 00:04:28,656 --> 00:04:30,658 ARE GOING TO BRING THE 134 00:04:30,658 --> 00:04:31,359 MICROPHONE OVER FOR YOU. 135 00:04:31,359 --> 00:04:33,261 DON'T NEED TO MOVE AT ALL. 136 00:04:33,261 --> 00:04:35,130 FOR THE BREAKOUT SESSIONS WHICH 137 00:04:35,130 --> 00:04:36,498 WILL BE IN SMALLER ROOMS YOU'RE 138 00:04:36,498 --> 00:04:39,067 NOT GOING IT NEED ANY 139 00:04:39,067 --> 00:04:40,502 MICROPHONES SO YOU CAN ASK YOUR 140 00:04:40,502 --> 00:04:42,303 QUESTION IN SPACE. 141 00:04:42,303 --> 00:04:43,972 THEY'RE SMALLER SPACES. 142 00:04:43,972 --> 00:04:46,508 NOW THE HOUSEKEEPING IS TAKEN 143 00:04:46,508 --> 00:04:49,511 CARE OF I'M PLEASED TO INTRODUCE 144 00:04:49,511 --> 00:04:55,116 TRISHA AND LEE GROSSMAN. 145 00:04:55,116 --> 00:04:57,685 TRISHA WORKS WITH VARIOUS 146 00:04:57,685 --> 00:04:58,620 STAKEHOLDERS TO ADVANCE THE 147 00:04:58,620 --> 00:05:01,489 MISSION TO SUPPORT PATIENTS AND 148 00:05:01,489 --> 00:05:03,224 ACCELERATE RESEARCH. 149 00:05:03,224 --> 00:05:07,595 SHE CURRENTLY SERVES ON DREXEL 150 00:05:07,595 --> 00:05:09,631 UNIVERSITY'S HEALTH 151 00:05:09,631 --> 00:05:10,832 ADMINISTRATION DEPARTMENT 152 00:05:10,832 --> 00:05:11,933 ADVISORY COUNCIL AND STARING 153 00:05:11,933 --> 00:05:12,200 COMMITTEE. 154 00:05:12,200 --> 00:05:14,502 SHE DEDICATED HER CAREER TO 155 00:05:14,502 --> 00:05:18,406 IMPROVING THE LIVES WITH THOSE 156 00:05:18,406 --> 00:05:20,608 WITH RARE DISEASE AND WITH OTHER 157 00:05:20,608 --> 00:05:23,978 CORRELATION WORK HERE. 158 00:05:23,978 --> 00:05:31,820 THE CO-CHAIR LEE GROSSMAN BUILDS 159 00:05:31,820 --> 00:05:33,488 IMPORTANT PARTNERSHIP TO ADVANCE 160 00:05:33,488 --> 00:05:37,492 THE OREFs MISSION. 161 00:05:37,492 --> 00:05:43,097 SHE'S -- HE'S A PRESENTER ON 162 00:05:43,097 --> 00:05:44,332 CHRONIC HEALTH CONDITIONS AND 163 00:05:44,332 --> 00:05:45,066 MENTAL HEALTH. 164 00:05:45,066 --> 00:05:47,936 IT'S BEEN AN ABSOLUTE HONOR 165 00:05:47,936 --> 00:05:49,704 WORKING WITH TRISHA AND LEE AND 166 00:05:49,704 --> 00:05:51,673 OTHER COALITION MEMBERS OVER THE 167 00:05:51,673 --> 00:05:52,207 PAST SIX YEARS. 168 00:05:52,207 --> 00:05:54,976 I'M NOW GOING TO TURN IT OVER TO 169 00:05:54,976 --> 00:05:57,545 TRISHA AND LEE TO INTRODUCE OUR 170 00:05:57,545 --> 00:06:04,752 FIRST SPEAKER. 171 00:06:04,752 --> 00:06:06,087 >> SO WELCOME EVERYONE. 172 00:06:06,087 --> 00:06:11,192 WE'RE SO EXCITED TO SEE 173 00:06:11,192 --> 00:06:16,464 EVERYBODY HERE. 174 00:06:16,464 --> 00:06:17,498 WE'RE HOPE YOU'LL HAVE 175 00:06:17,498 --> 00:06:18,933 CONNECTIONS BY THE END OF THE 176 00:06:18,933 --> 00:06:19,500 DAY. 177 00:06:19,500 --> 00:06:20,435 HOPEFULLY YOU'LL KNOW LOTS OF 178 00:06:20,435 --> 00:06:22,637 PEOPLE YOU DIDN'T BEFORE AND BE 179 00:06:22,637 --> 00:06:25,106 ABLE TO BUILD THAT OUT. 180 00:06:25,106 --> 00:06:26,174 WE'RE NOT GOING TO TAKE UP TOO 181 00:06:26,174 --> 00:06:27,609 MUCH TIME BECAUSE WE'LL BE 182 00:06:27,609 --> 00:06:28,676 PRESENTING LATER BUT WELCOME TO 183 00:06:28,676 --> 00:06:29,043 YOU ALL. 184 00:06:29,043 --> 00:06:30,445 WE'RE EXCITED TO GET STARTED AND 185 00:06:30,445 --> 00:06:31,679 WITH THAT I'M GOING TO PASS IT 186 00:06:31,679 --> 00:06:33,882 OVER TO LEE WHO WILL INTRODUCE 187 00:06:33,882 --> 00:06:35,250 OUR FIRST SPEAKER. 188 00:06:35,250 --> 00:06:36,050 >> THROUGHOUT THIS MORNING 189 00:06:36,050 --> 00:06:39,254 YOU'LL SEE THAT TRISHA ANDRY 190 00:06:39,254 --> 00:06:41,022 DOING TAG TEAM QUITE A BIT SO 191 00:06:41,022 --> 00:06:42,023 WE'LL BE GOING BACK AND FORTH 192 00:06:42,023 --> 00:06:43,191 BUT GOOD MORNING EVERYONE. 193 00:06:43,191 --> 00:06:46,327 IT'S WONDERFUL TO SEE YOU HERE. 194 00:06:46,327 --> 00:06:48,663 IT'S BEEN A LONG HAUL OVER THE 195 00:06:48,663 --> 00:06:49,497 LAST FEW YEARS. 196 00:06:49,497 --> 00:06:50,965 LIFE HAS CHANGED DRAMATICALLY 197 00:06:50,965 --> 00:06:52,000 AND IT'S GREAT TO HAVE US ALL 198 00:06:52,000 --> 00:06:55,236 HERE IN PERSON AGAIN. 199 00:06:55,236 --> 00:06:58,940 HAVE THE UNIQUE HONOR OF 200 00:06:58,940 --> 00:06:59,874 INTRODUCING OUR FIRST SPEAKER 201 00:06:59,874 --> 00:07:07,248 TODAY AND THAT'S DR. LINDSEY 202 00:07:07,248 --> 00:07:08,950 CRISWELL THE DIRECTOR OF NIAMS 203 00:07:08,950 --> 00:07:10,785 AND WILL PROVIDE THE STATE OF 204 00:07:10,785 --> 00:07:11,586 THE INSTITUTE. 205 00:07:11,586 --> 00:07:13,488 SHE'S OVERSEES THE INSTITUTE'S 206 00:07:13,488 --> 00:07:19,193 ANNUAL BUDGET OF MORE THAN $685 207 00:07:19,193 --> 00:07:19,894 MILLION WHICH SUPPORTS RESEARCH 208 00:07:19,894 --> 00:07:24,866 INTO THE CAUSES, PREVENTION OF 209 00:07:24,866 --> 00:07:29,470 ARTHRITIS AND MUSCULOSKELETAL 210 00:07:29,470 --> 00:07:33,308 SKIN DISEASES. 211 00:07:33,308 --> 00:07:36,444 SHE WAS AT CALIFORNIA SAN 212 00:07:36,444 --> 00:07:40,114 FRANCISCO AND IS A CERTIFIED 213 00:07:40,114 --> 00:07:45,586 RHEUMATOLOGIST AND SHE IS A 214 00:07:45,586 --> 00:07:48,056 PRINCIPLE INVESTIGATOR OF 215 00:07:48,056 --> 00:07:49,691 MULTIPLE NIH GRANTS AND 216 00:07:49,691 --> 00:07:51,225 PUBLISHED MORE THAN 250 217 00:07:51,225 --> 00:07:51,960 PEER-REVIEWED PAPERS. 218 00:07:51,960 --> 00:07:55,496 HER RESEARCH FOCUSES ON THE 219 00:07:55,496 --> 00:07:58,232 GENETICS AND EPIDEMIOLOGY OF 220 00:07:58,232 --> 00:07:59,167 HUMAN AUTOIMMUNE DISEASE AND IN 221 00:07:59,167 --> 00:08:02,136 2021 WAS ELECTED TO THE 222 00:08:02,136 --> 00:08:03,237 ASSOCIATION OF AMERICAN 223 00:08:03,237 --> 00:08:06,507 PHYSICIANS, AN HONOR EXTENDED TO 224 00:08:06,507 --> 00:08:09,043 PHYSICIANS WITH OUTSTANDING 225 00:08:09,043 --> 00:08:10,144 CREDENTIALS IN BIOMEDICAL 226 00:08:10,144 --> 00:08:10,678 RESEARCH. 227 00:08:10,678 --> 00:08:13,381 ON A PERSONAL NOTE I'VE BEEN TO 228 00:08:13,381 --> 00:08:14,582 NUMEROUS ORTHOPEDIC MEETINGS 229 00:08:14,582 --> 00:08:17,151 THIS YEAR AND HAVE BEEN ABLE TO 230 00:08:17,151 --> 00:08:19,053 ENGAGE WITH DR. CRISWELL AND 231 00:08:19,053 --> 00:08:21,456 FIND HER EXTREMELY ENGAGING AND 232 00:08:21,456 --> 00:08:23,091 OPEN AND ACCESSIBLE. 233 00:08:23,091 --> 00:08:25,226 THESE ARE TREMENDOUS TRAITS FOR 234 00:08:25,226 --> 00:08:26,894 ANY LEADER AND ONE OF THE 235 00:08:26,894 --> 00:08:29,063 REASONS WHY SHE MAKES SUCH A 236 00:08:29,063 --> 00:08:30,565 WONDERFUL PARTNER TO THE NIAMS 237 00:08:30,565 --> 00:08:30,832 COALITION. 238 00:08:30,832 --> 00:08:34,268 SO ON BEHALF OF THE NIAMS 239 00:08:34,268 --> 00:08:36,904 COALITION, PLEASE ACCEPT OUR 240 00:08:36,904 --> 00:08:38,906 WARM WELCOME AND WE ARE ANXIOUS 241 00:08:38,906 --> 00:08:39,474 TO HEAR THE STATE OF THE 242 00:08:39,474 --> 00:08:39,741 INSTITUTE. 243 00:08:39,741 --> 00:08:49,917 THANK YOU. 244 00:09:10,138 --> 00:09:15,009 >> SO, WELL, MORNING. 245 00:09:15,009 --> 00:09:17,045 AND LET ME SEE -- I DON'T WANT 246 00:09:17,045 --> 00:09:18,079 DO CREATE BIG ECHO. 247 00:09:18,079 --> 00:09:21,382 VERY NICE TO SEE YOU ALL. 248 00:09:21,382 --> 00:09:23,084 MY FIRST IN PERSON OUTREACH AND 249 00:09:23,084 --> 00:09:23,584 EDUCATION DAY. 250 00:09:23,584 --> 00:09:26,354 IT'S A PLEASURE TO MEET SOME OF 251 00:09:26,354 --> 00:09:27,555 YOU I HAVEN'T HAD THE 252 00:09:27,555 --> 00:09:28,222 OPPORTUNITY TO MEET IN PERSON 253 00:09:28,222 --> 00:09:30,058 AND WE'RE GRATEFUL FOR YOUR 254 00:09:30,058 --> 00:09:30,291 SUPPORT. 255 00:09:30,291 --> 00:09:31,859 THANKS TO TRISHA AND LEE FOR THE 256 00:09:31,859 --> 00:09:32,960 KIND INTRODUCTION. 257 00:09:32,960 --> 00:09:35,163 IT'S AN HONOR TO BE GIVING THIS 258 00:09:35,163 --> 00:09:36,831 STATE OF THE INSTITUTE ADDRESS 259 00:09:36,831 --> 00:09:38,232 TODAY AND I'M DELIGHTED TO HAVE 260 00:09:38,232 --> 00:09:40,635 ALL OF YOU HERE ON THE NIH 261 00:09:40,635 --> 00:09:40,868 CAMPUS. 262 00:09:40,868 --> 00:09:43,204 NEEDLESS TO SAY THIS MEETING IS 263 00:09:43,204 --> 00:09:44,705 POSSIBLE DUE TO THE DEDICATED 264 00:09:44,705 --> 00:09:46,340 EFFORTS OF NUMEROUS PEOPLE AND I 265 00:09:46,340 --> 00:09:48,743 HAVE TIME TO MENTION ONLY A FEW 266 00:09:48,743 --> 00:09:53,347 OF THEM HERE BUT WANTED TO 267 00:09:53,347 --> 00:10:00,354 PARTICULARLY THANK MS. DUNNDAS 268 00:10:00,354 --> 00:10:01,856 AND THE NIAMS COALITION 269 00:10:01,856 --> 00:10:03,891 CO-CHAIRS YOU JUST HEARD FROM 270 00:10:03,891 --> 00:10:05,793 TRISHA LEE AND LEE GROSSMAN. 271 00:10:05,793 --> 00:10:09,397 I'D LIKE TO THANK ALL MEMBERS OF 272 00:10:09,397 --> 00:10:14,302 THE ORGANIZING COMMITTEE AND 273 00:10:14,302 --> 00:10:17,071 CO-SPONSORS FOR THEIR 274 00:10:17,071 --> 00:10:17,472 GENEROSITY. 275 00:10:17,472 --> 00:10:18,706 I APPRECIATE THE STEERING 276 00:10:18,706 --> 00:10:19,874 COMMITTEE MEMBERS. 277 00:10:19,874 --> 00:10:21,476 I KNOW YOU PLAY A CRITICAL ROLE 278 00:10:21,476 --> 00:10:23,978 IN SUPPORTING THE CO-CHAIRS AND 279 00:10:23,978 --> 00:10:25,480 LEADING THE COALITION. 280 00:10:25,480 --> 00:10:27,548 I'LL DO A QUICK CHECK THE SOUND 281 00:10:27,548 --> 00:10:28,483 IS OKAY. 282 00:10:28,483 --> 00:10:31,886 IT SOUNDS ECHOEY UP HERE BUT 283 00:10:31,886 --> 00:10:33,154 OKAY IN THE BACK? 284 00:10:33,154 --> 00:10:34,155 ALL RIGHT. 285 00:10:34,155 --> 00:10:36,057 SO MY TALK TODAY IS ORGANIZED 286 00:10:36,057 --> 00:10:37,258 INTO TWO PARTS. 287 00:10:37,258 --> 00:10:38,893 I'LL START WITH A BRIEF 288 00:10:38,893 --> 00:10:41,496 INTRODUCTION TO THE NIH AS I 289 00:10:41,496 --> 00:10:43,865 UNDERSTAND SOME OF THE GROUPS 290 00:10:43,865 --> 00:10:44,899 ARE NEW TO THE NIAMS COALITION 291 00:10:44,899 --> 00:10:48,803 FOLLOWED BY AN UPDATE ON THE NIH 292 00:10:48,803 --> 00:10:50,538 AND NIAMS BUDGETS BUT THE 293 00:10:50,538 --> 00:10:54,142 MAJORITY WILL PROVIDE AN 294 00:10:54,142 --> 00:10:56,677 OVERVIEW OF NIH AND NIAMS 295 00:10:56,677 --> 00:10:57,745 ACTIVES OF POTENTIAL INTEREST TO 296 00:10:57,745 --> 00:10:58,012 YOU. 297 00:10:58,012 --> 00:11:00,414 AS YOU MIGHT KNOW, NIAMS IS ONE 298 00:11:00,414 --> 00:11:03,284 OF 27 INSTITUTES AND CENTERS 299 00:11:03,284 --> 00:11:04,952 THAT COMPRISE THE NIH. 300 00:11:04,952 --> 00:11:07,889 AND I CONSIDER THESE SIBLING 301 00:11:07,889 --> 00:11:13,161 INSTITUTES AND CENTERS AS AN 302 00:11:13,161 --> 00:11:16,330 INVALUABLE ASSET AND WE'RE 303 00:11:16,330 --> 00:11:18,566 LOOKING TO ESTABLISH PARTNERSHIP 304 00:11:18,566 --> 00:11:19,834 AND LEVERAGE OPPORTUNITIES OF 305 00:11:19,834 --> 00:11:21,536 COMMON INTEREST. 306 00:11:21,536 --> 00:11:23,504 LIKE THE REST NIH, NIAMS INVESTS 307 00:11:23,504 --> 00:11:26,440 MOST OF THE MONEY AT 308 00:11:26,440 --> 00:11:28,209 INSTITUTIONS AROUND THE COUNTRY 309 00:11:28,209 --> 00:11:30,945 APPROXIMATELY 11% GOES IT OUR 310 00:11:30,945 --> 00:11:32,513 INTRAMURAL RESEARCH PROGRAM HERE 311 00:11:32,513 --> 00:11:36,517 IN BETHESDA AND THE SLICE YOU 312 00:11:36,517 --> 00:11:39,720 SEE RMS, RESEARCH AND MANAGEMENT 313 00:11:39,720 --> 00:11:41,989 SUPPORT IS WHAT YOUR 314 00:11:41,989 --> 00:11:42,890 ORGANIZATIONS WOULD CALL 315 00:11:42,890 --> 00:11:43,624 OVERHEAD. 316 00:11:43,624 --> 00:11:46,194 YOU CAN SEE WITH THE TWO PIE 317 00:11:46,194 --> 00:11:48,162 CHARTS THE INSTITUTE'S 318 00:11:48,162 --> 00:11:48,896 INVESTMENT IN INTRAMURAL 319 00:11:48,896 --> 00:11:50,298 RESEARCH AND THE RMS EXPENSES 320 00:11:50,298 --> 00:11:55,436 ARE ON PAR WITH THE ENTIRE NIH 321 00:11:55,436 --> 00:11:58,372 AND THE EXTRAMURAL INVESTMENTS 322 00:11:58,372 --> 00:12:00,141 SLIGHTLY LARGER. 323 00:12:00,141 --> 00:12:05,479 SO THIS SLIDE BRIEFLY EXPLAINS 324 00:12:05,479 --> 00:12:07,081 HOW THE NIH EXTRAMURAL WITH 325 00:12:07,081 --> 00:12:10,551 GRANT PROPOSALS ARE EVALUATED 326 00:12:10,551 --> 00:12:10,751 WORKS. 327 00:12:10,751 --> 00:12:13,688 THE APPLICANT DEVELOPS AN 328 00:12:13,688 --> 00:12:19,427 ORIGINAL IDEA AND SUBMITS AND 329 00:12:19,427 --> 00:12:21,395 THE EXPERTS REVIEW THE 330 00:12:21,395 --> 00:12:21,729 APPLICATIONS. 331 00:12:21,729 --> 00:12:25,099 NOW, THE FIRST LEVEL OF PEER 332 00:12:25,099 --> 00:12:27,034 REVIEW IS ESSENTIAL FOR LETTING 333 00:12:27,034 --> 00:12:27,735 INVESTIGATORS AND THE INSTITUTE 334 00:12:27,735 --> 00:12:29,470 INFORMATION THE STRENGTHS AND 335 00:12:29,470 --> 00:12:32,039 THE WEAKNESSES OF THE PROPOSED 336 00:12:32,039 --> 00:12:32,306 PROJECTS. 337 00:12:32,306 --> 00:12:33,608 BUT BEFORE AN INSTITUTE OR 338 00:12:33,608 --> 00:12:35,876 CENTER CAN FUND AN APPLICATION, 339 00:12:35,876 --> 00:12:37,178 IT MUST UNDER GO A SECOND LEVEL 340 00:12:37,178 --> 00:12:40,414 OF PEER REVIEW BY ITS ADVISORY 341 00:12:40,414 --> 00:12:40,681 COUNCIL. 342 00:12:40,681 --> 00:12:42,550 ADVISORY COUNCIL MEMBERS ARE 343 00:12:42,550 --> 00:12:43,384 APPOINTED BY THE SECRETARY OF 344 00:12:43,384 --> 00:12:45,453 THE DEPARTMENT OF HUMAN HEALTH 345 00:12:45,453 --> 00:12:47,655 AND SERVICES AND INCLUDE MEMBERS 346 00:12:47,655 --> 00:12:49,490 OF THE PUBLIC SUCH AS 347 00:12:49,490 --> 00:12:50,625 REPRESENTATIVES OF 348 00:12:50,625 --> 00:12:53,828 PATIENT-FOCUSSED ORGANIZATIONS. 349 00:12:53,828 --> 00:12:55,596 AND SCIENTIFIC AND LAY MEMBERS 350 00:12:55,596 --> 00:12:58,232 ARE SELECTED FOR DIVERSITY OF 351 00:12:58,232 --> 00:13:01,869 INTEREST, WIDE GEOGRAPHICAL 352 00:13:01,869 --> 00:13:02,770 REPRESENTATION AND THE ABILITY 353 00:13:02,770 --> 00:13:04,472 TO TAKE IN THE ISSUES THAT COME 354 00:13:04,472 --> 00:13:06,040 BEFORE THE BODY. 355 00:13:06,040 --> 00:13:09,443 SO NOW MOVING ON TO THE NIH AND 356 00:13:09,443 --> 00:13:10,711 NIAMS BUDGET. 357 00:13:10,711 --> 00:13:13,080 ON MARCH 9 PRESIDENT BIDEN 358 00:13:13,080 --> 00:13:15,750 RELEASED HIS FISCAL YEAR 2024 359 00:13:15,750 --> 00:13:17,418 BUDGET REQUEST TO CONGRESS. 360 00:13:17,418 --> 00:13:21,455 THE AMOUNT FOR NIH IS $51.1 361 00:13:21,455 --> 00:13:25,459 BILLION AN INCREASE OF 3.9% OVER 362 00:13:25,459 --> 00:13:27,662 THE FISCAL YEAR 2023 ENACTED 363 00:13:27,662 --> 00:13:27,895 BUDGET. 364 00:13:27,895 --> 00:13:29,964 FOR NIAMS THE AMOUNT IS $688 365 00:13:29,964 --> 00:13:31,899 MILLION WHICH REPRESENTS NO 366 00:13:31,899 --> 00:13:34,669 CHANGE FROM FISCAL YEAR 2023. 367 00:13:34,669 --> 00:13:36,304 THAT'S THE CURRENT YEAR. 368 00:13:36,304 --> 00:13:37,905 NOW, SINCE THEN THE HOUSE AND 369 00:13:37,905 --> 00:13:39,840 SENATE HAVE RELEASED THEIR OWN 370 00:13:39,840 --> 00:13:41,008 BUDGET PROPOSALS. 371 00:13:41,008 --> 00:13:43,377 AND IN A TIME WHEN MANY AGENCIES 372 00:13:43,377 --> 00:13:44,712 ARE FACING THE PROSPECT OF 373 00:13:44,712 --> 00:13:45,980 BUDGET CUTS WE'RE GRATEFUL TO 374 00:13:45,980 --> 00:13:48,049 THE AMERICAN PUBLIC AND OUR 375 00:13:48,049 --> 00:13:51,485 ELECTED OFFICIALS FOR KEEPING 376 00:13:51,485 --> 00:13:53,321 ARTHRITIS AND MUSCULOSKELETAL 377 00:13:53,321 --> 00:13:54,889 AND SKIN DISEASES AS A PRIORITY. 378 00:13:54,889 --> 00:13:57,358 AS NEXT STEP THE HOUSE AND 379 00:13:57,358 --> 00:13:59,260 SENATE MUST CONVENE A CONFERENCE 380 00:13:59,260 --> 00:14:01,295 COMMITTEE WHERE THEY AGREE ON 381 00:14:01,295 --> 00:14:02,830 NUMBERS NOT JUST FOR NIH BUT THE 382 00:14:02,830 --> 00:14:04,065 ENTIRE DEPARTMENT OF HEALTH AND 383 00:14:04,065 --> 00:14:05,833 HUMAN SERVICES AS WELL AS THE 384 00:14:05,833 --> 00:14:06,801 DEPARTMENTS OF LABOR AND 385 00:14:06,801 --> 00:14:07,301 EDUCATION. 386 00:14:07,301 --> 00:14:08,836 AND THEN THAT VERSION OF THE 387 00:14:08,836 --> 00:14:10,971 BILL MUST PASS BOTH CHAMBERS 388 00:14:10,971 --> 00:14:13,507 BEFORE GOING TO THE PRESIDENT 389 00:14:13,507 --> 00:14:15,676 FOR SIGNATURE. 390 00:14:15,676 --> 00:14:18,479 NOW, THIS MAY OR MAY NOT OCCUR 391 00:14:18,479 --> 00:14:20,781 BEFORE OUR CURRENT FISCAL YEAR 392 00:14:20,781 --> 00:14:23,718 ENDS SEPTEMBER 30 SO WE WON'T BE 393 00:14:23,718 --> 00:14:25,953 SURPRISED IF WE BEGIN FISCAL 394 00:14:25,953 --> 00:14:28,122 2024 ON A CONTINUED RESOLUTION, 395 00:14:28,122 --> 00:14:29,824 HOPEFULLY, AND THIS MEANS WE CAN 396 00:14:29,824 --> 00:14:31,559 CONTINUE TO OPERATE AT OR 397 00:14:31,559 --> 00:14:37,498 SLIGHTLY BELOW OUR FISCAL YEAR 398 00:14:37,498 --> 00:14:38,899 2023 LEVEL. 399 00:14:38,899 --> 00:14:40,668 SO WE'RE ALWAYS EXPLORING 400 00:14:40,668 --> 00:14:42,403 OPPORTUNITIES TO BROADEN OUR 401 00:14:42,403 --> 00:14:44,872 RESOURCES SUPPORTING ARTHRITIS 402 00:14:44,872 --> 00:14:48,242 AND MUSCULOSKELETAL AND SKIN 403 00:14:48,242 --> 00:14:50,344 DISEASE NOT IN BUT ALSO OUTSIDE 404 00:14:50,344 --> 00:14:54,915 NIH. 405 00:14:54,915 --> 00:14:59,987 IT'S A FABULOUS EXAMPLE OF ONE 406 00:14:59,987 --> 00:15:01,322 PUBLIC-PRIVATE AMONG THE NIH, 407 00:15:01,322 --> 00:15:04,024 FDA AND INDUSTRY AND NON-PROFIT 408 00:15:04,024 --> 00:15:04,925 GROUPS INCLUDING SOME NIAMS 409 00:15:04,925 --> 00:15:05,493 COALITION MEMBERS AND OTHER 410 00:15:05,493 --> 00:15:08,396 ORGANIZATIONS. 411 00:15:08,396 --> 00:15:13,801 OVER THE PAST EIGHT YEARS THE 412 00:15:13,801 --> 00:15:17,471 AMP PROGRAM AND RM LUPUS HAS 413 00:15:17,471 --> 00:15:18,205 MADE PROGRESS IN UNDERSTANDING 414 00:15:18,205 --> 00:15:25,479 THE CELL POPULATIONS AN PATHWAYS 415 00:15:25,479 --> 00:15:29,483 THAT DRIVE THE DISEASES AND WE 416 00:15:29,483 --> 00:15:31,919 GOT INSIGHTS INTO TARGET 417 00:15:31,919 --> 00:15:33,888 IDENTIFICATION AT EARLY DISEASE 418 00:15:33,888 --> 00:15:36,957 STAGES, ENABLING ADDITIONAL 419 00:15:36,957 --> 00:15:39,293 STUDIES USING THE BIO SPECIMENS 420 00:15:39,293 --> 00:15:40,928 COLLECTED AND ADVANCING ANALYTIC 421 00:15:40,928 --> 00:15:42,396 APPROACHES AND TECHNOLOGY. 422 00:15:42,396 --> 00:15:46,100 SO BUILDING ON THIS SUCCESS, THE 423 00:15:46,100 --> 00:15:47,568 AMP AUTOIMMUNE AND IMMUNE 424 00:15:47,568 --> 00:15:50,171 MEDIATED PROGRAM WAS LAUNCHED IN 425 00:15:50,171 --> 00:15:50,371 2021. 426 00:15:50,371 --> 00:15:53,474 AMP AIM AS WE REFER TO IT 427 00:15:53,474 --> 00:16:04,018 EXTENDS BEYOND RA AND LUPUS TO 428 00:16:05,019 --> 00:16:06,854 SJOGREN'S DISEASE AND OTHER 429 00:16:06,854 --> 00:16:08,088 DISEASES AND THERAPEUTIC TARGETS 430 00:16:08,088 --> 00:16:11,725 AND BENCHMARK FOR THE MOLECULAR 431 00:16:11,725 --> 00:16:12,693 CLASSIFICATION OF DISEASES, AMP 432 00:16:12,693 --> 00:16:14,728 AIM WILL PUT THE PIECES BACK 433 00:16:14,728 --> 00:16:17,064 TOGETHER TO DISCOVER HOW IMMUNE 434 00:16:17,064 --> 00:16:20,201 CELLS AND CELLS IN THE TISSUES 435 00:16:20,201 --> 00:16:22,570 INACT TO CAUSE INFLAMMATION AND 436 00:16:22,570 --> 00:16:24,405 DISEASE AND ACCELERATE DISEASE 437 00:16:24,405 --> 00:16:24,972 MECHANISMS AND THERAPEUTIC 438 00:16:24,972 --> 00:16:28,576 TARGETS. 439 00:16:28,576 --> 00:16:31,712 NOW, AS WITH AMP, RA AND LUPUS, 440 00:16:31,712 --> 00:16:32,680 COLLABORATION AND TEAM SCIENCE 441 00:16:32,680 --> 00:16:37,485 ARE KEY COMPONENTS OF AMP AIM. 442 00:16:37,485 --> 00:16:39,253 THE PROGRAM BRINGS TOGETHER 443 00:16:39,253 --> 00:16:40,454 MULTI-DISCIPLINARY RESEARCHERS 444 00:16:40,454 --> 00:16:41,489 AND ENGAGES EARLY CAREER 445 00:16:41,489 --> 00:16:43,924 INVESTIGATORS TO DEFINE SHARED 446 00:16:43,924 --> 00:16:45,459 IMMUNE MECHANISMS AMONG THESE 447 00:16:45,459 --> 00:16:46,427 DISORDERS AS WELL AS MECHANISMS 448 00:16:46,427 --> 00:16:49,263 THAT MAY BE UNIQUE TO EACH 449 00:16:49,263 --> 00:16:49,864 DISEASE. 450 00:16:49,864 --> 00:16:50,898 SO WE EXPECT THIS WILL ENABLE 451 00:16:50,898 --> 00:16:55,269 THE DEVELOPMENT OF NEW AND 452 00:16:55,269 --> 00:16:59,240 EFFECTIVE THERAPIES FOR PEOPLE 453 00:16:59,240 --> 00:17:02,643 WITH AUTO IMMUNE DISEASE AND 454 00:17:02,643 --> 00:17:04,678 ADDRESSING CHRONIC DISEASE MORE 455 00:17:04,678 --> 00:17:07,915 GENERALLY. 456 00:17:07,915 --> 00:17:09,483 IMPORTANTLY, THE PROGRAM ALSO 457 00:17:09,483 --> 00:17:15,890 HAS DEVELOPED THE ARTHRITIS AND 458 00:17:15,890 --> 00:17:21,195 AUTOIMMUNE PORTAL TO ACCELERATE 459 00:17:21,195 --> 00:17:22,096 SHARING IN THE RESEARCH 460 00:17:22,096 --> 00:17:22,463 COMMUNITY. 461 00:17:22,463 --> 00:17:23,998 FURTHER, WE THOUGHT YOU MIGHT BE 462 00:17:23,998 --> 00:17:26,333 INTERESTED IN HEARING AN UPDATE 463 00:17:26,333 --> 00:17:28,636 ABOUT THE BESPOKE GENE THERAPY 464 00:17:28,636 --> 00:17:32,239 CONSORTIUM WHICH IS THE LATEST 465 00:17:32,239 --> 00:17:34,008 AMP COMPONENT THAT WAS LAUNCHED 466 00:17:34,008 --> 00:17:35,142 SHORTLY AFTER THE LAST MEETING 467 00:17:35,142 --> 00:17:36,176 IN 2021. 468 00:17:36,176 --> 00:17:40,147 SO BECAUSE GENE THERAPY HAS SUCH 469 00:17:40,147 --> 00:17:41,949 POTENTIAL ACROSS DISEASE SPACES 470 00:17:41,949 --> 00:17:44,718 AND DISORDERS, BDTC APPLICANTS 471 00:17:44,718 --> 00:17:47,321 PROPOSE THE DISEASES TO BE 472 00:17:47,321 --> 00:17:48,188 STUDIED. 473 00:17:48,188 --> 00:17:50,090 SUCCESSFUL APPLICATIONS FOCUS ON 474 00:17:50,090 --> 00:17:51,525 DISEASES AMONG OTHER 475 00:17:51,525 --> 00:17:52,593 CHARACTERISTICS HAVE A CLEARLY 476 00:17:52,593 --> 00:17:54,828 DEFINED PATIENT GROUP ALREADY 477 00:17:54,828 --> 00:17:56,196 ASSEMBLED TO HELP MOVE POTENTIAL 478 00:17:56,196 --> 00:17:57,431 THERAPIES INTO CLINICAL TESTING 479 00:17:57,431 --> 00:18:01,402 AND THE GOAL IS TO GENERATE A 480 00:18:01,402 --> 00:18:04,071 STREAMLINED CLINICAL AND 481 00:18:04,071 --> 00:18:05,139 REGULATORY FRAMEWORK FOR GENE 482 00:18:05,139 --> 00:18:07,107 THERAPY LEADING TO STANDARDIZED, 483 00:18:07,107 --> 00:18:08,075 FASTER AND LESS EXPENSIVE 484 00:18:08,075 --> 00:18:10,444 TREATMENT DEVELOPMENT INSTEAD OF 485 00:18:10,444 --> 00:18:15,082 THE ONE-OFF APPROACHES USED FOR 486 00:18:15,082 --> 00:18:15,583 CURRENT THERAPIES. 487 00:18:15,583 --> 00:18:18,419 IN MAY, THE FOUNDATION FOR THE 488 00:18:18,419 --> 00:18:21,221 NIH OR THE FNIH WHO MANAGES THE 489 00:18:21,221 --> 00:18:25,159 AMP PROGRAM ANNOUNCED THE AMP 490 00:18:25,159 --> 00:18:29,163 BGTC SELECTED EIGHT RARE 491 00:18:29,163 --> 00:18:31,298 DISEASES FOR THE CLINICAL TRIAL 492 00:18:31,298 --> 00:18:33,567 PORTFOLIO BY A PANEL OF EXPERTS 493 00:18:33,567 --> 00:18:35,202 FOLLOWING RIGOROUS SCIENTIFIC 494 00:18:35,202 --> 00:18:40,374 AND TECHNICAL REVIEW USING THE 495 00:18:40,374 --> 00:18:41,375 BGTC ESTABLISHED CRITERIA 496 00:18:41,375 --> 00:18:43,911 INCLUDING THE ADEQUACY OF THE 497 00:18:43,911 --> 00:18:48,616 GENE FOR INSERTION INTO AN ADENO 498 00:18:48,616 --> 00:18:49,183 ASSOCIATED VIRUS VECTOR, 499 00:18:49,183 --> 00:18:51,251 SUFFICIENT PROOF OF CONCEPT AND 500 00:18:51,251 --> 00:18:53,587 NATURAL HISTORY DATA, THE 501 00:18:53,587 --> 00:18:57,024 EXISTENCE OF AN ESTABLISHED 502 00:18:57,024 --> 00:18:58,292 DISEASE MODEL, LACK OF AVAILABLE 503 00:18:58,292 --> 00:19:00,294 TREATMENT AND READINESS FOR 504 00:19:00,294 --> 00:19:01,161 ENTERING INTO CLINICAL TRIAL. 505 00:19:01,161 --> 00:19:02,029 AND AS SHOWN IN THE SLIDE AT 506 00:19:02,029 --> 00:19:07,568 LEAST TWO OF THE DISEASES SELECT 507 00:19:07,568 --> 00:19:13,974 ED ARE OF GREAT INTEREST TO THE 508 00:19:13,974 --> 00:19:18,946 NIAMS COMMUNITY. 509 00:19:18,946 --> 00:19:29,456 MORQUIRO SYNDROME IS A LYSOSOMAL 510 00:19:29,456 --> 00:19:39,900 DISEASE OF CONDROITON AND 511 00:19:44,304 --> 00:19:47,708 PROPIONIC HAS AN ENZYME INVOLVED 512 00:19:47,708 --> 00:19:53,480 IN THE BREAKDOWN OF AMINNOW -- 513 00:19:53,480 --> 00:19:59,286 AMINO ACIDS WITH DIMINISHED 514 00:19:59,286 --> 00:20:01,889 MUSCLE DONE AND DEHYDRATION AND 515 00:20:01,889 --> 00:20:03,924 SEIZURES. 516 00:20:03,924 --> 00:20:05,125 WITH THE SELECT OF THE 517 00:20:05,125 --> 00:20:09,997 CONDITIONS BGTC WILL STREAMLINE 518 00:20:09,997 --> 00:20:13,400 THE PROCESS TO DEVELOP THERAPIES 519 00:20:13,400 --> 00:20:13,901 MORE GENERALIZABLE AND 520 00:20:13,901 --> 00:20:17,471 ACCESSIBLE SO OTHERS CAN 521 00:20:17,471 --> 00:20:17,705 BENEFIT. 522 00:20:17,705 --> 00:20:18,605 WE'RE EXCITE ABOUT THE PROGRESS 523 00:20:18,605 --> 00:20:23,043 AND LOOK FORWARD IT HEARING MORE 524 00:20:23,043 --> 00:20:25,479 FROM DR. GERBERD IG THIS 525 00:20:25,479 --> 00:20:35,622 MORNING. 526 00:20:42,062 --> 00:20:44,431 AND THE AMP CELL BASED THERAPY 527 00:20:44,431 --> 00:20:46,967 CONSORTIUM OR CBTC WILL LEVERAGE 528 00:20:46,967 --> 00:20:51,438 THE BESPOKE GENE THERAPY MODEL. 529 00:20:51,438 --> 00:20:52,372 RESPONSES TO THIS REQUEST 530 00:20:52,372 --> 00:20:53,774 INFORMATION SHOULD BE SUBMITTED 531 00:20:53,774 --> 00:20:55,042 BY SEPTEMBER 25 AND INFORMATION 532 00:20:55,042 --> 00:20:55,709 GATHERED WILL BE DISCUSSED 533 00:20:55,709 --> 00:20:59,947 FURTHER IN A TWO-HOUR WEBINAR 534 00:20:59,947 --> 00:21:00,981 SEPTEMBER 28. 535 00:21:00,981 --> 00:21:02,082 I WANTED TO MAKE SURE THOSE THAT 536 00:21:02,082 --> 00:21:05,486 MAY BE INTERESTED ARE AWARE. 537 00:21:05,486 --> 00:21:08,355 AS NOTED ON THE PROPOSED FISCAL 538 00:21:08,355 --> 00:21:11,225 YEAR 2024 BUDGET SIDE THE 539 00:21:11,225 --> 00:21:16,130 BUDGETS INCLUDE FUNDING FOR 540 00:21:16,130 --> 00:21:17,931 ARPA-H. 541 00:21:17,931 --> 00:21:20,300 ARPA STANDING FOR ADVANCED 542 00:21:20,300 --> 00:21:21,268 RESEARCH PROJECT AGENCY AND THE 543 00:21:21,268 --> 00:21:25,472 H FOR HEALTH IS BASED ON DARPA 544 00:21:25,472 --> 00:21:27,608 WHICH IS THE DEFENSE ADVANCE 545 00:21:27,608 --> 00:21:28,742 RESEARCH PROJECT AGENCY THE 546 00:21:28,742 --> 00:21:29,777 CENTRAL RESEARCH AND DEVELOPMENT 547 00:21:29,777 --> 00:21:32,379 AGENCY FOR THE DEPARTMENT OF 548 00:21:32,379 --> 00:21:32,613 DEFENSE. 549 00:21:32,613 --> 00:21:34,114 SO ARPA-H WOULD USE DARPA AS A 550 00:21:34,114 --> 00:21:37,417 MODEL TO ESTABLISH A CULTURE OF 551 00:21:37,417 --> 00:21:38,952 CHAMPIONING INNOVATIVE IDEAS IN 552 00:21:38,952 --> 00:21:41,488 HEALTH AND MEDICINE BY FOCUSSING 553 00:21:41,488 --> 00:21:43,690 ON MULTIPLE TIME-LIMITED 554 00:21:43,690 --> 00:21:44,224 PROJECTS WITH DIFFERENT 555 00:21:44,224 --> 00:21:46,693 APPROACHES TO ACHIEVE A 556 00:21:46,693 --> 00:21:49,496 QUANTIFIABLE GOAL RELYING ON 557 00:21:49,496 --> 00:21:51,398 DEFINED METRICS AND INJECTING 558 00:21:51,398 --> 00:21:52,032 ACCOUNTABILITY THROUGH MEETING 559 00:21:52,032 --> 00:21:55,502 THE METRICS AND SUPPORTING 560 00:21:55,502 --> 00:21:56,703 USE-DRIVEN IDEAS FOCUSSED ON 561 00:21:56,703 --> 00:21:58,272 SOLVING PRACTICAL PROBLEMS THAT 562 00:21:58,272 --> 00:22:00,874 ADVANCE EQUITY AND RAPIDLY 563 00:22:00,874 --> 00:22:02,810 TRANSFORM BREAKTHROUGHS INTO 564 00:22:02,810 --> 00:22:03,377 TANGIBLE SOLUTIONS FOR ALL 565 00:22:03,377 --> 00:22:09,483 PATIENTS. 566 00:22:09,483 --> 00:22:11,418 ARPA-H ANNOUNCE THE THE FIRST 567 00:22:11,418 --> 00:22:13,887 PROGRAM IN MAY THE NOVEL 568 00:22:13,887 --> 00:22:16,757 REGENERATION FOR TISSUE 569 00:22:16,757 --> 00:22:18,091 REGENERATION WHICH AIMS TO SOLVE 570 00:22:18,091 --> 00:22:19,893 TREATMENT CHALLENGES IN OA. 571 00:22:19,893 --> 00:22:21,862 WE WERE DELIGHTED TO SEE THIS 572 00:22:21,862 --> 00:22:32,306 IDENTIFIED AS A PRIORITY. 573 00:22:32,506 --> 00:22:37,010 NITRO WILL LOOK AT THREE AREAS. 574 00:22:37,010 --> 00:22:38,111 IT WILL FUND SEVERAL RESEARCH 575 00:22:38,111 --> 00:22:39,713 TEAMS TO DEVELOP AND LEVERAGE 576 00:22:39,713 --> 00:22:41,782 INNOVATIVE FORMS OF REGENERATIVE 577 00:22:41,782 --> 00:22:44,184 MEDICINE TO CREATE MINIMALLY 578 00:22:44,184 --> 00:22:47,321 INVASIVE THERAPEUTICS THAT FULLY 579 00:22:47,321 --> 00:22:48,422 REGENERATE DAMAGED JOINTS. 580 00:22:48,422 --> 00:22:52,926 SINCE THE LAUNCH OF NITRO 581 00:22:52,926 --> 00:22:54,261 THERE'S BEEN SEVERAL MORE 582 00:22:54,261 --> 00:22:55,295 PROGRAMS ANNOUNCED FROM ARPA-H 583 00:22:55,295 --> 00:22:57,231 AND HOPE YOU'LL HEAR THEM FROM 584 00:22:57,231 --> 00:22:58,298 THE ARPA-H DIRECTOR WHO WILL BE 585 00:22:58,298 --> 00:23:06,506 SPEAK TO THIS GROUP. 586 00:23:06,506 --> 00:23:13,347 IN ADDITION TO THIS THERE'S 587 00:23:13,347 --> 00:23:15,215 VOLUNTARY PATIENT ORGANIZATIONS 588 00:23:15,215 --> 00:23:24,892 THROUGH THE MDCC THE 589 00:23:24,892 --> 00:23:25,959 MUSCULODYSTROPHY CORE CENTER. 590 00:23:25,959 --> 00:23:27,060 COMMITTEE MEETINGS ARE HELD 591 00:23:27,060 --> 00:23:28,896 TWICE A YEAR AND OPEN TO THE 592 00:23:28,896 --> 00:23:30,764 PUBLIC AND THE ARE WEBCAST FOR 593 00:23:30,764 --> 00:23:33,467 THOSE WHO CAN'T ATTEND IN 594 00:23:33,467 --> 00:23:34,668 PERSON. 595 00:23:34,668 --> 00:23:37,037 TWO-THIRDS OF THE MEMBERS 596 00:23:37,037 --> 00:23:37,971 REPRESENT GOVERNMENT AGENCIES 597 00:23:37,971 --> 00:23:39,439 ONE-THIRD REPRESENT THE PUBLIC 598 00:23:39,439 --> 00:23:42,776 AND PATIENTS, FAMILIES AND 599 00:23:42,776 --> 00:23:44,444 PATIENT ADVOCATES ARE ALWAYS 600 00:23:44,444 --> 00:23:46,647 WELCOME TO ATTEND MEETINGS AND 601 00:23:46,647 --> 00:23:47,281 PROVIDE COMMENTS. 602 00:23:47,281 --> 00:23:52,286 THE MEMBERSHIP HAS A BROAD RANGE 603 00:23:52,286 --> 00:23:59,660 OF EXPERTISE ON MUSCULAR 604 00:23:59,660 --> 00:24:00,594 DYSTROPHY AND THE ISSUES FACING 605 00:24:00,594 --> 00:24:03,463 THE PROVIDERS AND PATIENTS AND 606 00:24:03,463 --> 00:24:04,564 FAMILIES AND CURRENT VIEWS AND 607 00:24:04,564 --> 00:24:05,499 STRATEGIES FOR THE GROUP. 608 00:24:05,499 --> 00:24:06,934 LOOKING TO THE FUTURE, IT'S NOW 609 00:24:06,934 --> 00:24:08,902 TIME TO RENEW THE ACTION PLAN 610 00:24:08,902 --> 00:24:10,938 AND THE COMMITTEE HAS BEGUN 611 00:24:10,938 --> 00:24:12,205 DISCUSSING A PROPOSED APPROACH 612 00:24:12,205 --> 00:24:14,141 WHICH WAS PRESENTED AT THE MOST 613 00:24:14,141 --> 00:24:14,775 RECENT COMMITTEE MEETING HELD IN 614 00:24:14,775 --> 00:24:17,277 APRIL. 615 00:24:17,277 --> 00:24:19,680 THE 2025 ACTION PLAN RENEWAL 616 00:24:19,680 --> 00:24:21,481 WILL INCORPORATE A VARIETY OF 617 00:24:21,481 --> 00:24:24,051 STAKEHOLDER PERSPECTIVES IN 618 00:24:24,051 --> 00:24:26,353 ADDITION, THE COMMITTEE PLANS TO 619 00:24:26,353 --> 00:24:27,354 INTEGRATE WORKFORCE TRAINING AND 620 00:24:27,354 --> 00:24:28,322 CAREER DEVELOPMENT FOR 621 00:24:28,322 --> 00:24:29,389 INDIVIDUALS AND LASTLY THE 622 00:24:29,389 --> 00:24:31,224 COMMITTEE WOULD LIKE TO REFLECT 623 00:24:31,224 --> 00:24:33,527 THE STRATEGY PLAN'S DEVELOPMENT 624 00:24:33,527 --> 00:24:39,399 BY MDCC MEMBER ORGANIZATIONS AND 625 00:24:39,399 --> 00:24:41,501 OTHER ADVOCACY GROUPS. 626 00:24:41,501 --> 00:24:44,438 NOW WITHIN THE NIH, NIAMS 627 00:24:44,438 --> 00:24:45,505 PARTICIPATES IN MANY 628 00:24:45,505 --> 00:24:46,807 COLLABORATIVE EFFORTS WITH OTHER 629 00:24:46,807 --> 00:24:48,575 INSTITUTES, CENTERS AND OFFICES 630 00:24:48,575 --> 00:24:49,409 THAT HAVE SHARED INTERESTS. 631 00:24:49,409 --> 00:24:54,481 THIS FISCAL YEAR, CONGRESSIONAL 632 00:24:54,481 --> 00:24:54,881 KA 633 00:24:54,881 --> 00:24:57,484 -- CONGRESS ALLOCATED $10 634 00:24:57,484 --> 00:25:00,220 MILLION TO ESTABLISH THE OFFICE 635 00:25:00,220 --> 00:25:00,954 OF AUTOIMMUNE DISEASE RESEARCH. 636 00:25:00,954 --> 00:25:02,522 THE FUNDING WAS INCLUDED TO 637 00:25:02,522 --> 00:25:05,492 IMPLEMENT THE RECOMMENDATIONS OF 638 00:25:05,492 --> 00:25:06,493 A RECENT NASEM REPORT. 639 00:25:06,493 --> 00:25:10,063 AS A LEADING FUNDER OF 640 00:25:10,063 --> 00:25:10,697 AUTOIMMUNE DISEASES RESEARCH 641 00:25:10,697 --> 00:25:12,366 NIAMS IS WORKING WITH THE NEW 642 00:25:12,366 --> 00:25:16,636 OFFICE AS IT BEGINS TO 643 00:25:16,636 --> 00:25:19,206 ACCOMPLISH ITS GOAL THE 644 00:25:19,206 --> 00:25:19,906 MULTI-INSTITUTE AND RESEARCH 645 00:25:19,906 --> 00:25:21,508 STRATEGIC PLAN AND IDENTIFYING 646 00:25:21,508 --> 00:25:24,311 EMERGING AREAS OF INNOVATION AND 647 00:25:24,311 --> 00:25:25,479 RESEARCH OPPORTUNITIES FOR THE 648 00:25:25,479 --> 00:25:28,749 STRATEGY PLAN, COORDINATING AND 649 00:25:28,749 --> 00:25:31,184 FOSTERING COLLABORATIVE RESEARCH 650 00:25:31,184 --> 00:25:33,553 ACROSS THE NIH, ANNUALLY 651 00:25:33,553 --> 00:25:35,589 EVALUATING THE NIH RESEARCH 652 00:25:35,589 --> 00:25:37,457 PORTFOLIO AND PROVIDING 653 00:25:37,457 --> 00:25:39,326 RESOURCES TO SUPPORT RESEARCH, 654 00:25:39,326 --> 00:25:40,660 COLLABORATION AND DEVELOPING AND 655 00:25:40,660 --> 00:25:45,999 OVERSEEING A PUBLICLY ACCESSIBLE 656 00:25:45,999 --> 00:25:49,302 CENTRAL REPOSITORY FOR 657 00:25:49,302 --> 00:25:50,003 AUTOIMMUNE RESEARCH RESULT. 658 00:25:50,003 --> 00:25:52,672 IN LINE WITH THE NEW OFFICE, THE 659 00:25:52,672 --> 00:25:54,408 OFFICE OF RESEARCH IN WOMEN'S 660 00:25:54,408 --> 00:25:56,943 HEALTH AND OTHER INSTITUTES AND 661 00:25:56,943 --> 00:26:00,714 CENTERS AND NIAMS PUBLISHED ON 662 00:26:00,714 --> 00:26:04,251 THE EXPOSOME IN AUTOIMMUNE 663 00:26:04,251 --> 00:26:07,220 DISEASE IT'S A COLLABORATING 664 00:26:07,220 --> 00:26:08,655 TEAM PLANNING AWARDS EXACT PLAN 665 00:26:08,655 --> 00:26:10,557 AND IT'S AN EFFORT BETWEEN THE 666 00:26:10,557 --> 00:26:13,860 OFFICE OF RESEARCH ON WOMEN'S 667 00:26:13,860 --> 00:26:15,429 HEALTH, THE NATIONAL INSTITUTE 668 00:26:15,429 --> 00:26:16,530 OF ENVIRONMENTAL HEALTH SCIENCE 669 00:26:16,530 --> 00:26:19,199 AND OTHER INSTITUTES AND CENTERS 670 00:26:19,199 --> 00:26:19,833 ENGAGED IN AUTOIMMUNE DISEASE 671 00:26:19,833 --> 00:26:20,100 RESEARCH. 672 00:26:20,100 --> 00:26:24,838 THE GOAL IS TO INVITE 673 00:26:24,838 --> 00:26:25,705 APPLICATIONS FOR EXPLORATORY, 674 00:26:25,705 --> 00:26:27,307 EARLY AROUND CONCEPTUAL PLANNING 675 00:26:27,307 --> 00:26:28,809 PROJECTS AIMED AT DEVELOPING A 676 00:26:28,809 --> 00:26:29,409 FUTURE TEAM SCIENCE RESEARCH 677 00:26:29,409 --> 00:26:31,111 NETWORK. 678 00:26:31,111 --> 00:26:33,480 SO THE IDEA WOULD BE TO CONDUCT 679 00:26:33,480 --> 00:26:35,615 RESEARCH TO DISCOVER THE 680 00:26:35,615 --> 00:26:37,017 ENVIRONMENTAL EXPOSURES THAT 681 00:26:37,017 --> 00:26:38,985 INFLUENCE DISEASE SUSCEPTIBLE, 682 00:26:38,985 --> 00:26:40,787 ONSET AND OUTCOMES AND TO 683 00:26:40,787 --> 00:26:43,657 DEVELOP NEW APPROACHES TO 684 00:26:43,657 --> 00:26:45,692 UNDERSTANDING THE MECHANISMS 685 00:26:45,692 --> 00:26:49,496 UNDERLYING HOW EXPOSURES PERTURB 686 00:26:49,496 --> 00:26:51,131 CELLULAR, ORGAN AND TISSUE 687 00:26:51,131 --> 00:26:51,698 FUNCTION ACROSS AUTOIMMUNE 688 00:26:51,698 --> 00:26:55,368 DISEASES. 689 00:26:55,368 --> 00:26:58,505 ANOTHER TRANS-NIH EFFORT I'D 690 00:26:58,505 --> 00:27:00,107 LAKE TO HIGHLIGHT IS THE 691 00:27:00,107 --> 00:27:03,877 MOLECULAR TRANSDUCERS OF 692 00:27:03,877 --> 00:27:06,279 PHYSICAL ACTIVITY CONSORTIUM AS 693 00:27:06,279 --> 00:27:07,747 THE EARLY RESULTS FROM THE 694 00:27:07,747 --> 00:27:13,487 PROGRAM ARE FORTHCOMING. 695 00:27:13,487 --> 00:27:15,755 MOTRPAC IS A COMMON FUND PROGRAM 696 00:27:15,755 --> 00:27:16,623 LED BY NIAMS, THE NATIONAL 697 00:27:16,623 --> 00:27:20,894 INSTITUTE OF AGING AND THE 698 00:27:20,894 --> 00:27:21,094 NIDDK. 699 00:27:21,094 --> 00:27:22,295 IT'S A NATIONAL RESEARCH 700 00:27:22,295 --> 00:27:24,898 CONSORTIUM WHICH WAS FIRST 701 00:27:24,898 --> 00:27:29,469 FUNDED IN 2017 TO DISCOVER AND 702 00:27:29,469 --> 00:27:30,904 CHARACTERIZE THE RANGE OF 703 00:27:30,904 --> 00:27:33,473 MOLECULAR TRANSDUCERS THAT UNDER 704 00:27:33,473 --> 00:27:35,442 LIE THE AFFECT OF PHYSICAL 705 00:27:35,442 --> 00:27:38,011 ACTIVITY IN HUMANS AND RATS OF 706 00:27:38,011 --> 00:27:38,912 VARIOUS AGES. 707 00:27:38,912 --> 00:27:40,413 THE PROGRAMS' GOAL IS TO 708 00:27:40,413 --> 00:27:42,482 UNDERSTAND THE MOLECULAR CHANGES 709 00:27:42,482 --> 00:27:43,783 DURING AND AFTER EXERCISE AND 710 00:27:43,783 --> 00:27:45,051 ULTIMATELY TO ADVANCE THE 711 00:27:45,051 --> 00:27:47,854 UNDERSTANDING OF HOW PHYSICAL 712 00:27:47,854 --> 00:27:48,488 ACTIVITY IMPROVES AND PRESERVES 713 00:27:48,488 --> 00:27:51,424 HEALTH. 714 00:27:51,424 --> 00:27:53,660 RESULTS FROM PROFILING MOLECULES 715 00:27:53,660 --> 00:27:58,498 IN WHOLE BLOOD, PLASMA AND 18 716 00:27:58,498 --> 00:27:59,599 SOLID TISSUES FROM SIX-MONTH-OLD 717 00:27:59,599 --> 00:28:01,468 RATS THAT UNDERWENT A TRAINING 718 00:28:01,468 --> 00:28:03,270 PROGRAM HAVE BEEN PROVISIONALLY 719 00:28:03,270 --> 00:28:05,138 ACCEPTED FOR PUBLICATION AND THE 720 00:28:05,138 --> 00:28:08,642 PRE PRINT IS AVAILABLE NOW. 721 00:28:08,642 --> 00:28:10,510 MY INSTITUTE DIRECTOR COLLEAGUES 722 00:28:10,510 --> 00:28:12,412 AND I LEADING THE PROGRAM WROTE 723 00:28:12,412 --> 00:28:13,980 A COMMENTARY THAT WILL BE 724 00:28:13,980 --> 00:28:15,482 PUBLISHED WHEN THE PAPER IS 725 00:28:15,482 --> 00:28:15,916 FORMALLY RELEASED. 726 00:28:15,916 --> 00:28:17,484 WE'RE EXCITED ABOUT THIS 727 00:28:17,484 --> 00:28:19,986 PROGRAM. 728 00:28:19,986 --> 00:28:22,222 NOW MOVING ON TO THE IMPORTANT 729 00:28:22,222 --> 00:28:23,924 TOPIC OF PAIN RESEARCH. 730 00:28:23,924 --> 00:28:25,392 THE NIH HEAL INITIATIVE, THAT IS 731 00:28:25,392 --> 00:28:29,529 THE HELPING TO END ADDICTION 732 00:28:29,529 --> 00:28:31,331 LONG-TERM INITIATIVE IS AN 733 00:28:31,331 --> 00:28:32,766 EFFORT TO SPEED SCIENTIFIC 734 00:28:32,766 --> 00:28:35,068 SOLUTION TO STEM THE NATIONAL 735 00:28:35,068 --> 00:28:37,103 OPIOID PUBLIC HEALTH CRISIS. 736 00:28:37,103 --> 00:28:37,871 ALMOST EVERY NIH INSTITUTE AND 737 00:28:37,871 --> 00:28:41,474 CENTER IS ACCELERATING RESEARCH 738 00:28:41,474 --> 00:28:43,710 TO ADDRESS THIS PUBLIC HEALTH 739 00:28:43,710 --> 00:28:46,079 EMERGENCY FROM ALL ANGLES. 740 00:28:46,079 --> 00:28:48,748 AMONG THE EFFORTS NIAMS IS 741 00:28:48,748 --> 00:28:49,983 LEADING THE BACPAC RESEARCH 742 00:28:49,983 --> 00:28:53,453 PROGRAM WHICH IS A TRANSLATIONAL 743 00:28:53,453 --> 00:28:54,387 PATIENT-CENTERED COLLABORATION 744 00:28:54,387 --> 00:28:55,956 TO ADDRESS THE NEED FOR 745 00:28:55,956 --> 00:28:58,091 EFFECTIVE AND PERSONALIZED 746 00:28:58,091 --> 00:29:00,493 THERAPIES FOR CHRONIC LOW BACK 747 00:29:00,493 --> 00:29:00,860 PAIN. 748 00:29:00,860 --> 00:29:02,395 NIAMS IS ALSO LEADING THE 749 00:29:02,395 --> 00:29:03,663 RESTORING JOINT HEALTH AND 750 00:29:03,663 --> 00:29:06,967 FUNCTION TO REDUCE PAIN OR 751 00:29:06,967 --> 00:29:08,034 REJOIN CONSORTIUM WHICH CONSISTS 752 00:29:08,034 --> 00:29:09,869 OF RESEARCH TEAMS WORKING 753 00:29:09,869 --> 00:29:12,239 TOGETHER TO MAP THE NETWORK OF 754 00:29:12,239 --> 00:29:15,275 SENSORY NERVES THAT CONNECTS TO 755 00:29:15,275 --> 00:29:18,511 TWO JOINTS THE TEMPOROMANDIBULAR 756 00:29:18,511 --> 00:29:19,946 JOINT AND THE KNEE. 757 00:29:19,946 --> 00:29:21,114 THE RESEARCH AIMS TO UNDERSTAND 758 00:29:21,114 --> 00:29:23,550 HOW THE TYPES AND PATTERNS OF 759 00:29:23,550 --> 00:29:25,318 SENSORY NERVE NETWORKS IN JOINTS 760 00:29:25,318 --> 00:29:25,919 CHANGE WITH DISEASE AND WITH 761 00:29:25,919 --> 00:29:29,356 AGING. 762 00:29:29,356 --> 00:29:30,757 FURTHER, THE NATIONAL CENTER OF 763 00:29:30,757 --> 00:29:31,791 COMPLIMENTARY AND INTEGRATIVE 764 00:29:31,791 --> 00:29:34,894 HEALTH OR NCCIH ALSO LEADS AN 765 00:29:34,894 --> 00:29:37,497 EFFORT THAT SEEKS TO DEVELOP 766 00:29:37,497 --> 00:29:41,501 QUANTITATIVE IMAGING AND OTHER 767 00:29:41,501 --> 00:29:44,037 RELEVANT BIOMARKERS OF 768 00:29:44,037 --> 00:29:45,972 MYOFASCIAL TISSUES AND THE HEAL 769 00:29:45,972 --> 00:29:48,041 INITIATIVE PRECISION HUMAN PAIN 770 00:29:48,041 --> 00:29:49,442 NETWORK LED BY THE NATIONAL 771 00:29:49,442 --> 00:29:50,844 INSTITUTE OF NEUROLOGICAL 772 00:29:50,844 --> 00:29:52,712 DISORDERS AND STROKE AIMS TO USE 773 00:29:52,712 --> 00:29:54,014 PRIMARY HUMAN TISSUES AND CELLS 774 00:29:54,014 --> 00:29:56,883 TO BUILD COMPREHENSIVE DATA SETS 775 00:29:56,883 --> 00:29:59,286 OF MOLECULAR SIGNATURES, CELL 776 00:29:59,286 --> 00:30:00,787 TYPES AND CELL FUNCTIONED 777 00:30:00,787 --> 00:30:02,722 PHENOTYPES OR SIGNATURES THAT 778 00:30:02,722 --> 00:30:05,625 UNDER LIE HUMAN PAIN SIGNAL 779 00:30:05,625 --> 00:30:06,259 TRANSDUCTION, TRANSMISSION AND 780 00:30:06,259 --> 00:30:09,496 PROCESSING. 781 00:30:09,496 --> 00:30:12,065 SO A CRITICAL PART OF HEAL IS 782 00:30:12,065 --> 00:30:14,801 COLLECTING DATA THAT CAN BE 783 00:30:14,801 --> 00:30:16,436 INTEGRATED ACROSS MODELS AND 784 00:30:16,436 --> 00:30:18,605 ACROSS THE MAINS TO BETTER 785 00:30:18,605 --> 00:30:19,506 UNDERSTAND CHRONIC PAIN. 786 00:30:19,506 --> 00:30:22,175 SO WE'RE STARTING TO CREATE AN 787 00:30:22,175 --> 00:30:23,376 ECO SYSTEM ADDRESSING THE 788 00:30:23,376 --> 00:30:25,912 MULTIPLE DOMAINS ESSENTIAL TO 789 00:30:25,912 --> 00:30:27,647 UNDERSTAND AND TREAT JOINT PAIN 790 00:30:27,647 --> 00:30:29,416 FROM THE ENVIRONMENT, BEHAVIORAL 791 00:30:29,416 --> 00:30:32,986 AND PSYCHOSOCIAL FACTORS TO 792 00:30:32,986 --> 00:30:34,254 COMPLEX MOLECULAR INTERACTIONS. 793 00:30:34,254 --> 00:30:37,490 AND NOW WITH COLLABORATIVE 794 00:30:37,490 --> 00:30:38,758 EFFORTS AMONG HEAL PROGRAMS CAN 795 00:30:38,758 --> 00:30:40,960 START TO MAKE SIGNIFICANT 796 00:30:40,960 --> 00:30:41,594 ADVANCES AGAINST THE CHRONIC 797 00:30:41,594 --> 00:30:43,596 PAIN THAT PLAIN OUR PATIENTS AND 798 00:30:43,596 --> 00:30:43,830 SOCIETY. 799 00:30:43,830 --> 00:30:46,032 AS WE WILL MOVE FORWARD 800 00:30:46,032 --> 00:30:48,968 UNDERSTANDING PAIN REMAINS A 801 00:30:48,968 --> 00:30:50,904 PRIORITY FOR NIAMS. 802 00:30:50,904 --> 00:30:54,240 RELATED TO HEAL, I'D LIKE TO 803 00:30:54,240 --> 00:30:55,875 ALSO HIGHLIGHT THE HEAL KIDS' 804 00:30:55,875 --> 00:30:57,377 PAIN INITIATIVE. 805 00:30:57,377 --> 00:30:58,678 KIDS STANDING FOR KNOWLEDGE, 806 00:30:58,678 --> 00:31:00,914 INNOVATION AND DISCOVERY 807 00:31:00,914 --> 00:31:01,481 STUDIES. 808 00:31:01,481 --> 00:31:05,218 SO THE EUNICE KENNEDY SCHRIEVER 809 00:31:05,218 --> 00:31:08,788 NATIONAL HEALTH OF HUMAN HEALTH 810 00:31:08,788 --> 00:31:09,756 AND DEVELOPMENT ISSUED TWO 811 00:31:09,756 --> 00:31:10,590 NOTICES OF FUNDING 812 00:31:10,590 --> 00:31:10,924 OPPORTUNITIES. 813 00:31:10,924 --> 00:31:13,526 ONE NOTICE IS FOR A PAIN 814 00:31:13,526 --> 00:31:16,830 RESOURCE AND DATA CENTER AND THE 815 00:31:16,830 --> 00:31:19,632 OTHER FOR SUPPORTING AN ACUTE 816 00:31:19,632 --> 00:31:20,700 PAIN CLINICAL TRIALS PROGRAM. 817 00:31:20,700 --> 00:31:22,469 NIAMS SIGNED ON TO BOTH AND 818 00:31:22,469 --> 00:31:24,270 WE'RE VERY ENTHUSIASTIC ABOUT 819 00:31:24,270 --> 00:31:25,472 THE OPPORTUNITY TO SUPPORT PAIN 820 00:31:25,472 --> 00:31:27,374 RESEARCH IN INFANTS, CHILDREN 821 00:31:27,374 --> 00:31:30,043 AND ADOLESCENTS WHICH IS A 822 00:31:30,043 --> 00:31:33,313 COMMON ISSUE BUT OFTEN UNDER 823 00:31:33,313 --> 00:31:34,848 RECOGNIZED IN CONSISTENTLY 824 00:31:34,848 --> 00:31:36,516 ASSESSED OR MEASURED AND 825 00:31:36,516 --> 00:31:37,484 INADEQUATELY TREAT. 826 00:31:37,484 --> 00:31:38,985 WITHIN THE NIAMS EFFORT IT CAN 827 00:31:38,985 --> 00:31:41,955 RELATE TO ACUTE ORTHOPEDIC PAIN 828 00:31:41,955 --> 00:31:44,023 FROM COMMON INJURIES OR TO ACUTE 829 00:31:44,023 --> 00:31:54,167 PAIN CAUSED BY DISEASE FLARES IN 830 00:31:54,167 --> 00:31:55,101 CHILDREN WITH CHRONIC CONDITIONS 831 00:31:55,101 --> 00:31:57,036 WITHIN OUR INITIATIVE AND THIS 832 00:31:57,036 --> 00:31:58,204 UNDER SCORES NIAMS' COMMITMENT 833 00:31:58,204 --> 00:31:59,539 TO BETTER UNDERSTANDING HEALTH 834 00:31:59,539 --> 00:32:02,642 AND DISEASE IN DIVERSE 835 00:32:02,642 --> 00:32:06,780 POPULATIONS AS SPECIFIED IN OUR 836 00:32:06,780 --> 00:32:09,115 CURRENT STRATEGY PLAN. 837 00:32:09,115 --> 00:32:12,385 ON THE FRONT, NIAMS PARTICIPATES 838 00:32:12,385 --> 00:32:14,020 IN ANOTHER TRANS-NIH EFFORT LED 839 00:32:14,020 --> 00:32:16,823 BY THE OFFICE OF RESEARCH ON 840 00:32:16,823 --> 00:32:17,991 WOMEN'S HEALTH TO BETTER 841 00:32:17,991 --> 00:32:20,026 UNDERSTAND CHRONIC CONDITIONS 842 00:32:20,026 --> 00:32:22,896 UNDER STUDIED AMONG WOMEN AND/OR 843 00:32:22,896 --> 00:32:23,763 DISPROPORTIONATELY AFFECT 844 00:32:23,763 --> 00:32:25,031 POPULATIONS OF WITH UNDER 845 00:32:25,031 --> 00:32:26,099 STUDIED AND UNDER REPRESENTED 846 00:32:26,099 --> 00:32:27,100 AND UNDER REPORTED IN BIOMEDICAL 847 00:32:27,100 --> 00:32:30,437 RESEARCH. 848 00:32:30,437 --> 00:32:32,672 WE ALSO PUBLISHED TWO NOTICES OF 849 00:32:32,672 --> 00:32:35,909 SPECIAL INTEREST THIS SUMMER. 850 00:32:35,909 --> 00:32:38,745 THESE NOSIS ANNOUNCED OUR 851 00:32:38,745 --> 00:32:40,180 INTEREST IN RECEIVING 852 00:32:40,180 --> 00:32:40,814 ADMINISTRATIVE SUPPLEMENT TO 853 00:32:40,814 --> 00:32:44,050 GRANT AND GRANT APPLICATIONS 854 00:32:44,050 --> 00:32:46,619 THAT FOCUSSED ON SKIN RESEARCH 855 00:32:46,619 --> 00:32:50,423 UNCOVER THE BASIS FOR SUBOPTIMAL 856 00:32:50,423 --> 00:32:53,059 DIAGNOSES, INCREASED PREVALENCE 857 00:32:53,059 --> 00:32:54,360 AND ELEVATED CLINICAL SEVERITY 858 00:32:54,360 --> 00:32:58,631 AND TREATMENT RESPONSES IN BLACK 859 00:32:58,631 --> 00:33:00,767 AMERICANS AND HISPANICS AND 860 00:33:00,767 --> 00:33:02,035 LATINOS AND AMERICAN INDIANS AND 861 00:33:02,035 --> 00:33:05,505 ALASKAN NATIVES AND ASIAN AND 862 00:33:05,505 --> 00:33:08,041 ASIAN AMERICANS AND PACIFIC 863 00:33:08,041 --> 00:33:10,443 ISLANDERS WITH SKIN DISEASES. 864 00:33:10,443 --> 00:33:12,712 FURTHER, AS PART OF THE NIH-WIDE 865 00:33:12,712 --> 00:33:14,414 UNITE INITIATIVE TO END 866 00:33:14,414 --> 00:33:16,416 STRUCTURAL RACISM, THE NIH 867 00:33:16,416 --> 00:33:18,852 ANNOUNCED ITS RESEARCH WITH 868 00:33:18,852 --> 00:33:21,454 ACTIVITIES RELATED TO DIVERSITY 869 00:33:21,454 --> 00:33:24,958 OR REWARD PROGRAM IN THIS PAST 870 00:33:24,958 --> 00:33:25,458 MARCH. 871 00:33:25,458 --> 00:33:28,428 REWARD PROVIDES SUPPORT FOR 872 00:33:28,428 --> 00:33:30,396 SCIENTISTS MAKING A SIGNIFICANT 873 00:33:30,396 --> 00:33:32,265 CONTRIBUTION TO DIVERSITY, 874 00:33:32,265 --> 00:33:34,467 EQUITY, INCLUSION AND 875 00:33:34,467 --> 00:33:37,203 ACCESSIBILITY IN THE RESEARCH 876 00:33:37,203 --> 00:33:38,905 ENTERPRISE AND WHO HAVE NO 877 00:33:38,905 --> 00:33:40,640 CURRENT RESEARCH GRANT FUNDING. 878 00:33:40,640 --> 00:33:43,476 THIS FILLS AN IMPORTANT GAP. 879 00:33:43,476 --> 00:33:46,079 APPLICANTS WILL RECEIVE THE RO1 880 00:33:46,079 --> 00:33:50,316 MECHANISM FOR AND DEIA 881 00:33:50,316 --> 00:33:51,985 ACTIVITIES IF SUCCESSFUL. 882 00:33:51,985 --> 00:33:55,355 WITH THE NIAMS AS REPORTED IN 883 00:33:55,355 --> 00:33:57,423 THE LAST DAY IN 2021 WE'RE 884 00:33:57,423 --> 00:33:59,325 COMMITTED TO ELIMINATING 885 00:33:59,325 --> 00:34:01,461 STRUCTURAL RACISM IN THE WO 886 00:34:01,461 --> 00:34:04,464 WORKPLACE AND HEALTH CARE 887 00:34:04,464 --> 00:34:04,731 SETTINGS. 888 00:34:04,731 --> 00:34:05,932 FIRST THE STEPS WE'RE TAKING 889 00:34:05,932 --> 00:34:06,799 WITHIN THE INSTITUTE. 890 00:34:06,799 --> 00:34:08,768 WE CONTINUE TO FOCUS ON 891 00:34:08,768 --> 00:34:09,736 EMPOWERING AND SUPPORTING OUR 892 00:34:09,736 --> 00:34:11,638 STAFF WITH OPPORTUNITIES TO 893 00:34:11,638 --> 00:34:13,106 SHARE AND LEARN ABOUT DEIA. 894 00:34:13,106 --> 00:34:18,978 THIS YEAR WE PARTNERED WITH THE 895 00:34:18,978 --> 00:34:21,514 NIH EQUITY, DIVERSITY AND 896 00:34:21,514 --> 00:34:24,817 INCLUSION SESSIONS FOR INFORMAL 897 00:34:24,817 --> 00:34:27,353 CONVERSATION ON DEIA WITH THE 898 00:34:27,353 --> 00:34:28,821 NIH EQUITY, DIVERSITY AND 899 00:34:28,821 --> 00:34:29,422 INCLUSION DIRECTOR. 900 00:34:29,422 --> 00:34:31,424 THE SESSIONS OCCURRED BETWEEN 901 00:34:31,424 --> 00:34:32,592 MAY AND JULY. 902 00:34:32,592 --> 00:34:35,495 IN 2020 THE INSTITUTE 903 00:34:35,495 --> 00:34:37,163 ESTABLISHED THE NIAMS CULTURE 904 00:34:37,163 --> 00:34:39,666 COMMITTEE TO PROMOTE AN 905 00:34:39,666 --> 00:34:42,168 ORGANIZATIONAL CLIMATE DESIGN BY 906 00:34:42,168 --> 00:34:43,102 INCLUSIVITY, CIVILITY AND 907 00:34:43,102 --> 00:34:43,403 DIVERSITY. 908 00:34:43,403 --> 00:34:45,738 AMONG THE ACTIVITY THE COMMITTEE 909 00:34:45,738 --> 00:34:47,206 ADVISES THE INSTITUTE'S 910 00:34:47,206 --> 00:34:49,042 LEADERSHIP ON RECRUITING, 911 00:34:49,042 --> 00:34:50,443 RETAINING AND PROMOTION 912 00:34:50,443 --> 00:34:53,479 EMPLOYEES FROM UNDER REPRESENTED 913 00:34:53,479 --> 00:34:53,947 BACKGROUNDS. 914 00:34:53,947 --> 00:34:56,082 AND AS WE LOOK TO BRING PEOPLE 915 00:34:56,082 --> 00:34:57,183 INTO THE NIAMS FOLD, WE'RE 916 00:34:57,183 --> 00:35:00,119 SEEKING TO ENSURE A CIVIL 917 00:35:00,119 --> 00:35:01,921 WORKPLACE ENVIRONMENT IN WHICH 918 00:35:01,921 --> 00:35:03,990 WE EMPHASIZE WORKING TOGETHER 919 00:35:03,990 --> 00:35:06,659 TOWARD A COMMON GOAL WITH 920 00:35:06,659 --> 00:35:07,327 INTEGRITY, ACCOUNTABILITY AND 921 00:35:07,327 --> 00:35:09,495 RESPECT FOR DIVERSITY OF 922 00:35:09,495 --> 00:35:10,897 EXPERIENCES AND PERSPECTIVES. 923 00:35:10,897 --> 00:35:12,432 SO TO THIS END THE NIAMS CULTURE 924 00:35:12,432 --> 00:35:15,401 COMMITTEE HAS BEEN WORKING WITH 925 00:35:15,401 --> 00:35:19,072 STAFF AND LEADERSHIP TO UPDATE 926 00:35:19,072 --> 00:35:20,807 THE CORE VALUES DEVELOPED WITH 927 00:35:20,807 --> 00:35:22,175 BROAD INPUT FROM STAFF AND 928 00:35:22,175 --> 00:35:24,177 ROLLED OUT THIS MONTH. 929 00:35:24,177 --> 00:35:25,912 THE NIAMS CORE VALUES UNDER 930 00:35:25,912 --> 00:35:28,581 SCORE THE COMMITMENT TO 931 00:35:28,581 --> 00:35:29,949 CULTIVATING A WORKPLACE THAT IS 932 00:35:29,949 --> 00:35:30,183 RESPECT. 933 00:35:30,183 --> 00:35:32,051 AND INCLUSIVE AND WILL INSPIRE 934 00:35:32,051 --> 00:35:32,986 AND SUPPORT US AS WE ADVANCE 935 00:35:32,986 --> 00:35:37,490 RESEARCH TO IMPROVE THE HEALTH 936 00:35:37,490 --> 00:35:40,793 OF PEOPLE IN THE UNITED STATES. 937 00:35:40,793 --> 00:35:43,062 THE NIAMS STRATEGIC PLAN FOR 938 00:35:43,062 --> 00:35:51,604 FISCAL YEARS 2020 TO 2024 939 00:35:51,604 --> 00:35:54,607 RECOGNIZING THE MISSION MAY 940 00:35:54,607 --> 00:35:55,675 DISPROPORTIONATELY IMPACT 941 00:35:55,675 --> 00:35:57,377 CERTAIN GROUPS AND LOOKING TO 942 00:35:57,377 --> 00:35:59,045 ENHANCE WORKFORCE DIVERSITY IN 943 00:35:59,045 --> 00:36:00,113 OUR MISSION AREAS. 944 00:36:00,113 --> 00:36:01,114 THROUGH OUR SCIENCE 945 00:36:01,114 --> 00:36:02,081 COMMUNICATION AND OUTREACH 946 00:36:02,081 --> 00:36:04,651 BRANCH, NIAMS ENGAGES AND SERVES 947 00:36:04,651 --> 00:36:06,586 AMERICANS FROM DIVERSE 948 00:36:06,586 --> 00:36:10,056 BACKGROUNDS IN ADDITION THE 949 00:36:10,056 --> 00:36:13,493 INSTITUTE ESTABLISHED A 950 00:36:13,493 --> 00:36:15,395 DIVERSITY SCHOLARS PROGRAM TO 951 00:36:15,395 --> 00:36:17,330 PROVIDE SUPPORT AND ENHANCE WITH 952 00:36:17,330 --> 00:36:18,031 OUR SUPPLEMENT AWARDEES AND 953 00:36:18,031 --> 00:36:23,536 MENTORS. 954 00:36:23,536 --> 00:36:24,804 TO HELP US ADVANCE ALL THE 955 00:36:24,804 --> 00:36:27,140 EFFORTS I'M DELIGHTED TO 956 00:36:27,140 --> 00:36:27,940 ANNOUNCE NIAMS HAS NAMED 957 00:36:27,940 --> 00:36:30,743 DR. ROBERT WALKER JR. AS THE 958 00:36:30,743 --> 00:36:33,246 INSTITUTE'S FIRST CHIEF 959 00:36:33,246 --> 00:36:33,680 DIVERSITY OFFICER. 960 00:36:33,680 --> 00:36:35,481 UNTIL APRIL HE SERVED AS THE 961 00:36:35,481 --> 00:36:38,117 DIRECTOR OF THE OFFICE FOR 962 00:36:38,117 --> 00:36:41,921 STRATEGIC OPERATIONS WITHIN OUR 963 00:36:41,921 --> 00:36:42,922 INTRAMURAL RESEARCH PROGRAM. 964 00:36:42,922 --> 00:36:46,559 THERE HIS RESPONSIBLES INCLUDED 965 00:36:46,559 --> 00:36:48,227 LEADING CAREER DEVELOPMENT FOR 966 00:36:48,227 --> 00:36:50,296 THE TRAINING AWARDEES, 967 00:36:50,296 --> 00:36:53,900 TECHNOLOGY TRANSFER, INNOVATION 968 00:36:53,900 --> 00:36:54,534 DEVELOPMENT, SCIENTIFIC 969 00:36:54,534 --> 00:36:56,069 COMMUNICATION, POLICY, INCLUSION 970 00:36:56,069 --> 00:36:58,104 AND LOGISTICS AND IN HIS NEW 971 00:36:58,104 --> 00:37:01,040 ROLE DR. WALKER WILL LEAD THE 972 00:37:01,040 --> 00:37:02,508 DEVELOPMENT AND IMPLEMENTATION 973 00:37:02,508 --> 00:37:04,077 OF RESEARCH, RESEARCH CAPACITY 974 00:37:04,077 --> 00:37:06,112 BUILDING, TRAINING AND CAREER 975 00:37:06,112 --> 00:37:07,213 DEVELOPMENT PROGRAMS TO SUPPORT 976 00:37:07,213 --> 00:37:08,815 THE SCIENTIFIC MISSION OF NIAMS 977 00:37:08,815 --> 00:37:09,482 AND ENHANCE SCIENTIFIC 978 00:37:09,482 --> 00:37:12,485 DIVERSITY. 979 00:37:12,485 --> 00:37:14,087 HE'LL PROVIDE RECOMMENDATIONS ON 980 00:37:14,087 --> 00:37:15,755 SCIENTIFIC DIVERSITY GOALS AND 981 00:37:15,755 --> 00:37:17,423 OBJECTIVES TO ENSURE DIVERSITY 982 00:37:17,423 --> 00:37:19,726 IS CONSIDERED IN THE 983 00:37:19,726 --> 00:37:21,027 DEVELOPMENT, FUNDING AND 984 00:37:21,027 --> 00:37:22,895 ADMINISTRATION OF GRANT AWARDS, 985 00:37:22,895 --> 00:37:24,530 COOPERATIVE AGREEMENTS AND 986 00:37:24,530 --> 00:37:26,599 CONTRACTS AND IN ADDITION HE'LL 987 00:37:26,599 --> 00:37:28,401 SERVE AS THE NIAMS LIAISON WITH 988 00:37:28,401 --> 00:37:30,470 THE SCIENTIFIC COMMUNITY AND 989 00:37:30,470 --> 00:37:32,905 PARTNER WITH THE NIH CHIEF 990 00:37:32,905 --> 00:37:34,507 OFFICER FOR SCIENTIFIC WORKFORCE 991 00:37:34,507 --> 00:37:37,210 DIVERSITY, THE OFFICE OF EQUITY, 992 00:37:37,210 --> 00:37:39,579 DIVERSITY AND INCLUSION AND 993 00:37:39,579 --> 00:37:41,647 CHIEF DIVERSITY OFFICERS FROM 994 00:37:41,647 --> 00:37:44,784 OTHER NIH INSTITUTES AND 995 00:37:44,784 --> 00:37:45,017 CENTERS. 996 00:37:45,017 --> 00:37:47,754 FINALLY, I'D LIKE TO QUICKLY 997 00:37:47,754 --> 00:37:50,490 UPDATE YOU ABOUT THE NIAMS 998 00:37:50,490 --> 00:37:52,024 STRATEGIC PLANNING PROCESS AND 999 00:37:52,024 --> 00:37:53,226 EXPECT YOU'LL HEAR MORE FROM 1000 00:37:53,226 --> 00:37:57,230 DR. BURROWS THE CHIEF OF OUR 1001 00:37:57,230 --> 00:37:58,030 PLANNING AND POLICY ANALYSIS 1002 00:37:58,030 --> 00:37:59,799 BRANCH THIS AFTERNOON. 1003 00:37:59,799 --> 00:38:01,601 I'M GRATEFUL TO THOSE WHO 1004 00:38:01,601 --> 00:38:03,202 VOLUNTEERED YOUR TIME TO ATTEND 1005 00:38:03,202 --> 00:38:05,371 THE THREE-DAY MEETING LAST WE 1006 00:38:05,371 --> 00:38:09,208 CAN OR WHO MADE THE EXTRA EFFORT 1007 00:38:09,208 --> 00:38:12,311 TO FIND A COLLEAGUE TO 1008 00:38:12,311 --> 00:38:14,247 PARTICIPATE IN YOUR PLACE. 1009 00:38:14,247 --> 00:38:17,016 RESEARCHERS AND STAFF ACROSS THE 1010 00:38:17,016 --> 00:38:18,518 NIH AND SEVERAL PATIENT 1011 00:38:18,518 --> 00:38:19,418 REPRESENTATIVES JOINED US TO 1012 00:38:19,418 --> 00:38:22,488 SHARE IDEAS ON CROSS-CUTTING 1013 00:38:22,488 --> 00:38:23,322 TOPICS THE INSTITUTE WILL PURSUE 1014 00:38:23,322 --> 00:38:24,991 THROUGH THE END OF THE DECADE. 1015 00:38:24,991 --> 00:38:27,994 IT WAS A FABULOUS EVENT FOR 1016 00:38:27,994 --> 00:38:29,262 THOSE THAT PARTICIPATED KNOW AND 1017 00:38:29,262 --> 00:38:33,399 I'M THRILLED WITH THE OUTCOME. 1018 00:38:33,399 --> 00:38:35,668 NOW, NIAMS STRATEGIC PLANS ARE A 1019 00:38:35,668 --> 00:38:37,003 PUBLIC STATEMENT OF THE 1020 00:38:37,003 --> 00:38:38,805 INSTITUTE'S INTEREST, A GUIDE 1021 00:38:38,805 --> 00:38:41,340 POST FOR THE SCIENTIFIC 1022 00:38:41,340 --> 00:38:42,875 COMMUNITY AND INTERNAL REFERENCE 1023 00:38:42,875 --> 00:38:43,142 DOCUMENT. 1024 00:38:43,142 --> 00:38:44,577 THERE ARE WE'RE MAKE CONCERTED 1025 00:38:44,577 --> 00:38:48,748 EFFORT TO CANVAS AND PROVIDE 1026 00:38:48,748 --> 00:38:50,883 OPPORTUNITIES TO PROVIDE INPUT 1027 00:38:50,883 --> 00:38:53,452 AND PARTICIPATING IN THE 1028 00:38:53,452 --> 00:38:54,954 INVITATION ONLY GENERATION 1029 00:38:54,954 --> 00:38:57,490 MEETING I REFERRED TO OR VIA 1030 00:38:57,490 --> 00:38:58,691 REQUEST FOR INFORMATION SUCH AS 1031 00:38:58,691 --> 00:39:00,626 THE ONE WE ISSUED LAST FALL. 1032 00:39:00,626 --> 00:39:02,094 THIS FALL THE INSTITUTE WILL 1033 00:39:02,094 --> 00:39:04,764 AGAIN ISSUE AN RFI TO GET 1034 00:39:04,764 --> 00:39:07,333 FURTHER INPUT ON A SUBSET OF 1035 00:39:07,333 --> 00:39:10,469 TOPICS THAT WERE IDENTIFIED BY 1036 00:39:10,469 --> 00:39:13,539 PARTICIPANTS AT THE STRATEGIC 1037 00:39:13,539 --> 00:39:14,106 PLANNING MEETING NEXT WEEK. 1038 00:39:14,106 --> 00:39:14,941 IN THIS WAY EVERYONE WILL HAVE A 1039 00:39:14,941 --> 00:39:16,943 CHANCE FOR THE VOICES TO BE 1040 00:39:16,943 --> 00:39:18,845 HEARD EVEN IF THEY DIDN'T ATTEND 1041 00:39:18,845 --> 00:39:19,912 THAT IN PERSON MEETING. 1042 00:39:19,912 --> 00:39:22,048 I SHOULD SAY THE IDEA GENERATION 1043 00:39:22,048 --> 00:39:22,882 MEETING. 1044 00:39:22,882 --> 00:39:24,550 IT WAS SO GOOD IT FELT IN 1045 00:39:24,550 --> 00:39:25,151 PERSON. 1046 00:39:25,151 --> 00:39:26,252 WE HOPE YOU'LL SPREAD THE WORD 1047 00:39:26,252 --> 00:39:27,820 ABOUT THE RFI WHEN IT'S 1048 00:39:27,820 --> 00:39:30,289 PUBLISHED. 1049 00:39:30,289 --> 00:39:32,124 SO BEFORE I CLOSE THOUGH I'D 1050 00:39:32,124 --> 00:39:36,529 LIKE TO DRAWER YOUR ATTENTION TO 1051 00:39:36,529 --> 00:39:39,432 A REQUEST FOR INFORMATION NIH 1052 00:39:39,432 --> 00:39:41,100 PUBLISHED WEEKS AGO IN RESPONSE 1053 00:39:41,100 --> 00:39:41,868 FROM THE ADVISORY COMMITTEE TO 1054 00:39:41,868 --> 00:39:44,103 THE DIRECTOR WORKING GROUP ON 1055 00:39:44,103 --> 00:39:47,073 DIVERSITY, NIH HAS DEVELOPED A 1056 00:39:47,073 --> 00:39:47,907 PROPOSED REVISED MISSION 1057 00:39:47,907 --> 00:39:49,909 STATEMENT AND SEEKING INPUT FROM 1058 00:39:49,909 --> 00:39:53,012 INTEREST GROUPS THROUGHOUT THE 1059 00:39:53,012 --> 00:39:54,347 SCIENTIFIC RESEARCH, ADVOCACY 1060 00:39:54,347 --> 00:39:57,483 AND CLINICAL PRACTICE COMMUNITY. 1061 00:39:57,483 --> 00:39:59,418 THOSE EMPLOYED BY NIH OR 1062 00:39:59,418 --> 00:40:00,019 INSTITUTIONS RECEIVING NIH 1063 00:40:00,019 --> 00:40:01,487 SUPPORT AND THE PUBLIC ON THE 1064 00:40:01,487 --> 00:40:03,723 PROPOSED STATEMENT. 1065 00:40:03,723 --> 00:40:04,824 ADDITIONAL INFORMATION ABOUT THE 1066 00:40:04,824 --> 00:40:06,826 EFFORT AND HOW TO PROVIDE INPUT 1067 00:40:06,826 --> 00:40:08,127 IS AVAILABLE ON THE NIH WEBSITE 1068 00:40:08,127 --> 00:40:09,829 AND I ENCOURAGE ALL OF YOU TO 1069 00:40:09,829 --> 00:40:12,498 REVIEW THE PROPOSAL, SHARE IT 1070 00:40:12,498 --> 00:40:14,133 WITH YOUR COMMUNITIES AND 1071 00:40:14,133 --> 00:40:17,770 CONSIDER PROVIDING YOUR INPUT. 1072 00:40:17,770 --> 00:40:18,804 FINALLY, FOR THOSE INTERESTED IN 1073 00:40:18,804 --> 00:40:21,274 LEARNING MORE ABOUT OUR 1074 00:40:21,274 --> 00:40:22,875 PROGRAMS, PLEASE VISIT THE NIAMS 1075 00:40:22,875 --> 00:40:23,109 WEBSITE. 1076 00:40:23,109 --> 00:40:26,112 YOU CAN ALSO FIND US ON 1077 00:40:26,112 --> 00:40:28,147 FACEBOOK, LINKEDIN AND YOUTUBE 1078 00:40:28,147 --> 00:40:31,317 AND TO LEARN MORE ABOUT OUR 1079 00:40:31,317 --> 00:40:33,486 FUNDING PROGRAMS SUBSCRIBE TO 1080 00:40:33,486 --> 00:40:40,092 OUR NEWSLETTER AND FOLLOW OUR 1081 00:40:40,092 --> 00:40:40,793 FORMERLY KNOWN AS TWITTER 1082 00:40:40,793 --> 00:40:41,394 ACCOUNT. 1083 00:40:41,394 --> 00:40:42,995 THAT CONCLUDES MY REMARKS. 1084 00:40:42,995 --> 00:40:45,698 I'M HAPPY TO TAKE ANY QUESTIONS 1085 00:40:45,698 --> 00:40:56,175 YOU MIGHT HAVE AT THIS TIME. 1086 00:40:57,944 --> 00:40:58,077 OKAY. 1087 00:40:58,077 --> 00:41:05,484 I'M AFRAID I CAN'T SEE NAME 1088 00:41:05,484 --> 00:41:09,355 TAGS. 1089 00:41:09,355 --> 00:41:13,092 >> MY QUESTION IS THERE'S BEEN 1090 00:41:13,092 --> 00:41:14,527 SUCH PUSHBACK ON DEI IN THE 1091 00:41:14,527 --> 00:41:16,629 FEDERAL GOVERNMENT. 1092 00:41:16,629 --> 00:41:16,829 SORRY. 1093 00:41:16,829 --> 00:41:21,267 THERE'S BEEN SUCH A PUSHBACK ON 1094 00:41:21,267 --> 00:41:22,668 DEI IN THE FEDERAL GOVERNMENT 1095 00:41:22,668 --> 00:41:23,502 GOVERNMENT PARTICULARLY IN THE 1096 00:41:23,502 --> 00:41:25,137 STATE OF FLORIDA. 1097 00:41:25,137 --> 00:41:28,841 SO HAVE YOU RUN INTO OR GETTING 1098 00:41:28,841 --> 00:41:30,376 STARTED ON YOUR NEW DIVISION 1099 00:41:30,376 --> 00:41:33,512 WITH DEI, DO YOU THINK YOU'LL 1100 00:41:33,512 --> 00:41:35,848 RUN INTO ANY PUSHBACK ON THAT 1101 00:41:35,848 --> 00:41:36,682 BECAUSE IT SEEMS LIKE THEY'RE 1102 00:41:36,682 --> 00:41:39,151 TRYING TO GET RID OF DEI IN A 1103 00:41:39,151 --> 00:41:40,720 LOT OF THE DIFFERENT 1104 00:41:40,720 --> 00:41:42,588 CORPORATIONS AND ORGANIZATIONS. 1105 00:41:42,588 --> 00:41:43,389 >> RIGHT. 1106 00:41:43,389 --> 00:41:46,125 WELL, WE AT THE NIH ARE UNIFIED 1107 00:41:46,125 --> 00:41:49,261 IN OUR SUPPORT OF DIVERSITY, 1108 00:41:49,261 --> 00:41:51,998 EQUITY, INCLUSION AND 1109 00:41:51,998 --> 00:41:53,366 ACCESSIBILITY ISSUES AND 1110 00:41:53,366 --> 00:41:55,034 CONCERNS AND PROGRAMS SO WE ARE 1111 00:41:55,034 --> 00:41:56,035 MOVING AHEAD AND DOING 1112 00:41:56,035 --> 00:41:58,404 EVERYTHING THAT WE CAN. 1113 00:41:58,404 --> 00:42:02,441 WE FEEL MORALLY OBLIGED TO MAKE 1114 00:42:02,441 --> 00:42:04,143 PROGRESS IN THE AREA AND IT'S A 1115 00:42:04,143 --> 00:42:05,578 MAJOR INITIATIVE AND WE'RE BEING 1116 00:42:05,578 --> 00:42:08,114 MINDFUL OF CONSIDERATIONS SUCH 1117 00:42:08,114 --> 00:42:11,751 AS GUIDANCE FROM THE GENERAL 1118 00:42:11,751 --> 00:42:13,285 COUNSEL AND OTHER GUIDANCE WE 1119 00:42:13,285 --> 00:42:15,354 MAY BECOME AWARE OF BUT WE'RE 1120 00:42:15,354 --> 00:42:16,355 COMMITTED TO MAKING PROGRESS IN 1121 00:42:16,355 --> 00:42:18,524 THIS AREA AND ACTUALLY OUR 1122 00:42:18,524 --> 00:42:19,658 ACTING NIH DIRECTOR JUST WALKED 1123 00:42:19,658 --> 00:42:22,561 IN AND I APPLAUD HIS DEEP 1124 00:42:22,561 --> 00:42:23,562 COMMITMENT TO THIS AREA. 1125 00:42:23,562 --> 00:42:24,997 YOU'LL HEAR FROM HIM IN A COUPLE 1126 00:42:24,997 --> 00:42:26,732 MINUTES BUT WE COULD HAVE NOT 1127 00:42:26,732 --> 00:42:29,568 ASKED FOR A MORE SUPPORTED AND 1128 00:42:29,568 --> 00:42:31,537 COMMITTED LEADER ON THAT FRONT. 1129 00:42:31,537 --> 00:42:33,472 I SHARE YOUR CONCERN BUT I WANT 1130 00:42:33,472 --> 00:42:35,341 TO REASSURE YOU, WE'RE REALLY 1131 00:42:35,341 --> 00:42:35,941 COMMITTED TO PROGRESS IN THIS 1132 00:42:35,941 --> 00:42:41,480 AREA. 1133 00:42:41,480 --> 00:42:44,784 OTHER QUESTIONS? 1134 00:42:44,784 --> 00:42:47,653 I'M AVAILABLE ALL DAY FOR THOSE 1135 00:42:47,653 --> 00:42:49,155 WHO WANT TO CATCH ME IN PRIVATE. 1136 00:42:49,155 --> 00:42:50,489 HAPPY TO TAKE QUESTIONS AT THIS 1137 00:42:50,489 --> 00:42:50,723 TIME. 1138 00:42:50,723 --> 00:43:01,133 WE HAVE PLENTY OF TIME. 1139 00:43:01,934 --> 00:43:04,537 >> THANK YOU, DR. CRISWELL. 1140 00:43:04,537 --> 00:43:04,937 GREAT TALK. 1141 00:43:04,937 --> 00:43:06,072 WE HAVE A LOT OF RARE DISEASES 1142 00:43:06,072 --> 00:43:07,039 IN THE ROOM HERE TODAY. 1143 00:43:07,039 --> 00:43:10,276 I KNOW YOU MENTIONED A FEW OF 1144 00:43:10,276 --> 00:43:10,843 THE RARE DISEASES GETTING 1145 00:43:10,843 --> 00:43:12,378 SPECIFIC FOCUS AND ATTENTION BUT 1146 00:43:12,378 --> 00:43:16,749 A LOT OF THE FOLKS ARE ALWAYS 1147 00:43:16,749 --> 00:43:17,883 ASKING QUESTIONS ABOUT HOW DO 1148 00:43:17,883 --> 00:43:19,919 THEY BETTER ENGAGE WITH THE NIH 1149 00:43:19,919 --> 00:43:21,454 AND WOULD LOVE TO HEAR GUIDANCE 1150 00:43:21,454 --> 00:43:31,931 FROM YOU ON THAT. 1151 00:43:31,931 --> 00:43:33,732 >> RARE DISEASES ARE EXTREMELY 1152 00:43:33,732 --> 00:43:35,568 IMPORTANT AND NIAMS HAS A 1153 00:43:35,568 --> 00:43:36,135 HISTORY OF SUPPORTING RARE 1154 00:43:36,135 --> 00:43:37,503 DISEASE AND I'M PROUD OF THAT 1155 00:43:37,503 --> 00:43:41,140 AND OTHER INSTITUTES AND CENTERS 1156 00:43:41,140 --> 00:43:42,441 RECOGNIZE THE IMPORTANT AND WE 1157 00:43:42,441 --> 00:43:44,176 HAVE A LOT TO LEARN IN DRILLING 1158 00:43:44,176 --> 00:43:45,978 DOWN TO THE ROOT CAUSES OF RARE 1159 00:43:45,978 --> 00:43:46,979 DISEASES BECAUSE THEY CANNOT 1160 00:43:46,979 --> 00:43:49,148 ONLY PROVIDE SOLUTIONS FOR THOSE 1161 00:43:49,148 --> 00:43:51,050 WHO SUFFER WITH THOSE CONDITIONS 1162 00:43:51,050 --> 00:43:52,985 BUT PROVIDE INSIGHT INTO OTHER 1163 00:43:52,985 --> 00:43:54,253 MORE COMMON CONDITIONS. 1164 00:43:54,253 --> 00:43:57,022 SO I THINK THERE IS ABSOLUTELY 1165 00:43:57,022 --> 00:44:02,761 EVERY REASON TO BE PURSUING 1166 00:44:02,761 --> 00:44:03,896 EFFORTS IN RARE DISEASE AS WELL 1167 00:44:03,896 --> 00:44:07,433 AS COMMON DISEASE. 1168 00:44:07,433 --> 00:44:08,467 INCREASINGLY, WE RECOGNIZE THE 1169 00:44:08,467 --> 00:44:10,002 DEFINITIONS THAT WE HAVE 1170 00:44:10,002 --> 00:44:12,071 DEVELOPED FOR DISEASES AND 1171 00:44:12,071 --> 00:44:13,472 CONDITIONS ARE REALLY OFFICIAL. 1172 00:44:13,472 --> 00:44:15,174 THEY DON'T REFLECT THE 1173 00:44:15,174 --> 00:44:17,042 UNDERLYING BIOLOGY AND IN SOME 1174 00:44:17,042 --> 00:44:18,477 RESPECTS THEY POSE SOME 1175 00:44:18,477 --> 00:44:18,944 CONSTRAINT. 1176 00:44:18,944 --> 00:44:20,246 WE'RE TRYING THROUGH THE 1177 00:44:20,246 --> 00:44:22,548 ACCELERATED MEDICINES 1178 00:44:22,548 --> 00:44:23,749 PARTNERSHIP AND OTHER PROGRAMS 1179 00:44:23,749 --> 00:44:27,520 RECOGNIZE WE NEED TO MAKE SURE 1180 00:44:27,520 --> 00:44:30,022 THAT THE DISEASE DEFINITIONS AND 1181 00:44:30,022 --> 00:44:32,558 HOW WE'RE ORGANIZED IN OUR 1182 00:44:32,558 --> 00:44:34,493 STRUCTURES DON'T INTERFERE WITH 1183 00:44:34,493 --> 00:44:35,394 UNDERSTANDING THE BIOLOGY OF THE 1184 00:44:35,394 --> 00:44:35,694 DISEASE. 1185 00:44:35,694 --> 00:44:37,463 I'M EXCITE ABOUT A NEW EFFORT I 1186 00:44:37,463 --> 00:44:43,302 DIDN'T MENTION HAPPENING IT'S 1187 00:44:43,302 --> 00:44:44,003 CALLED SYSTEMS BIOLOGY OF 1188 00:44:44,003 --> 00:44:47,373 INFLAMMATION AND RECOGNIZES THE 1189 00:44:47,373 --> 00:44:49,375 FACT THAT IF WE CAN INTEGRATE 1190 00:44:49,375 --> 00:44:50,709 KNOWLEDGE AND DATA ACROSS 1191 00:44:50,709 --> 00:44:52,678 MULTIPLE DIFFERENT TYPES OF 1192 00:44:52,678 --> 00:44:54,079 DISEASE, WE'LL DISCOVER 1193 00:44:54,079 --> 00:44:55,614 CONNECTIONS WE HADN'T 1194 00:44:55,614 --> 00:44:56,815 APPRECIATED AND WE MAY NOT EVER 1195 00:44:56,815 --> 00:44:59,718 DISCOVER IF WE CONTINUE TO FOCUS 1196 00:44:59,718 --> 00:45:01,020 ON THE DISEASE AND CONDITION 1197 00:45:01,020 --> 00:45:03,289 DEFINITIONS WE CURRENTLY HAVE. 1198 00:45:03,289 --> 00:45:05,524 SO ANYWAY, I HOPE THAT HELPS 1199 00:45:05,524 --> 00:45:06,125 ADDRESS SOME OF YOUR CONCERNS 1200 00:45:06,125 --> 00:45:10,829 THERE. 1201 00:45:10,829 --> 00:45:13,499 ANY OTHER QUESTIONS AT THIS 1202 00:45:13,499 --> 00:45:15,301 POINT? 1203 00:45:15,301 --> 00:45:24,677 LOOKS LIKE LEE HAS A QUESTION. 1204 00:45:24,677 --> 00:45:27,713 WE'RE ALL GATHERED HERE, 40 PLUS 1205 00:45:27,713 --> 00:45:28,814 ADVOCACY ORGANIZATIONS HERE. 1206 00:45:28,814 --> 00:45:30,115 WHAT DO YOU THINK WOULD BE THE 1207 00:45:30,115 --> 00:45:32,484 BEST WAY FOR US TO SUPPORT NIAMS 1208 00:45:32,484 --> 00:45:38,157 GOING FORWARD? 1209 00:45:38,157 --> 00:45:41,493 >> YOU CAN HELP US TREMENDOUSLY 1210 00:45:41,493 --> 00:45:44,897 BY MAKING MORE VISIBLE THE 1211 00:45:44,897 --> 00:45:45,731 IMPORTANCE OF THE CONDITIONS 1212 00:45:45,731 --> 00:45:48,567 WITHIN OUR MISSION AREAS, THE 1213 00:45:48,567 --> 00:45:50,803 CHALLENGES THAT INDIVIDUALS AND 1214 00:45:50,803 --> 00:45:53,339 THEIR FAMILIES, THE IMPACT IN 1215 00:45:53,339 --> 00:45:56,375 TERMS OF QUALITY OF LIFE, LENGTH 1216 00:45:56,375 --> 00:45:58,410 OF LIFE, THE FINANCIAL IMPACT. 1217 00:45:58,410 --> 00:46:03,983 WE'RE SOMETIMES CHALLENGED TO BE 1218 00:46:03,983 --> 00:46:07,453 AS VISIBLE AS WE THINK WE SHOULD 1219 00:46:07,453 --> 00:46:08,454 BECAUSE MANY OF THE DISEASES 1220 00:46:08,454 --> 00:46:18,998 DON'T RESULT IN THE END OF LIFE. 1221 00:46:20,466 --> 00:46:22,234 AND THEY IMPACT LIFE. 1222 00:46:22,234 --> 00:46:23,469 SOMETIMES THE IMPORTANCE OF 1223 00:46:23,469 --> 00:46:26,171 THOSE CONDITIONS IS NOT 1224 00:46:26,171 --> 00:46:28,474 ADEQUATELY APPRECIATED. 1225 00:46:28,474 --> 00:46:30,876 I WOULD ALSO ENCOURAGE YOU TO 1226 00:46:30,876 --> 00:46:37,182 WORK TOGETHER SO THAT INSTEAD OF 1227 00:46:37,182 --> 00:46:40,519 SPEAKING 90 PLUS INDIVIDUAL 1228 00:46:40,519 --> 00:46:43,756 ORGANIZATIONS YOU'RE SPEAKING AS 1229 00:46:43,756 --> 00:46:44,723 THE COALITION. 1230 00:46:44,723 --> 00:46:46,225 IF I WAS TRYING TO UNDERSTAND 1231 00:46:46,225 --> 00:46:47,826 THE LANDSCAPE IT WOULD BE 1232 00:46:47,826 --> 00:46:49,995 HELPFUL TO ME SO I ENCOURAGE YOU 1233 00:46:49,995 --> 00:46:50,896 TO THINK WITH THE ISSUES AND 1234 00:46:50,896 --> 00:46:53,999 CONCERNS YOU SHARE AND HOW YOU 1235 00:46:53,999 --> 00:46:56,168 CAN WORK TOGETHER TO REPRESENT 1236 00:46:56,168 --> 00:47:00,172 OUR MISSION AREAS. 1237 00:47:00,172 --> 00:47:01,907 I HOPE THAT THAT SORT OF CONCEPT 1238 00:47:01,907 --> 00:47:03,108 IS SOMETHING YOU CAN THINK 1239 00:47:03,108 --> 00:47:03,342 ABOUT. 1240 00:47:03,342 --> 00:47:05,611 I THINK THAT WOULD BE REALLY 1241 00:47:05,611 --> 00:47:08,180 HELPFUL. 1242 00:47:08,180 --> 00:47:18,524 OTHER QUESTIONS AT THIS POINT? 1243 00:47:18,524 --> 00:47:20,292 WELL, WE'RE A LITTLE HEAD OF 1244 00:47:20,292 --> 00:47:20,926 SCHEDULE. 1245 00:47:20,926 --> 00:47:25,464 I SEE DR. TABAK SO MAYBE WE'LL 1246 00:47:25,464 --> 00:47:28,000 MOVE AHEAD. 1247 00:47:28,000 --> 00:47:29,468 THANK YOU FOR YOUR ENGAGEMENT ON 1248 00:47:29,468 --> 00:47:31,837 MY STATE OF THE INSTITUTE AND 1249 00:47:31,837 --> 00:47:33,539 I'LL INTRODUCE DR. TABAK THE 1250 00:47:33,539 --> 00:47:35,240 DIRECTOR OF THE NATIONAL 1251 00:47:35,240 --> 00:47:37,876 INSTITUTES OF HEALTH WHO 1252 00:47:37,876 --> 00:47:39,211 OFFICIALLY TOOK OFFICE DECEMBER 1253 00:47:39,211 --> 00:47:40,446 20, 2021. 1254 00:47:40,446 --> 00:47:42,147 NEEDLESS TO SAY HIS LIST OF 1255 00:47:42,147 --> 00:47:45,417 ACCOMPLISHMENTS AND SERVICE TO 1256 00:47:45,417 --> 00:47:46,952 THE NIH IS LONG BUT I'D LIKE TO 1257 00:47:46,952 --> 00:47:48,187 SHARE SOME HIGHLIGHTS. 1258 00:47:48,187 --> 00:47:51,790 DR. TABAK HAS SERVED AS THE 1259 00:47:51,790 --> 00:47:55,527 PRINCIPLE DEPUTY DIRECTOR AND 1260 00:47:55,527 --> 00:47:57,463 DEPUTY ETHICS COUNSELOR SINCE 1261 00:47:57,463 --> 00:48:07,539 2010 AND SERVED THERE'S ACTING 1262 00:48:07,539 --> 00:48:10,142 DIRECTOR OF NIH AND THE DIRECTOR 1263 00:48:10,142 --> 00:48:17,783 OF CRANIOFACIAL RESEARCH FRAND S 1264 00:48:17,783 --> 00:48:19,451 THE SENIOR ASSOCIATE DEAN FOR 1265 00:48:19,451 --> 00:48:21,053 RESEARCH AND PROFESSOR OF 1266 00:48:21,053 --> 00:48:25,891 DENTISTRY AND BIO CHEMISTRY AT 1267 00:48:25,891 --> 00:48:31,130 THE SCHOOL OF DENTISTRY AT THE 1268 00:48:31,130 --> 00:48:34,466 SCHOOL OF RODCHESTER, NEW YORK 1269 00:48:34,466 --> 00:48:38,570 AND A MERIT AWARD RECIPIENT 1270 00:48:38,570 --> 00:48:40,239 EXTENDING RESEARCH IN TIME. 1271 00:48:40,239 --> 00:48:42,541 THAT MEANS HE WAS A FANTASTIC 1272 00:48:42,541 --> 00:48:45,477 NIH AWARD RECIPIENT AND HIS 1273 00:48:45,477 --> 00:48:46,745 MAJOR RESEARCH FOCUS HAS BEEN ON 1274 00:48:46,745 --> 00:48:48,046 THE STRUCTURE AND FUNCTION OF 1275 00:48:48,046 --> 00:48:50,949 GLYCOPROTEINS. 1276 00:48:50,949 --> 00:48:53,352 HE CONTINUES TO WORK ON HIS AREA 1277 00:48:53,352 --> 00:48:56,155 MAINTAINING AN ACTIVE RESEARCH 1278 00:48:56,155 --> 00:49:00,392 LABORATORY WITHIN THE NIH 1279 00:49:00,392 --> 00:49:03,128 PROGRAM IN ADDITION TO HIS MANY 1280 00:49:03,128 --> 00:49:04,596 ADMINISTRATIVE DUTIES AND IS 1281 00:49:04,596 --> 00:49:06,565 ELECTED TO THE NATIONAL ACADEMY 1282 00:49:06,565 --> 00:49:08,634 OF MEDICINE AF THE NATIONAL 1283 00:49:08,634 --> 00:49:11,570 ACADEMIES AND RECEIVED HIS 1284 00:49:11,570 --> 00:49:12,438 UNDERGRADUATE FROM COLLEGE OF 1285 00:49:12,438 --> 00:49:15,073 NEW YORK AND DDSD FROM COLUMBIA 1286 00:49:15,073 --> 00:49:16,175 UNIVERSITY AND Ph.D. FROM THE 1287 00:49:16,175 --> 00:49:17,242 UNIVERSITY OF BUFFALO. 1288 00:49:17,242 --> 00:49:19,511 DR. TABAK, THANK YOU FOR BEING 1289 00:49:19,511 --> 00:49:21,780 HERE TO WELCOME PARTICIPANTS TO 1290 00:49:21,780 --> 00:49:23,282 THE 2023 NIAMS COALITION 1291 00:49:23,282 --> 00:49:28,120 OUTREACH AND EDUCATION DAY AND I 1292 00:49:28,120 --> 00:49:33,492 KNOW THAT YOU WERE ABLE TO 1293 00:49:33,492 --> 00:49:36,695 WELCOME US VIA VIDEO IN 2019 AND 1294 00:49:36,695 --> 00:49:37,496 NOW THANK YOU SO MUCH FOR BEING 1295 00:49:37,496 --> 00:49:47,639 WITH US. 1296 00:49:56,315 --> 00:50:01,487 >> THANK YOU FOR THAT ELABORATE 1297 00:50:01,487 --> 00:50:10,295 INTRODUCTION. 1298 00:50:10,295 --> 00:50:13,732 SO IT'S GREAT TO SEE ALL OF YOU 1299 00:50:13,732 --> 00:50:14,199 HERE IN PERSON. 1300 00:50:14,199 --> 00:50:19,004 I ACTUALLY SEE A COUPLE OF 1301 00:50:19,004 --> 00:50:22,241 FAMILIAR FACES FROM MY TIME AT 1302 00:50:22,241 --> 00:50:22,441 NIDCR. 1303 00:50:22,441 --> 00:50:30,849 THERE WAS SOME OVERLAP IN OUR 1304 00:50:30,849 --> 00:50:32,217 MISSION. 1305 00:50:32,217 --> 00:50:37,890 I WANTED TO DO THIS BECAUSE 1306 00:50:37,890 --> 00:50:39,925 YOU'RE WHY WE HAVE NIH. 1307 00:50:39,925 --> 00:50:41,393 IT'S JUST WONDERFUL TO HAVE SO 1308 00:50:41,393 --> 00:50:42,661 MANY OF YOU HERE IN ONE ROOM 1309 00:50:42,661 --> 00:50:46,798 TOGETHER. 1310 00:50:46,798 --> 00:50:48,634 IT'S BEEN ALL TOO LONG ACTUALLY. 1311 00:50:48,634 --> 00:50:53,839 SO I'VE BEEN ACTING DIRECTOR NOW 1312 00:50:53,839 --> 00:50:56,842 SINCE DECEMBER OF '21. 1313 00:50:56,842 --> 00:51:01,480 SO NEXT MONTH IS 22 MONTHS AND 1314 00:51:01,480 --> 00:51:06,685 COUNTING THOUGH THERE IS HOPE ON 1315 00:51:06,685 --> 00:51:10,522 THE HORIZON AND WE'RE VERY MUCH 1316 00:51:10,522 --> 00:51:12,291 LOOKING FORWARD TO 1317 00:51:12,291 --> 00:51:14,860 DR. BERTAGNOLLI'S SPEEDY 1318 00:51:14,860 --> 00:51:19,665 CONFIRMATION TO WHICH WE SAY 1319 00:51:19,665 --> 00:51:19,998 AMEN. 1320 00:51:19,998 --> 00:51:21,667 BUT I'VE BEEN AROUND HERE FOR A 1321 00:51:21,667 --> 00:51:21,867 WHILE. 1322 00:51:21,867 --> 00:51:24,503 SOME WOULD THINK I CAN'T HOLD A 1323 00:51:24,503 --> 00:51:30,175 JOB ANY PLACE BECAUSE OF THE 1324 00:51:30,175 --> 00:51:31,376 LITANY OF THINGS I'VE BEEN DOING 1325 00:51:31,376 --> 00:51:37,215 AND THROUGH ALL THOSE ACTIVITIES 1326 00:51:37,215 --> 00:51:38,517 ONE THING COMES BACK OVER AND 1327 00:51:38,517 --> 00:51:39,284 OVER AGAIN. 1328 00:51:39,284 --> 00:51:42,654 I'LL TALK INTO THIS THING. 1329 00:51:42,654 --> 00:51:43,221 THIS WORKS. 1330 00:51:43,221 --> 00:51:43,522 LET'S ADAPT. 1331 00:51:43,522 --> 00:51:49,494 IT WILL BE OKAY. 1332 00:51:49,494 --> 00:51:51,463 I'VE LEARNED OVER AND OVER AGAIN 1333 00:51:51,463 --> 00:51:56,201 HOW IMPORTANT YOUR VOICES ARE 1334 00:51:56,201 --> 00:51:59,972 AND I APPRECIATE THAT YOU EACH 1335 00:51:59,972 --> 00:52:00,872 REPRESENT YOUR OWN SPECIFIC AREA 1336 00:52:00,872 --> 00:52:03,141 OF INTEREST AND THAT'S GREAT BUT 1337 00:52:03,141 --> 00:52:07,112 AS DR. CRISWELL SAID, SOMETIMES 1338 00:52:07,112 --> 00:52:09,481 BANDING TOGETHER IS MUCH MORE 1339 00:52:09,481 --> 00:52:11,550 POWERFUL AND IF YOU APPROACH 1340 00:52:11,550 --> 00:52:13,952 MEMBER OF CONGRESS AND TALK 1341 00:52:13,952 --> 00:52:16,755 ABOUT 90 DIFFERENT ORGANIZATIONS 1342 00:52:16,755 --> 00:52:17,823 REPRESENTING HOWEVER, MANY 1343 00:52:17,823 --> 00:52:19,224 THOUSANDS AND THOUSANDS OF 1344 00:52:19,224 --> 00:52:22,127 PEOPLE, TENS OF THOUSANDS OF 1345 00:52:22,127 --> 00:52:29,468 PEOPLE, THAT HAS TREMENDOUS 1346 00:52:29,468 --> 00:52:30,736 EFFECT. 1347 00:52:30,736 --> 00:52:32,204 WE HAVE WORKED CLOSELY WITH 1348 00:52:32,204 --> 00:52:33,538 ORGANIZATIONS SUCH AS THE ONES 1349 00:52:33,538 --> 00:52:34,539 YOU REPRESENT FOR MANY YEARS. 1350 00:52:34,539 --> 00:52:41,446 I CAN TELL YOU AS AN INSTITUTE 1351 00:52:41,446 --> 00:52:42,681 DIRECTOR IT INFLUENCED 1352 00:52:42,681 --> 00:52:47,519 DRAMATICALLY HOW WE POSITIONED 1353 00:52:47,519 --> 00:52:49,054 OURSELVES, HOW WE REORGANIZED 1354 00:52:49,054 --> 00:52:49,655 PRIORITIES TO BE MORE PATIENT 1355 00:52:49,655 --> 00:52:56,228 CENTRIC. 1356 00:52:56,228 --> 00:53:01,166 AND I KNOW NIAMS HAS A HISTORY 1357 00:53:01,166 --> 00:53:02,234 OF THAT AND THE LATE STEVE KATZ 1358 00:53:02,234 --> 00:53:04,236 AND I WERE COLLEAGUES AND WE 1359 00:53:04,236 --> 00:53:06,571 USED TO TALK ABOUT THAT A LOT 1360 00:53:06,571 --> 00:53:08,273 AND DR. CRISWELL HAS CONTINUED 1361 00:53:08,273 --> 00:53:11,176 AND BUILT UPON THAT IN A VERY 1362 00:53:11,176 --> 00:53:21,353 REAL WAY. 1363 00:53:23,321 --> 00:53:26,224 WE'RE REALLY TRYING TO BE MUCH 1364 00:53:26,224 --> 00:53:28,794 MORE RESPONSIVE TO PATIENT 1365 00:53:28,794 --> 00:53:29,027 GROUPS. 1366 00:53:29,027 --> 00:53:29,961 THE SPECIFIC ISSUE OF RARE 1367 00:53:29,961 --> 00:53:33,365 DISEASES BROUGHT UP AS A WALKED 1368 00:53:33,365 --> 00:53:39,204 IN, CONGRESS IS ALWAYS ASKING ME 1369 00:53:39,204 --> 00:53:41,473 ABOUT RARE DISEASES. 1370 00:53:41,473 --> 00:53:46,712 THEY TAKE OUT THEIR CALCULATORS 1371 00:53:46,712 --> 00:53:48,080 AND I DON'T KNOW HOW YOU 1372 00:53:48,080 --> 00:53:49,448 CALCULATE A PERSON'S LIFE BUT IF 1373 00:53:49,448 --> 00:53:56,221 YOU HAVE THE DISEASE IT'S NOT SO 1374 00:53:56,221 --> 00:53:56,421 RARE. 1375 00:53:56,421 --> 00:53:58,657 THAT USUALLY GETS THEM TO THINK 1376 00:53:58,657 --> 00:54:01,626 ABOUT THIS IN A SOMEWHAT 1377 00:54:01,626 --> 00:54:07,065 DIFFERENT WAY. 1378 00:54:07,065 --> 00:54:10,202 I DO THINK YOU HAVE COMING UP A 1379 00:54:10,202 --> 00:54:15,273 WHOLE SERIES OF IMPORTANT 1380 00:54:15,273 --> 00:54:17,242 VISITORS TO YOUR GROUP YOU HAVE 1381 00:54:17,242 --> 00:54:19,377 SPEAKERS FROM THE FOUNDATION OF 1382 00:54:19,377 --> 00:54:19,678 NIH. 1383 00:54:19,678 --> 00:54:24,316 DR. CRISWELL MENTIONED SOME OF 1384 00:54:24,316 --> 00:54:27,986 THE AMP PROGRAMS, ACCELERATING 1385 00:54:27,986 --> 00:54:30,489 MEDICINE PARTNERS PROGRAM WHICH 1386 00:54:30,489 --> 00:54:32,190 NIMS HAS TAKEN A LEADERSHIP ROLE 1387 00:54:32,190 --> 00:54:33,992 AND BOB CARTER MADE AN AMAZING 1388 00:54:33,992 --> 00:54:44,336 ROLE AND I THANK HIM FOR THAT. 1389 00:54:44,336 --> 00:54:45,670 WHAT THE AMP PROGRAMS HAVE DONE 1390 00:54:45,670 --> 00:54:50,509 AND HE CAN TELL YOU MORE THAN I 1391 00:54:50,509 --> 00:54:52,611 CAN, HAVE FORGED A RELATIONSHIP 1392 00:54:52,611 --> 00:54:55,914 WITH NON FOR PROFITS, PATIENT 1393 00:54:55,914 --> 00:54:57,516 GROUPS AND THE NIH AND THEY'RE 1394 00:54:57,516 --> 00:55:01,486 IN AREAS NEAR AND DEAR TO MANY 1395 00:55:01,486 --> 00:55:02,020 OF YOUR INTERESTS. 1396 00:55:02,020 --> 00:55:05,257 YOUR ALSO GOING TO HEAR FROM OUR 1397 00:55:05,257 --> 00:55:07,926 COLLEAGUES AT ARPA-H THE NEWEST 1398 00:55:07,926 --> 00:55:08,827 ENTITY WITHIN THE DEPARTMENT OF 1399 00:55:08,827 --> 00:55:19,337 HEALTH AND HUMAN SERVICES AND 1400 00:55:20,205 --> 00:55:22,574 THEY'LL TELL YOU WITH THEIR 1401 00:55:22,574 --> 00:55:29,214 CUTTING-EDGE IDEAS THEY'RE 1402 00:55:29,214 --> 00:55:29,548 IMPLEMENTING. 1403 00:55:29,548 --> 00:55:31,349 THERE'S A POSTER SESSION AND A 1404 00:55:31,349 --> 00:55:33,118 TIME TO SHARE BEST PRACTICES 1405 00:55:33,118 --> 00:55:38,256 FROM EACH OF YOUR ORGANIZATIONS 1406 00:55:38,256 --> 00:55:43,695 AND MOST IMPORTANTLY TIME WITH 1407 00:55:43,695 --> 00:55:44,095 THE STAFF. 1408 00:55:44,095 --> 00:55:51,436 MAKE GOOD USE OF THAT TIME. 1409 00:55:51,436 --> 00:55:52,938 THAT'S THE WHOLE POINT. 1410 00:55:52,938 --> 00:55:54,506 WE WANT TO INFORMALLY LEARN FROM 1411 00:55:54,506 --> 00:55:55,807 ONE ANOTHER AND THE TIME WITH 1412 00:55:55,807 --> 00:55:58,176 STAFF WILL GO AN ALONG WAY IN 1413 00:55:58,176 --> 00:55:58,844 DOING THAT. 1414 00:55:58,844 --> 00:56:03,048 WHEN YOU LEAVE THE MEETING, WHAT 1415 00:56:03,048 --> 00:56:08,253 I HOPE YOU LEAVE WITH IS AN 1416 00:56:08,253 --> 00:56:09,621 INCREASED APPRECIATION FOR NIMS 1417 00:56:09,621 --> 00:56:13,425 AND THE NIH IN GENERAL THAT YOU 1418 00:56:13,425 --> 00:56:15,794 HAVE EXPANDED YOUR NETWORK OF 1419 00:56:15,794 --> 00:56:16,561 COLLEAGUES SO IF YOU'RE 1420 00:56:16,561 --> 00:56:19,464 CURRENTLY SEATED WITH PEOPLE YOU 1421 00:56:19,464 --> 00:56:21,533 KNOW, THE BREAK, SIT DOWN WITH 1422 00:56:21,533 --> 00:56:25,503 PEOPLE YOU DON'T KNOW. 1423 00:56:25,503 --> 00:56:26,271 IT'S IMPORTANT BECAUSE BY THE 1424 00:56:26,271 --> 00:56:27,272 TIME YOU LEAVE YOU SHOULD KNOW 1425 00:56:27,272 --> 00:56:36,815 EVERYBODY IN THE ROOM. 1426 00:56:36,815 --> 00:56:40,118 YOU'LL COME AWAY WITH RESOURCES 1427 00:56:40,118 --> 00:56:41,786 NIMS ARE ABLE TO PROVIDE AND 1428 00:56:41,786 --> 00:56:43,221 ADDITIONAL ONES YOU'LL LEARN 1429 00:56:43,221 --> 00:56:43,822 ABOUT FROM ARPA-H AND MAYBE 1430 00:56:43,822 --> 00:56:48,326 THINGS FROM THE FOUNDATION. 1431 00:56:48,326 --> 00:56:53,665 ADD TO YOUR TOOL KIDS. 1432 00:56:53,665 --> 00:56:55,667 I DO HAVE A QUICK REQUEST. 1433 00:56:55,667 --> 00:56:57,802 I CAN'T COME WITHOUT A REQUEST, 1434 00:56:57,802 --> 00:56:58,336 RIGHT. 1435 00:56:58,336 --> 00:57:00,705 SO WE'RE IN THE PROCESS OF 1436 00:57:00,705 --> 00:57:03,875 REWORDING OUR MISSION STATEMENT. 1437 00:57:03,875 --> 00:57:06,845 I HEARD A LITTLE BIT ABOUT OUR 1438 00:57:06,845 --> 00:57:11,283 COMMITMENT TO ENSURING THAT THE 1439 00:57:11,283 --> 00:57:12,984 "A" IN DEIA ACTIVITIES IS WELL 1440 00:57:12,984 --> 00:57:18,523 REPRESENTED AND ADDRESSED. 1441 00:57:18,523 --> 00:57:20,759 WE PUT OUT A REQUEST FOR 1442 00:57:20,759 --> 00:57:24,062 INFORMATION ABOUT THE MISSION 1443 00:57:24,062 --> 00:57:26,131 STATEMENT AND WE REALLY 1444 00:57:26,131 --> 00:57:27,265 ENCOURAGE ALL OF TO YOU RESPOND 1445 00:57:27,265 --> 00:57:31,970 TO THE RFI, REQUEST FOR 1446 00:57:31,970 --> 00:57:33,471 INFORMATION FROM YOUR RESPECTIVE 1447 00:57:33,471 --> 00:57:33,772 VIEW POINTS. 1448 00:57:33,772 --> 00:57:35,774 I'M SURE IF I SPEAK TO THREE OF 1449 00:57:35,774 --> 00:57:37,142 YOU THERE'LL BE FIVE VIEW POINTS 1450 00:57:37,142 --> 00:57:38,343 AND THAT'S FINE, THAT'S WHAT WE 1451 00:57:38,343 --> 00:57:42,280 WANT TO HEAR. 1452 00:57:42,280 --> 00:57:43,915 BECAUSE THESE CHANGES -- MISSION 1453 00:57:43,915 --> 00:57:45,450 STATEMENTS MATTER. 1454 00:57:45,450 --> 00:57:47,652 MAY THINK, OH, WHAT'S THE BIG 1455 00:57:47,652 --> 00:57:47,953 DEAL. 1456 00:57:47,953 --> 00:57:50,288 MISSION STATEMENTS MATTER. 1457 00:57:50,288 --> 00:57:52,190 AND WE REALLY FEEL THE INPUT 1458 00:57:52,190 --> 00:57:53,291 FROM ORGANIZATIONS SUCH AS THE 1459 00:57:53,291 --> 00:57:55,694 ONES YOU ALL REPRESENT ARE 1460 00:57:55,694 --> 00:57:56,895 CRITICALLY IMPORTANT SO WE CAN 1461 00:57:56,895 --> 00:58:00,498 TRY AND GET IT RIGHT. 1462 00:58:00,498 --> 00:58:01,466 WILL EVERYBODY AGREE? 1463 00:58:01,466 --> 00:58:05,971 NO. 1464 00:58:05,971 --> 00:58:10,075 BUT WE WANT TO GET AS CLOSE TO 1465 00:58:10,075 --> 00:58:11,009 CONSENSUS AS IS POSSIBLE BECAUSE 1466 00:58:11,009 --> 00:58:13,345 NOT ONLY WHAT WE DO BUT WHAT WE 1467 00:58:13,345 --> 00:58:18,016 STAY HAS AN AFFECT ON PEOPLE. 1468 00:58:18,016 --> 00:58:18,850 THAT MISSION STATEMENT CAN HAVE 1469 00:58:18,850 --> 00:58:21,119 AN EFFECT ON PEOPLE AND THAT'S 1470 00:58:21,119 --> 00:58:22,854 WHY WE'RE IN THE SPACE WE ARE 1471 00:58:22,854 --> 00:58:26,725 NOW CONSIDERING ITS REVISION. 1472 00:58:26,725 --> 00:58:28,727 I HOPE TODAY'S MEETING WILL 1473 00:58:28,727 --> 00:58:30,161 REINFORCE THE IMPORTANCE OF THE 1474 00:58:30,161 --> 00:58:30,895 PARTNERSHIP WE HAVE. 1475 00:58:30,895 --> 00:58:34,132 THE FACT THAT YOU TOOK THE TIME 1476 00:58:34,132 --> 00:58:37,469 AND TROUBLE TO BE HERE SPEAKS 1477 00:58:37,469 --> 00:58:40,305 VOLUMES ABOUT YOUR COMMITMENT TO 1478 00:58:40,305 --> 00:58:43,274 NIH AND NIMS AND TO ONE ANOTHER 1479 00:58:43,274 --> 00:58:45,477 SUPPORTING EACH OTHER. 1480 00:58:45,477 --> 00:58:48,380 I REALLY THINK THIS IS THE 1481 00:58:48,380 --> 00:58:51,149 PRICELESS ASSET YOU PROVIDE TO 1482 00:58:51,149 --> 00:58:51,649 US. 1483 00:58:51,649 --> 00:58:53,051 AND REALLY JUST WANT TO COMMEND 1484 00:58:53,051 --> 00:58:56,287 ALL OF YOU FOR THE GREAT WORK 1485 00:58:56,287 --> 00:58:58,056 THAT YOU DO. 1486 00:58:58,056 --> 00:58:59,958 AND SO I DON'T KNOW, LINDSEY, IF 1487 00:58:59,958 --> 00:59:02,827 YOU WANTED ME TO TAKE ANY QUICK 1488 00:59:02,827 --> 00:59:03,161 QUESTIONS. 1489 00:59:03,161 --> 00:59:04,129 IF THERE'S ANY QUICK QUESTIONS 1490 00:59:04,129 --> 00:59:07,098 PEOPLE HAVE, I'M HAPPY TO TRY 1491 00:59:07,098 --> 00:59:09,300 AND ANSWER THEM BUT IF NOT WE'LL 1492 00:59:09,300 --> 00:59:18,510 TURN IT BACK TO DR. CRISWELL. 1493 00:59:18,510 --> 00:59:20,311 >> HERE'S A RARE OPPORTUNITY. 1494 00:59:20,311 --> 00:59:26,284 >> YES. 1495 00:59:29,287 --> 00:59:34,959 >> THANK YOU FOR SHARING WITH US 1496 00:59:34,959 --> 00:59:35,960 TODAY. 1497 00:59:35,960 --> 00:59:40,965 WE WERE HEARING FROM 1498 00:59:40,965 --> 00:59:44,335 DR. CRISWELL AND WE WERE 1499 00:59:44,335 --> 00:59:45,336 CHATTING ABOUT THE COMMONALITY 1500 00:59:45,336 --> 00:59:48,039 ACROSS OUR DISEASES AND HOW DO 1501 00:59:48,039 --> 00:59:49,407 YOU WORK ACROSS SO MANY 1502 00:59:49,407 --> 00:59:53,478 INSTITUTES AND CENTERS? 1503 00:59:53,478 --> 00:59:54,946 >> THAT'S AN IMPORTANT QUESTION. 1504 00:59:54,946 --> 00:59:56,815 ONE THAT WE SORT OF STRUGGLE 1505 00:59:56,815 --> 01:00:01,052 WITH EACH AND EVERY DAY. 1506 01:00:01,052 --> 01:00:04,856 SO MUCH OF THIS IS DONE AT THE 1507 01:00:04,856 --> 01:00:05,623 INSTITUTE LEVEL. 1508 01:00:05,623 --> 01:00:08,293 STAFF MEMBERS INTERACTING WITH 1509 01:00:08,293 --> 01:00:10,528 STAFF MEMBERS TO KEEP EACH OTHER 1510 01:00:10,528 --> 01:00:11,663 APPRISED OF WHAT'S ACTUALLY 1511 01:00:11,663 --> 01:00:16,468 GOING ON AT THE GROUND LEVEL. 1512 01:00:16,468 --> 01:00:18,937 WE HAVE AN INSTITUTE AND CENTERS 1513 01:00:18,937 --> 01:00:21,806 DIRECTORS MEETING USUALLY EVERY 1514 01:00:21,806 --> 01:00:22,574 WEEK WHERE PEOPLE SHARE WHAT IT 1515 01:00:22,574 --> 01:00:26,344 IS THEY HAVE COMING UP TO TRY 1516 01:00:26,344 --> 01:00:29,481 AND ENTICE PEOPLE TO WORK 1517 01:00:29,481 --> 01:00:33,885 TOGETHER ON CERTAIN THINGS. 1518 01:00:33,885 --> 01:00:35,954 WE HAVE FORMAL PLANNING ACROSS 1519 01:00:35,954 --> 01:00:37,322 THE AGENCY THROUGH A DIVISION 1520 01:00:37,322 --> 01:00:39,591 WITHIN THE OFFICE OF THE 1521 01:00:39,591 --> 01:00:45,497 DIRECTOR THE ACRONYM IS DPCPSI. 1522 01:00:45,497 --> 01:00:46,931 IT'S SOMETHING ABOUT STRATEGIC 1523 01:00:46,931 --> 01:00:49,367 PLANNING AND COORDINATION AND SO 1524 01:00:49,367 --> 01:00:50,335 FORTH. 1525 01:00:50,335 --> 01:00:53,438 ONLY THE CONGRESS COULD -- BUT 1526 01:00:53,438 --> 01:00:56,941 THAT ALLOWS FOR A MORE FORMAL 1527 01:00:56,941 --> 01:00:58,610 LANDSCAPE ANALYSIS, IF YOU WILL. 1528 01:00:58,610 --> 01:01:03,982 AND WE HAVE MANY TOOLS NOW THAT 1529 01:01:03,982 --> 01:01:13,591 ALLOW US TO INTER -- INTERROGATE 1530 01:01:13,591 --> 01:01:15,126 AND LOOK FOR SYNERGY AND LOOK 1531 01:01:15,126 --> 01:01:17,328 FOR GAPS AND I THINK WHEN YOU 1532 01:01:17,328 --> 01:01:20,665 TAKE ALL THOSE THINGS TOGETHER, 1533 01:01:20,665 --> 01:01:22,600 THAT'S HOW WE GO FORWARD AND TRY 1534 01:01:22,600 --> 01:01:23,902 TO INTEGRATE. 1535 01:01:23,902 --> 01:01:25,637 WE'RE A DECENTRALIZED 1536 01:01:25,637 --> 01:01:26,671 ORGANIZATION BUT THE LEADERSHIP 1537 01:01:26,671 --> 01:01:29,140 AT THE LEADERSHIP LEVEL OF 1538 01:01:29,140 --> 01:01:34,479 INSTITUTE AND CENTER DIRECTORS 1539 01:01:34,479 --> 01:01:37,549 THERE IS ALMOST UNANIMITY WITH 1540 01:01:37,549 --> 01:01:39,450 COHERENCE AND APPROACH TO 1541 01:01:39,450 --> 01:01:41,219 INTEGRATE AS MUCH AS POSSIBLE. 1542 01:01:41,219 --> 01:01:44,322 WE SAW THIS IN A VERY 1543 01:01:44,322 --> 01:01:49,394 SIGNIFICANT WAY DURING THE 1544 01:01:49,394 --> 01:01:49,661 PANDEMIC. 1545 01:01:49,661 --> 01:01:52,397 SOME OF THE THINGS DURING THE 1546 01:01:52,397 --> 01:01:54,032 PANDEMIC HAVE CARRIED OVER IN IF 1547 01:01:54,032 --> 01:01:56,334 WE WORK TOGETHER MAYBE WE CAN 1548 01:01:56,334 --> 01:01:58,636 ENGAGE COMMUNITIES IN A ROBUST 1549 01:01:58,636 --> 01:01:58,836 WAY. 1550 01:01:58,836 --> 01:02:05,076 WE'RE CONTINUING THOSE TYPES OF 1551 01:02:05,076 --> 01:02:05,376 ACTIVITIES. 1552 01:02:05,376 --> 01:02:08,012 I WISH THERE WAS ONE SINGLE 1553 01:02:08,012 --> 01:02:09,480 THING I COULD POINT TO BUT I 1554 01:02:09,480 --> 01:02:10,782 HAVE TO POINT TO A SERIES OF 1555 01:02:10,782 --> 01:02:12,650 THINGS TO ALLOW US TO DO THIS IN 1556 01:02:12,650 --> 01:02:13,785 AN OPTIMAL WAY. 1557 01:02:13,785 --> 01:02:15,720 NOW THAT WE HAVE ARPA-H, WE HAVE 1558 01:02:15,720 --> 01:02:18,923 TO ADD THAT INTO THE MIX AS WELL 1559 01:02:18,923 --> 01:02:20,825 BECAUSE THE FUNDAMENTAL QUESTION 1560 01:02:20,825 --> 01:02:22,961 THAT THEY ASK THAT WE ASK AND 1561 01:02:22,961 --> 01:02:25,129 CONGRESS ASKED IS ARE YOU DOING 1562 01:02:25,129 --> 01:02:29,434 SOMETHING NEW? 1563 01:02:29,434 --> 01:02:33,071 ARE YOU DOING PURPOSE LY 1564 01:02:33,071 --> 01:02:34,639 AUGMENTING WHAT IS BEING DONE. 1565 01:02:34,639 --> 01:02:40,044 YEAR INVOKING THE APPROACH TO -- 1566 01:02:40,044 --> 01:02:42,347 WE'RE INVOKING THE APPROACHES TO 1567 01:02:42,347 --> 01:02:43,548 NAVIGATE THAT AS WELL. 1568 01:02:43,548 --> 01:02:47,085 >> HI, I'M OLIVIA CASEY WITH THE 1569 01:02:47,085 --> 01:02:48,453 AUTOIMMUNE ASSOCIATION. 1570 01:02:48,453 --> 01:02:52,357 HOW DO YOU SEE THE OADR 1571 01:02:52,357 --> 01:02:53,458 INTERACTING AND FUNCTIONING -- 1572 01:02:53,458 --> 01:02:54,993 >> HOW DO I SEE? 1573 01:02:54,993 --> 01:02:59,397 >> THE OADR, OFFICE OF 1574 01:02:59,397 --> 01:02:59,998 AUTOIMMUNE DISEASE RESEARCH. 1575 01:02:59,998 --> 01:03:05,436 >> THIS IS THE NEWEST MEMBER OF 1576 01:03:05,436 --> 01:03:08,806 THE NIH FAMILY AND IT'S STILL 1577 01:03:08,806 --> 01:03:09,474 NASCENT. 1578 01:03:09,474 --> 01:03:13,511 I CAN ONLY DRAW UPON HOW OTHER 1579 01:03:13,511 --> 01:03:16,547 SUCH OFFICES AND PROGRAMS WORK 1580 01:03:16,547 --> 01:03:26,124 AND IT'S MOSTLY CONVENING POWER. 1581 01:03:26,124 --> 01:03:28,092 DON'T MINIMIZE THAT BECAUSE WHEN 1582 01:03:28,092 --> 01:03:30,595 YOU CONVENE, TYPICALLY PROGRAM 1583 01:03:30,595 --> 01:03:31,129 OFFICERS COME WITH THEIR 1584 01:03:31,129 --> 01:03:37,468 CHECKBOOKS. 1585 01:03:37,468 --> 01:03:38,336 THEY'RE LOOKING TO LEVERAGE 1586 01:03:38,336 --> 01:03:39,570 THEIR ACTIVITY WITH SOMEBODY 1587 01:03:39,570 --> 01:03:41,205 ELSE BECAUSE IF THEY BRING A 1588 01:03:41,205 --> 01:03:42,774 DOLLAR AND YOU BRING A DOLLAR, 1589 01:03:42,774 --> 01:03:44,242 NOW YOU HAVE TWO DOLLARS TO 1590 01:03:44,242 --> 01:03:49,614 SPEND TO ATTACK THE PROBLEM. 1591 01:03:49,614 --> 01:03:51,549 INITIALLY IT WILL BE LARGELY 1592 01:03:51,549 --> 01:03:56,387 CONVENING BUT FROM THAT I'M SURE 1593 01:03:56,387 --> 01:03:59,157 WILL COME SYNERGIES IN TERMS OF 1594 01:03:59,157 --> 01:04:04,429 JOINT FUNDING, IN TERMS OF NEW 1595 01:04:04,429 --> 01:04:06,497 PROGRAMS THAT REQUIRE MULTIPLE 1596 01:04:06,497 --> 01:04:08,533 INSTITUTES AND CENTER TO 1597 01:04:08,533 --> 01:04:09,133 PARTICIPATE. 1598 01:04:09,133 --> 01:04:10,635 AND DR. CRISWELL MENTION THE 1599 01:04:10,635 --> 01:04:13,471 WHOLE IDEA OF INFLAMMATION AS 1600 01:04:13,471 --> 01:04:15,206 SORT OF A COMMON THEME ACROSS SO 1601 01:04:15,206 --> 01:04:19,043 MANY DISEASES AND CONDITIONS. 1602 01:04:19,043 --> 01:04:20,345 VIRTUALLY EVERY INSTITUTE AND 1603 01:04:20,345 --> 01:04:23,114 CENTER SHOULD BE CONCERNED ABOUT 1604 01:04:23,114 --> 01:04:24,582 INFLAMMATION AT SOME LEVEL BUT 1605 01:04:24,582 --> 01:04:29,420 MANY HAVE ALWAYS -- NO, THAT'S 1606 01:04:29,420 --> 01:04:32,156 NIAID OR THAT'S NIMS OR WHO ARE 1607 01:04:32,156 --> 01:04:33,658 THEY POINT TO WHEN IN FACT THEY 1608 01:04:33,658 --> 01:04:35,426 SHOULD BE DOING THAT. 1609 01:04:35,426 --> 01:04:37,495 HAVING THAT CONVENING POWER AT 1610 01:04:37,495 --> 01:04:38,996 LEAST INITIALLY IS VERY CRUCIAL 1611 01:04:38,996 --> 01:04:40,131 BUT STAY TUNED BECAUSE IT REALLY 1612 01:04:40,131 --> 01:04:50,575 IS A NASCENT ORGANIZATION. 1613 01:05:00,385 --> 01:05:05,490 >> WE HEARD A LOT TODAY AND WHAT 1614 01:05:05,490 --> 01:05:15,900 IS THE MOST HELPFUL FOR 1615 01:05:16,701 --> 01:05:17,502 [INAUDIBLE] 1616 01:05:17,502 --> 01:05:21,205 >> I THINK MEETINGS LIKE THIS 1617 01:05:21,205 --> 01:05:23,040 ONE IS IMPORTANT BECAUSE THIS IS 1618 01:05:23,040 --> 01:05:27,211 WHAT CATALYZES US INTO ACTION. 1619 01:05:27,211 --> 01:05:29,480 YOU HAVE 90 DIFFERENT 1620 01:05:29,480 --> 01:05:33,017 ORGANIZATIONS REPRESENTED HERE. 1621 01:05:33,017 --> 01:05:35,987 THAT HOLDS OUR FEET TO THE FIRE, 1622 01:05:35,987 --> 01:05:36,287 IF YOU WILL. 1623 01:05:36,287 --> 01:05:37,922 IT HOLDS US ACCOUNTABLE. 1624 01:05:37,922 --> 01:05:39,624 WHAT WE ALSO LEARNED AND THIS 1625 01:05:39,624 --> 01:05:41,726 WAS PARTICULARLY TRUE DURING THE 1626 01:05:41,726 --> 01:05:43,828 PANDEMIC BUT IT'S CERTAINLY 1627 01:05:43,828 --> 01:05:46,631 SPILLED OVER INTO OTHER THINGS 1628 01:05:46,631 --> 01:05:50,468 UNLESS WE ENGAGE WITH PATIENTS 1629 01:05:50,468 --> 01:05:53,471 DIRECTLY AND WITH PEOPLE WITH 1630 01:05:53,471 --> 01:05:56,641 LIVED EXPERIENCE THE ANSWER IS 1631 01:05:56,641 --> 01:05:57,775 OVER HERE AND WE'RE OVER HERE 1632 01:05:57,775 --> 01:06:04,482 AND WE WANT TO MEET IN THE 1633 01:06:04,482 --> 01:06:04,715 MIDDLE. 1634 01:06:04,715 --> 01:06:06,184 I THINK THE CONTINUED EMPHASIS 1635 01:06:06,184 --> 01:06:07,285 BY ORGANIZATIONS SUCH AS 1636 01:06:07,285 --> 01:06:11,355 YOURSELVES AND SUPPORT FROM THE 1637 01:06:11,355 --> 01:06:14,358 CONGRESS FROM WHICH WE DERIVE 1638 01:06:14,358 --> 01:06:17,495 OUR FUNDING AND THE CONTINUING 1639 01:06:17,495 --> 01:06:19,764 UNDERSTANDING, THE EVOLUTION OF 1640 01:06:19,764 --> 01:06:20,631 SCIENTIFIC THOUGHT BIOMEDICAL 1641 01:06:20,631 --> 01:06:23,100 RESEARCH THOUGHT THAT YOU GOT TO 1642 01:06:23,100 --> 01:06:24,869 GET THE PATIENTS INVOLVED THAT 1643 01:06:24,869 --> 01:06:26,370 ARE IN A SERIOUS WAY. 1644 01:06:26,370 --> 01:06:29,207 I'M INTIMATELY INVOLVED WITH 1645 01:06:29,207 --> 01:06:29,874 SOMETHING CALLED THE HEAL 1646 01:06:29,874 --> 01:06:31,209 INITIATIVE WHICH I KNOW SOME OF 1647 01:06:31,209 --> 01:06:33,444 YOU ARE FAMILIAR WITH RELATED TO 1648 01:06:33,444 --> 01:06:34,245 PAIN AND OPIOID USE DISORDER. 1649 01:06:34,245 --> 01:06:37,415 I HAVE TO TELL YOU, WITHOUT 1650 01:06:37,415 --> 01:06:39,016 ENGAGING THE PATIENTS AND THOSE 1651 01:06:39,016 --> 01:06:40,284 WITH LIVED EXPERIENCES WE'D BE 1652 01:06:40,284 --> 01:06:45,990 IN A VERY DIFFERENT PLACE. 1653 01:06:45,990 --> 01:06:47,258 THE SAME FOR DISEASES AND 1654 01:06:47,258 --> 01:06:47,758 CONDITIONS EACH OF YOU 1655 01:06:47,758 --> 01:06:54,365 REPRESENT. 1656 01:06:54,365 --> 01:06:58,436 AND IT'S THE SAME THEME OF 1657 01:06:58,436 --> 01:06:59,604 COURSE. 1658 01:06:59,604 --> 01:07:02,139 I WILL TELL YOU DR. BERTAGNOLLI 1659 01:07:02,139 --> 01:07:04,075 HAS CLEARLY IS A VERY 1660 01:07:04,075 --> 01:07:05,243 PATIENT-CENTRIC INDIVIDUAL WITH 1661 01:07:05,243 --> 01:07:13,484 ALL THE WORK THAT SHE'S DONE IN 1662 01:07:13,484 --> 01:07:17,321 CANCER AS I PROJECT TO THE 1663 01:07:17,321 --> 01:07:21,492 FUTURE HOPEFULLY WITH A 1664 01:07:21,492 --> 01:07:23,761 CONFIRMATION WE'LL PROCEED IN A 1665 01:07:23,761 --> 01:07:34,305 VERY ROBUST WAY DOWN THAT PATH. 1666 01:07:35,606 --> 01:07:37,909 >> HI. 1667 01:07:37,909 --> 01:07:40,311 KAREN BALL WITH THE STURJ 1668 01:07:40,311 --> 01:07:40,878 FOUNDATION ONE OF THE RARE 1669 01:07:40,878 --> 01:07:41,379 DISEASES YOU MENTIONED. 1670 01:07:41,379 --> 01:07:43,481 I WAS HAPPY TO HEAR YOU TALK 1671 01:07:43,481 --> 01:07:44,081 ABOUT INFLAMMATION. 1672 01:07:44,081 --> 01:07:47,218 JUST WANTED TO THANK YOU AND 1673 01:07:47,218 --> 01:07:51,522 DR. CRISWELL AND DR. CARTER 1674 01:07:51,522 --> 01:07:53,291 BECAUSE FOR THE LAST 36 YEARS 1675 01:07:53,291 --> 01:07:57,461 THE MEETING OF THE DIVERSE 1676 01:07:57,461 --> 01:07:59,730 ORGANIZATIONS HAS DRIVEN OUR 1677 01:07:59,730 --> 01:08:01,465 INQUISITIVE UNDERSTANDING OF THE 1678 01:08:01,465 --> 01:08:08,372 FOUNDATION AND THE DISEASE. 1679 01:08:08,372 --> 01:08:14,145 SO MULTI INSTITUTES WE INTERACT 1680 01:08:14,145 --> 01:08:16,714 WITH AND NOW WE'RE BURGEONING ON 1681 01:08:16,714 --> 01:08:18,049 MORE CLINICAL TRIALS SINCE 1682 01:08:18,049 --> 01:08:19,750 DISCOVERING THE PPG AND THAT'S 1683 01:08:19,750 --> 01:08:22,553 OUR ONLY HOPE OF GETTING A LEG 1684 01:08:22,553 --> 01:08:22,720 UP. 1685 01:08:22,720 --> 01:08:23,888 ARE YOU GOING CONTINUE THAT OR 1686 01:08:23,888 --> 01:08:24,355 EXPAND IT? 1687 01:08:24,355 --> 01:08:27,124 >> WE'RE TALKING ABOUT HOW WE 1688 01:08:27,124 --> 01:08:28,326 MIGHT EXPAND THAT. 1689 01:08:28,326 --> 01:08:30,528 OBVIOUSLY IN THE SPACE OF RARE 1690 01:08:30,528 --> 01:08:32,363 DISEASE TRIALS TAKE ON THEIR OWN 1691 01:08:32,363 --> 01:08:34,599 COMPLEXITIES BECAUSE OF NUMBERS. 1692 01:08:34,599 --> 01:08:38,369 AND SO YOU NEED TO CONTEMPLATE 1693 01:08:38,369 --> 01:08:41,505 UNIQUE TRIAL DESIGN AND SO FO 1694 01:08:41,505 --> 01:08:41,706 FORTH. 1695 01:08:41,706 --> 01:08:43,074 THAT'S ALL THE MORE REASON TO 1696 01:08:43,074 --> 01:08:49,480 STRENGTHEN THE PPP APPROACH 1697 01:08:49,480 --> 01:08:52,016 BECAUSE UNLESS YOU'RE ABLE TO 1698 01:08:52,016 --> 01:08:53,384 ENGAGE ALL THE PATIENTS 1699 01:08:53,384 --> 01:08:55,019 SOMETIMES AND UNLESS YOU'RE ABLE 1700 01:08:55,019 --> 01:08:57,455 TO PARTNER WITH INDUSTRY UP 1701 01:08:57,455 --> 01:08:59,690 FRONT, IT DOES NOT MAKE FOR THE 1702 01:08:59,690 --> 01:09:00,925 OPTIMAL WAY FORWARD. 1703 01:09:00,925 --> 01:09:04,261 WE ARE TALKING ABOUT HOW WE CAN 1704 01:09:04,261 --> 01:09:05,329 STRENGTHEN THAT. 1705 01:09:05,329 --> 01:09:06,731 FOUNDATION AND YOU'LL HEAR FROM 1706 01:09:06,731 --> 01:09:07,732 THAT IN A BIT. 1707 01:09:07,732 --> 01:09:13,471 THEY'VE BEEN AN AMAZING PARTNER 1708 01:09:13,471 --> 01:09:20,077 AND I CAN'T SAY ENOUGH ABOUT 1709 01:09:20,077 --> 01:09:21,445 THEM THREE THE AMP SERIES OF 1710 01:09:21,445 --> 01:09:23,881 PROGRAMS AND OTHERS. 1711 01:09:23,881 --> 01:09:27,752 PLEASE CONTINUE TO ADVOCATE FOR 1712 01:09:27,752 --> 01:09:27,952 THAT. 1713 01:09:27,952 --> 01:09:29,720 AND KNOW THAT THE NIH LEADERSHIP 1714 01:09:29,720 --> 01:09:31,922 IS VERY MUCH SUPPORTIVE. 1715 01:09:31,922 --> 01:09:32,156 OKAY. 1716 01:09:32,156 --> 01:09:33,224 WITH THAT, THANK YOU SO MUCH 1717 01:09:33,224 --> 01:09:38,362 BECAUSE I SEE MY COLLEAGUE 1718 01:09:38,362 --> 01:09:41,599 DR. GERBERDING IN THE BACK 1719 01:09:41,599 --> 01:09:50,041 THERE. 1720 01:09:50,041 --> 01:09:53,511 >> THANK YOU SO MUCH, DR. TABAK. 1721 01:09:53,511 --> 01:09:56,380 I'M GLAD HE WAS ABLE TO TAKE 1722 01:09:56,380 --> 01:09:56,647 QUESTIONS. 1723 01:09:56,647 --> 01:09:59,884 IN THE NEXT PORTION WE'LL HEAR 1724 01:09:59,884 --> 01:10:02,353 FROM THE CURRENT NIAMS COALITION 1725 01:10:02,353 --> 01:10:04,955 CO-CHAIRS, TRISHA AND LEE 1726 01:10:04,955 --> 01:10:07,425 PROVIDING AN OVERVIEW OF 1727 01:10:07,425 --> 01:10:08,225 ACCOMPLISHMENTS AND AT EACH 1728 01:10:08,225 --> 01:10:09,894 MEETING WE TAKE A MOMENT TO 1729 01:10:09,894 --> 01:10:11,328 RECOGNIZE THE FORMER AND 1730 01:10:11,328 --> 01:10:14,398 OUTGOING CO-CHAIRS FOR THEIR 1731 01:10:14,398 --> 01:10:16,767 DEDICATION AND LEADERSHIP OF THE 1732 01:10:16,767 --> 01:10:19,970 NIAMS COALITION. 1733 01:10:19,970 --> 01:10:24,341 I'D FIRST LIKE TO RECOGNIZE MS. 1734 01:10:24,341 --> 01:10:29,180 MARCIOLLO CO-CHAIR FROM 2020 TO 1735 01:10:29,180 --> 01:10:29,413 2021. 1736 01:10:29,413 --> 01:10:33,484 WE HAVE A CERTIFICATE FOR HER. 1737 01:10:33,484 --> 01:10:43,794 I HOPE SHE'S HERE. 1738 01:11:01,545 --> 01:11:05,316 SO NEXT, I'D LIKE TO EXTEND OUR 1739 01:11:05,316 --> 01:11:09,120 APPRECIATION TO MS. TRISHA 1740 01:11:09,120 --> 01:11:11,856 SHIVAS AS THE SPENDS THE NEXT 1741 01:11:11,856 --> 01:11:13,157 MONTH WRAPPING UP HER SERVICE AS 1742 01:11:13,157 --> 01:11:13,491 CO-CHAIR. 1743 01:11:13,491 --> 01:11:14,158 WE ALSO HAVE A CERTIFICATE FOR 1744 01:11:14,158 --> 01:11:24,235 YOU. 1745 01:11:27,271 --> 01:11:27,404 OKAY. 1746 01:11:27,404 --> 01:11:29,473 SO WE LOOK FORWARD TO YOUR 1747 01:11:29,473 --> 01:11:30,474 CONTINUED PARTICIPATION AND 1748 01:11:30,474 --> 01:11:31,075 COALITION ACTIVITIES OVER THE 1749 01:11:31,075 --> 01:11:32,877 COMING YEARS. 1750 01:11:32,877 --> 01:11:34,812 SO I THINK WE'RE GOING TO HAVE A 1751 01:11:34,812 --> 01:11:43,788 PHOTO WITH CO-CHAIRS NOW. 1752 01:11:43,788 --> 01:11:47,158 WE'LL NOW TURN THINGS OVER TO 1753 01:11:47,158 --> 01:11:48,659 TRISHA AND LEE TO PROVIDE AN 1754 01:11:48,659 --> 01:11:50,261 OVERVIEW OF THE NIAMS ACTIVITIES 1755 01:11:50,261 --> 01:11:53,497 AND ACCOMPLISHMENTS. 1756 01:11:53,497 --> 01:12:03,874 LOOKING FORWARD TO IT. 1757 01:12:16,220 --> 01:12:19,757 >> SO WE WANTED TO KICK IT OFF 1758 01:12:19,757 --> 01:12:21,492 WITH SOMETHING A LITTLE FIN. 1759 01:12:21,492 --> 01:12:22,827 WE DON'T ALWAYS WANT THE 1760 01:12:22,827 --> 01:12:23,894 CELEBRITIES TO HAVE ALL THE FUN 1761 01:12:23,894 --> 01:12:27,665 WITH SELFIES AND WANTED TO DID A 1762 01:12:27,665 --> 01:12:30,634 GIGANTIC NIAMS' SELFIE AND SHOW 1763 01:12:30,634 --> 01:12:31,735 HOW INCREDIBLE IT IS ALL THE 1764 01:12:31,735 --> 01:12:33,304 PEOPLE IN THE ROOM AND LEE WILL 1765 01:12:33,304 --> 01:12:35,739 TAKE HIS BEST SHOT AT CAPTURING 1766 01:12:35,739 --> 01:12:36,140 EVERYBODY. 1767 01:12:36,140 --> 01:12:37,474 PUT YOUR BEST SMILES ON. 1768 01:12:37,474 --> 01:12:44,381 >> I'M REALLY BAD AT THIS. 1769 01:12:44,381 --> 01:12:49,520 THIS IS INDULGING US A LITTLE 1770 01:12:49,520 --> 01:12:59,597 BIT. 1771 01:13:01,932 --> 01:13:05,236 >> WE'RE GOING TO POST THAT AS 1772 01:13:05,236 --> 01:13:07,872 NOT OUR FORMAL PICTURE BUT A 1773 01:13:07,872 --> 01:13:08,239 MORE FUN. 1774 01:13:08,239 --> 01:13:10,641 >> I'M GOING APOLOGIZE IN 1775 01:13:10,641 --> 01:13:10,875 ADVANCE. 1776 01:13:10,875 --> 01:13:13,477 NEVER LET A BOOMER TAKE A 1777 01:13:13,477 --> 01:13:16,146 SELFIE. 1778 01:13:16,146 --> 01:13:17,648 >> WE'RE SO EXCITED TO HAVE YOU 1779 01:13:17,648 --> 01:13:20,384 HERE AND WANT TO WELCOME YOU 1780 01:13:20,384 --> 01:13:20,985 AGAIN. 1781 01:13:20,985 --> 01:13:23,254 THIS IS GOING TO BE A CHOCK-FULL 1782 01:13:23,254 --> 01:13:24,488 CONVERSATION AND ALSO AN 1783 01:13:24,488 --> 01:13:25,456 OPPORTUNITY FOR EVERYONE TO GET 1784 01:13:25,456 --> 01:13:27,524 TO KNOW ONE ANOTHER AND SHARE 1785 01:13:27,524 --> 01:13:29,693 BECAUSE ONE OF THE THINGS WE 1786 01:13:29,693 --> 01:13:31,629 HEARD YEAR AND YEAR FROM 1787 01:13:31,629 --> 01:13:33,297 EVALUATIONS IS HOW IMPORTANT IT 1788 01:13:33,297 --> 01:13:35,032 IS THE CONVERSATIONS YOU ARE ALL 1789 01:13:35,032 --> 01:13:35,599 HAVING WITH EACH OTHER. 1790 01:13:35,599 --> 01:13:38,435 WE ENCOURAGE YOU TO TAKE UP 1791 01:13:38,435 --> 01:13:39,637 OPPORTUNITIES DURING LUNCH, FIND 1792 01:13:39,637 --> 01:13:41,138 SOMEONE TO HAVE LUNCH WITH 1793 01:13:41,138 --> 01:13:44,408 DURING THE CONVERSATIONS AND GET 1794 01:13:44,408 --> 01:13:44,842 TO KNOW EACH OTHER. 1795 01:13:44,842 --> 01:13:47,845 >> AS YOU CAN SEE HERE, THIS IS 1796 01:13:47,845 --> 01:13:50,281 FROM 2019 THE LAST TIME THAT WE 1797 01:13:50,281 --> 01:13:51,048 MET IN PERSON. 1798 01:13:51,048 --> 01:13:53,484 THERE'S SOME OF YOU THAT ARE IN 1799 01:13:53,484 --> 01:13:58,489 THE ROOM TODAY THAT WERE IN THE 1800 01:13:58,489 --> 01:14:00,357 PICTURE AND FOR ALL OF US, 1801 01:14:00,357 --> 01:14:01,458 THERE'S SO MUCH THAT'S HAPPENED 1802 01:14:01,458 --> 01:14:05,963 IN THE LAST FOUR YEARS. 1803 01:14:05,963 --> 01:14:09,433 I THINK IT CAUSES US ALL TO BE 1804 01:14:09,433 --> 01:14:10,634 REFLECTIVE OF WHAT WE'VE GONE 1805 01:14:10,634 --> 01:14:12,636 THROUGH AND HOW THE WORLD'S 1806 01:14:12,636 --> 01:14:14,405 LITERALLY CHANGED IN SO MANY 1807 01:14:14,405 --> 01:14:14,605 WAYS. 1808 01:14:14,605 --> 01:14:17,107 I LIKE TO LOOK AT THIS AS BEING 1809 01:14:17,107 --> 01:14:18,275 A POSITIVE EFFECT. 1810 01:14:18,275 --> 01:14:20,744 WE'VE NOW ARE IN THE ASPECT OF 1811 01:14:20,744 --> 01:14:21,111 TRANSFORMATION. 1812 01:14:21,111 --> 01:14:21,845 THAT'S PART OF WHAT WE'RE TRYING 1813 01:14:21,845 --> 01:14:23,614 TO DO HERE WITH THE COALITION. 1814 01:14:23,614 --> 01:14:29,453 AND WHY WE'RE ALL HERE TODAY TO 1815 01:14:29,453 --> 01:14:31,455 LOOK AT WAYS TO TRANSFORM WHAT 1816 01:14:31,455 --> 01:14:32,389 WE'RE DOING AS AN ORGANIZATION 1817 01:14:32,389 --> 01:14:35,025 AND COALITION TO MOVE IT FORWARD 1818 01:14:35,025 --> 01:14:36,860 TO WE'RE MORE PRODUCTIVE IN 1819 01:14:36,860 --> 01:14:37,394 SUPPORTING NIAMS AND OUR 1820 01:14:37,394 --> 01:14:43,534 ORGANIZATIONS. 1821 01:14:43,534 --> 01:14:46,036 I WANT TO THANK OUR COALITION 1822 01:14:46,036 --> 01:14:46,704 STEERING COMMITTEE. 1823 01:14:46,704 --> 01:14:48,472 I WON'T NAME ALL THE PEOPLE HERE 1824 01:14:48,472 --> 01:14:51,008 BUT PLEASE TAKE NOTE OF ALL OF 1825 01:14:51,008 --> 01:14:52,977 THOSE NAMES AND AS YOU GO 1826 01:14:52,977 --> 01:14:54,712 THROUGH THE DAY TAKE TIME ALSO 1827 01:14:54,712 --> 01:14:57,414 TO THANK EACH AND EVERY ONE OF 1828 01:14:57,414 --> 01:15:01,151 THESE INDIVIDUALS FOR THEIR 1829 01:15:01,151 --> 01:15:05,356 SUPPORT AND FOR HELPING TRISHA 1830 01:15:05,356 --> 01:15:08,158 AND I IN KEEPING THE COALITION 1831 01:15:08,158 --> 01:15:12,062 MOVING FORWARD. 1832 01:15:12,062 --> 01:15:14,131 PLEASE SPEND TIME WITH THEM 1833 01:15:14,131 --> 01:15:15,132 THEY'RE ALL WONDERFUL PEOPLE 1834 01:15:15,132 --> 01:15:15,866 THAT DEDICATED TIME AND ENERGY 1835 01:15:15,866 --> 01:15:16,567 TO THE COALITION AND WE'RE 1836 01:15:16,567 --> 01:15:20,170 GRATEFUL TO THEM. 1837 01:15:20,170 --> 01:15:25,376 >> ALSO, I WANT TO EXTEND A 1838 01:15:25,376 --> 01:15:26,977 SPECIAL THANK YOU TO LAUREN AND 1839 01:15:26,977 --> 01:15:28,679 OTHERS WHO HELPED DEVELOP THE 1840 01:15:28,679 --> 01:15:31,048 PROGRAM AND I'LL PUT IN 1841 01:15:31,048 --> 01:15:31,915 SHAMELESS PLUGS DURING THE 1842 01:15:31,915 --> 01:15:32,549 PRESENTATION FOR OPPORTUNITIES 1843 01:15:32,549 --> 01:15:33,450 TO HEAR FROM YOUR VOICES. 1844 01:15:33,450 --> 01:15:35,386 WE WANT TO HEAR FROM YOU. 1845 01:15:35,386 --> 01:15:37,788 WE WANT YOU TO JOIN US AS WE 1846 01:15:37,788 --> 01:15:40,991 PLAN FOR THE NEXT ONE DAY OR FOR 1847 01:15:40,991 --> 01:15:42,393 OTHER PROGRAMS AND ENGAGEMENT WE 1848 01:15:42,393 --> 01:15:46,830 WANT TO DO AT THE NIH. 1849 01:15:46,830 --> 01:15:47,664 PLEASE CONSIDER SHARING YOUR 1850 01:15:47,664 --> 01:15:49,366 VOICE IT'S REALLY IMPORTANT TO 1851 01:15:49,366 --> 01:15:51,668 US WHETHER YOU'RE IN A SURVEY OR 1852 01:15:51,668 --> 01:15:52,603 ABLE TO VOLUNTEER TO BE PART OF 1853 01:15:52,603 --> 01:15:53,937 THE PLANNING COMMITTEE. 1854 01:15:53,937 --> 01:15:56,440 IT'S A REWARDING EXPERIENCE AND 1855 01:15:56,440 --> 01:16:01,545 A GREAT OPPORTUNITY TO MAKE SURE 1856 01:16:01,545 --> 01:16:03,047 WHAT YOU'RE ORGANIZATION IS 1857 01:16:03,047 --> 01:16:04,615 HEARING AND HEARING FROM OTHER 1858 01:16:04,615 --> 01:16:05,482 ORGANIZATIONS GETS HIGHLIGHTED 1859 01:16:05,482 --> 01:16:05,983 TO BE SURE TO HAVE THE 1860 01:16:05,983 --> 01:16:12,823 CONVERSATION. 1861 01:16:12,823 --> 01:16:17,227 >> I PRIVILEGE OF THANKING THE 1862 01:16:17,227 --> 01:16:19,363 NIAMS' STAFF I'VE BEEN 1863 01:16:19,363 --> 01:16:20,064 OVERWHELMED WITH HOW GENEROUS 1864 01:16:20,064 --> 01:16:21,965 THEY ARE WITH THE TIME AND HOW 1865 01:16:21,965 --> 01:16:23,400 AVAILABLE THEY ARE AND THEIR 1866 01:16:23,400 --> 01:16:26,437 CONCERN AND INTEREST IN HAVING 1867 01:16:26,437 --> 01:16:31,041 THIS ORGANIZATION GROW AND 1868 01:16:31,041 --> 01:16:31,575 THRIVE. 1869 01:16:31,575 --> 01:16:32,843 PUTTING THIS COALITION MEETING 1870 01:16:32,843 --> 01:16:35,012 TOGETHER IS MONUMENTAL AND THE 1871 01:16:35,012 --> 01:16:36,346 AMOUNT OF EFFORT AND ENERGY THEY 1872 01:16:36,346 --> 01:16:38,215 PUT INTO IT IS JUST INDICATIVE 1873 01:16:38,215 --> 01:16:41,185 OF THEIR COMMITMENT TO ALL OF 1874 01:16:41,185 --> 01:16:43,087 YOU AND OUR ORGANIZATION. 1875 01:16:43,087 --> 01:16:49,526 AGAIN, THANK YOU, NIAMS'STAFF. 1876 01:16:49,526 --> 01:16:51,562 >> QUICKLY, TO GIVE A LITTLE BIT 1877 01:16:51,562 --> 01:16:53,263 OF BACKGROUND BECAUSE WE HAVE SO 1878 01:16:53,263 --> 01:16:55,099 MANY NEW FACES IN THE ROOM 1879 01:16:55,099 --> 01:16:55,632 TODAY. 1880 01:16:55,632 --> 01:16:58,402 I WANT TO SAY THAT'S ONE OF THE 1881 01:16:58,402 --> 01:17:00,037 THINGS WE'RE MOST ENERGIZED 1882 01:17:00,037 --> 01:17:02,773 ABOUT WHEN WE ASK WHAT GIVES YOU 1883 01:17:02,773 --> 01:17:04,007 HOPE FOR THE FUTURE. 1884 01:17:04,007 --> 01:17:06,043 ONE THING FOR US IS HOW ENGAGED 1885 01:17:06,043 --> 01:17:08,412 THE COMMISSION HAS BECOME. 1886 01:17:08,412 --> 01:17:10,547 HOW INTERESTED AND ENGAGED WE 1887 01:17:10,547 --> 01:17:10,714 ARE. 1888 01:17:10,714 --> 01:17:15,419 THIS IS A 20-YEAR-OLD COMMISSION 1889 01:17:15,419 --> 01:17:16,253 PUT TOGETHER BY THE 1890 01:17:16,253 --> 01:17:17,521 ORGANIZATIONS YOU SEE LISTED 1891 01:17:17,521 --> 01:17:20,491 THERE FROM A DECADE AGO WE 1892 01:17:20,491 --> 01:17:24,628 ORGANIZED BUT THE WHOLE GOAL OF 1893 01:17:24,628 --> 01:17:25,696 THIS GROUP IS TO COME TOGETHER 1894 01:17:25,696 --> 01:17:27,264 AND TO REALLY THINK ABOUT HOW DO 1895 01:17:27,264 --> 01:17:29,466 WE GET THE WORD OUT. 1896 01:17:29,466 --> 01:17:31,535 THIS WAS SOMETHING DR. CRISWELL 1897 01:17:31,535 --> 01:17:33,470 SAID IN HER TALK, HOW DO WE GET 1898 01:17:33,470 --> 01:17:35,105 THE WORD OUT FOR PEOPLE TO 1899 01:17:35,105 --> 01:17:37,474 UNDERSTAND WHAT IS IMPACTING 1900 01:17:37,474 --> 01:17:39,409 THOSE WE SERVE AND HOW DO WE GET 1901 01:17:39,409 --> 01:17:41,478 THE WORD OUT WHAT NIAMS IS DOING 1902 01:17:41,478 --> 01:17:43,914 TO HELP ADDRESS THAT. 1903 01:17:43,914 --> 01:17:46,650 >> SO WHERE ARE WE TODAY WITH 1904 01:17:46,650 --> 01:17:47,851 THE COALITION? 1905 01:17:47,851 --> 01:17:50,621 JUST A SHORT STORY, WHEN I FIRST 1906 01:17:50,621 --> 01:17:53,357 BEGAN MY NON-PROFIT LEADERSHIP 1907 01:17:53,357 --> 01:17:55,959 POSITIONS ON A NATIONAL LEVEL 1908 01:17:55,959 --> 01:17:57,461 MANY YEARS AGO, PROBABLY 18 1909 01:17:57,461 --> 01:18:03,367 YEARS AGO, I WAS AT AN INFORMAL 1910 01:18:03,367 --> 01:18:05,469 CONFERENCE THAT WAS HELD IN 1911 01:18:05,469 --> 01:18:05,669 TEXAS. 1912 01:18:05,669 --> 01:18:07,171 AND A GENTLEMAN THERE GOT UP TO 1913 01:18:07,171 --> 01:18:08,605 TALK ABOUT WHAT COALITIONS ARE 1914 01:18:08,605 --> 01:18:10,874 AND HOW THEY CAN BEST MOVE 1915 01:18:10,874 --> 01:18:12,809 FORWARD AND THEIR REAL PURPOSE. 1916 01:18:12,809 --> 01:18:14,411 AND SUCCINCTLY HE SAID THE 1917 01:18:14,411 --> 01:18:17,481 COALITIONS ARE A GROUP OF PEOPLE 1918 01:18:17,481 --> 01:18:20,684 WITH SIMILAR INTEREST THAT FORM 1919 01:18:20,684 --> 01:18:22,352 TOGETHER WHERE NO ONE PUTS THEIR 1920 01:18:22,352 --> 01:18:25,455 INTEREST ABOVE ANY OTHERS. 1921 01:18:25,455 --> 01:18:27,624 THAT WAS TRULY INSPIRING TO ME 1922 01:18:27,624 --> 01:18:29,459 AND THE GENTLEMAN BECAME ONE OF 1923 01:18:29,459 --> 01:18:32,429 MY MENTORS BECAUSE I JUST FELT 1924 01:18:32,429 --> 01:18:34,565 THAT FOR US IN THIS ADVOCACY 1925 01:18:34,565 --> 01:18:36,466 ROLE THAT WE PLAY IN NON-PROFIT 1926 01:18:36,466 --> 01:18:38,368 ROLES AND LEADERSHIP ROLES WE 1927 01:18:38,368 --> 01:18:41,872 HAVE, IT IS SO CRITICAL FOR US 1928 01:18:41,872 --> 01:18:43,207 TO WORK COLLABORATIVELY. 1929 01:18:43,207 --> 01:18:44,675 WE CANNOT ACCOMPLISH WHAT OUR 1930 01:18:44,675 --> 01:18:47,077 MEANS ARE AND OUR MISSION FOR 1931 01:18:47,077 --> 01:18:48,845 OUR ORGANIZATIONS IN A VACUUM. 1932 01:18:48,845 --> 01:18:50,147 WE HAVE TO WORK COLLABORATIVELY 1933 01:18:50,147 --> 01:18:50,981 AND HAVE TO JOIN WITH OTHERS TO 1934 01:18:50,981 --> 01:18:54,084 MAKE THAT HAPPEN. 1935 01:18:54,084 --> 01:18:58,222 THAT IS THE PURPOSE OF THIS 1936 01:18:58,222 --> 01:18:59,356 COALITION. 1937 01:18:59,356 --> 01:19:03,727 THIS -- WHAT WE REPRESENT HERE 1938 01:19:03,727 --> 01:19:09,466 AND I'LL USE LEE CALLAHANOVER 1939 01:19:09,466 --> 01:19:13,804 THERE THEY HAVE A WONDERFUL 1940 01:19:13,804 --> 01:19:20,544 STUDY CALLED BEMIS AND IT'S A 1941 01:19:20,544 --> 01:19:22,679 TRILLION DOLLAR ANNUALLY OF WHAT 1942 01:19:22,679 --> 01:19:25,015 THE BURDEN IS IN THE U.S. ALONE 1943 01:19:25,015 --> 01:19:27,150 OF A DISEASE AND WHEN YOU 1944 01:19:27,150 --> 01:19:29,453 COMBINE IT WITH OTHER DISORDERS 1945 01:19:29,453 --> 01:19:38,996 REPRESENTED HERE, WE DOMINATE 1946 01:19:38,996 --> 01:19:40,163 HEALTH CARE AND WE HAVE THAT 1947 01:19:40,163 --> 01:19:41,531 POWER AND REPRESENT THAT GROUP 1948 01:19:41,531 --> 01:19:50,741 OF ADVOCATES AND PATIENTS WE CAN 1949 01:19:50,741 --> 01:19:51,775 IMPROVE NIAMS AND GETTING MORE 1950 01:19:51,775 --> 01:19:52,976 FUNDING AND SUPPORTING THEIR 1951 01:19:52,976 --> 01:19:56,747 EFFORTS IT HELPS US AS WELL. 1952 01:19:56,747 --> 01:19:59,750 >> I'M GOING TO SKIP US AHEAD 1953 01:19:59,750 --> 01:20:01,485 QUICKLY BECAUSE I WANT TO HAVE 1954 01:20:01,485 --> 01:20:02,686 ENOUGH TIME TO TALK ABOUT KEY 1955 01:20:02,686 --> 01:20:02,919 THINGS. 1956 01:20:02,919 --> 01:20:06,623 THE MEMBERSHIP IS OPEN. 1957 01:20:06,623 --> 01:20:11,128 WE ENCOURAGE YOU TO GET THE WORD 1958 01:20:11,128 --> 01:20:13,230 OUT TO HAVE ADDITIONAL MEMBERS. 1959 01:20:13,230 --> 01:20:14,998 I'LL SKIP OVER TO THE ADVOCACY 1960 01:20:14,998 --> 01:20:16,700 PIECE AND SAY ONE OF THE MOST 1961 01:20:16,700 --> 01:20:20,871 IMPORTANT THINGS WE DO IS SHARE 1962 01:20:20,871 --> 01:20:21,638 OUR VOICE. 1963 01:20:21,638 --> 01:20:25,475 SHARE OUR STORY AND DR. CRISWELL 1964 01:20:25,475 --> 01:20:26,843 SAID THIS BUT I'LL KEEP 1965 01:20:26,843 --> 01:20:28,278 EMPHASIZING THE MORE WE TALK 1966 01:20:28,278 --> 01:20:32,416 ABOUT THE BURDEN THE MORE WE 1967 01:20:32,416 --> 01:20:42,392 MAKE IT AWARE WHAT SOME PEOPLE 1968 01:20:42,392 --> 01:20:44,161 LIVE WITH. 1969 01:20:44,161 --> 01:20:49,166 >> AND BIANNUALLY WE PUT IN TO 1970 01:20:49,166 --> 01:20:53,236 THE MEETING YOU'RE HERE FOR 1971 01:20:53,236 --> 01:20:59,076 TODAY AND WILL BE ORGANIZING OUR 1972 01:20:59,076 --> 01:21:00,744 CONGRESSIONAL TOUR DAY. 1973 01:21:00,744 --> 01:21:02,245 TO BE DETERMINED BUT PLEASE STAY 1974 01:21:02,245 --> 01:21:02,446 TUNED. 1975 01:21:02,446 --> 01:21:04,314 >> AND WHAT THINGS YOU'D LIKE TO 1976 01:21:04,314 --> 01:21:05,482 SEE FROM WEBINAR. 1977 01:21:05,482 --> 01:21:12,189 THESE ARE A FEW WE HAD AND THEY 1978 01:21:12,189 --> 01:21:12,989 COME FROM YOU AND WHAT THINGS 1979 01:21:12,989 --> 01:21:14,958 ARE IMPACTING YOU AND THE 1980 01:21:14,958 --> 01:21:16,460 EDUCATION AND THIS IS A GREAT 1981 01:21:16,460 --> 01:21:17,327 OPPORTUNITY TO ANSWER THE 1982 01:21:17,327 --> 01:21:17,761 QUESTION. 1983 01:21:17,761 --> 01:21:19,096 WE'LL ASK YOU TO THINK ABOUT 1984 01:21:19,096 --> 01:21:20,497 THAT AND BY THEN OF TODAY YOU 1985 01:21:20,497 --> 01:21:22,165 SHOULD HAVE LOTS OF IDEAS FOR 1986 01:21:22,165 --> 01:21:26,470 WEBINARS TO GET THOSE MOVING. 1987 01:21:26,470 --> 01:21:29,005 >> FOR THE COALITION ENGAGEMENT 1988 01:21:29,005 --> 01:21:30,674 THERE'S A LIST OF OPPORTUNITIES 1989 01:21:30,674 --> 01:21:30,941 THERE. 1990 01:21:30,941 --> 01:21:32,642 I WANT TO EMPHASIZE EVERYBODY 1991 01:21:32,642 --> 01:21:35,779 HERE SHOULD CONTRIBUTE TO OUR 1992 01:21:35,779 --> 01:21:37,147 ROUND UP AS WELL AS JOIN THE 1993 01:21:37,147 --> 01:21:43,120 LINKED IN PAGE BUT NOT ONLY TO 1994 01:21:43,120 --> 01:21:44,888 SHARE AMONG THE COALITION 1995 01:21:44,888 --> 01:21:45,889 MEMBERS BUT TAKE THE INFORMATION 1996 01:21:45,889 --> 01:21:47,958 AND SHARE IT WITH YOUR MEMBERS 1997 01:21:47,958 --> 01:21:48,925 AND ORGANIZATION AND RESEARCHERS 1998 01:21:48,925 --> 01:21:52,095 TO GET THE WORD OUT WHAT THE 1999 01:21:52,095 --> 01:21:53,397 COALITION IS DOING. 2000 01:21:53,397 --> 01:21:55,365 >> I'LL ECHO THAT BECAUSE THAT 2001 01:21:55,365 --> 01:21:57,234 COLLABORATIVE PIECE DR. TABAK 2002 01:21:57,234 --> 01:21:58,068 WAS TALKING ABOUT ONLY COMES 2003 01:21:58,068 --> 01:22:01,471 WHEN PEOPLE UNDERSTAND WHAT 2004 01:22:01,471 --> 01:22:05,041 OTHER PEOPLE ARE DOING. 2005 01:22:05,041 --> 01:22:07,778 SOMETIMES YOU THINK PEOPLE ONLY 2006 01:22:07,778 --> 01:22:09,279 CARE ABOUT CERTAIN THINGS AND 2007 01:22:09,279 --> 01:22:10,547 THERE'S OVERLAP IN WE'RE DOING 2008 01:22:10,547 --> 01:22:13,483 AND IF WE SHARE THAT OUT YOU CAN 2009 01:22:13,483 --> 01:22:16,686 SPARK SOMETHING IN SOMEBODY YOU 2010 01:22:16,686 --> 01:22:22,292 DIDN'T KNOW NEEDED THE SPARK. 2011 01:22:22,292 --> 01:22:24,161 WE HAVE WORKING GROUPS AND 2012 01:22:24,161 --> 01:22:26,463 OTHERS NOT LISTED. 2013 01:22:26,463 --> 01:22:27,197 WE TALKED ABOUT LEGISLATIVE 2014 01:22:27,197 --> 01:22:28,198 ADVOCACY WORKING GROUP AND 2015 01:22:28,198 --> 01:22:29,466 COMMUNICATIONS WORKING GROUP. 2016 01:22:29,466 --> 01:22:30,100 JOIN US. 2017 01:22:30,100 --> 01:22:31,435 IT'S A GREAT OPPORTUNITY FOR YOU 2018 01:22:31,435 --> 01:22:32,169 TO GET INVOLVED TO GET YOUR 2019 01:22:32,169 --> 01:22:40,877 VOICE AT THE TABLE. 2020 01:22:40,877 --> 01:22:43,580 >> AND PLEASE GET INVOLVED BY 2021 01:22:43,580 --> 01:22:44,481 JOINING THE STEERING COMMITTEE. 2022 01:22:44,481 --> 01:22:46,950 I'LL BE WITHOUT A CO-CHAIR SOON. 2023 01:22:46,950 --> 01:22:49,219 I'M HOPING SOMEBODY WILL STEP UP 2024 01:22:49,219 --> 01:22:50,887 TO WORK WITH ME AS DIFFICULT AS 2025 01:22:50,887 --> 01:22:53,457 THAT MAY SEEM AT TIMES BUT 2026 01:22:53,457 --> 01:22:56,626 PLEASE, WE'LL BE ACCEPTING 2027 01:22:56,626 --> 01:22:57,727 ANYBODY THAT'S INTERESTED, 2028 01:22:57,727 --> 01:23:02,265 PLEASE CONTACT US SO WE CAN HAVE 2029 01:23:02,265 --> 01:23:04,234 ANOTHER CO-CHAIR FOR US. 2030 01:23:04,234 --> 01:23:05,335 THIS IS THE WEBSITE DRAWING 2031 01:23:05,335 --> 01:23:06,369 ATTENTION TO IT. 2032 01:23:06,369 --> 01:23:07,370 A LOT HAS GONE INTO IT TO 2033 01:23:07,370 --> 01:23:08,939 IMPROVE IT AND MORE IS GOING TO 2034 01:23:08,939 --> 01:23:14,411 GO INTO IT SO IT BECOMES A 2035 01:23:14,411 --> 01:23:15,512 RESOURCE FOR THE COALITION. 2036 01:23:15,512 --> 01:23:17,080 >> AND A REMINDER TO REACH OUT 2037 01:23:17,080 --> 01:23:19,049 TO COLLEEN IF YOU HAVE UPDATES. 2038 01:23:19,049 --> 01:23:20,984 THIS SAY REALLY WELL SEARCHED 2039 01:23:20,984 --> 01:23:21,184 TOOL. 2040 01:23:21,184 --> 01:23:24,754 I WANT TO SAY THANK YOU TO THOSE 2041 01:23:24,754 --> 01:23:26,056 WHO HAVE LED THIS EFFORT IN 2042 01:23:26,056 --> 01:23:27,290 PUTTING THIS TOGETHER. 2043 01:23:27,290 --> 01:23:30,694 IT WAS A HERCULEAN EFFORT TO 2044 01:23:30,694 --> 01:23:34,898 PULL THIS TOGETHER AND WITH THAT 2045 01:23:34,898 --> 01:23:36,900 WE'LL PASS IT BACK TO 2046 01:23:36,900 --> 01:23:40,504 DR. CRISWELL FOR OUR NEXT STEP 2047 01:23:40,504 --> 01:23:42,405 BUT WE LOOK FORWARD TO WORKING 2048 01:23:42,405 --> 01:23:44,774 WITH ALL OF YOU TODAY AND 2049 01:23:44,774 --> 01:23:54,818 BEYOND. 2050 01:23:54,818 --> 01:23:56,253 >> THANK YOU SO MUCH TRISHA AND 2051 01:23:56,253 --> 01:23:56,419 LEE. 2052 01:23:56,419 --> 01:23:57,621 WHAT A FANTASTIC START TO THE 2053 01:23:57,621 --> 01:23:58,855 DAY. 2054 01:23:58,855 --> 01:24:00,257 AT THIS POINT WE'RE GOING 2055 01:24:00,257 --> 01:24:01,458 TRANSITION FOR A QUICK GROUP 2056 01:24:01,458 --> 01:24:01,658 PHOTO. 2057 01:24:01,658 --> 01:24:07,731 I DO WANT TO LET EVERYONE KNOW 2058 01:24:07,731 --> 01:24:08,532 THERE ARE BADGES THAT WERE STUCK 2059 01:24:08,532 --> 01:24:09,466 IN TRAFFIC THIS MORNING BUT 2060 01:24:09,466 --> 01:24:10,934 THEY'VE ARRIVED. 2061 01:24:10,934 --> 01:24:13,370 THEY'LL BE LOCATED JUST OUTSIDE 2062 01:24:13,370 --> 01:24:16,106 E1 AND E2 IN THE HALLWAY CLOSE 2063 01:24:16,106 --> 01:24:17,307 TO THE REGISTRATION TABLE. 2064 01:24:17,307 --> 01:24:18,608 PLEASE WAIT TO PICK UP YOUR 2065 01:24:18,608 --> 01:24:20,844 BADGE UNTIL AFTER THE PHOTO. 2066 01:24:20,844 --> 01:24:24,080 AT THIS STABLE WE'RE GOING TO 2067 01:24:24,080 --> 01:24:24,681 ASK OUR LOVELY NIAMS STAFF 2068 01:24:24,681 --> 01:24:27,884 AROUND THAT HAVE GUIDANCE HOW TO 2069 01:24:27,884 --> 01:24:29,452 HELP OTHERS ORGANIZE FOR THE 2070 01:24:29,452 --> 01:24:31,254 GROUP PHOTO TO HELP COALITION 2071 01:24:31,254 --> 01:24:32,856 MEMBERS, UP THE STAIRS ON THE 2072 01:24:32,856 --> 01:24:33,757 RIGHT-HAND SIDE WHEN YOU WALK 2073 01:24:33,757 --> 01:24:34,558 OUT THE DOOR HERE AND WE'RE 2074 01:24:34,558 --> 01:24:36,159 GOING TO GO OUTSIDE. 2075 01:24:36,159 --> 01:24:42,432 WE'LL HAVE OUR PHOTO OUTSIDE AND 2076 01:24:42,432 --> 01:24:43,800 AGAIN, NIAMS STAFF JUST HELP 2077 01:24:43,800 --> 01:24:44,901 EVERYONE AND OUR LOVELY 2078 01:24:44,901 --> 01:24:45,902 PHOTOGRAPH, LESLIE SHOULD BE UP 2079 01:24:45,902 --> 01:24:46,770 THERE WAITING FOR US. 2080 01:24:46,770 --> 01:24:49,472 I THINK THAT'S ALL FOR 2081 01:24:49,472 --> 01:24:50,507 ANNOUNCEMENTS. 2082 01:24:50,507 --> 01:24:52,342 BADGES, NIAMS STAFF, YEP, AND 2083 01:24:52,342 --> 01:24:53,577 PLEASE ENSURE, THERE'S A LITTLE 2084 01:24:53,577 --> 01:24:56,513 BIT OF A BREAK BUT TRY IT GET 2085 01:24:56,513 --> 01:24:58,481 BACK LEER BY 10:45. 2086 01:24:58,481 --> 01:25:02,552 WE HAVE OUR WONDERFUL NEXT 2087 01:25:02,552 --> 01:25:04,321 SPEAKER DR. GERBERDING SO THANK 2088 01:25:04,321 --> 01:25:17,085 YOU SO MUCH. 2089 01:25:17,085 --> 01:25:21,828 DR. GERGERDING IS WITH 2090 01:25:21,828 --> 01:25:24,931 NON-PROFIT ORGANIZATION THAT 2091 01:25:24,931 --> 01:25:25,998 BUILDS PUBLIC-PRIVATE 2092 01:25:25,998 --> 01:25:27,066 PARTNERSHIP TO SUPPORT THE 2093 01:25:27,066 --> 01:25:28,067 MISSION OF THE NIH. 2094 01:25:28,067 --> 01:25:28,868 WE HEARD SOME DISCUSSION ABOUT 2095 01:25:28,868 --> 01:25:31,003 THE IMPORTANCE OF THOSE 2096 01:25:31,003 --> 01:25:32,305 ACTIVITIES EARLIER. 2097 01:25:32,305 --> 01:25:35,975 SHE CO-CHAIRS THE CSIS 2098 01:25:35,975 --> 01:25:36,743 BIPARTISAN ALLIANCE ON GLOBAL 2099 01:25:36,743 --> 01:25:39,712 HEALTH SECURITY AND SHE'S A 2100 01:25:39,712 --> 01:25:40,413 MEMBER OF THE COMMONWEALTH FUND 2101 01:25:40,413 --> 01:25:41,848 COMMISSION ON A NATIONAL PUBLIC 2102 01:25:41,848 --> 01:25:43,683 HEALTH SYSTEM. 2103 01:25:43,683 --> 01:25:46,385 PREVIOUSLY, SHE SERVED AS 2104 01:25:46,385 --> 01:25:49,222 PRESIDENT OF MERK VACCINES AND 2105 01:25:49,222 --> 01:25:50,189 EXECUTIVE VICE PRESIDENT AND THE 2106 01:25:50,189 --> 01:25:51,057 CHIEF PATIENT OFFICER AT MERK 2107 01:25:51,057 --> 01:25:58,364 AND COMPANY. 2108 01:25:58,364 --> 01:26:08,908 FROM 2003 TO 2009 SHE SERVES ON 2109 01:26:09,208 --> 01:26:11,077 MANY BOARDS. 2110 01:26:11,077 --> 01:26:12,979 SHE'S A MEMBER OF THE NATIONAL 2111 01:26:12,979 --> 01:26:16,048 ACADEMY OF MEDICINE AND THE 2112 01:26:16,048 --> 01:26:18,251 ADJUNCT FACULTIES OF THE 2113 01:26:18,251 --> 01:26:21,154 UNIVERSITY OF CALIFORNIA SAN 2114 01:26:21,154 --> 01:26:24,857 FRANCISCO, YAY, AND CASE WESTERN 2115 01:26:24,857 --> 01:26:26,726 RESERVE UNIVERSITY. 2116 01:26:26,726 --> 01:26:29,462 FROM THEIR EARLY YEARS TO HER 2117 01:26:29,462 --> 01:26:30,563 CURRENT ROLE MAINTAINED KEEPING 2118 01:26:30,563 --> 01:26:32,131 PATIENT AS THE THE EPICENTER OF 2119 01:26:32,131 --> 01:26:33,166 HER WORK. 2120 01:26:33,166 --> 01:26:35,067 SHE VALUES PROFESSIONAL AND 2121 01:26:35,067 --> 01:26:36,068 PATIENT ADVOCATES SUCH AS THE 2122 01:26:36,068 --> 01:26:36,936 NIAMS COALITION AND AIMS TO 2123 01:26:36,936 --> 01:26:40,239 BRING YOUR INSIGHTS AND YOUR 2124 01:26:40,239 --> 01:26:41,073 VOICES INTO THE BIOMEDICAL 2125 01:26:41,073 --> 01:26:41,474 RESEARCH PROCESS. 2126 01:26:41,474 --> 01:26:43,376 SO THANK YOU SO MUCH FOR JOINING 2127 01:26:43,376 --> 01:26:52,919 US. 2128 01:26:52,919 --> 01:26:59,125 >> WHEN I SAW THE MEMBERSHIP I 2129 01:26:59,125 --> 01:27:00,660 WAS IMPRESSED AND AWKWARD TO 2130 01:27:00,660 --> 01:27:07,967 TALK ABOUT THE NIH WHICH IS IN 2131 01:27:07,967 --> 01:27:10,636 PART A PUBLIC-PRIVATE 2132 01:27:10,636 --> 01:27:12,038 PARTNERSHIP AND I FEEL HONORED 2133 01:27:12,038 --> 01:27:13,239 TO BE HERE AND TO HAVE TIME TO 2134 01:27:13,239 --> 01:27:16,242 TELL YOU ABOUT OUR WORK AND HOW 2135 01:27:16,242 --> 01:27:19,545 MUCH WE VALUE THE PARTNERSHIP 2136 01:27:19,545 --> 01:27:23,716 WITH OUR MANY PATIENT ORIENTED 2137 01:27:23,716 --> 01:27:24,517 ORGANIZATIONS. 2138 01:27:24,517 --> 01:27:26,586 ALSO I'LL SAY NIAMS IS AN 2139 01:27:26,586 --> 01:27:28,054 INCREDIBLE PARTNER. 2140 01:27:28,054 --> 01:27:29,956 WE HAVE A NUMBER OF IMPORTANT 2141 01:27:29,956 --> 01:27:31,457 ACTIVITIES THAT I'LL TELL YOU A 2142 01:27:31,457 --> 01:27:32,558 LITTLE BIT ABOUT THAT HAVE GONE 2143 01:27:32,558 --> 01:27:34,360 ON FOR SEVERAL YEARS AND REALLY 2144 01:27:34,360 --> 01:27:37,730 THE KIND OF PARTNERSHIP AND 2145 01:27:37,730 --> 01:27:38,798 STAKEHOLDER EVOLUTION THAT THIS 2146 01:27:38,798 --> 01:27:41,300 INSTITUTE OF NIH IS SO GOOD AT 2147 01:27:41,300 --> 01:27:42,501 IS PART OF THE REASON WHY THE 2148 01:27:42,501 --> 01:27:45,137 SCIENCE IN THE AREA HAS BEEN 2149 01:27:45,137 --> 01:27:45,771 ABLE TO ADVANCE SO FAST. 2150 01:27:45,771 --> 01:27:48,107 SO I'LL JUST TELL YOU A LITTLE 2151 01:27:48,107 --> 01:27:51,010 BIT ABOUT THE WORK THAT WE DO AT 2152 01:27:51,010 --> 01:27:53,346 THE FOUNDATION TO SUPPORT THE 2153 01:27:53,346 --> 01:27:55,748 NIH AND THEN HELP YOU KIND OF 2154 01:27:55,748 --> 01:27:58,184 GET INTRODUCED TO SOME BROADER 2155 01:27:58,184 --> 01:28:00,486 ISSUES LIKE TRUST IN SCIENCE AND 2156 01:28:00,486 --> 01:28:02,555 I'M SURE IT'S BEEN ON 2157 01:28:02,555 --> 01:28:03,923 EVERYBODY'S AGENDA IN YOUR HOME 2158 01:28:03,923 --> 01:28:04,624 ORGANIZATIONS AS WELL. 2159 01:28:04,624 --> 01:28:06,325 SO LET ME JUST START WITH OUR 2160 01:28:06,325 --> 01:28:08,527 THEME WHICH IS BUILDING BRIDGES 2161 01:28:08,527 --> 01:28:09,195 TO BREAKTHROUGH. 2162 01:28:09,195 --> 01:28:15,635 SO WE DO SEE OURSELVES AS TRYING 2163 01:28:15,635 --> 01:28:16,569 TO BE A BRIDGE BETWEEN THE 2164 01:28:16,569 --> 01:28:19,705 PRIVATE AND PUBLIC SECTORS AND 2165 01:28:19,705 --> 01:28:20,940 BUILDING BRIDGES OF SCIENCE TO 2166 01:28:20,940 --> 01:28:21,173 PEOPLE. 2167 01:28:21,173 --> 01:28:22,341 I THOUGHT IT WAS INTERESTING TO 2168 01:28:22,341 --> 01:28:24,343 SEE THE TAGLINE FOR THE 2169 01:28:24,343 --> 01:28:27,780 COALITION CONNECTING TO SCIENCE 2170 01:28:27,780 --> 01:28:33,185 SO IT THEMATICALLY FITS. 2171 01:28:33,185 --> 01:28:40,593 OUR AMBITION IS TO ACCELERATE 2172 01:28:40,593 --> 01:28:44,397 AND AMPLIFY THE NIH WITH BETTER 2173 01:28:44,397 --> 01:28:45,097 HEALTH EQUITY. 2174 01:28:45,097 --> 01:28:46,832 ONE IS THROUGH TEAM SCIENCE 2175 01:28:46,832 --> 01:28:51,837 TRYING TO BUILD THESE PLATFORMS 2176 01:28:51,837 --> 01:28:53,973 OF COLLABORATIVE SCIENCE AND 2177 01:28:53,973 --> 01:28:56,175 EXPEDITE THAT AND WE SUPPORT 2178 01:28:56,175 --> 01:28:57,810 SCIENTISTS AND IN THIS DAY AND 2179 01:28:57,810 --> 01:28:59,779 AGE WHEN EVERYONE IS WORRIED 2180 01:28:59,779 --> 01:29:03,549 ABOUT SUPPORT FOR POSTDOCS AND 2181 01:29:03,549 --> 01:29:06,752 EARLY CAREER SCIENTISTS IT'S 2182 01:29:06,752 --> 01:29:09,989 BECOMING AN INCREASING APPROACH 2183 01:29:09,989 --> 01:29:11,624 HOW WE BUILD BETTER SUPPORT FOR 2184 01:29:11,624 --> 01:29:12,992 SCIENTIFIC STARS. 2185 01:29:12,992 --> 01:29:15,528 AND LASTLY TRYING TO CONTRIBUTE 2186 01:29:15,528 --> 01:29:19,966 TO BUILDING THE TRUST IN SCIENCE 2187 01:29:19,966 --> 01:29:21,734 OR REBUILDING THE TRUST IN 2188 01:29:21,734 --> 01:29:22,868 SCIENCE WHICH IS THE BIGGEST 2189 01:29:22,868 --> 01:29:24,337 THREAT TO HUMAN HEALTH IN THE 2190 01:29:24,337 --> 01:29:25,371 U.S. IF NOT GLOBALLY. 2191 01:29:25,371 --> 01:29:29,041 I WANTED TO SHARE WITH YOU A 2192 01:29:29,041 --> 01:29:31,110 VIDEO THAT EXPLAINS THIS BETTER 2193 01:29:31,110 --> 01:29:34,013 THAN I CAN DO IT. 2194 01:29:34,013 --> 01:29:35,114 IF YOU BEAR WITH ME I'LL BRING 2195 01:29:35,114 --> 01:29:36,415 THIS UP AND YOU CAN HEAR OUR 2196 01:29:36,415 --> 01:29:42,488 STORY FROM OTHER SOURCES. 2197 01:29:42,488 --> 01:29:45,191 >> MY DAUGHTER, TAYLOR, WHEN SHE 2198 01:29:45,191 --> 01:29:49,862 WAS DIAGNOSED AT THE AGE OF 7 2199 01:29:49,862 --> 01:29:54,600 WITH CLM BATTANT DISEASE THE 2200 01:29:54,600 --> 01:29:55,768 GENETICIST SAYS THERE'D NOTHING 2201 01:29:55,768 --> 01:29:56,669 YOU CAN DO. 2202 01:29:56,669 --> 01:29:59,772 I KNEW I HAD A NEW GOAL IN LIFE, 2203 01:29:59,772 --> 01:30:01,741 IF I COULDN'T HELP MY CHILD 2204 01:30:01,741 --> 01:30:03,309 THERE HAD TO BE AN ANSWER FOR 2205 01:30:03,309 --> 01:30:07,079 FAMILIES AND CHILDREN WHO WOULD 2206 01:30:07,079 --> 01:30:07,680 FOLLOW MINE. 2207 01:30:07,680 --> 01:30:09,448 >> SCIENCE HAS THE POWER TO CURE 2208 01:30:09,448 --> 01:30:11,384 BUT NO SINGLE ORGANIZATION CAN 2209 01:30:11,384 --> 01:30:13,686 DO THAT ALONE. 2210 01:30:13,686 --> 01:30:16,956 AT FNIH WE BUILD BRIDGES BY 2211 01:30:16,956 --> 01:30:19,091 FORGE TEAMS AT THE BEST 2212 01:30:19,091 --> 01:30:22,194 SCIENTISTS AT NIH IN ACADEME 2213 01:30:22,194 --> 01:30:24,497 ANDACROSS THE BIO PHARMACEUTICAL 2214 01:30:24,497 --> 01:30:25,731 ECHO SYSTEM. 2215 01:30:25,731 --> 01:30:28,134 THROUGH THE PUBLIC-PRIVATE 2216 01:30:28,134 --> 01:30:29,368 PARTNERSHIP WE ACCELERATE NEW 2217 01:30:29,368 --> 01:30:31,103 DIAGNOSTICS, THERAPIES AND 2218 01:30:31,103 --> 01:30:34,140 POTENTIAL CURES. 2219 01:30:34,140 --> 01:30:36,175 >> FNIH HAS BEEN CHARGED BY 2220 01:30:36,175 --> 01:30:37,576 CONGRESS TO FILL A GAP IN THE 2221 01:30:37,576 --> 01:30:40,179 ECO SYSTEM OF INNOVATION. 2222 01:30:40,179 --> 01:30:43,783 BEFORE FNIH WAS REALLY DIFFICULT 2223 01:30:43,783 --> 01:30:44,884 TO ESTABLISH COLLABORATIVE 2224 01:30:44,884 --> 01:30:46,652 EFFORTS OF EFFORTS BETWEEN 2225 01:30:46,652 --> 01:30:49,989 PUBLIC AND PRIVATE SECTORS. 2226 01:30:49,989 --> 01:30:51,190 FNIH BRINGS ITS OWN SPECIAL 2227 01:30:51,190 --> 01:30:52,024 EXPERTISE TO PUTTING THESE 2228 01:30:52,024 --> 01:30:52,992 TOGETHER IN A WAY THAT CAN BE 2229 01:30:52,992 --> 01:30:55,061 PRODUCTIVE. 2230 01:30:55,061 --> 01:30:57,897 THE FNIH IS THE CONSUMMATE 2231 01:30:57,897 --> 01:30:58,164 CONVENER. 2232 01:30:58,164 --> 01:31:01,367 >> THAT MEANS BRINGING TOGETHER 2233 01:31:01,367 --> 01:31:03,035 THE BEST SCIENCE AND TECHNOLOGY, 2234 01:31:03,035 --> 01:31:04,637 OUTSTANDING PEOPLE WHO USED 2235 01:31:04,637 --> 01:31:06,172 THEIR COMBINED EXPERTISE AND 2236 01:31:06,172 --> 01:31:07,039 AMBITION TO ACCELERATE PROGRESS 2237 01:31:07,039 --> 01:31:08,974 TO PATIENTS. 2238 01:31:08,974 --> 01:31:10,810 THE MORE HANDS YOU HAVE ON DECK 2239 01:31:10,810 --> 01:31:12,044 THE MORE LIKELY YOU ARE TO 2240 01:31:12,044 --> 01:31:13,612 ANSWER THE VEXING PROBLEMS. 2241 01:31:13,612 --> 01:31:15,681 >> WE BRING TOGETHER THE 2242 01:31:15,681 --> 01:31:16,549 RESOURCES, WE PROVIDE THE 2243 01:31:16,549 --> 01:31:17,950 INFRASTRUCTURE, AND REALLY FORM 2244 01:31:17,950 --> 01:31:20,853 THAT BRIDGE TO THE BREAKTHROUGH. 2245 01:31:20,853 --> 01:31:24,523 >> AT FNIH, WE SUPPORT TEAM 2246 01:31:24,523 --> 01:31:26,692 SCIENCE IN SOLVING SOME OF THE 2247 01:31:26,692 --> 01:31:30,129 TOUGHEST BIO MEDICAL CHALLENGES. 2248 01:31:30,129 --> 01:31:32,031 SINCE OUR INCEPTION WE RAISED 2249 01:31:32,031 --> 01:31:33,833 MORE THAN A BILLION AND A HALF 2250 01:31:33,833 --> 01:31:35,067 DOLLARS TO SUPPORT THE MISSION 2251 01:31:35,067 --> 01:31:37,269 OF THE NIH AND DEPLOYED THEM FOR 2252 01:31:37,269 --> 01:31:39,138 PROGRAMS LIKE ACCELERATING 2253 01:31:39,138 --> 01:31:42,541 MEDICINES PARTNERSHIP AND THE 2254 01:31:42,541 --> 01:31:43,042 BIOMARKERS CONSORTIUM. 2255 01:31:43,042 --> 01:31:44,910 THESE PROGRAMS BRING TREATMENTS 2256 01:31:44,910 --> 01:31:47,046 AND MOST IMPORTANTLY HOPE TO 2257 01:31:47,046 --> 01:31:50,616 PEOPLE LIVING WITH CANCER, 2258 01:31:50,616 --> 01:31:51,650 NEUROLOGIC DISEASE AND RARE 2259 01:31:51,650 --> 01:31:55,054 DISEASES AND OTHER INSEEMINGLY 2260 01:31:55,054 --> 01:31:55,988 INCURRABLE HEALTH CONDITIONS. 2261 01:31:55,988 --> 01:31:57,656 >> WITH EVERY PARTNERSHIP WE 2262 01:31:57,656 --> 01:31:59,425 FOSTER WE'RE SEEKING TO 2263 01:31:59,425 --> 01:32:00,960 ACCELERATE SCIENTIFIC INNOVATION 2264 01:32:00,960 --> 01:32:02,294 SO WE CAN REALIZE GLOBAL HEALTH 2265 01:32:02,294 --> 01:32:04,663 EQUITY IN OUR LIFE TIME. 2266 01:32:04,663 --> 01:32:07,600 >> WE'RE WORKING WITH NIH, THE 2267 01:32:07,600 --> 01:32:09,034 GATES FOUNDATION AND OTHER 2268 01:32:09,034 --> 01:32:11,070 PARTNERS ON SOME OF THE GRAND 2269 01:32:11,070 --> 01:32:13,439 CHALLENGES IN GLOBAL HEALTH LIKE 2270 01:32:13,439 --> 01:32:17,376 MATERNAL MORTALITY, MALARIA, 2271 01:32:17,376 --> 01:32:18,744 TUBERCULOSIS AND HIV AIDS. 2272 01:32:18,744 --> 01:32:21,147 >> THE DISCOVERIES THAT HAPPEN 2273 01:32:21,147 --> 01:32:23,048 AT FNIH AFFECT THE HEALTH OF 2274 01:32:23,048 --> 01:32:24,283 EVERYONE IN THE WORLD. 2275 01:32:24,283 --> 01:32:26,886 >> THESE BREAKTHROUGHS WOULDN'T 2276 01:32:26,886 --> 01:32:28,287 HAPPEN WITHOUT WORLD CLASS 2277 01:32:28,287 --> 01:32:28,587 SCIENTISTS. 2278 01:32:28,587 --> 01:32:30,189 THAT'S WHY WE TAKE TIME TO HONER 2279 01:32:30,189 --> 01:32:31,323 THE CREATIVE INVESTIGATORS WHO 2280 01:32:31,323 --> 01:32:35,060 ARE PUSHING THE BOUNDARIES OF 2281 01:32:35,060 --> 01:32:37,596 POSSIBILITY WITH AWARDS LIKE THE 2282 01:32:37,596 --> 01:32:39,932 PRIZE IN BIOMEDICAL SCIENCE AND 2283 01:32:39,932 --> 01:32:40,332 TRAILBLAZER PRIZE. 2284 01:32:40,332 --> 01:32:44,737 >> THE FNIH HAS SUPPORTED NEARLY 2285 01:32:44,737 --> 01:32:48,007 25,000 SCIENTISTS OVER THE LAST 2286 01:32:48,007 --> 01:32:50,476 25 YEARS WITH TRAINING PROGRAMS, 2287 01:32:50,476 --> 01:32:53,746 FELLOWSHIPS AND AWARDS. 2288 01:32:53,746 --> 01:32:59,051 >> OUR PARTNERS AT NIH AND THE 2289 01:32:59,051 --> 01:33:04,423 AM ACADEMICS THEY ARE FROM HELP 2290 01:33:04,423 --> 01:33:06,292 DISCOVER MEDICINE. 2291 01:33:06,292 --> 01:33:07,493 FNIH BUILD THE BRIDGE FROM THE 2292 01:33:07,493 --> 01:33:09,261 BENCH TO THE BEDSIDE AND REDUCE 2293 01:33:09,261 --> 01:33:12,464 THE TIME IT TAKES TO BRING THE 2294 01:33:12,464 --> 01:33:13,532 PROMISING THERAPEUTICS TO 2295 01:33:13,532 --> 01:33:16,735 PATIENT WHO'S CAN'T WAIT. 2296 01:33:16,735 --> 01:33:20,239 >> TAYLOR LIVED ALMOST 13 YEARS 2297 01:33:20,239 --> 01:33:21,240 WITH HER DIAGNOSIS. 2298 01:33:21,240 --> 01:33:23,809 I WANT MOTHERS THAT FOLLOW KNOW 2299 01:33:23,809 --> 01:33:24,310 HAVE MORE. 2300 01:33:24,310 --> 01:33:28,480 THE FNIH IS RUNNING A GREAT RACE 2301 01:33:28,480 --> 01:33:31,116 ON BEHALF OF PEOPLE LIKE MY 2302 01:33:31,116 --> 01:33:31,450 DAUGHTER. 2303 01:33:31,450 --> 01:33:33,285 >> I KNOW OF NO OTHER 2304 01:33:33,285 --> 01:33:35,521 ORGANIZATION IN THE WORLD THAT 2305 01:33:35,521 --> 01:33:37,356 CAN DO THIS THE WAY FNIH DOES. 2306 01:33:37,356 --> 01:33:39,091 >> WE CAN'T DO THIS ALONE. 2307 01:33:39,091 --> 01:33:40,192 WE NEED YOUR SUPPORT. 2308 01:33:40,192 --> 01:33:42,728 SO PLEASE JOIN US IN BUILDING 2309 01:33:42,728 --> 01:33:45,097 BRIDGES TO BREAKTHROUGHS, 2310 01:33:45,097 --> 01:33:53,572 PATIENTS EVERYWHERE ARE WAITING. 2311 01:33:53,572 --> 01:33:54,406 >> THANK YOU. 2312 01:33:54,406 --> 01:33:57,243 THAT WAS AN ADVERTISEMENT IF YOU 2313 01:33:57,243 --> 01:33:59,712 DIDN'T GET IT. 2314 01:33:59,712 --> 01:34:03,282 I THINK IT DOES HELP THE STORY 2315 01:34:03,282 --> 01:34:07,052 THAT WE'RE A SMALL ORGANIZATION 2316 01:34:07,052 --> 01:34:10,389 BUT WE DO TRY TO THE CONVENER 2317 01:34:10,389 --> 01:34:11,724 AND AN HONOR TO BE WITH YOU 2318 01:34:11,724 --> 01:34:12,191 TODAY. 2319 01:34:12,191 --> 01:34:15,527 LET ME TALK MORE ABOUT SOME OF 2320 01:34:15,527 --> 01:34:19,431 THE SCIENTIFIC PROJECTS AND HOW 2321 01:34:19,431 --> 01:34:20,499 WE DO WORK. 2322 01:34:20,499 --> 01:34:23,002 IF I CAN NAME ONE THING THAT MAY 2323 01:34:23,002 --> 01:34:24,703 BE THE SECRET SAUCE OF THE FNIH 2324 01:34:24,703 --> 01:34:26,639 IS WE'RE GOOD AT PROJECT 2325 01:34:26,639 --> 01:34:28,440 MANAGEMENT. 2326 01:34:28,440 --> 01:34:29,708 AND YOU'LL SEE SOMETIMES OUR 2327 01:34:29,708 --> 01:34:32,845 PROGRAMS HAVE 30 OR MORE 2328 01:34:32,845 --> 01:34:35,014 PARTNERS AND HERDING THOSE LIONS 2329 01:34:35,014 --> 01:34:37,683 ISN'T EASY BUT IT'S A WAY TO 2330 01:34:37,683 --> 01:34:39,051 REALLY KEEP THE TRAINS RUNNING, 2331 01:34:39,051 --> 01:34:41,320 SET THE MILESTONES, MAKE SURE 2332 01:34:41,320 --> 01:34:43,289 THERE'S ONGOING PROGRESS AND TO 2333 01:34:43,289 --> 01:34:44,323 FACILITATE SOME OF THE PART 2334 01:34:44,323 --> 01:34:45,224 THINGS THAT MAKE IT DIFFICULT TO 2335 01:34:45,224 --> 01:34:45,724 WORK DIRECTLY WITH THE 2336 01:34:45,724 --> 01:34:47,826 GOVERNMENT. 2337 01:34:47,826 --> 01:34:49,828 I NOTICED WHEN I CAME IN THERE 2338 01:34:49,828 --> 01:34:53,098 WAS A COFFEE THAT SAID THE FOOD 2339 01:34:53,098 --> 01:34:54,366 WASN'T PAID FOR BY FEDERAL 2340 01:34:54,366 --> 01:34:54,900 TAXPAYER DOLLARS. 2341 01:34:54,900 --> 01:34:58,871 WE LIVE IN A COUNTRY WHERE JUST 2342 01:34:58,871 --> 01:35:00,272 IMPOSSIBLE FOR THE PRIVATE 2343 01:35:00,272 --> 01:35:01,674 SECTOR TO ENGAGE WITH GOVERNMENT 2344 01:35:01,674 --> 01:35:03,742 ORGANIZATIONS SO THAT WAS WHY 2345 01:35:03,742 --> 01:35:04,343 CONGRESS AUTHORIZED THE 2346 01:35:04,343 --> 01:35:08,013 FOUNDATION IN THE BEGINNING. 2347 01:35:08,013 --> 01:35:09,682 WE HAVE CRITERIA FOR THE KINDS 2348 01:35:09,682 --> 01:35:13,085 OF PARTNERSHIPS WE ENGAGE IN. 2349 01:35:13,085 --> 01:35:14,920 I THINK THE FIRST IS THE MOST 2350 01:35:14,920 --> 01:35:15,187 IMPORTANT. 2351 01:35:15,187 --> 01:35:18,223 WENT DO LIKE TO GET INVOLVED IN 2352 01:35:18,223 --> 01:35:20,326 THINGS THAT AREN'T REALLY 2353 01:35:20,326 --> 01:35:21,293 IMPORTANT AND HAVE A BIG IMPACT 2354 01:35:21,293 --> 01:35:25,564 ON PATIENTS. 2355 01:35:25,564 --> 01:35:26,231 WE'RE LOOKING FOR THINGS THAT 2356 01:35:26,231 --> 01:35:27,966 HAVE TO BE DONE IN A WISE CROWD 2357 01:35:27,966 --> 01:35:29,768 AND NOT COULD BE DONE BY A 2358 01:35:29,768 --> 01:35:34,807 SINGLE ORGANIZATION OR COMPANY 2359 01:35:34,807 --> 01:35:37,276 OR THINGS THAT ARE ALREADYING 2360 01:35:37,276 --> 01:35:40,846 DONE AND WE AVOID DUPLICATION 2361 01:35:40,846 --> 01:35:42,414 AND HAVE TO BE PARSIMONIOUS IN 2362 01:35:42,414 --> 01:35:45,250 THE RESOURCES WE HAVE. 2363 01:35:45,250 --> 01:35:49,188 WE ALSO LOOK FOR WAYS TO TRULY 2364 01:35:49,188 --> 01:35:51,190 LEVERAGE THE NIH CAPABILITY AND 2365 01:35:51,190 --> 01:35:51,457 RESOURCES. 2366 01:35:51,457 --> 01:35:54,226 IT'S A TRICKY SITUATION BECAUSE 2367 01:35:54,226 --> 01:35:55,327 IF YOU ASK THE AVERAGE AMERICAN 2368 01:35:55,327 --> 01:35:57,963 THEY THINK THE NIH HAS BILLIONS 2369 01:35:57,963 --> 01:35:59,131 AND BILLIONS WHY WOULD THEY NEED 2370 01:35:59,131 --> 01:36:01,100 FUNDS RAISED BY SOMEONE ELSE. 2371 01:36:01,100 --> 01:36:02,434 YET, ALL YOU HAVE TO DO IS LOOK 2372 01:36:02,434 --> 01:36:06,472 AT THE PAY LINE FOR GRANTS AND 2373 01:36:06,472 --> 01:36:07,673 RECOGNIZE IF WE COULD JUST HAVE 2374 01:36:07,673 --> 01:36:09,241 ANOTHER 10 POINTS TO GET IN THE 2375 01:36:09,241 --> 01:36:11,076 FUNDING RANGE THE AMOUNT OF 2376 01:36:11,076 --> 01:36:13,145 SCIENCE THAT GOES WASTED BECAUSE 2377 01:36:13,145 --> 01:36:14,947 WE CAN'T AFFORD TO PAY FOR IT SO 2378 01:36:14,947 --> 01:36:16,815 ANYTHING WE CAN DO TO LEVERAGE 2379 01:36:16,815 --> 01:36:18,450 THE OPPORTUNITY TO MOVE GOOD 2380 01:36:18,450 --> 01:36:23,222 SCIENCE FORWARD BY THE RESEARCH 2381 01:36:23,222 --> 01:36:24,289 PARTNERS IS SOMETHING THAT COMES 2382 01:36:24,289 --> 01:36:25,824 TO OUR POINTS OF VIEW. 2383 01:36:25,824 --> 01:36:29,461 HOW WE WORK IS CUSTOMIZED TO A 2384 01:36:29,461 --> 01:36:30,262 GREAT EXTENT. 2385 01:36:30,262 --> 01:36:31,530 I'M SURE BOB KNOWS THIS FROM THE 2386 01:36:31,530 --> 01:36:33,198 THINGS HE WORKED ON BUT WE HAVE 2387 01:36:33,198 --> 01:36:35,033 VARIOUS MODELS FOR HOW THE 2388 01:36:35,033 --> 01:36:38,470 PARTNERSHIPS COME TOGETHER. 2389 01:36:38,470 --> 01:36:43,142 BUT IN GENERAL, NIH RESOURCES 2390 01:36:43,142 --> 01:36:45,244 HAVE GRANTS AND PEER REVIEW AND 2391 01:36:45,244 --> 01:36:47,079 STUDY SECTION AND GRANTS GO OUT 2392 01:36:47,079 --> 01:36:56,555 TO THE ACADEMIES AND WE FUND 2393 01:36:56,555 --> 01:36:58,123 THINGS LIKE THE DATA 2394 01:36:58,123 --> 01:37:00,692 COORDINATING CENTER FOR OUR 2395 01:37:00,692 --> 01:37:04,563 PLATFORM PROGRAMS AND THEN 2396 01:37:04,563 --> 01:37:06,331 SOMETIMES WE SHARE RESOURCES 2397 01:37:06,331 --> 01:37:08,534 WITH DIAGNOSTIC COMPANIES, 2398 01:37:08,534 --> 01:37:08,867 ETCETERA. 2399 01:37:08,867 --> 01:37:11,804 IN THE MIDDLE IS A SHARED 2400 01:37:11,804 --> 01:37:12,704 GOVERNANCE. 2401 01:37:12,704 --> 01:37:14,306 IN ADDITION TO THE SECRETE SAUCE 2402 01:37:14,306 --> 01:37:16,809 OF PROJECT MANAGEMENT I THINK 2403 01:37:16,809 --> 01:37:19,044 THE SHARED MANAGEMENT IS 2404 01:37:19,044 --> 01:37:20,012 CRITICAL I'LL POINT OUT IN A 2405 01:37:20,012 --> 01:37:20,879 COUPLE PLACES. 2406 01:37:20,879 --> 01:37:24,683 WE TEND TO WORK IN PLATFORMS 2407 01:37:24,683 --> 01:37:27,052 INSTEAD OF HAVING A STABLE OF 2408 01:37:27,052 --> 01:37:29,188 DISPARATE PROJECTS WE HAVE A 2409 01:37:29,188 --> 01:37:29,955 PLATFORM APPROACH WHERE 2410 01:37:29,955 --> 01:37:31,557 DIFFERENT THERAPEUTIC AREAS ARE 2411 01:37:31,557 --> 01:37:33,091 APPROACHED IN PRETTY MUCH THE 2412 01:37:33,091 --> 01:37:33,659 SAME DIRECTION. 2413 01:37:33,659 --> 01:37:34,760 I'LL SPEND A BIT OF TIME ON SOME 2414 01:37:34,760 --> 01:37:39,765 OF THESE BUT THESE ARE THE MAJOR 2415 01:37:39,765 --> 01:37:41,967 PLATFORMS ACTIVE FOR THE COVID 2416 01:37:41,967 --> 01:37:44,903 PANDEMIC, ACCELERATED MEDICINES 2417 01:37:44,903 --> 01:37:46,238 PARTNERSHIP WHICH IS MOSTLY 2418 01:37:46,238 --> 01:37:47,739 ABOUT PATHWAY AND TARGET 2419 01:37:47,739 --> 01:37:50,309 IDENTIFICATION, ACCELERATING 2420 01:37:50,309 --> 01:37:51,043 CANCER THERAPIES. 2421 01:37:51,043 --> 01:37:54,246 THE PACT IS ONE EFFORT TO CREATE 2422 01:37:54,246 --> 01:37:56,615 MASTER PROTOCOLS WITH LUNG MAP 2423 01:37:56,615 --> 01:37:59,718 TO MOVE PATIENTS THROUGH THE 2424 01:37:59,718 --> 01:38:03,055 PROCESS OF GETTING THE RIGHT 2425 01:38:03,055 --> 01:38:05,224 CHEMOTHERAPY FOR THEIR ANSWER. 2426 01:38:05,224 --> 01:38:09,862 THE ADNI COLLABORATION HAS ENDED 2427 01:38:09,862 --> 01:38:12,731 BUT IT WAS A LONG COHORT STUDY 2428 01:38:12,731 --> 01:38:13,932 THAT WAS FOUNDATION TO 2429 01:38:13,932 --> 01:38:17,169 DISCOVERING THE BIOMARKERS THAT 2430 01:38:17,169 --> 01:38:19,471 HAVE ULTIMATELY LED TO BETTER 2431 01:38:19,471 --> 01:38:21,240 DIAGNOSTICS AND ENROLLMENT IN 2432 01:38:21,240 --> 01:38:22,608 CLINICAL TRIALS FOR PATIENTS 2433 01:38:22,608 --> 01:38:23,742 LIKELY TO PROGRESS IN THEIR 2434 01:38:23,742 --> 01:38:27,279 ALZHEIMER'S DISEASE. 2435 01:38:27,279 --> 01:38:28,780 THE GENE CONVENED AND GLOBAL 2436 01:38:28,780 --> 01:38:30,182 HEALTH PORTFOLIO WAS INHERITED 2437 01:38:30,182 --> 01:38:31,583 FROM THE GATES FOUNDATION. 2438 01:38:31,583 --> 01:38:35,053 THE GRAND CHALLENGE AS MANY ARE 2439 01:38:35,053 --> 01:38:37,122 FAMILIAR WITH THE INITIATION OF 2440 01:38:37,122 --> 01:38:39,057 GRANT CHALLENGES YEARS AGO AND 2441 01:38:39,057 --> 01:38:41,460 WHEN THEY GREW OUT OF THE GATES 2442 01:38:41,460 --> 01:38:42,594 FOUNDATION, MR. GATES MOVED 2443 01:38:42,594 --> 01:38:47,065 THOSE TO THE NIH AND THE FNIH 2444 01:38:47,065 --> 01:38:49,234 MANAGES THE GLOBAL PROGRAMS AND 2445 01:38:49,234 --> 01:38:51,103 HAVE BEEN PRODUCTIVE. 2446 01:38:51,103 --> 01:38:55,107 YOU MAY HAVE HEARD ABOUT THE 2447 01:38:55,107 --> 01:38:56,508 A-PLUS TRIAL WITH THE INSTITUTE 2448 01:38:56,508 --> 01:39:01,146 FOR CHILD HEALTH DEVELOPMENT IN 2449 01:39:01,146 --> 01:39:03,081 30,000 SOME WOMEN 2450 01:39:03,081 --> 01:39:06,218 INTERNATIONALLY A SINGLE DOSE 2451 01:39:06,218 --> 01:39:17,329 OFFER REEGEOOO --- - -ER 2452 01:39:18,497 --> 01:39:25,237 AND THERE'S THERE'S A BIG IMPACT 2453 01:39:25,237 --> 01:39:26,405 AND THE BIOMARKER CONSORTIUM 2454 01:39:26,405 --> 01:39:27,139 WHERE NIAMS HAS BEEN AN 2455 01:39:27,139 --> 01:39:34,713 INCREDIBLE PARTNER. 2456 01:39:34,713 --> 01:39:37,349 AND THERE'S ACCELERATED CLINICAL 2457 01:39:37,349 --> 01:39:38,383 TRIALS FOR THERAPEUTICS FOR THE 2458 01:39:38,383 --> 01:39:40,819 COVID PANDEMIC. 2459 01:39:40,819 --> 01:39:46,258 YOU LOOK AT THIS PANOPLY OF 2460 01:39:46,258 --> 01:39:48,994 PARTNERS AND IMAGINE WHAT HAD TO 2461 01:39:48,994 --> 01:39:54,299 HAPPEN TO DEVELOP A GREED UPON 2462 01:39:54,299 --> 01:39:57,069 PROTOCOLS BETWEEN FDA AND 2463 01:39:57,069 --> 01:39:58,770 PARTNERS AND GOVERNMENT AND 2464 01:39:58,770 --> 01:40:01,239 PROSECUTE BY THE NUMBERS. 2465 01:40:01,239 --> 01:40:07,079 800 COMPOUNDS WORE SCREENED FOR 2466 01:40:07,079 --> 01:40:11,350 POTENTIALLY UTILITY AND 6 OF 33 2467 01:40:11,350 --> 01:40:13,485 HAVE BEEN SHOWN TO HAVE CLINICAL 2468 01:40:13,485 --> 01:40:14,920 BENEFIT AND WE'RE NOT DONE YET. 2469 01:40:14,920 --> 01:40:16,888 SOME TRIALS ARE STILL ONGOING. 2470 01:40:16,888 --> 01:40:18,357 ONE OF MY BIG CONCERNS IS HOW DO 2471 01:40:18,357 --> 01:40:22,494 WE KEEP THE NETWORK OF NETWORKS 2472 01:40:22,494 --> 01:40:23,895 ACROSS THE 620 SITES WHO 2473 01:40:23,895 --> 01:40:25,564 ACTUALLY ENROLLED A TOTAL OF 2474 01:40:25,564 --> 01:40:31,470 MORE THAN 23,000 PATIENTS HOW DO 2475 01:40:31,470 --> 01:40:34,806 WE KEEP THEM WARM SO NEXT TIME 2476 01:40:34,806 --> 01:40:35,540 WE HAVE THE INFRASTRUCTURE READY 2477 01:40:35,540 --> 01:40:37,209 TO BE HEATED UP AND WE DON'T 2478 01:40:37,209 --> 01:40:41,580 HAVE TO START FROM SCRATCH LIKE 2479 01:40:41,580 --> 01:40:41,980 WE DID. 2480 01:40:41,980 --> 01:40:45,784 AT THE TIME THE PROTOCOL STARTED 2481 01:40:45,784 --> 01:40:47,319 THERE WAS NO ONE RESOURCE AT NIH 2482 01:40:47,319 --> 01:40:49,221 WHO KNEW ALL THE STUDY SITES AND 2483 01:40:49,221 --> 01:40:50,689 WHO WAS DOING WHAT. 2484 01:40:50,689 --> 01:40:52,924 PART OF THE EFFORT FOR THE FIRST 2485 01:40:52,924 --> 01:40:54,426 TIME BROUGHT TOGETHER THE 2486 01:40:54,426 --> 01:40:56,028 INTERNATIONAL PICTURE OF WHERE 2487 01:40:56,028 --> 01:40:57,729 CLINICAL RESEARCH WAS BEING 2488 01:40:57,729 --> 01:41:00,399 FUNDED BY NIH AND WHERE OTHER 2489 01:41:00,399 --> 01:41:02,467 PARTNERS COULD WEIGH IN. 2490 01:41:02,467 --> 01:41:05,337 THE BIOMARKERS CONSORTIUM IS 2491 01:41:05,337 --> 01:41:07,572 ALSO A LONG-STANDING PLATFORM 2492 01:41:07,572 --> 01:41:09,274 PROGRAM. 2493 01:41:09,274 --> 01:41:14,946 THE GOAL IS TO IDENTIFY AND 2494 01:41:14,946 --> 01:41:16,081 VALIDATE BIOMARKERS USED AS 2495 01:41:16,081 --> 01:41:18,283 SURROGATE END POINTS OR 2496 01:41:18,283 --> 01:41:21,286 DIAGNOSTICS TO ENRICH PATIENTS 2497 01:41:21,286 --> 01:41:22,788 OR PROGNOSTIC PATTERNS. 2498 01:41:22,788 --> 01:41:24,556 FDA IS AN IMPORTANT PARTNER IN 2499 01:41:24,556 --> 01:41:26,992 THIS PROCESS AND IT'S ONE OF THE 2500 01:41:26,992 --> 01:41:28,393 MOST FAVORED PARTS OF OUR 2501 01:41:28,393 --> 01:41:38,937 PORTFOLIO TO INDUSTRY PARTNERS. 2502 01:41:39,137 --> 01:41:41,640 IF YOU HAVE TO WAIT 10 YEARS FOR 2503 01:41:41,640 --> 01:41:43,375 SOMEONE TO DEVELOP A HIP 2504 01:41:43,375 --> 01:41:45,077 FRACTURE SO KNOW IF YOUR DRUG 2505 01:41:45,077 --> 01:41:46,545 WORKS TAKES A LONG TIME AND 2506 01:41:46,545 --> 01:41:48,346 TAKES A GAZILLION PEOPLE AND WHY 2507 01:41:48,346 --> 01:41:50,449 NO ONE IS DOING INNOVATIVE WORK 2508 01:41:50,449 --> 01:41:54,252 IN THIS SPACE OR AT LEAST 2509 01:41:54,252 --> 01:41:54,686 WASN'T. 2510 01:41:54,686 --> 01:41:56,588 IF YOU CAN VALIDATE A BIOMARKER 2511 01:41:56,588 --> 01:41:57,389 THAT'S A GOOD SURROGATE END 2512 01:41:57,389 --> 01:41:59,558 POINT FOR FRACTURE, YOU CAN GET 2513 01:41:59,558 --> 01:42:01,693 BACK IN THE GAME OF DRUG 2514 01:42:01,693 --> 01:42:05,997 DEVELOPMENT AND NEW INNOVATIONS 2515 01:42:05,997 --> 01:42:06,798 FOR OSTEOPOROSIS. 2516 01:42:06,798 --> 01:42:07,632 THAT APPROACH PLAYS OUT OVER AND 2517 01:42:07,632 --> 01:42:08,366 OVER AGAIN. 2518 01:42:08,366 --> 01:42:14,339 ONE OF OUR HOT AREAS RIGHT NOW 2519 01:42:14,339 --> 01:42:17,509 GOING INTO OUR NEXT AREA IS 2520 01:42:17,509 --> 01:42:18,076 MENTAL HEALTH. 2521 01:42:18,076 --> 01:42:21,012 THERE'S NO BIOMARKERS FOR MENTAL 2522 01:42:21,012 --> 01:42:25,250 HEALTH EXCEPT ONE FOR POSTPARTUM 2523 01:42:25,250 --> 01:42:26,017 DEPRESSION. 2524 01:42:26,017 --> 01:42:29,321 TO SAY SOMEONE'S DEPRESSED IS 2525 01:42:29,321 --> 01:42:31,056 LIKE SAYING SOMEONE IS HAVING 2526 01:42:31,056 --> 01:42:32,758 CHEST PAIN. 2527 01:42:32,758 --> 01:42:35,093 THERE COULD BE MANY DIAGNOSES 2528 01:42:35,093 --> 01:42:36,628 AND THE CONSORTIUM IS GETTING 2529 01:42:36,628 --> 01:42:37,295 RAMPED UP TO PARTICIPATE IN THAT 2530 01:42:37,295 --> 01:42:41,666 SPACE. 2531 01:42:41,666 --> 01:42:42,768 ACCELERATING MEDICINES 2532 01:42:42,768 --> 01:42:43,902 PARTNERSHIP IS OUR BIGGEST OVER 2533 01:42:43,902 --> 01:42:45,270 ALL PROGRAM. 2534 01:42:45,270 --> 01:42:47,606 THIS THE TIME LINE OF THE 2535 01:42:47,606 --> 01:42:48,540 VARIOUS THERAPEUTIC AREAS THAT 2536 01:42:48,540 --> 01:42:50,575 HAVE PARTICIPATED IN THE 2537 01:42:50,575 --> 01:42:51,676 COLLABORATIONS TO TRY TO 2538 01:42:51,676 --> 01:42:53,278 UNDERSTAND BETTER THE BIOLOGY OF 2539 01:42:53,278 --> 01:42:58,083 A PROBLEM OR TO UNDERSTAND THE 2540 01:42:58,083 --> 01:42:59,417 POTENTIAL TARGETS FOR 2541 01:42:59,417 --> 01:42:59,751 INTERVENTION. 2542 01:42:59,751 --> 01:43:01,820 ONE THING I LIKE ABOUT THE SLIDE 2543 01:43:01,820 --> 01:43:04,189 IS IT SHOWS GENERALLY THE 2544 01:43:04,189 --> 01:43:05,624 PROGRAMS ARE SORT OF DESIGN TO 2545 01:43:05,624 --> 01:43:09,261 OPERATE ON A FIVE TO SEVEN-YEAR 2546 01:43:09,261 --> 01:43:10,862 TIME HORIZON AND WHEN THE 2547 01:43:10,862 --> 01:43:15,667 OBJECTIVES ARE COMPLETED THE 2548 01:43:15,667 --> 01:43:16,134 PROJECT ENDS. 2549 01:43:16,134 --> 01:43:18,970 YOU NOTICE SOME GET RESTARTED 2550 01:43:18,970 --> 01:43:20,872 WITH PHASE 2 AND THAT'S AN 2551 01:43:20,872 --> 01:43:21,540 IMPORTANT INDICATOR THEY'RE 2552 01:43:21,540 --> 01:43:23,441 VALUABLE AND VALUABLE TO THE 2553 01:43:23,441 --> 01:43:26,444 PARTNERS BECAUSE THEY WOULDN'T 2554 01:43:26,444 --> 01:43:29,247 ANTE UP AND CONTINUE TO SUPPORT 2555 01:43:29,247 --> 01:43:30,649 THE COLLABORATION IF THEY DIDN'T 2556 01:43:30,649 --> 01:43:32,284 SEE IT CONTRIBUTING VALUE. 2557 01:43:32,284 --> 01:43:35,086 NEXT YEAR WE PLAN TO EVOLVE OR 2558 01:43:35,086 --> 01:43:37,956 LAUNCH AT LEAST FOR MORE AMPS. 2559 01:43:37,956 --> 01:43:42,027 THE SPI AMP SOME ARE INVOLVED 2560 01:43:42,027 --> 01:43:43,061 WITH SYSTEMS BIOLOGY AND THE ALS 2561 01:43:43,061 --> 01:43:44,296 AMP IS COMING NEXT YEAR. 2562 01:43:44,296 --> 01:43:46,631 I THINK WE'LL HAVE A MENTAL 2563 01:43:46,631 --> 01:43:47,499 HEALTH PROGRAM IN THE SPACE AS 2564 01:43:47,499 --> 01:43:52,771 WELL. 2565 01:43:52,771 --> 01:43:54,339 WE ALSO HAVE A WONDERFUL 2566 01:43:54,339 --> 01:43:58,143 OPPORTUNITY IN PEDIATRIC DEVICES 2567 01:43:58,143 --> 01:43:59,644 TO UNDERSTAND DUAL DEVICES AND 2568 01:43:59,644 --> 01:44:01,279 OTHER TOOLS THAT NEVER GET 2569 01:44:01,279 --> 01:44:02,180 STUDIED IN KIDS BECAUSE 2570 01:44:02,180 --> 01:44:05,483 CONDITIONS IN WHICH THEY WOULD 2571 01:44:05,483 --> 01:44:08,620 BE RELEVANT ARE UNCOMMON IN 2572 01:44:08,620 --> 01:44:09,287 CHILDREN. 2573 01:44:09,287 --> 01:44:13,825 THESE PROGRAMS HAVE SO FAR 2574 01:44:13,825 --> 01:44:17,529 EARNED $830 MILLION FROM OUTSIDE 2575 01:44:17,529 --> 01:44:18,597 PARTNERS AND INVOLVES MOST THE 2576 01:44:18,597 --> 01:44:19,030 NIH INSTITUTES. 2577 01:44:19,030 --> 01:44:21,299 WE HAVE A COUPLE MORE WE'RE WORK 2578 01:44:21,299 --> 01:44:22,100 ON TO BRING ADDITIONAL 2579 01:44:22,100 --> 01:44:24,436 THERAPEUTIC AREAS INTO THE 2580 01:44:24,436 --> 01:44:24,836 SPACE. 2581 01:44:24,836 --> 01:44:26,738 TO GIVE YOU A FLAVOR OF HOW 2582 01:44:26,738 --> 01:44:30,609 THINGS UNFOLDED, THE ALZHEIMER'S 2583 01:44:30,609 --> 01:44:34,212 DISEASE AMP REALLY STARTED OUT 2584 01:44:34,212 --> 01:44:35,647 REALLY IN A MORE TRADITIONAL 2585 01:44:35,647 --> 01:44:38,450 APPROACH TO LOOKING AT BRAIN 2586 01:44:38,450 --> 01:44:41,353 IMAGING AND FAIRLY CRUDE MARKERS 2587 01:44:41,353 --> 01:44:45,323 AND NOW THE 2.0 AMP IS DOWN TO 2588 01:44:45,323 --> 01:44:46,925 SINGLE-CELL PROFILING AND 2589 01:44:46,925 --> 01:44:51,062 LOOKING AT EPIGENETIC IMPACT ON 2590 01:44:51,062 --> 01:44:52,864 EXPRESSION OF THE DURABILITY AND 2591 01:44:52,864 --> 01:44:54,866 GENES THAT MAY HAVE A PREDICTIVE 2592 01:44:54,866 --> 01:44:57,302 OR PATHOGENIC ROLE. 2593 01:44:57,302 --> 01:45:00,138 THE WORK CONTINUES. 2594 01:45:00,138 --> 01:45:01,573 THIS IS A VERY EXCITING AREA 2595 01:45:01,573 --> 01:45:03,541 THAT IS KIND OF SERVING AS A 2596 01:45:03,541 --> 01:45:05,911 MODEL FOR HOW WE THINK ABOUT 2597 01:45:05,911 --> 01:45:08,313 OTHER NEURODEGENERATIVE 2598 01:45:08,313 --> 01:45:08,713 DISEASES. 2599 01:45:08,713 --> 01:45:10,081 THE TYPE 2 DIABETES PROGRAM IS 2600 01:45:10,081 --> 01:45:11,650 ALSO AN IMPORTANT ONE BECAUSE 2601 01:45:11,650 --> 01:45:14,686 IT'S SO GLOBAL. 2602 01:45:14,686 --> 01:45:16,021 THIS IS A KNOWLEDGE PORTAL 2603 01:45:16,021 --> 01:45:17,722 DESIGN INITIALLY TO LOOK FOR 2604 01:45:17,722 --> 01:45:20,725 GENETIC FINGERPRINTS FOR 2605 01:45:20,725 --> 01:45:21,893 DIABETES BUT SINCE WE'RE NOW 2606 01:45:21,893 --> 01:45:25,830 UNDERSTANDING THE CONVERGENCE OF 2607 01:45:25,830 --> 01:45:29,067 METABOLIC DISORDERS POTENTIALLY 2608 01:45:29,067 --> 01:45:30,502 BEING AN EXPRESSION OF UPSTREAM 2609 01:45:30,502 --> 01:45:34,706 SET OF FACTORS WE NEED TO 2610 01:45:34,706 --> 01:45:36,775 UNDERSTAND BETTER WE HAVE 2611 01:45:36,775 --> 01:45:38,410 EVOLVED THE TYPE 2 DIABETES 2612 01:45:38,410 --> 01:45:40,312 PROGRAM INTO A COMMON METABOLIC 2613 01:45:40,312 --> 01:45:42,113 DISEASE PROGRAM THAT'S LOOKING 2614 01:45:42,113 --> 01:45:43,081 SIMULTANEOUSLY AT A NUMBER OF 2615 01:45:43,081 --> 01:45:43,481 DISEASES. 2616 01:45:43,481 --> 01:45:45,317 THIS IS WHERE ONE OF THE BIGGEST 2617 01:45:45,317 --> 01:45:46,818 CHALLENGES THAT WE FACE COMES 2618 01:45:46,818 --> 01:45:49,321 INTO PLAY AND THAT IS THAT WE 2619 01:45:49,321 --> 01:45:51,756 DON'T HAVE DATA INTEROPERABILITY 2620 01:45:51,756 --> 01:45:55,460 ACROSS THE AMPS. 2621 01:45:55,460 --> 01:45:57,295 AS NIH GRAPPLES WITH THIS ACROSS 2622 01:45:57,295 --> 01:45:59,764 THE INSTITUTES WE'RE ON A SMALL 2623 01:45:59,764 --> 01:46:01,433 SCALE GRAPPLING WITH IT ACROSS 2624 01:46:01,433 --> 01:46:03,501 THE AMPS AND WE HAVE IDEAS HOW 2625 01:46:03,501 --> 01:46:07,639 TO CREATE A MORE FEDERATED DATA 2626 01:46:07,639 --> 01:46:10,375 PORTALS BECAUSE THEY'RE OPEN 2627 01:46:10,375 --> 01:46:16,614 ACCESS WANT PEOPLE TO BE ABLE TO 2628 01:46:16,614 --> 01:46:18,450 UTILIZE THEM AND INCREASING THE 2629 01:46:18,450 --> 01:46:20,051 UTILITY FOR HYPOTHESIS 2630 01:46:20,051 --> 01:46:21,519 GENERATION IF NOT ACTUAL 2631 01:46:21,519 --> 01:46:21,753 SCIENCE. 2632 01:46:21,753 --> 01:46:25,857 I'M SURE SOME ARE AWARE OF OR 2633 01:46:25,857 --> 01:46:28,026 PARTICIPATED IN THE AUTOIMMUNE 2634 01:46:28,026 --> 01:46:29,894 AND IMMUNE-MEDIATED DISEASE AMP. 2635 01:46:29,894 --> 01:46:33,298 THIS IS EVOLVING TO THE NEXT 2636 01:46:33,298 --> 01:46:37,702 GENERATION AND AFTER THAT. 2637 01:46:37,702 --> 01:46:41,473 I WON'T GO IN THE DETAILS BUT 2638 01:46:41,473 --> 01:46:43,074 BUT I THINK IT'S ANOTHER EXAMPLE 2639 01:46:43,074 --> 01:46:44,275 OF CONVERGENT THINKING. 2640 01:46:44,275 --> 01:46:46,811 WHAT I DID WANT TO SPEND A 2641 01:46:46,811 --> 01:46:48,980 COUPLE MINUTES ON IS THE BESPOKE 2642 01:46:48,980 --> 01:46:50,048 GENE THERAPY CONSORTIUM WHICH IS 2643 01:46:50,048 --> 01:46:51,383 ALSO AN AMP. 2644 01:46:51,383 --> 01:46:53,785 THE GENE THERAPY CONSORTIUM IS A 2645 01:46:53,785 --> 01:46:57,956 LITTLE BIT UNIQUE IN OUR 2646 01:46:57,956 --> 01:46:58,590 PORTFOLIO. 2647 01:46:58,590 --> 01:47:01,092 OBVIOUSLY THE GOAL IS TO GO 2648 01:47:01,092 --> 01:47:02,260 AFTER RARE DISEASES WITH A 2649 01:47:02,260 --> 01:47:03,128 GENETIC BASIS. 2650 01:47:03,128 --> 01:47:05,530 THE INITIAL PROGRAM IS FOCUSSING 2651 01:47:05,530 --> 01:47:08,566 ON AAV VECTORED GENE THERAPIES. 2652 01:47:08,566 --> 01:47:13,138 IT'S ACTUALLY AN AMP THAT IS NOT 2653 01:47:13,138 --> 01:47:14,472 SO MUCH ORIENTED TOWARDS SOLVING 2654 01:47:14,472 --> 01:47:16,741 THE UNIVERSE OF GENETIC DISEASES 2655 01:47:16,741 --> 01:47:20,612 BUT AN AMP INTERESTED IN TRYING 2656 01:47:20,612 --> 01:47:23,048 TO FIGURE OUT HOW TO CREATE A 2657 01:47:23,048 --> 01:47:26,084 REGULATORY FRAMEWORK FOR 2658 01:47:26,084 --> 01:47:27,685 MANUFACTURING OF THESE BIOLOGIC 2659 01:47:27,685 --> 01:47:29,154 S SO EVERY COMPANY WITH A GOOD 2660 01:47:29,154 --> 01:47:31,089 IDEA FOR A GENE THERAPY DOESN'T 2661 01:47:31,089 --> 01:47:34,292 HAVE TO START FROM SCRATCH. 2662 01:47:34,292 --> 01:47:35,260 EVERYBODY'S MIXING THIS UP IN 2663 01:47:35,260 --> 01:47:37,062 THEIR BATHTUB AND IT WOULD BE 2664 01:47:37,062 --> 01:47:39,064 NICE IF THERE WAS A MORE 2665 01:47:39,064 --> 01:47:39,964 STANDARDIZED APPROACH TO 2666 01:47:39,964 --> 01:47:41,633 ACCELERATE THE AVAILABILITY AND 2667 01:47:41,633 --> 01:47:45,136 TAKE THAT DEGREE OF UNCERTAINTY 2668 01:47:45,136 --> 01:47:48,840 OUT OF IT FOR THE MANUFACTURERS. 2669 01:47:48,840 --> 01:47:51,042 LIKEWISE WE NEED MORE REGULATORY 2670 01:47:51,042 --> 01:47:53,211 CERTAINTY HOW TO PROSECUTE 2671 01:47:53,211 --> 01:47:54,279 ADVANCED STAGE CLINICAL TRIALS 2672 01:47:54,279 --> 01:47:56,548 WHEN YOU CAN'T DO A CLINICAL 2673 01:47:56,548 --> 01:47:59,050 STUDIES BECAUSE THERE'S NOT 2674 01:47:59,050 --> 01:48:02,353 ENOUGH PATIENTS TO THAT STUDY 2675 01:48:02,353 --> 01:48:03,721 DESIGN MAKE SENSE. 2676 01:48:03,721 --> 01:48:04,923 THE FIRST AID CONDITIONS MAY BE 2677 01:48:04,923 --> 01:48:06,591 OF INTEREST TO SOME OF YOU ON 2678 01:48:06,591 --> 01:48:07,225 THE RIGHT. 2679 01:48:07,225 --> 01:48:10,695 THEY WERE ANNOUNCED THIS YEAR. 2680 01:48:10,695 --> 01:48:12,864 THE MANUFACTURING PROCESS ARE IN 2681 01:48:12,864 --> 01:48:16,367 PLAY AND WE'RE GETTING THE 2682 01:48:16,367 --> 01:48:18,336 CONTRACTS ORGANIZED WITH 2683 01:48:18,336 --> 01:48:18,870 INDUSTRY PARTNERS. 2684 01:48:18,870 --> 01:48:20,672 I LOVE THE QUOTE BECAUSE MY 2685 01:48:20,672 --> 01:48:26,010 COUSIN'S KID HAS MUSCULAR 2686 01:48:26,010 --> 01:48:27,545 DISTROPHY AND I KNOW ABOUT BAKE 2687 01:48:27,545 --> 01:48:28,646 SALES AND WALKS AND HOW HARD IT 2688 01:48:28,646 --> 01:48:31,416 IS TO RAISE MONEY FOR DISEASES 2689 01:48:31,416 --> 01:48:33,251 TO KNOW THERE'S BEEN TRUE 2690 01:48:33,251 --> 01:48:35,620 INVESTMENT AND WE CAN MAKE IT 2691 01:48:35,620 --> 01:48:38,957 EASIER FOR THE BIO SCIENCE 2692 01:48:38,957 --> 01:48:43,094 PARTNERS TO BE WILLING TO PUT 2693 01:48:43,094 --> 01:48:46,698 FORWARD THE RESOURCE MEANS 2694 01:48:46,698 --> 01:48:53,037 EVERYTHING. 2695 01:48:53,037 --> 01:48:56,941 THE TEAM DECIDED WE'D MOVE INTO 2696 01:48:56,941 --> 01:48:58,776 NON-VECTOR GENE THERAPIES AND 2697 01:48:58,776 --> 01:49:01,045 WORKING WITH INDUSTRY PARTNERS 2698 01:49:01,045 --> 01:49:04,482 KNOWN AS HEVE. 2699 01:49:04,482 --> 01:49:07,085 THE HEADS OF R AND D FROM THE 2700 01:49:07,085 --> 01:49:09,320 MAJOR PHARMACEUTICAL COMPANIES. 2701 01:49:09,320 --> 01:49:13,691 WE BROUGHT THE NOTION OF AN AMP 2702 01:49:13,691 --> 01:49:15,326 THAT LOOKED BEYOND AAV AND 2703 01:49:15,326 --> 01:49:17,228 THERE'S OTHER VIRAL AND 2704 01:49:17,228 --> 01:49:20,131 NON-VIRAL VECTORS AND CRISPR 2705 01:49:20,131 --> 01:49:21,666 TECHNOLOGY WE CAME TO CONCLUDE 2706 01:49:21,666 --> 01:49:24,169 IT WAS TIME TO MOVE PAST THE ONE 2707 01:49:24,169 --> 01:49:25,103 POINT APPROACH. 2708 01:49:25,103 --> 01:49:30,708 THAT WOULD BE A NEXT CHAPTER OF 2709 01:49:30,708 --> 01:49:34,913 THIS AS WELL AND THERE'S NON-NIH 2710 01:49:34,913 --> 01:49:37,515 AND GOVERNMENT PARTNERS AND CIM 2711 01:49:37,515 --> 01:49:41,019 IS THE CALIFORNIA INSTITUTE FOR 2712 01:49:41,019 --> 01:49:42,620 REGENERATIVE MEDICINE A 2713 01:49:42,620 --> 01:49:43,288 QUASI-GOVERNMENTAL ORGANIZATION 2714 01:49:43,288 --> 01:49:44,556 AND YOU SEE LITTLE 2715 01:49:44,556 --> 01:49:45,390 ORGANIZATIONS, BIG COMPANIES, 2716 01:49:45,390 --> 01:49:46,758 PATIENT ORGANIZATIONS, A WHOLE 2717 01:49:46,758 --> 01:49:49,527 SET OF STAKEHOLDERS WORKING 2718 01:49:49,527 --> 01:49:59,304 COLLABORATIVELY ON THE PROGRAMS. 2719 01:49:59,304 --> 01:50:06,010 AND BILL AND MELINDA GATES 2720 01:50:06,010 --> 01:50:13,585 LOOKED AT IN VIVO AND EX VIVO IN 2721 01:50:13,585 --> 01:50:23,728 DEVELOPING COUNTRIES WHERE MOST 2722 01:50:23,728 --> 01:50:26,364 SICKLE CELL DISEASE AND TO 2723 01:50:26,364 --> 01:50:27,332 ADVANCE TRUST IN THE COMMUNITY 2724 01:50:27,332 --> 01:50:29,000 AND THE SCIENTIFIC CAPABILITY TO 2725 01:50:29,000 --> 01:50:34,839 WORK ON A PROBLEM LIKE THIS IS A 2726 01:50:34,839 --> 01:50:36,274 LONG RUNWAY BUT WORTH DOING AND 2727 01:50:36,274 --> 01:50:37,475 SUCH A DISEASE OF YOUNG KIDS IN 2728 01:50:37,475 --> 01:50:39,110 THE AREAS IT SEEMS LIKE A 2729 01:50:39,110 --> 01:50:45,250 PROGRAM WORTH PURSUING. 2730 01:50:45,250 --> 01:50:48,019 THE BIOMARKERS PROGRAMS ARE AN 2731 01:50:48,019 --> 01:50:49,354 AMP WE'RE LAUNCHING NEXT YEAR 2732 01:50:49,354 --> 01:50:51,322 ARE LISTED HERE AND ONE THING 2733 01:50:51,322 --> 01:50:52,857 ABOUT THE ALS PROGRAM BECAUSE 2734 01:50:52,857 --> 01:50:55,994 CONGRESS PUT I THINK $100 2735 01:50:55,994 --> 01:50:57,195 MILLION IN THE CONGRESSIONAL 2736 01:50:57,195 --> 01:50:59,664 BUDGET FOR ALS. 2737 01:50:59,664 --> 01:51:00,832 THAT HAS MADE THIS A FEASIBLE 2738 01:51:00,832 --> 01:51:02,467 PLACE FOR ENGAGEMENT AND THE 2739 01:51:02,467 --> 01:51:04,369 INDUSTRY PARTNERS HAVE REALLY 2740 01:51:04,369 --> 01:51:04,869 STEPPED UP. 2741 01:51:04,869 --> 01:51:07,071 WE'RE STARTING TO UNDERSTAND THE 2742 01:51:07,071 --> 01:51:11,075 BIOLOGY BUT IT'S ALSO A 2743 01:51:11,075 --> 01:51:15,313 WONDERFUL MIXTURE OF SCIENCE AND 2744 01:51:15,313 --> 01:51:18,016 ADVOCACY INCLUDING DR. DOTOROV 2745 01:51:18,016 --> 01:51:21,452 IS A FORMER DEPUTY MAYOR OF NEW 2746 01:51:21,452 --> 01:51:23,855 YORK CITY BUT ALSO A PERSON 2747 01:51:23,855 --> 01:51:25,590 WHOSE FATHER AND UNCLE DIED OF 2748 01:51:25,590 --> 01:51:28,660 ALS ON A GENETIC BASIS AND NOW 2749 01:51:28,660 --> 01:51:31,362 HE HAS ALS NOT GENETIC AT LEAST 2750 01:51:31,362 --> 01:51:33,331 NOT THE SAME GENE THEY DO. 2751 01:51:33,331 --> 01:51:34,632 IT'S MYSTERIOUS. 2752 01:51:34,632 --> 01:51:37,535 HIS DISEASE IS PROGRESSES BUT 2753 01:51:37,535 --> 01:51:43,074 STILL BUZZES AROUND ON HIS VESPA 2754 01:51:43,074 --> 01:51:48,313 MOTORCYCLE AND GENE TO BE THE 2755 01:51:48,313 --> 01:51:50,782 ENERGIZER AND WE ENGAGE DIRECTLY 2756 01:51:50,782 --> 01:51:54,786 AND THE OTHER THING ABOUT THE 2757 01:51:54,786 --> 01:51:56,821 AMP ALS I'M EXCITE ABOUT IS WHEN 2758 01:51:56,821 --> 01:52:02,160 I WAS LEARNING ABOUT FNIH AND 2759 01:52:02,160 --> 01:52:03,995 NIH AND SPEAKING TO EXTERNAL 2760 01:52:03,995 --> 01:52:08,533 STAKEHOLDERS THE ONE THING THAT 2761 01:52:08,533 --> 01:52:10,768 DISAPPOINTED MOST IS BECAUSE 2762 01:52:10,768 --> 01:52:12,770 WE'RE FLOW. 2763 01:52:12,770 --> 01:52:14,072 FNIH DOESN'T START WORK UNTIL WE 2764 01:52:14,072 --> 01:52:15,039 FULLY FUNDED I. 2765 01:52:15,039 --> 01:52:17,709 WE RAISE ALL THE MONEY BECAUSE 2766 01:52:17,709 --> 01:52:22,313 WE COULDN'T AFFORD TO BE CAUGHT 2767 01:52:22,313 --> 01:52:23,414 HATHAWAY WITHOUT BEING ABLE TO 2768 01:52:23,414 --> 01:52:24,716 COMPLETE THE JOB. 2769 01:52:24,716 --> 01:52:27,218 WE'RE WORKING ON WAYS TO SPEED 2770 01:52:27,218 --> 01:52:28,553 THIS UP. 2771 01:52:28,553 --> 01:52:31,656 AND SOME HAS TO DO WITH SPEEDING 2772 01:52:31,656 --> 01:52:34,258 UP THE CONCEPT AND DEVELOPMENT 2773 01:52:34,258 --> 01:52:35,727 PHASE DOING IT ALL AT ONCE AND 2774 01:52:35,727 --> 01:52:39,397 WE'LL HAVE A CALL THIS MONTH AND 2775 01:52:39,397 --> 01:52:42,266 THEN ENERGY CALL MONTH AFTER 2776 01:52:42,266 --> 01:52:42,934 MONTH AND LET'S SIT DOWN AND GO 2777 01:52:42,934 --> 01:52:51,342 WITH IT. 2778 01:52:51,342 --> 01:52:52,977 WE'RE LAUNCHING A SIGNIFICANT 2779 01:52:52,977 --> 01:52:54,779 FUND RAISING PROGRAM AND THAT 2780 01:52:54,779 --> 01:52:56,314 VIDEO IS A TOOL WE'LL BE USING 2781 01:52:56,314 --> 01:52:59,050 BUT THE IDEA IS IF WE HAD A POOL 2782 01:52:59,050 --> 01:53:00,451 OF FLEXIBLE RESOURCES WE COULD 2783 01:53:00,451 --> 01:53:02,320 JUMP START THESE THINGS. 2784 01:53:02,320 --> 01:53:04,055 IF FNIH HAS A CONTINUING 2785 01:53:04,055 --> 01:53:05,690 RESOLUTION AND CAN'T GET A NEW 2786 01:53:05,690 --> 01:53:06,524 PROGRAM STARTED BECAUSE THEY 2787 01:53:06,524 --> 01:53:08,526 CAN'T FUND IT THROUGH THE 2788 01:53:08,526 --> 01:53:10,661 CONGRESSIONAL AUTHORIZATION, WE 2789 01:53:10,661 --> 01:53:13,464 CAN START IT IF WE HAVE HIGH 2790 01:53:13,464 --> 01:53:14,532 CONFIDENCE EVENTUALLY IT WILL BE 2791 01:53:14,532 --> 01:53:15,066 FUNDED. 2792 01:53:15,066 --> 01:53:16,434 WE'RE WORKING ON HOW WE CAN 2793 01:53:16,434 --> 01:53:19,837 IMPROVE OUR OWN PROCESSES AND 2794 01:53:19,837 --> 01:53:21,339 HOW WE CAN ADDITIONAL RESOURCES 2795 01:53:21,339 --> 01:53:25,743 SO WE CAN MOVE FOMORE QUICKLY 2796 01:53:25,743 --> 01:53:34,619 BECAUSE PATIENTS ARE WAITING. 2797 01:53:34,619 --> 01:53:36,387 AND ONE OF THE THINGS WE'RE 2798 01:53:36,387 --> 01:53:38,022 DOING WHICH IS REQUIRING A LOT 2799 01:53:38,022 --> 01:53:43,094 FROM THE FDA IS WORKING ON 2800 01:53:43,094 --> 01:53:46,964 DIGITAL BIOMARKERS. 2801 01:53:46,964 --> 01:53:49,934 AND HOW TO USE THEM RELIABLELY 2802 01:53:49,934 --> 01:53:53,404 IN AN FDA APPROVED MANNER FOR 2803 01:53:53,404 --> 01:53:54,338 CLINICAL TRIALS. 2804 01:53:54,338 --> 01:53:55,339 EVERYONE'S USING DIGITAL DEVICES 2805 01:53:55,339 --> 01:53:56,774 BUT THERE'S NO STANDARDIZATION. 2806 01:53:56,774 --> 01:53:58,242 IF YOU'RE A CLINICIAN YOUR 2807 01:53:58,242 --> 01:54:01,546 PATIENTS ARE CONSTANTLY COMING 2808 01:54:01,546 --> 01:54:04,215 IN WITH THEIR SLEEP RING 2809 01:54:04,215 --> 01:54:08,619 PRINTOUT OR HEART RATE 2810 01:54:08,619 --> 01:54:09,320 INFORMATION, ETCETERA. 2811 01:54:09,320 --> 01:54:11,522 YOU CAN'T EXPECT THIS TO BE 2812 01:54:11,522 --> 01:54:13,257 PARTICULARLY HELPFUL FOR FDA 2813 01:54:13,257 --> 01:54:14,992 DRUG APPROVAL OR DEVICE APREFL 2814 01:54:14,992 --> 01:54:16,360 FOR THAT MATTER WITHOUT SOME 2815 01:54:16,360 --> 01:54:17,762 DEGREE OF STANDARDIZATION. 2816 01:54:17,762 --> 01:54:19,130 WE'RE WORKING CLOSELY WITH FDA 2817 01:54:19,130 --> 01:54:25,770 TO FIGURE OUT HOW WE MIGHT BE 2818 01:54:25,770 --> 01:54:30,007 ABLE TO CREATE INTEROPERABLE 2819 01:54:30,007 --> 01:54:35,446 STANDARDS AND WHEN WE WERE 2820 01:54:35,446 --> 01:54:44,188 IMAGING FOR ALZHEIMER'S SIEMENS 2821 01:54:44,188 --> 01:54:47,225 AND IBM HAS DEVICES AND THAT 2822 01:54:47,225 --> 01:54:48,159 PROVED TO BE VALUABLE TO THE 2823 01:54:48,159 --> 01:54:53,764 INDUSTRY PARTNERS AND TO THE 2824 01:54:53,764 --> 01:54:54,131 FDA. 2825 01:54:54,131 --> 01:54:59,337 I SUSPECT SOME SIMILAR MECHANISM 2826 01:54:59,337 --> 01:55:02,306 AND WE HAD A CONVENING ON 2827 01:55:02,306 --> 01:55:03,341 BIOMARKERS AND I THINK IT WOULD 2828 01:55:03,341 --> 01:55:06,944 BE RELEVANT TO THE DISEASE AREAS 2829 01:55:06,944 --> 01:55:08,980 NIAMS IS FOCUSSED ON. 2830 01:55:08,980 --> 01:55:11,349 I WANT TO SAY SOMETHING ABOUT 2831 01:55:11,349 --> 01:55:14,552 PATIENT CENTRICITY. 2832 01:55:14,552 --> 01:55:22,727 NIH IS PATIENT CENTRIC AND I WAS 2833 01:55:22,727 --> 01:55:26,130 AT MERCK AND WE LOOKED AT 2834 01:55:26,130 --> 01:55:33,971 PATIENT OUTCOMES BUT WE CREATED 2835 01:55:33,971 --> 01:55:35,773 A POSITION FOR AN EMPLOYEE ONE 2836 01:55:35,773 --> 01:55:39,043 OF OUR PROJECT OFFICERS BUT ALSO 2837 01:55:39,043 --> 01:55:41,779 IS NOW OUR CHIEF PATIENT 2838 01:55:41,779 --> 01:55:42,046 ORGANIZER. 2839 01:55:42,046 --> 01:55:43,114 OVER THE LAST YEAR WE'VE DONE 2840 01:55:43,114 --> 01:55:44,782 THINGS TO TRY TO BRING THE 2841 01:55:44,782 --> 01:55:47,084 VOICES OF PATIENTS IN A MORE 2842 01:55:47,084 --> 01:55:49,253 DISTRICT WAY INCLUDING LAUNCHING 2843 01:55:49,253 --> 01:55:50,955 A PATIENT ENGAGEMENT COUNCIL 2844 01:55:50,955 --> 01:55:52,423 WHICH INCLUDES A NUMBER OF 2845 01:55:52,423 --> 01:55:56,027 PATIENT ADVOCATES. 2846 01:55:56,027 --> 01:55:57,428 MORE IMPORTANTLY, INCORPORATING 2847 01:55:57,428 --> 01:56:00,464 AS PROJECTS ARE DESIGN THE INPUT 2848 01:56:00,464 --> 01:56:04,635 OF THE PATIENT ORGANIZATIONS AND 2849 01:56:04,635 --> 01:56:06,037 INDIVIDUALS WHO ARE MOST 2850 01:56:06,037 --> 01:56:08,172 INTERESTED IN HOW THE PROGRAMS 2851 01:56:08,172 --> 01:56:08,506 PROGRESS. 2852 01:56:08,506 --> 01:56:11,108 WE DO NOT -- I DO NOT APPROVE OF 2853 01:56:11,108 --> 01:56:12,777 A NEW PROJECT UNLESS THE PLAN 2854 01:56:12,777 --> 01:56:15,079 INCLUDES IN A MEANINGFUL WAY NOT 2855 01:56:15,079 --> 01:56:17,081 JUST CHECK A BOX, WE TALK TO A 2856 01:56:17,081 --> 01:56:18,683 PATIENT BUT MEANINGFUL INPUT AND 2857 01:56:18,683 --> 01:56:20,051 WE'RE LEARNING AND THAT'S ONE OF 2858 01:56:20,051 --> 01:56:21,419 THE THINGS THE PATIENT 2859 01:56:21,419 --> 01:56:22,753 ENGAGEMENT COUNCIL IS HELPING US 2860 01:56:22,753 --> 01:56:25,957 WITH WE ALSO HAVE A NUMBER OF 2861 01:56:25,957 --> 01:56:27,058 PATIENT AMBASSADORS AND WE HAVE 2862 01:56:27,058 --> 01:56:29,527 PATIENT ARE MONTHLY ALL HANDS 2863 01:56:29,527 --> 01:56:33,664 MEETING TO COME IN AND SHARE 2864 01:56:33,664 --> 01:56:37,501 WITH US THEIR LIVED EXPERIENCE 2865 01:56:37,501 --> 01:56:40,371 WITH THE DISEASES. 2866 01:56:40,371 --> 01:56:43,074 WE HAD SOMEONE COME SPEAK ABOUT 2867 01:56:43,074 --> 01:56:45,710 THEIR EXPERIENCE WITH ALS. 2868 01:56:45,710 --> 01:56:47,378 AND SOME 25,000 PEOPLE 2869 01:56:47,378 --> 01:56:48,613 PARTICIPATED IN VARIOUS TRAINING 2870 01:56:48,613 --> 01:56:51,382 AND MENTORSHIP AND FELLOWSHIP 2871 01:56:51,382 --> 01:56:55,686 PROGRAMS BUT OUR MOST RELEVANT 2872 01:56:55,686 --> 01:56:57,054 VISUAL CONTRIBUTION ARE OUR 2873 01:56:57,054 --> 01:56:57,388 TRAILBLAZERS. 2874 01:56:57,388 --> 01:57:02,493 THE PEOPLE WHO ARE SINGLED OUT 2875 01:57:02,493 --> 01:57:04,128 FOR BEING RISING STARS OUR 2876 01:57:04,128 --> 01:57:05,963 ANNUAL CEREMONY TO HONOR THE 2877 01:57:05,963 --> 01:57:07,264 INDIVIDUALS IS COMING FORWARD IN 2878 01:57:07,264 --> 01:57:11,569 OCTOBER. 2879 01:57:11,569 --> 01:57:13,270 FOR SOME REASON SEVERAL OF THE 2880 01:57:13,270 --> 01:57:14,472 CANDIDATES AND TWO OR THREE OF 2881 01:57:14,472 --> 01:57:22,246 THE PEOPLE WHO ARE GOING TO BE 2882 01:57:22,246 --> 01:57:23,581 HONORED ARE INVOLVED IN 2883 01:57:23,581 --> 01:57:24,248 MITOCHONDRIAL RESEARCH SO GUESS 2884 01:57:24,248 --> 01:57:26,083 WHAT WE MIGHT BE WORKING ON NEXT 2885 01:57:26,083 --> 01:57:26,317 YEAR? 2886 01:57:26,317 --> 01:57:30,254 THE TIME HAS COME. 2887 01:57:30,254 --> 01:57:31,489 I'VE TALKED ABOUT TEAM SCIENCE 2888 01:57:31,489 --> 01:57:34,625 AND SUPPORT FOR SCIENCE AND END 2889 01:57:34,625 --> 01:57:36,093 WITH THE NOTION THAT IS TO TELL 2890 01:57:36,093 --> 01:57:37,762 YOU ABOUT EARNING TRUST IN 2891 01:57:37,762 --> 01:57:39,597 SCIENCE AND THE COALITION FOR 2892 01:57:39,597 --> 01:57:41,198 TRUST IN HEALTH AND SCIENCE 2893 01:57:41,198 --> 01:57:42,600 THAT'S BEEN ESTABLISHED. 2894 01:57:42,600 --> 01:57:44,101 THERE'S NOW MORE THAN 80 2895 01:57:44,101 --> 01:57:45,836 ORGANIZATIONS THAT HAVE SIGNED 2896 01:57:45,836 --> 01:57:47,038 ON TO THE COALITION INCLUDING 2897 01:57:47,038 --> 01:57:51,642 SOME THAT ARE INCLUDED IN THE 2898 01:57:51,642 --> 01:57:52,009 COALITION HERE. 2899 01:57:52,009 --> 01:57:53,377 THE PURPOSE OF THIS IS TO 2900 01:57:53,377 --> 01:57:55,379 RECOGNIZE EVERYONE'S TRYING TO 2901 01:57:55,379 --> 01:57:57,248 DO SOMETHING ABOUT 2902 01:57:57,248 --> 01:57:58,449 MISINFORMATION AND 2903 01:57:58,449 --> 01:57:59,817 DISINFORMATION AND TRUST BUT 2904 01:57:59,817 --> 01:58:01,452 WE'RE NOT ADDING UP TO HAVING 2905 01:58:01,452 --> 01:58:03,054 MUCH IMPACT BECAUSE EVERYBODY'S 2906 01:58:03,054 --> 01:58:06,157 DOING THEIR THING AND THEIR 2907 01:58:06,157 --> 01:58:07,758 SPACE AND THE VECTORS ARE NOT 2908 01:58:07,758 --> 01:58:10,161 POINTING IN THE SAME DIRECTION. 2909 01:58:10,161 --> 01:58:12,997 SO THIS ORGANIZATION HAS COME 2910 01:58:12,997 --> 01:58:15,132 TOGETHER TO JOIN YOU HAVE TO 2911 01:58:15,132 --> 01:58:17,668 AGREE TO DO THREE THINGS. 2912 01:58:17,668 --> 01:58:18,903 ONE, AGREE TO CONTRIBUTE 2913 01:58:18,903 --> 01:58:19,670 INFORMATION ABOUT WHAT YOU ARE 2914 01:58:19,670 --> 01:58:21,972 DOING AND WHETHER OR NOT IT'S 2915 01:58:21,972 --> 01:58:23,808 WORKING TO A LEARNING COMPENDIUM 2916 01:58:23,808 --> 01:58:25,976 SO THAT HOPEFULLY AT A LOCAL 2917 01:58:25,976 --> 01:58:27,478 LEVEL PEOPLE CAN CONNECT UP WITH 2918 01:58:27,478 --> 01:58:28,245 OTHERS WORKING ON THE SAME SORT 2919 01:58:28,245 --> 01:58:33,551 OF THINGS. 2920 01:58:33,551 --> 01:58:36,887 AND AGREE WHEN YOU HEAR 2921 01:58:36,887 --> 01:58:38,222 MISINFORMATION YOU'LL TAKE STEPS 2922 01:58:38,222 --> 01:58:40,558 TO CORRECT IT PREFERABLY ON 2923 01:58:40,558 --> 01:58:41,158 SOCIAL MEDIA BECAUSE THAT'S 2924 01:58:41,158 --> 01:58:43,694 WHERE MOST THE DISINFORMATION IS 2925 01:58:43,694 --> 01:58:45,896 CIRCULATING AND PUSHBACK ON 2926 01:58:45,896 --> 01:58:46,897 DANGEROUS DISINFORMATION. 2927 01:58:46,897 --> 01:58:51,936 THAT'S ONE PLACE WE'RE TRYING TO 2928 01:58:51,936 --> 01:58:53,904 HELP TO GIVE PEOPLE INFORMATION 2929 01:58:53,904 --> 01:58:55,806 AND WHEN YOU ADD UP THE PEOPLE 2930 01:58:55,806 --> 01:58:58,275 IN THE ORGANIZATIONS INCLUDING 2931 01:58:58,275 --> 01:59:01,212 THE TRIPLE AAAS WE'RE TOUCHING 2932 01:59:01,212 --> 01:59:02,780 HUNDREDS OF THOUSANDS OF MEMBERS 2933 01:59:02,780 --> 01:59:07,184 IN COMMUNITY ORGANIZATIONS. 2934 01:59:07,184 --> 01:59:09,420 IF WE MOBILIZE OUR OWN CHANNELS 2935 01:59:09,420 --> 01:59:10,688 ON SOCIAL WE'D BE A POWERFUL 2936 01:59:10,688 --> 01:59:11,555 SOURCE OF INFORMATION AND THAT'S 2937 01:59:11,555 --> 01:59:12,623 THE VISION HERE. 2938 01:59:12,623 --> 01:59:14,525 I WANTED TO MAKE YOU AWARE OF IT 2939 01:59:14,525 --> 01:59:16,460 AND SOME OF YOU MAY HAVE A 2940 01:59:16,460 --> 01:59:18,395 PARTICULAR INTEREST IN THIS 2941 01:59:18,395 --> 01:59:18,763 SPACE. 2942 01:59:18,763 --> 01:59:23,334 THE HEALTH RESEARCH ALLIANCE IS 2943 01:59:23,334 --> 01:59:26,470 A MEMBER AS ARE SEVERAL OTHER 2944 01:59:26,470 --> 01:59:26,637 OHS. 2945 01:59:26,637 --> 01:59:33,277 I'LL END THERE AND SAY WE ARE 2946 01:59:33,277 --> 01:59:34,411 AMBITIOUS AND EXCITED I LOVE 2947 01:59:34,411 --> 01:59:36,514 GOING TO WORK EVERY DAY IT'S THE 2948 01:59:36,514 --> 01:59:38,816 MOST FUN I'VE HAD AT A JOB EVER 2949 01:59:38,816 --> 01:59:40,718 AND GOOD TO BE CLOSE TO THE 2950 01:59:40,718 --> 01:59:42,086 SCIENCE AGAIN AND WE HAVE WORK 2951 01:59:42,086 --> 01:59:43,354 TO DO AND HOPE YOU'LL BE PART OF 2952 01:59:43,354 --> 01:59:45,422 THE BRIDGE. 2953 01:59:45,422 --> 01:59:55,766 THANK YOU VERY MUCH. 2954 01:59:57,201 --> 01:59:58,135 QUESTIONS OR COMMENTS? 2955 02:00:05,309 --> 02:00:07,344 >> MY QUESTION IS RELATED TO 2956 02:00:07,344 --> 02:00:09,280 ENGAGEMENT OF UNIVERSITIES 2957 02:00:09,280 --> 02:00:09,647 DIRECTLY. 2958 02:00:09,647 --> 02:00:14,518 IT SEEMS LIKE YOU'RE ENGAGING 2959 02:00:14,518 --> 02:00:16,053 ASPECTS OF THE HEALTH SCIENCE 2960 02:00:16,053 --> 02:00:18,289 CONTINUUM AND THERE'S MEDICAL 2961 02:00:18,289 --> 02:00:19,824 CENTER AND UNIVERSITIES 2962 02:00:19,824 --> 02:00:20,524 RECEIVING RESOURCES FROM NIH. 2963 02:00:20,524 --> 02:00:22,226 DO YOU DO ANYTHING TO ENGAGE 2964 02:00:22,226 --> 02:00:24,128 WITH THEM OR WHAT'S THAT LOOK 2965 02:00:24,128 --> 02:00:28,732 LIKE IN TERMS OF COLLABORATION? 2966 02:00:28,732 --> 02:00:34,271 >> I VISITED BAYLOR MEDICAL 2967 02:00:34,271 --> 02:00:43,681 CENTER AND WE MET WITH THE CEO 2968 02:00:43,681 --> 02:00:46,851 AND THAT'S ACTUALLY WHERE I 2969 02:00:46,851 --> 02:00:48,652 FIRST REALLY BECAME CONVINCE THE 2970 02:00:48,652 --> 02:00:51,055 NUMBER ONE ISSUE IS THE RESEARCH 2971 02:00:51,055 --> 02:00:56,727 IS POSTDOCS. 2972 02:00:56,727 --> 02:00:58,329 AND THE NIH ADVISORY COMMITTEE 2973 02:00:58,329 --> 02:01:02,900 HAS SPECIAL WORKING GROUP ON 2974 02:01:02,900 --> 02:01:04,134 POSTDOC SUPPORT AND I HAD A 2975 02:01:04,134 --> 02:01:07,071 CHANCE TO INTERACT WITH THEM AND 2976 02:01:07,071 --> 02:01:09,406 MAY INCREASE TRAINING AND 2977 02:01:09,406 --> 02:01:12,576 ACADEMIA AND TRAINING AND 2978 02:01:12,576 --> 02:01:13,510 INDUSTRY COULD FACILITATE EYE 2979 02:01:13,510 --> 02:01:15,679 SOLUTION THAT COULD BE WIN-WIN 2980 02:01:15,679 --> 02:01:20,317 AND NOT JUST ALLOW INDUSTRY TO 2981 02:01:20,317 --> 02:01:27,057 HARVEST THE BEST POSTDOCS. 2982 02:01:27,057 --> 02:01:33,364 IN THE CONVERSATIONS AND THERE'S 2983 02:01:33,364 --> 02:01:35,432 A HUGE RESEARCH LAB SO THEY'RE 2984 02:01:35,432 --> 02:01:39,403 INTERESTED IN HOW THE 2985 02:01:39,403 --> 02:01:41,205 PARTNERSHIP MODELS WORK AND THEY 2986 02:01:41,205 --> 02:01:44,241 ASKED THE EXACT QUESTION YOU 2987 02:01:44,241 --> 02:01:44,408 DID. 2988 02:01:44,408 --> 02:01:47,044 WE DEVELOPED A LEGAL OPINION 2989 02:01:47,044 --> 02:01:48,846 WHICH SAYS WE'RE NOT PROHIBITED 2990 02:01:48,846 --> 02:01:51,081 FROM DOING IT AND NOT 2991 02:01:51,081 --> 02:01:52,149 SPECIFICALLY AUTHORIZED. 2992 02:01:52,149 --> 02:01:54,485 MAKE SURE WE DON'T ARE UP AFOUL. 2993 02:01:54,485 --> 02:01:56,287 I THINK WE CAN MOVE IN THAT 2994 02:01:56,287 --> 02:01:56,887 DIRECTION AS WELL. 2995 02:01:56,887 --> 02:02:00,257 THAT MOVES FOR ACADEMIA BECAUSE 2996 02:02:00,257 --> 02:02:03,060 THEY'RE TRYING TO BUILD 2997 02:02:03,060 --> 02:02:04,094 PUBLIC-PRIVATE PARTNERSHIPS. 2998 02:02:04,094 --> 02:02:06,864 AS LONG AS WE DO IT WITH THE 2999 02:02:06,864 --> 02:02:08,766 FULL INCLUSION OF NIH AND 3000 02:02:08,766 --> 02:02:09,400 CONVERSATION AND FULL 3001 02:02:09,400 --> 02:02:11,902 TRANSPARENCY IT COULD BE 3002 02:02:11,902 --> 02:02:12,136 HELPFUL. 3003 02:02:12,136 --> 02:02:13,170 THE SMALLER COMPANIES ARE 3004 02:02:13,170 --> 02:02:16,941 INTERESTED IN THIS. 3005 02:02:16,941 --> 02:02:21,312 IS ANYONE HERE FROM IC? 3006 02:02:21,312 --> 02:02:23,347 THE NIAID EFFORT TO DO THE 3007 02:02:23,347 --> 02:02:24,682 COUNTER MEASURE DEVELOPMENT THE 3008 02:02:24,682 --> 02:02:26,717 STATE HAS PUT MONEY INTO THAT 3009 02:02:26,717 --> 02:02:28,352 BUT THEY'RE RAISING MON Y FROM 3010 02:02:28,352 --> 02:02:31,088 THE PRIVATE SECTOR TO DO THE 3011 02:02:31,088 --> 02:02:32,056 TRANSLATIONAL PIECE AND THE 3012 02:02:32,056 --> 02:02:33,424 MODEL THAT LOOKS SOMETHING LIKE 3013 02:02:33,424 --> 02:02:41,865 THIS. 3014 02:02:41,865 --> 02:02:44,335 I CO-CHAIRED A COMMISSION AND 3015 02:02:44,335 --> 02:02:45,135 IT'S A MODEL WE MAY BE ABLE TO 3016 02:02:45,135 --> 02:02:55,279 EXPAND. 3017 02:03:07,324 --> 02:03:16,433 >> HOW DO SPIRs AND STPRs GET 3018 02:03:16,433 --> 02:03:17,601 [INAUDIBLE] 3019 02:03:17,601 --> 02:03:19,937 >> I'M NOT AN EXPERT ON THOSE 3020 02:03:19,937 --> 02:03:25,409 GRANTS BUT I READ THE ONE THAT 3021 02:03:25,409 --> 02:03:30,314 JUST CAME OUT AND THEY GO TO A 3022 02:03:30,314 --> 02:03:32,616 SINGLE ENTITY AND WE WOUL NOT 3023 02:03:32,616 --> 02:03:41,358 REALLY WANT TO HAVE A SINGLE -- 3024 02:03:41,358 --> 02:03:45,262 I'M SORRY, I NEED TO TURN THIS 3025 02:03:45,262 --> 02:03:45,863 ON. 3026 02:03:45,863 --> 02:03:48,766 OUR INDUSTRY MODEL IS 3027 02:03:48,766 --> 02:03:51,435 MULTIPLE INDUSTRIES. 3028 02:03:51,435 --> 02:03:55,072 WE LIKE TO HAVE MULTIPLE 3029 02:03:55,072 --> 02:03:58,776 PARTNERS AND ALSO IP IS NOT OUR 3030 02:03:58,776 --> 02:03:58,976 GOAL. 3031 02:03:58,976 --> 02:04:01,612 THESE ARE PRE-COMPETITIVE 3032 02:04:01,612 --> 02:04:03,447 COLLABORATIONS AND THAT MAKES IT 3033 02:04:03,447 --> 02:04:04,615 DIFFERENT. 3034 02:04:04,615 --> 02:04:05,215 DO YOU WANT TO SAY ANYTHING 3035 02:04:05,215 --> 02:04:06,483 ABOUT THE SBIR MODEL BECAUSE I 3036 02:04:06,483 --> 02:04:06,950 DON'T KNOW THE OTHER 3037 02:04:06,950 --> 02:04:17,194 DISTINCTIONS. 3038 02:04:17,895 --> 02:04:20,597 WE'RE AFFORDED A CERTAIN 3039 02:04:20,597 --> 02:04:21,999 PROPORTION OF OUR BUDGET THAT 3040 02:04:21,999 --> 02:04:23,967 GOES WITH SMALL BUSINESS ARE 3041 02:04:23,967 --> 02:04:25,102 INTERESTED IN DEVELOPING A 3042 02:04:25,102 --> 02:04:26,804 DEVICE OR APPROACH AND WE REVIEW 3043 02:04:26,804 --> 02:04:28,906 IT AS A GREAT COMPLIMENT TO SOME 3044 02:04:28,906 --> 02:04:31,075 OF THE OTHER WORK WE DO BUT I 3045 02:04:31,075 --> 02:04:32,943 AGREE IT'S A DIFFERENT MODEL 3046 02:04:32,943 --> 02:04:35,746 THAN THE FNIH MODEL IN TERMS OF 3047 02:04:35,746 --> 02:04:39,283 THE STAGE OF THE PROCESS AND THE 3048 02:04:39,283 --> 02:04:40,651 COLLABORATIVE MULTI-PARTNER 3049 02:04:40,651 --> 02:04:40,951 NATURE. 3050 02:04:40,951 --> 02:04:44,021 IF ANY OF MY COLLEAGUES WANT IT 3051 02:04:44,021 --> 02:04:54,531 ADD TO THAT, PLEASE FEEL FREE. 3052 02:05:19,656 --> 02:05:19,756 >> 3053 02:05:19,756 --> 02:05:29,933 [OFF-MIC] 3054 02:05:35,539 --> 02:05:39,009 -- SO THE QUESTION I WAS ASKING 3055 02:05:39,009 --> 02:05:43,213 IS OPPORTUNITIES FOR PROJECTS 3056 02:05:43,213 --> 02:05:49,086 WITHIN THE FNIH TO BE PASSED TO 3057 02:05:49,086 --> 02:05:52,055 OTHER PARTNERING S WITH THE FNIH 3058 02:05:52,055 --> 02:05:53,390 AND THE AMP AIM PROGRAM IS 3059 02:05:53,390 --> 02:05:55,025 CREATING A TREMENDOUS AMOUNT OF 3060 02:05:55,025 --> 02:05:58,028 INFORMATION ON TARGETS FOR 3061 02:05:58,028 --> 02:05:59,796 POTENTIAL BIOMARKERS THAT I 3062 02:05:59,796 --> 02:06:01,398 WOULD LOVE TO SEE WORKING INTO 3063 02:06:01,398 --> 02:06:04,168 THE BIOMARKERS CONSORTIUM. 3064 02:06:04,168 --> 02:06:06,236 DOES SUCH A STRUCTURAL MECHANISM 3065 02:06:06,236 --> 02:06:08,539 EXIST WITHIN THAT AND ARE THERE 3066 02:06:08,539 --> 02:06:10,974 OPPORTUNITIES FOR GROUPS LIKE 3067 02:06:10,974 --> 02:06:19,082 OURS TO ADVOCATE WHEN THOSE 3068 02:06:19,082 --> 02:06:20,117 OPPORTUNITIES MIGHT PEAK 3069 02:06:20,117 --> 02:06:20,484 INTEREST? 3070 02:06:20,484 --> 02:06:21,718 >> I UNDERSTAND YOUR QUESTION 3071 02:06:21,718 --> 02:06:24,421 AND THE ANSWER IS YES BUT NOT 3072 02:06:24,421 --> 02:06:24,755 SYSTEMICALLY. 3073 02:06:24,755 --> 02:06:26,523 IT'S NOT LIKE WE HAVE A PLANNED 3074 02:06:26,523 --> 02:06:29,293 ARCHITECTURE TO DO IT. 3075 02:06:29,293 --> 02:06:30,327 ONE EXAMPLE IS ALZHEIMER'S 3076 02:06:30,327 --> 02:06:33,430 DISEASE WHERE IT START AS A 3077 02:06:33,430 --> 02:06:35,933 LONGITUDINAL COHORT AND 3078 02:06:35,933 --> 02:06:37,634 BIOMARKERS WERE DISCOVERED AND 3079 02:06:37,634 --> 02:06:39,036 THEY WENT INTO THE BIOMARKERS 3080 02:06:39,036 --> 02:06:41,371 CONSORTIUM FOR THAT DISEASE AND 3081 02:06:41,371 --> 02:06:46,643 WE HAVE OBVIOUSLY AN ALZHEIMER'S 3082 02:06:46,643 --> 02:06:49,413 AMP AS WELL AND THIS IS THE 3083 02:06:49,413 --> 02:06:51,081 CHALLENGE I MENTIONED THE 3084 02:06:51,081 --> 02:06:52,182 INTEROPERABILITY CHALLENGE AND 3085 02:06:52,182 --> 02:06:54,818 AS WE THINK MORE SYSTEMS BILLING 3086 02:06:54,818 --> 02:06:55,852 AND LESS ABOUT A SPECIFIC 3087 02:06:55,852 --> 02:06:57,454 THERAPEUTIC AREA WE'RE GOING TO 3088 02:06:57,454 --> 02:07:01,158 NEED TO FIGURE THIS OUT. 3089 02:07:01,158 --> 02:07:02,693 BECAUSE IN TIMES THE PARTNERS 3090 02:07:02,693 --> 02:07:04,094 AND PEOPLE ARE THE SAME 3091 02:07:04,094 --> 02:07:05,495 PARTICULARLY ON THE INDUSTRY 3092 02:07:05,495 --> 02:07:06,663 SIDE YOU CAN IMAGINE THERE'S 3093 02:07:06,663 --> 02:07:08,966 ALREADY AN ELEMENT OF 3094 02:07:08,966 --> 02:07:12,302 INTEGRATION BUT THE DATA SYSTEMS 3095 02:07:12,302 --> 02:07:15,205 WERE NOT DESIGN UP FRONT TO MAKE 3096 02:07:15,205 --> 02:07:23,714 THAT EEFBL. 3097 02:07:23,714 --> 02:07:24,114 -- FEASIBLE. 3098 02:07:24,114 --> 02:07:26,717 WE'RE THINKING SOME OF THE WORK 3099 02:07:26,717 --> 02:07:29,019 BEING STARTED AS PHASE 1 STUDIES 3100 02:07:29,019 --> 02:07:33,423 OF EXISTING DRUGS THAT ARE 3101 02:07:33,423 --> 02:07:37,894 APPROVED FOR SAY DEPRESSION BUT 3102 02:07:37,894 --> 02:07:38,929 FOR SUBTYPES OF PEOPLE THAT 3103 02:07:38,929 --> 02:07:40,230 RESPOND IF WE COULD DESIGN THE 3104 02:07:40,230 --> 02:07:41,732 DATA TO ACCOMMODATE THAT WITH 3105 02:07:41,732 --> 02:07:43,166 THE IDEA IN MIND THAT WE'RE 3106 02:07:43,166 --> 02:07:47,104 GOING TO BE MOVING THIS FORWARD 3107 02:07:47,104 --> 02:07:50,340 INTO A BC PROJECT OR AMP WE 3108 02:07:50,340 --> 02:07:51,441 WOULD DESIGN THE DATA COLLECTION 3109 02:07:51,441 --> 02:07:54,878 AS CLOSE TO WHAT WE THINK WOULD 3110 02:07:54,878 --> 02:08:00,817 BE THE FUTURE OF THAT NEED GOING 3111 02:08:00,817 --> 02:08:01,051 FORWARD. 3112 02:08:01,051 --> 02:08:05,322 AND IT'S PART OF TO BE CANDID IS 3113 02:08:05,322 --> 02:08:07,357 THAT INSTITUTE HAVE THEIR OWN 3114 02:08:07,357 --> 02:08:08,358 APPROACH HOW THEY MANAGE DATA. 3115 02:08:08,358 --> 02:08:13,897 WE DID A CROSS-WALK OF ALL THE 3116 02:08:13,897 --> 02:08:17,167 PROGRAMS SOME ARE AT SAGE, SOME 3117 02:08:17,167 --> 02:08:20,771 MANAGED AT THE NIH AND SOME AT 3118 02:08:20,771 --> 02:08:23,040 ACADEMIC DATA CENTER AND COMING 3119 02:08:23,040 --> 02:08:25,042 UP WITH A COMMON CORE DATA SET 3120 02:08:25,042 --> 02:08:25,876 FOR STANDARDS THAT DON'T HAVE TO 3121 02:08:25,876 --> 02:08:29,446 DO WITH THE OMICS SITUATION IT'S 3122 02:08:29,446 --> 02:08:29,946 A BIG LIFT. 3123 02:08:29,946 --> 02:08:32,883 I THINK NCI AND MONICA ARE VERY 3124 02:08:32,883 --> 02:08:35,285 INTERESTED IN THIS SO IT MAY BE 3125 02:08:35,285 --> 02:08:40,190 SNAG WILL GEZ -- GET EASIER IN 3126 02:08:40,190 --> 02:08:40,924 THE FUTURE. 3127 02:08:40,924 --> 02:08:43,460 I THINK THE AMPS COULD BE A TEST 3128 02:08:43,460 --> 02:08:46,963 BED OR THE NEW AMPS COMING WE 3129 02:08:46,963 --> 02:08:48,131 MAY BE ABLE TO FACILITATE THAT 3130 02:08:48,131 --> 02:08:52,636 BUT IF YOU HAVE IDEAS TALK TO 3131 02:08:52,636 --> 02:08:53,737 BECAUSE I'M TALKING ABOUT USE 3132 02:08:53,737 --> 02:08:54,271 CASE. 3133 02:08:54,271 --> 02:08:56,807 >> I LOVE THE LINE ABOUT HERDING 3134 02:08:56,807 --> 02:08:57,007 LIONS. 3135 02:08:57,007 --> 02:09:01,178 >> I THINK MY TIME IS -- SHE'S 3136 02:09:01,178 --> 02:09:03,380 HOLDING ME THE ONE MINUTE TO END 3137 02:09:03,380 --> 02:09:03,580 SIGN. 3138 02:09:03,580 --> 02:09:07,084 I'LL AGAIN THANK YOU FOR THE 3139 02:09:07,084 --> 02:09:09,386 WORK YOU DO AND FOR THOSE 3140 02:09:09,386 --> 02:09:10,287 CLOSEST TO THE PATIENTS THANK 3141 02:09:10,287 --> 02:09:11,521 YOU FOR BEING ADVOCATES. 3142 02:09:11,521 --> 02:09:14,324 I WAS GLAD TO SEE THAT WAS AN 3143 02:09:14,324 --> 02:09:15,459 IMPORTANT PART OF THE 3144 02:09:15,459 --> 02:09:19,529 COALITION'S WORK BECAUSE WE 3145 02:09:19,529 --> 02:09:21,164 CAN'T DO THAT AND WE'RE GLAD 3146 02:09:21,164 --> 02:09:24,735 THERE'S A UNIVERSE OF PEOPLE WHO 3147 02:09:24,735 --> 02:09:25,502 ARE BECAUSE NIAMS NEEDS YOUR 3148 02:09:25,502 --> 02:09:27,070 SUPPORT. 3149 02:09:27,070 --> 02:09:37,247 THANK YOU. 3150 02:09:52,462 --> 02:09:58,468 >> THANK YOU DR. GERBERDING AND 3151 02:09:58,468 --> 02:09:59,302 FOR TAKING THE TIME TO BE WITH 3152 02:09:59,302 --> 02:10:00,036 US TODAY. 3153 02:10:00,036 --> 02:10:02,139 I'M PLEASED TO KICK OFF THE NEXT 3154 02:10:02,139 --> 02:10:05,675 SESSION OUR LAST SESSION OF THE 3155 02:10:05,675 --> 02:10:08,412 MORNING BY INTRODUCING DR. GAIL 3156 02:10:08,412 --> 02:10:10,213 LESTER DIRECTOR OF THE DIVISION 3157 02:10:10,213 --> 02:10:11,047 OF EXTRAMURAL RESEARCH AT NIAMS 3158 02:10:11,047 --> 02:10:13,049 WHO WILL KICK OFF THE NEXT 3159 02:10:13,049 --> 02:10:15,051 SESSION TODAY. 3160 02:10:15,051 --> 02:10:17,053 IN ADDITION TO HER PROGRAMMATIC 3161 02:10:17,053 --> 02:10:18,889 MANAGEMENT OF GRANT, SHE SERVES 3162 02:10:18,889 --> 02:10:22,692 AS THE PROJECT OFFICER FOR THE 3163 02:10:22,692 --> 02:10:23,393 PUBLIC-PRIVATE PARTNERSHIP 3164 02:10:23,393 --> 02:10:24,828 OSTEOARTHRITIS INITIATIVE AND AS 3165 02:10:24,828 --> 02:10:29,132 THE PROJECT DIRECTOR FOR THE 3166 02:10:29,132 --> 02:10:30,233 FNIH BIOMARKER CONSORTIUM BONE 3167 02:10:30,233 --> 02:10:31,101 QUALITY PROJECT. 3168 02:10:31,101 --> 02:10:33,370 PRIOR TO HER ARRIVAL IN NIAMS IN 3169 02:10:33,370 --> 02:10:34,805 2001 SHE WAS A PROFESSOR IN THE 3170 02:10:34,805 --> 02:10:37,007 DEPARTMENT OF ORTHOPEDICS AT THE 3171 02:10:37,007 --> 02:10:40,644 UNIVERSITY OF NORTH CAROLINA AT 3172 02:10:40,644 --> 02:10:42,312 CHAPEL HILL AND AUTHORED MORE 3173 02:10:42,312 --> 02:10:45,515 THAN 60 PEER-REVIEWED 3174 02:10:45,515 --> 02:10:48,952 PUBLICATION AND SEVERAL BOOK 3175 02:10:48,952 --> 02:10:50,086 CHAPTERS FROM THE SEGMENT OF HER 3176 02:10:50,086 --> 02:10:50,320 CAREER. 3177 02:10:50,320 --> 02:10:57,027 OVER TO YOU. 3178 02:10:57,027 --> 02:11:03,066 >> HELLO, I'M DELIGHTED TO GIVE 3179 02:11:03,066 --> 02:11:10,373 YOU THE INTRODUCTION TO NIAMS 3180 02:11:10,373 --> 02:11:11,541 EXTRAMURAL PROGRAMS AND THOSE 3181 02:11:11,541 --> 02:11:14,444 HERE TO TALK ABOUT THE SCIENCE 3182 02:11:14,444 --> 02:11:15,545 WE SUPPORT AT NIAMS. 3183 02:11:15,545 --> 02:11:18,014 MY TALK IS GOING TO BE PRETTY 3184 02:11:18,014 --> 02:11:19,049 SHORT. 3185 02:11:19,049 --> 02:11:24,521 I ONLY HAVE EIGHT SLIDES AND 3186 02:11:24,521 --> 02:11:25,622 SEVERAL ARE NOT SPEAKABLE TO 3187 02:11:25,622 --> 02:11:27,457 LIKE THIS ONE BUT I'LL TRY TO 3188 02:11:27,457 --> 02:11:31,561 MOVE THROUGH RAPIDLY SO WE HAVE 3189 02:11:31,561 --> 02:11:32,395 MORE TIME TO BE TOGETHER IN THE 3190 02:11:32,395 --> 02:11:36,833 GROUPS THAT WE'RE GOING TO GO 3191 02:11:36,833 --> 02:11:37,367 INTO AS SOON AS I FINISH 3192 02:11:37,367 --> 02:11:44,608 PRESENTING TO YOU. 3193 02:11:44,608 --> 02:11:48,311 YOU ALREADY HAD AN INTRODUCTION 3194 02:11:48,311 --> 02:11:52,115 FROM DR. CRISWELL ABOUT THE 3195 02:11:52,115 --> 02:11:55,051 MAKEUP OF NIAMS FOR THOSE WHO 3196 02:11:55,051 --> 02:11:56,253 MAY BE HERE FOR THE FIRST TIME, 3197 02:11:56,253 --> 02:12:00,490 IT'S IMPORTANT FOR YOU TO 3198 02:12:00,490 --> 02:12:01,725 UNDERSTAND OUR MISSION WHICH IS 3199 02:12:01,725 --> 02:12:04,728 OUTLINED IN THE THREE BULLETS 3200 02:12:04,728 --> 02:12:05,862 AND TO UNDERSTAND THAT 3201 02:12:05,862 --> 02:12:10,400 APPROXIMATELY 83% OF THE FUNDING 3202 02:12:10,400 --> 02:12:12,202 TO THE INSTITUTE GOES TO THE 3203 02:12:12,202 --> 02:12:13,670 EXTRAMURAL RESEARCH COMMUNITY. 3204 02:12:13,670 --> 02:12:18,675 THAT'S WHERE WE ARE REALLY 3205 02:12:18,675 --> 02:12:21,011 CHARGE WITH ENSURING THE WORK 3206 02:12:21,011 --> 02:12:25,549 SUPPORTED IS OF HIGH QUALITY AND 3207 02:12:25,549 --> 02:12:26,182 CONTRIBUTING TO OUR 3208 02:12:26,182 --> 02:12:26,783 UNDERSTANDING OF DISEASE AND 3209 02:12:26,783 --> 02:12:31,521 PATIENT CARE. 3210 02:12:31,521 --> 02:12:33,890 SO TO GIVE YOU AN IDEA OF WHAT 3211 02:12:33,890 --> 02:12:38,929 THE MAKEUP OF THE INSTITUTE IS, 3212 02:12:38,929 --> 02:12:39,663 I AM THE DIRECTOR OF THE IS 3213 02:12:39,663 --> 02:12:48,138 THERE A POINTER? 3214 02:12:48,138 --> 02:12:53,009 I AM THE DIRECTOR OF THE 3215 02:12:53,009 --> 02:12:53,677 EXTRAMURAL RESEARCH PROGRAM AND 3216 02:12:53,677 --> 02:12:57,213 THE AND THE ENTIRE EXTRAMURAL 3217 02:12:57,213 --> 02:13:00,250 RESEARCH IS MADE UP OF TWO 3218 02:13:00,250 --> 02:13:00,617 DIVISIONS. 3219 02:13:00,617 --> 02:13:02,385 ONE IS THE EXTRAMURAL RESEARCH 3220 02:13:02,385 --> 02:13:05,088 GROUP I LEAD AND THE OTHER ONE 3221 02:13:05,088 --> 02:13:06,790 IS THE EXTRAMURAL ACTIVITIES. 3222 02:13:06,790 --> 02:13:11,628 THESE ARE REALLY BOTH CRITICAL 3223 02:13:11,628 --> 02:13:14,364 COMPONENTS TO ENSURING NOT ONLY 3224 02:13:14,364 --> 02:13:17,767 THE SCIENTIFIC QUALITY OF THE 3225 02:13:17,767 --> 02:13:19,903 RESEARCH IS CARRIED OUT BUT IN 3226 02:13:19,903 --> 02:13:21,638 THE EXTRAMURAL ACTIVITIES THE 3227 02:13:21,638 --> 02:13:23,940 MANAGEMENT OF CLINICAL TRIALS, 3228 02:13:23,940 --> 02:13:26,509 THE MANAGEMENT OF THE GRANT 3229 02:13:26,509 --> 02:13:27,611 FINANCIAL ASPECTS AND THE 3230 02:13:27,611 --> 02:13:30,447 SCIENTIFIC REVIEW BRANCH ARE 3231 02:13:30,447 --> 02:13:34,784 REALLY CRITICAL COMPONENTS TO 3232 02:13:34,784 --> 02:13:35,685 ENSURE WHAT'S HAPPENING ON THE 3233 02:13:35,685 --> 02:13:36,753 OTHER SIDE IS CARRIED OUT 3234 02:13:36,753 --> 02:13:46,062 APPROPRIATELY. 3235 02:13:46,062 --> 02:13:47,631 WHAT THE RESPONSIBILITY OF 3236 02:13:47,631 --> 02:13:48,031 PROGRAM? 3237 02:13:48,031 --> 02:13:52,702 I OVERSEE THE PROGRAM S WHO WORK 3238 02:13:52,702 --> 02:13:57,173 IN PARTICULAR SCIENTIFIC AREAS. 3239 02:13:57,173 --> 02:13:59,609 THESE SCIENTIFIC AREAS ARE 3240 02:13:59,609 --> 02:14:01,244 CLINICALLY OR BASIC SCIENCE 3241 02:14:01,244 --> 02:14:02,479 ORIENTED AND SOME PROBABLY A 3242 02:14:02,479 --> 02:14:04,881 LITTLE BIT OF BOTH AND ALL OF 3243 02:14:04,881 --> 02:14:06,182 THEM SEEM TO HAVE A LITTLE BIT 3244 02:14:06,182 --> 02:14:07,884 OF A TRANSLATIONAL COMPONENT. 3245 02:14:07,884 --> 02:14:11,121 EVEN IF A PROGRAM DIRECTOR IS 3246 02:14:11,121 --> 02:14:12,288 MANAGING A BASIC SCIENCE 3247 02:14:12,288 --> 02:14:13,590 COMPONENT, THERE'S GOING TO BE 3248 02:14:13,590 --> 02:14:18,962 THOUGHT ABOUT HOW THIS COULD 3249 02:14:18,962 --> 02:14:22,799 IMPACT DISEASE THE DISCOVERIES 3250 02:14:22,799 --> 02:14:24,868 IN THE BASIS OF DISEASE AND 3251 02:14:24,868 --> 02:14:25,435 HEALTH. 3252 02:14:25,435 --> 02:14:27,070 THE RESPONSIBILITY OF THE 3253 02:14:27,070 --> 02:14:27,737 PROGRAM DIRECTORS INVOLVE 3254 02:14:27,737 --> 02:14:30,507 SEVERAL ASPECTS. 3255 02:14:30,507 --> 02:14:31,841 THEY PROVIDE TECHNICAL 3256 02:14:31,841 --> 02:14:35,078 ASSISTANCE TO THE APPLICANTS. 3257 02:14:35,078 --> 02:14:37,547 THEY OVERSEE WHATEVER COMES TO 3258 02:14:37,547 --> 02:14:42,819 US IS APPROPRIATELY ASSIGNED TO 3259 02:14:42,819 --> 02:14:44,754 THE NIAMS. 3260 02:14:44,754 --> 02:14:46,389 WE HAVE 27 INSTITUTES AND 3261 02:14:46,389 --> 02:14:51,061 CENTERS AT NIH AND THERE'S A LOT 3262 02:14:51,061 --> 02:14:51,594 OF OVERLAP BETWEEN THESE. 3263 02:14:51,594 --> 02:14:53,163 WORK WITH THE OTHER PROGRAM 3264 02:14:53,163 --> 02:14:53,897 DIRECTORS AT OTHER INSTITUTES 3265 02:14:53,897 --> 02:15:00,036 AND CENTERS AND ENSURE OUR 3266 02:15:00,036 --> 02:15:01,705 ASSIGNMENTS ARE APPROPRIATELY 3267 02:15:01,705 --> 02:15:03,073 MADE AND THEY ALSO OBSERVE THE 3268 02:15:03,073 --> 02:15:05,408 SCIENTIFIC REVIEW PROCESS THAT 3269 02:15:05,408 --> 02:15:07,544 EVERY APPLICATION COMES IN IS 3270 02:15:07,544 --> 02:15:10,880 ACCEPTED AND UNDER GOES A 3271 02:15:10,880 --> 02:15:13,416 RIGOROUS SCIENTIFIC PEER REVIEW 3272 02:15:13,416 --> 02:15:13,650 PROCESS. 3273 02:15:13,650 --> 02:15:14,884 THEY MANAGE ANY QUESTIONS THAT 3274 02:15:14,884 --> 02:15:21,524 COME UP FROM THE APPLICANTS AND 3275 02:15:21,524 --> 02:15:24,427 ALSO PREPARE FUNDING 3276 02:15:24,427 --> 02:15:25,061 RECOMMENDATIONS BASED ON THE 3277 02:15:25,061 --> 02:15:26,262 QUALITY OF THE APPLICATIONS FROM 3278 02:15:26,262 --> 02:15:29,933 THE PEER REVIEW PROCESS. 3279 02:15:29,933 --> 02:15:31,801 ONCE FUNDING IS DONE AND THE 3280 02:15:31,801 --> 02:15:33,503 APPLICANTS RECEIVE FUNDS TO 3281 02:15:33,503 --> 02:15:37,240 CARRY OUT THE RESEARCH THEY 3282 02:15:37,240 --> 02:15:39,242 PROPOSED, THE PROGRAM DIRECTORS' 3283 02:15:39,242 --> 02:15:43,079 JOBS INCLUDE MANAGING ANY ISSUES 3284 02:15:43,079 --> 02:15:45,115 THE APPLICANTS RUN INTO WITH 3285 02:15:45,115 --> 02:15:46,549 REGARDS TO MAKING CHANGES IN THE 3286 02:15:46,549 --> 02:15:48,151 SCIENCE THAT MAYBE GO FROM ONE 3287 02:15:48,151 --> 02:15:52,956 MODEL TO ANOTHER BECAUSE THE 3288 02:15:52,956 --> 02:15:56,326 FIRST ONE DIDN'T WORK OR AND 3289 02:15:56,326 --> 02:15:57,427 THEY MONITOR THE PROGRESS PER 3290 02:15:57,427 --> 02:16:02,499 YEAR BECAUSE OUR FUNDING IN MOST 3291 02:16:02,499 --> 02:16:05,135 CASES IS YEARLY ONE OR TWO, FIVE 3292 02:16:05,135 --> 02:16:05,368 YEARS. 3293 02:16:05,368 --> 02:16:08,705 THOSE TYPES OF INTERVALS BUT 3294 02:16:08,705 --> 02:16:11,074 EVERY YEAR YOUR PROGRESS AS AN 3295 02:16:11,074 --> 02:16:12,642 APPLICANT RECEIVING FUNDS IS 3296 02:16:12,642 --> 02:16:13,143 REVIEWED BY THE PROGRAM 3297 02:16:13,143 --> 02:16:19,048 DIRECTORS. 3298 02:16:19,048 --> 02:16:21,985 POST FUNDING THEY WOULD BE 3299 02:16:21,985 --> 02:16:22,952 LOOKING AT THIS PROGRESS BUT 3300 02:16:22,952 --> 02:16:25,722 THEY ALSO GO TO MEETINGS AND 3301 02:16:25,722 --> 02:16:29,392 LOOK FOR PRESENTATIONS FROM THE 3302 02:16:29,392 --> 02:16:30,527 APPLICANTS AND EVALUATE HOW THE 3303 02:16:30,527 --> 02:16:34,764 SCIENCE THAT WE HAVE BEEN 3304 02:16:34,764 --> 02:16:35,832 FUNDING AS AN INSTITUTE FITS 3305 02:16:35,832 --> 02:16:37,667 INTO THE BIGGER PICTURE OF 3306 02:16:37,667 --> 02:16:43,072 WHAT'S BEING DONE IN THE OVER 3307 02:16:43,072 --> 02:16:44,107 ALL BOTH U.S. AND INTERNATIONAL 3308 02:16:44,107 --> 02:16:53,249 SCIENTIFIC AREAS. 3309 02:16:53,249 --> 02:16:54,450 HERE'S OTHER THINGS PROGRAM 3310 02:16:54,450 --> 02:16:55,151 DIRECTORS DO AND WHY IT'S 3311 02:16:55,151 --> 02:16:56,519 IMPORTANT FOR TO YOU MEET WITH 3312 02:16:56,519 --> 02:16:57,020 THEM TODAY. 3313 02:16:57,020 --> 02:16:59,055 THEY'RE THE PUBLIC FACE OF THE 3314 02:16:59,055 --> 02:16:59,355 GOVERNMENT. 3315 02:16:59,355 --> 02:17:01,090 THEY ATTEND SCIENTIFIC MEETINGS 3316 02:17:01,090 --> 02:17:05,428 AS I JUST MENTIONED AND ALSO 3317 02:17:05,428 --> 02:17:07,096 INTERACT WITH PUBLIC AND 3318 02:17:07,096 --> 02:17:09,199 VOLUNTARY ORGANIZATIONS SUCH AS 3319 02:17:09,199 --> 02:17:11,067 THE COALITION AND ARE VERY 3320 02:17:11,067 --> 02:17:13,203 IMPORTANT SOURCES OF INFORMATION 3321 02:17:13,203 --> 02:17:14,771 FOR PEOPLE LIKE YOU IF YOU'RE 3322 02:17:14,771 --> 02:17:15,705 CURIOUS ABOUT WHAT THE STATE OF 3323 02:17:15,705 --> 02:17:18,208 SCIENCE IS. 3324 02:17:18,208 --> 02:17:19,175 THEY CAN HELP YOU UNDERSTAND 3325 02:17:19,175 --> 02:17:21,511 WHERE THE NEEDS AND 3326 02:17:21,511 --> 02:17:22,545 OPPORTUNITIES ARE. 3327 02:17:22,545 --> 02:17:23,046 . 3328 02:17:23,046 --> 02:17:27,517 THEY FOLLOW THE BIOMEDICAL 3329 02:17:27,517 --> 02:17:31,054 DEVELOPMENTS AND ADVANCES AND 3330 02:17:31,054 --> 02:17:31,888 PROVIDE ADVANCES BASED ON WHAT 3331 02:17:31,888 --> 02:17:35,158 RESEARCH IS PUBLISHED ON A 3332 02:17:35,158 --> 02:17:36,960 TRI-YEARLY BASIS SO THE 3333 02:17:36,960 --> 02:17:38,294 INSTITUTE SO WE'RE UP TO DATE 3334 02:17:38,294 --> 02:17:44,167 WITH WHAT THE ACTIVITY IN EACH 3335 02:17:44,167 --> 02:17:48,371 INDIVIDUAL AREA OF RESEARCH. 3336 02:17:48,371 --> 02:17:53,243 THEY INITIATE SPECIFIC PROJECTS 3337 02:17:53,243 --> 02:17:54,777 AND INITIATING. 3338 02:17:54,777 --> 02:17:56,079 THEY DO THAT AND THESE 3339 02:17:56,079 --> 02:17:58,014 INITIATIVES ARE CONSIDERED BY 3340 02:17:58,014 --> 02:18:00,216 THE ENTIRE LEADERSHIP AND 3341 02:18:00,216 --> 02:18:04,087 PROGRAM DIRECTORS STAFF OF THE 3342 02:18:04,087 --> 02:18:06,923 INSTITUTE AND APPROVED FOR SENT 3343 02:18:06,923 --> 02:18:08,391 BACK FOR MORE WORK BASED ON THE 3344 02:18:08,391 --> 02:18:11,027 NEED AND THE CAPABILITIES TO 3345 02:18:11,027 --> 02:18:13,529 BRING IN SCIENCE AND IN THAT 3346 02:18:13,529 --> 02:18:14,964 PARTICULAR AREA. 3347 02:18:14,964 --> 02:18:21,471 THEY ALSO SERVE ON TRANS-NIH 3348 02:18:21,471 --> 02:18:21,771 COMMITTEES. 3349 02:18:21,771 --> 02:18:23,606 ONE OF THE THINGS WE HEARD IS 3350 02:18:23,606 --> 02:18:25,174 THERE'S LOTS OF INSTITUTES AND 3351 02:18:25,174 --> 02:18:26,342 CENTERS AND THEY'RE ALL DOING 3352 02:18:26,342 --> 02:18:27,243 REALLY EXCITING RESEARCH. 3353 02:18:27,243 --> 02:18:30,546 IN SOME CASES LIKE DR. CRISWELL 3354 02:18:30,546 --> 02:18:33,516 MENTIONED THE HE'LL INITIATIVE 3355 02:18:33,516 --> 02:18:37,186 OR THE AMP, THESE ARE MULTI-I.C. 3356 02:18:37,186 --> 02:18:38,154 INITIATIVES. 3357 02:18:38,154 --> 02:18:41,190 WORKING WITH YOUR COLLEAGUES AS 3358 02:18:41,190 --> 02:18:42,292 AN NIH EMPLOYEE IS VERY 3359 02:18:42,292 --> 02:18:43,059 IMPORTANT AND HELPFUL TO THE 3360 02:18:43,059 --> 02:18:48,598 INSTITUTE. 3361 02:18:48,598 --> 02:18:53,903 WE WORK WITH NEW INVESTIGATORS 3362 02:18:53,903 --> 02:18:57,173 AND WITH BRINGING IN MINORITY 3363 02:18:57,173 --> 02:18:59,909 INVESTIGATORS AND HELPING THEM 3364 02:18:59,909 --> 02:19:04,881 MENTORING THEM THROUGH PROVIDING 3365 02:19:04,881 --> 02:19:06,649 RESOURCES THAT WE'RE CAPABLE OF 3366 02:19:06,649 --> 02:19:08,818 DOING NOT FINANCIAL BUT OTHER 3367 02:19:08,818 --> 02:19:10,787 POINTING THEM IN THE PROPER 3368 02:19:10,787 --> 02:19:11,087 DIRECTIONS. 3369 02:19:11,087 --> 02:19:14,257 PART OF THIS IS ACCOMPLISHED 3370 02:19:14,257 --> 02:19:15,725 THROUGH OUR DIVERSITY SCHOLARS 3371 02:19:15,725 --> 02:19:18,227 PROGRAM FOR DIVERSITY 3372 02:19:18,227 --> 02:19:20,530 SUPPLEMENTS TO NIH GRANTS AND 3373 02:19:20,530 --> 02:19:22,765 OTHER THROUGH THE K FORUM WHERE 3374 02:19:22,765 --> 02:19:26,135 WE HAVE INVESTIGATORS WHO ARE 3375 02:19:26,135 --> 02:19:30,707 AWARDED CAREER DEVELOPMENT 3376 02:19:30,707 --> 02:19:32,642 AWARDS AND ARE BROUGHT TOGETHER 3377 02:19:32,642 --> 02:19:35,078 IN THE SECOND, THIRD OR FOURTH 3378 02:19:35,078 --> 02:19:38,948 YEAR OF THEIR AWARD AND MEET 3379 02:19:38,948 --> 02:19:43,086 WITH OTHERS AND SPEND TWO DAYS 3380 02:19:43,086 --> 02:19:45,555 WITH US AT THE INSTITUTE WITH 3381 02:19:45,555 --> 02:19:46,789 DR. CRISWELL AND DR. CARTER AND 3382 02:19:46,789 --> 02:19:50,293 ALL THE STAFF TO WORK WITH THEM 3383 02:19:50,293 --> 02:19:51,394 AND HELP THEM UNDERSTAND THE INS 3384 02:19:51,394 --> 02:19:57,433 AND OUTS OF NIH AND HELP THEM 3385 02:19:57,433 --> 02:20:01,604 GET MENTORING IF THEY'RE IN 3386 02:20:01,604 --> 02:20:01,804 NEED. 3387 02:20:01,804 --> 02:20:03,272 WE ALSO CONDUCT OUTREACH THROUGH 3388 02:20:03,272 --> 02:20:03,840 SCIENTIFIC CONFERENCES AND 3389 02:20:03,840 --> 02:20:07,310 WORKSHOPS. 3390 02:20:07,310 --> 02:20:08,811 QUE PROVIDE INPUT TO YOU AS YOU 3391 02:20:08,811 --> 02:20:17,987 WILL SEE TODAY WHEN WE MEET. 3392 02:20:17,987 --> 02:20:19,622 THIS IS SOME INSTRUCTION ON THE 3393 02:20:19,622 --> 02:20:21,758 BREAKOUT SESSIONS. 3394 02:20:21,758 --> 02:20:23,059 THE PROGRAM DIRECTORS DURING THE 3395 02:20:23,059 --> 02:20:24,460 SESSIONS WILL SHARE WITH YOU THE 3396 02:20:24,460 --> 02:20:29,699 BACKGROUND AND HIGHLIGHTS OF 3397 02:20:29,699 --> 02:20:31,100 THEIR SPECIFIC PORTFOLIOS. 3398 02:20:31,100 --> 02:20:33,603 THEY WILL TALK ABOUT OTHER 3399 02:20:33,603 --> 02:20:39,008 EXAMPLES WHERE MEMBERS OF THE 3400 02:20:39,008 --> 02:20:41,711 COALITION HAVE BEEN INVOLVED IN 3401 02:20:41,711 --> 02:20:43,546 AUGMENTING OR DIRECTING OR 3402 02:20:43,546 --> 02:20:45,815 HELPING US UNDERSTAND WHAT THE 3403 02:20:45,815 --> 02:20:47,050 NEEDS ARE FOR THE PARTICULAR 3404 02:20:47,050 --> 02:20:51,054 DISEASE AND PATIENT GROUP THAT 3405 02:20:51,054 --> 02:20:51,487 THEY'RE ADDRESSING. 3406 02:20:51,487 --> 02:20:53,489 THE THINGS THAT WE HOPE TO GET 3407 02:20:53,489 --> 02:20:57,193 FROM THIS IS OR HELP YOU GET IS 3408 02:20:57,193 --> 02:20:59,062 HOW WE COULD LEVERAGE THE 3409 02:20:59,062 --> 02:21:00,897 RESPECTIVE RESOURCES TO ACHIEVE 3410 02:21:00,897 --> 02:21:01,731 OUR SHARED GOALS. 3411 02:21:01,731 --> 02:21:05,034 WE ALL ARE LOOKING TO GET THE 3412 02:21:05,034 --> 02:21:07,970 BEST SCIENCE FROM THESE 3413 02:21:07,970 --> 02:21:09,439 INVESTIGATORS THAT WILL ADDRESS 3414 02:21:09,439 --> 02:21:13,176 THE PATIENT NEEDS. 3415 02:21:13,176 --> 02:21:14,977 AND SOMETIMES WE'RE A LITTLE IN 3416 02:21:14,977 --> 02:21:15,745 PROGRAM AT NIH WE'RE A LITTLE 3417 02:21:15,745 --> 02:21:17,814 BIT ADRIFT FROM THAT. 3418 02:21:17,814 --> 02:21:21,284 SO YOUR CONNECTION HELPS US 3419 02:21:21,284 --> 02:21:23,052 CONNECT WITH WHAT THE ACTUAL 3420 02:21:23,052 --> 02:21:26,389 NEEDS OF THE PATIENTS AND THE 3421 02:21:26,389 --> 02:21:27,056 INDIVIDUALS AFFECTED BY THE 3422 02:21:27,056 --> 02:21:34,464 DISEASES ARE. 3423 02:21:34,464 --> 02:21:36,399 AND HOW YOU CAN MORE EFFECTIVELY 3424 02:21:36,399 --> 02:21:41,504 ENGAGE WITH THE PROGRAM 3425 02:21:41,504 --> 02:21:43,606 DIRECTORS AND HOW YOU MAY BE 3426 02:21:43,606 --> 02:21:44,273 ABLE TO SUPPORT AND ENGAGE WITH 3427 02:21:44,273 --> 02:21:49,579 INVESTIGATORS. 3428 02:21:49,579 --> 02:21:51,547 SOMETIMES THEY'RE ADRIFT OF WHAT 3429 02:21:51,547 --> 02:21:52,315 THE PATIENT VOICE IS AND WHAT 3430 02:21:52,315 --> 02:21:58,454 THE PATIENT NEEDS ARE. 3431 02:21:58,454 --> 02:22:00,356 AND IN CERTAIN CASES IT COULD BE 3432 02:22:00,356 --> 02:22:02,492 HELPFUL TO MEET WITH ADVOCACY 3433 02:22:02,492 --> 02:22:05,595 GROUPS AND UNDERSTAND WHERE THE 3434 02:22:05,595 --> 02:22:07,063 DISCONNECT IS AND HOW THEY MIGHT 3435 02:22:07,063 --> 02:22:07,897 BETTER TARGET THEIR RESEARCH TO 3436 02:22:07,897 --> 02:22:10,766 BENEFIT THE PATIENTS. 3437 02:22:10,766 --> 02:22:12,568 AND THEN ALSO AWARENESS. 3438 02:22:12,568 --> 02:22:13,703 THAT'S A REALLY BIG FACTOR. 3439 02:22:13,703 --> 02:22:18,074 BECAUSE NOT ONLY DO WE NEED THE 3440 02:22:18,074 --> 02:22:21,144 COALITION TO HELP MAKE THE 3441 02:22:21,144 --> 02:22:23,412 PUBLIC AWARE OF WHAT NIAMS IS 3442 02:22:23,412 --> 02:22:26,949 DOING WE NEED TO HELP MAKE THEM 3443 02:22:26,949 --> 02:22:28,584 WEAR OF WHAT THE ISSUES ARE WITH 3444 02:22:28,584 --> 02:22:33,389 THE DISEASES THAT WE ARE 3445 02:22:33,389 --> 02:22:34,957 ADDRESSING IN OUR INSTITUTE. 3446 02:22:34,957 --> 02:22:39,061 AWARENESS OF THE DISEASES AND 3447 02:22:39,061 --> 02:22:40,263 DISORDERS -- SOMEONE THIS 3448 02:22:40,263 --> 02:22:44,233 MORNING ALREADY SAID THESE ARE 3449 02:22:44,233 --> 02:22:47,136 NOT DISEASES THAT WILL CAUSE 3450 02:22:47,136 --> 02:22:48,037 IMMEDIATE DEATH BUT CAUSE 3451 02:22:48,037 --> 02:22:50,907 LONG-TERM DISABILITY AND QUALITY 3452 02:22:50,907 --> 02:22:53,042 OF LIFE IS QUITE SIGNIFICANTLY 3453 02:22:53,042 --> 02:22:57,380 DEGRADED WITH MANY OF THE 3454 02:22:57,380 --> 02:22:59,048 DISEASES THAT ARE COVERED IN 3455 02:22:59,048 --> 02:23:05,154 NIAMS MISSION. 3456 02:23:05,154 --> 02:23:07,590 WE ENCOURAGE YOU TO ACTIVELY 3457 02:23:07,590 --> 02:23:09,892 PARTICIPATE BECAUSE I KNOW FROM 3458 02:23:09,892 --> 02:23:12,094 TALKING TO YOU HERE THAT YOU ARE 3459 02:23:12,094 --> 02:23:15,531 STRONG ADVOCATES AND YOU ARE NOT 3460 02:23:15,531 --> 02:23:17,867 SHY ABOUT ASKING QUESTIONS AND 3461 02:23:17,867 --> 02:23:19,502 EVEN SOME HARD QUESTIONS. 3462 02:23:19,502 --> 02:23:21,837 PLEASE FEEL FREE TO DO THAT. 3463 02:23:21,837 --> 02:23:24,974 THESE ARE A FEW RESOURCES WHICH 3464 02:23:24,974 --> 02:23:26,742 I THINK YOU HAVE PROBABLY BEEN 3465 02:23:26,742 --> 02:23:28,244 MADE FAMILIAR WITH BUT THE 3466 02:23:28,244 --> 02:23:30,313 SLIDES I THINK ARE GOING TO BE 3467 02:23:30,313 --> 02:23:30,813 AVAILABLE TO YOU. 3468 02:23:30,813 --> 02:23:33,416 HOW YOU CAN GET MORE INFORMATION 3469 02:23:33,416 --> 02:23:36,819 ABOUT WHAT NIAMS IS SUPPORTING 3470 02:23:36,819 --> 02:23:40,690 ABOUT WHAT IS GOING ON IN THE 3471 02:23:40,690 --> 02:23:41,123 EXTRAMURAL PROGRAM. 3472 02:23:41,123 --> 02:23:44,560 WE DEFINITELY HAVE WORKSHOPS AND 3473 02:23:44,560 --> 02:23:47,196 EVENT GOING ON AND BEING IN 3474 02:23:47,196 --> 02:23:50,967 TOUCH BEING ON OUR MAILING LIST 3475 02:23:50,967 --> 02:23:52,535 CAN BE VERY HELPFUL TO YOU. 3476 02:23:52,535 --> 02:23:56,672 AND FINALLY TO TRANSITION, WE 3477 02:23:56,672 --> 02:24:00,910 HAVE THESE BREAKOUT GROUPS AND 3478 02:24:00,910 --> 02:24:02,445 ANYBODY INTERESTED IN SYSTEMIC 3479 02:24:02,445 --> 02:24:03,846 RHEUMATIC DISEASES AND SKIN 3480 02:24:03,846 --> 02:24:06,182 DISEASES AREA WOULD GO TO ROOM 3481 02:24:06,182 --> 02:24:07,049 AB. 3482 02:24:07,049 --> 02:24:09,452 MUSCLE DISEASES AND BONE 3483 02:24:09,452 --> 02:24:13,789 DISEASES ROOM C1 AND C2 AND OA 3484 02:24:13,789 --> 02:24:17,059 AND ORTHOPEDIC DISORDERS, JOINT 3485 02:24:17,059 --> 02:24:20,096 DISEASES, G1 AND G2. 3486 02:24:20,096 --> 02:24:25,001 AND WE HAVE SOME WONDERFUL FOLKS 3487 02:24:25,001 --> 02:24:27,069 AVAILABLE. 3488 02:24:27,069 --> 02:24:31,440 DR. SABOTI AND MALL AND DR. CHEN 3489 02:24:31,440 --> 02:24:34,110 WILL BE COVERING ROOM C1 AND C 3490 02:24:34,110 --> 02:24:37,613 IT AND DR. TANG AND DR. LINDSEY 3491 02:24:37,613 --> 02:24:39,448 WILL BE DOING ROOM G1 AND G2. 3492 02:24:39,448 --> 02:24:41,183 I HOPE YOU'LL HAVE A REALLY 3493 02:24:41,183 --> 02:24:43,085 GREAT TIME WITH THIS AND LOOK 3494 02:24:43,085 --> 02:25:09,111 FORWARD TO HEARING FROM YOU. 3495 02:25:09,111 --> 02:25:11,213 NEXT SESSION I'M PLEASED TO 3496 02:25:11,213 --> 02:25:13,081 INTRODUCE THE NIAMS LEADER YOU 3497 02:25:13,081 --> 02:25:15,684 ALL KNOW THROUGH HIS LONG TIME 3498 02:25:15,684 --> 02:25:16,885 PARTNERSHIP WITH THE COALITION 3499 02:25:16,885 --> 02:25:18,487 EVIDENT WITH HIS SUPPORT AND 3500 02:25:18,487 --> 02:25:19,855 ENGAGEMENT DR. BOB CARTER. 3501 02:25:19,855 --> 02:25:22,257 DR. CARTER IS THE DEPUTY 3502 02:25:22,257 --> 02:25:24,459 DIRECTOR OF NIAMS A POSITION HE 3503 02:25:24,459 --> 02:25:26,762 HAS HELD SINCE 2008. 3504 02:25:26,762 --> 02:25:30,065 HE SERVED AS NIAMS' ACTING 3505 02:25:30,065 --> 02:25:34,236 DIRECTOR FROM DECEMBER 2018 TO 3506 02:25:34,236 --> 02:25:37,072 FEBRUARY 2022. 3507 02:25:37,072 --> 02:25:39,074 HE LEADS NUMEROUS NIAMS POLICY 3508 02:25:39,074 --> 02:25:40,041 INITIATIVES AND PROJECTS 3509 02:25:40,041 --> 02:25:41,643 INCLUDING THE NIAMS CENTERS 3510 02:25:41,643 --> 02:25:43,311 EVALUATION WORKING GROUP AND 3511 02:25:43,311 --> 02:25:45,781 CLINICAL TRIALS WORKING GROUP. 3512 02:25:45,781 --> 02:25:53,121 HE ALSO HELPED SPEARHEAD BACPAC 3513 02:25:53,121 --> 02:25:54,423 BOTH OF WHICH ARE PART OF THE 3514 02:25:54,423 --> 02:25:57,959 NIHs HELPING TO END ADDICTION 3515 02:25:57,959 --> 02:26:02,164 LONG-TERM OR HEAL INITIATIVE. 3516 02:26:02,164 --> 02:26:04,232 I CEDE THE FLOOR TO HIM TO 3517 02:26:04,232 --> 02:26:09,738 INTRODUCE THE NEXT SPEAKER. 3518 02:26:09,738 --> 02:26:11,473 >> LADIES AND GENTLEMEN, ISN'T 3519 02:26:11,473 --> 02:26:14,009 IT WONDERFUL TO ALL BE TOGETHER 3520 02:26:14,009 --> 02:26:14,209 AGAIN. 3521 02:26:14,209 --> 02:26:17,512 SINCE 2019 IT'S BEEN A LONG 3522 02:26:17,512 --> 02:26:17,712 PATH. 3523 02:26:17,712 --> 02:26:19,114 GREAT TO BE HERE. 3524 02:26:19,114 --> 02:26:25,854 IT'S MY PLEASURE TO INTRODUCE 3525 02:26:25,854 --> 02:26:28,223 OUR SPEAKER AND SHE'S HAVING AN 3526 02:26:28,223 --> 02:26:30,525 ISSUE WITH MUSCULOSKELETAL BUT 3527 02:26:30,525 --> 02:26:31,760 JOINING US VIRTUALLY BUT 3528 02:26:31,760 --> 02:26:33,962 HOPEFULLY SOMETHING YOU'RE 3529 02:26:33,962 --> 02:26:36,198 INTERESTED IN. 3530 02:26:36,198 --> 02:26:39,100 SHE IS THE INAUGURAL DIRECTOR OF 3531 02:26:39,100 --> 02:26:42,070 THE ADVANCED RESEARCH PROJECT 3532 02:26:42,070 --> 02:26:44,206 AGENCY FOR HEALTH OR ARPA-H. 3533 02:26:44,206 --> 02:26:48,210 AND SHE COMES TO THIS FROM A 3534 02:26:48,210 --> 02:26:50,111 BACKGROUND RELEVANT BUT WORKED 3535 02:26:50,111 --> 02:26:53,381 IN TWO OTHER RELATED AGENCIES 3536 02:26:53,381 --> 02:26:56,852 DEFENSE ADVANCE RESEARCH PROGRAM 3537 02:26:56,852 --> 02:27:01,122 AGENCY OR DARPA AS WELL AS THE 3538 02:27:01,122 --> 02:27:03,458 INTELLIGENCE RESEARCH PROJECT 3539 02:27:03,458 --> 02:27:06,595 ACTIVITY. 3540 02:27:06,595 --> 02:27:07,128 I-ARPA. 3541 02:27:07,128 --> 02:27:09,664 WAS AWARDED THE SUPERIOR PUBLIC 3542 02:27:09,664 --> 02:27:11,933 SERVICE MEDAL FOR SERVICE IN 3543 02:27:11,933 --> 02:27:12,767 THOSE AREAS. 3544 02:27:12,767 --> 02:27:17,439 SHE'S ALSO WORKED ON THE PRIVATE 3545 02:27:17,439 --> 02:27:20,809 SECTOR SIDE. 3546 02:27:20,809 --> 02:27:23,645 SHE ALSO WORKED AT THE COMPANY 3547 02:27:23,645 --> 02:27:27,516 OF GINKO BIO WORKS WHERE SHE HAD 3548 02:27:27,516 --> 02:27:30,819 POSITIONS BOTH AS AN INNOVATION 3549 02:27:30,819 --> 02:27:31,753 OFFICER AND BUSINESS 3550 02:27:31,753 --> 02:27:32,787 DEVELOPMENT. 3551 02:27:32,787 --> 02:27:36,224 BRIDGING BOTH ASPECTS IN. 3552 02:27:36,224 --> 02:27:41,096 A WONDERFUL COMBINATION. 3553 02:27:41,096 --> 02:27:44,065 WHAT SHE'S EXCITE ABOUT IS THE 3554 02:27:44,065 --> 02:27:50,472 FIRST OF THE ARPA-H PROGRAMS, 3555 02:27:50,472 --> 02:27:53,775 NITRO IS ARTHROARTHRITIS. 3556 02:27:53,775 --> 02:27:57,212 THE TASK FOR ARPA-H IS TO 3557 02:27:57,212 --> 02:27:59,047 IDENTIFY A CLINICAL NEED THEN 3558 02:27:59,047 --> 02:28:06,087 FOCUS ON WHERE A TOP-DOWN 3559 02:28:06,087 --> 02:28:08,056 DIRECTED INVESTMENT AND MOVING 3560 02:28:08,056 --> 02:28:11,927 ON AND CAN SOLVE A PROBLEM THAT 3561 02:28:11,927 --> 02:28:13,295 WOULD BE VERY DIFFICULT THROUGH 3562 02:28:13,295 --> 02:28:15,063 THE NIH PROCESS. 3563 02:28:15,063 --> 02:28:17,198 I THINK KNEE OSTEOARTHRITIS IS 3564 02:28:17,198 --> 02:28:21,269 UP THERE AS THE PERFECT MODEL TO 3565 02:28:21,269 --> 02:28:23,271 TAKE THE RISK, FAIL SOMETIMES 3566 02:28:23,271 --> 02:28:25,006 BUT GET A NEW SOLUTION TO A 3567 02:28:25,006 --> 02:28:26,841 PROBLEM THAT'S BEEN A LONG AND 3568 02:28:26,841 --> 02:28:28,577 HAS A HIGH PUBLIC IMPACT. 3569 02:28:28,577 --> 02:28:30,412 IT'S QUITE DIFFERENT FROM THE 3570 02:28:30,412 --> 02:28:32,280 NIH APPROACH WHERE WE GIVE AN 3571 02:28:32,280 --> 02:28:34,316 AWARD TO SOMEBODY AND IT'S QUITE 3572 02:28:34,316 --> 02:28:35,750 A BIT OF MONEY BUT BASICALLY 3573 02:28:35,750 --> 02:28:37,719 THROW THE MONEY OVER THE WALL TO 3574 02:28:37,719 --> 02:28:38,887 THE INSTITUTE WHERE THEY WORK 3575 02:28:38,887 --> 02:28:40,188 AND TELL THEM TO RECOMPETE IN 3576 02:28:40,188 --> 02:28:43,158 FIVE YEARS. 3577 02:28:43,158 --> 02:28:43,692 A DIFFERENT WAY OF DOING 3578 02:28:43,692 --> 02:28:46,261 BUSINESS. 3579 02:28:46,261 --> 02:28:54,269 I SERVED AS THE CONTACT BETWEEN 3580 02:28:54,269 --> 02:28:55,170 ARPA-H AND NIH AND THINGS ARE 3581 02:28:55,170 --> 02:29:05,480 DONE DIFFERENTLY. 3582 02:29:06,948 --> 02:29:08,249 AND IT ILLUSTRATES A DIFFERENT 3583 02:29:08,249 --> 02:29:09,818 WAY OF DOING BUSINESS OF NOT 3584 02:29:09,818 --> 02:29:12,253 THINKING ABOUT THE RULES, NOT 3585 02:29:12,253 --> 02:29:15,056 THINKING ABOUT HOW WE SUPPORT A 3586 02:29:15,056 --> 02:29:17,559 COMMUNITY BUT SOLVING A PROBLEM. 3587 02:29:17,559 --> 02:29:19,694 SO IT'S REAL EXCITING FOR ME TO 3588 02:29:19,694 --> 02:29:22,030 SEE IF THIS NEW APPROACH CAN 3589 02:29:22,030 --> 02:29:22,998 MAKE A DIFFERENCE IN 3590 02:29:22,998 --> 02:29:25,166 OSTEOARTHRITIS WHICH IS SUCH AN 3591 02:29:25,166 --> 02:29:27,268 UNMET NEED AND JUST WONDERFUL 3592 02:29:27,268 --> 02:29:27,569 OPPORTUNITY. 3593 02:29:27,569 --> 02:29:31,172 SO WITH THAT, DR. WEGGERSON. 3594 02:29:31,172 --> 02:29:34,409 THANK YOU. 3595 02:29:34,409 --> 02:29:36,244 >> I'M SORRY I COULDN'T BE THERE 3596 02:29:36,244 --> 02:29:37,178 TODAY. 3597 02:29:37,178 --> 02:29:39,681 I'M DISAPPOINTED NOT TO MAKE IT 3598 02:29:39,681 --> 02:29:42,050 BUT IN THE ULTIMATE IRONY 3599 02:29:42,050 --> 02:29:43,685 SUFFERING A HERNIATED DISK AND 3600 02:29:43,685 --> 02:29:45,520 I'M HAPPY TO SHARE THE MISSION 3601 02:29:45,520 --> 02:29:46,488 AND HOPEFULLY BE ABLE TO CONNECT 3602 02:29:46,488 --> 02:29:51,126 WITH YOU ALL SOON. 3603 02:29:51,126 --> 02:29:53,328 LET ME SHARE MY SCREEN FOR THIS 3604 02:29:53,328 --> 02:29:53,662 PRESENTATION. 3605 02:29:53,662 --> 02:29:55,263 CAN EVERYBODY SEE? 3606 02:29:55,263 --> 02:30:04,239 THUMBS UP? 3607 02:30:04,239 --> 02:30:07,142 YOU LED IN WELL TO WHAT ARPA-H 3608 02:30:07,142 --> 02:30:08,910 IS HERE TO DO AND I'LL SPEND 3609 02:30:08,910 --> 02:30:13,948 TIME ON WHAT IS THE ARPA 3610 02:30:13,948 --> 02:30:17,452 BUSINESS MODEL AND WHAT IS THE 3611 02:30:17,452 --> 02:30:19,621 FIRST PROGRAM IN THE 3612 02:30:19,621 --> 02:30:19,988 OSTEOARTHRITIS. 3613 02:30:19,988 --> 02:30:20,955 I'LL WALK YOU THROUGH THE 3614 02:30:20,955 --> 02:30:21,189 JOURNEY. 3615 02:30:21,189 --> 02:30:23,925 IT STARTED IN MARCH OF 2022 WHEN 3616 02:30:23,925 --> 02:30:25,994 PRESIDENT BIDEN CALLED ON 3617 02:30:25,994 --> 02:30:28,530 CONGRESS TO BRING THE INITIAL 3618 02:30:28,530 --> 02:30:30,699 APPROPRIATION FOR ARPA-H 3619 02:30:30,699 --> 02:30:30,932 FORWARD. 3620 02:30:30,932 --> 02:30:33,168 CREATING IN THE SPIRIT OF THE 3621 02:30:33,168 --> 02:30:34,769 BUSINESS MODEL OF DARPA TO 3622 02:30:34,769 --> 02:30:36,104 PURSUE AGENCY TO BRING THE MODEL 3623 02:30:36,104 --> 02:30:37,772 IN HOW WE SUPPORT RESEARCH AND 3624 02:30:37,772 --> 02:30:38,673 IN THE INTRODUCTION YOU HEARD A 3625 02:30:38,673 --> 02:30:40,008 LITTLE BIT ABOUT HOW WE WANT TO 3626 02:30:40,008 --> 02:30:41,676 DO THAT. 3627 02:30:41,676 --> 02:30:45,380 IT'S A PLACE WHERE WE TAKE ON 3628 02:30:45,380 --> 02:30:46,981 THE BIG AUDACIOUS BETS AND NOT 3629 02:30:46,981 --> 02:30:49,184 ALL ARE GOING TO BE SUCCESSFUL 3630 02:30:49,184 --> 02:30:54,823 BUT SOME OF THEM WILL BE AND WE 3631 02:30:54,823 --> 02:30:56,157 WANT TO BE ABLE TO HAVE A PLACE 3632 02:30:56,157 --> 02:30:58,326 TO LAUNCH THE PROJECTS IN A BIG 3633 02:30:58,326 --> 02:30:58,793 WAY. 3634 02:30:58,793 --> 02:31:01,229 WE'VE BEEN VERY LUCKY TO BE 3635 02:31:01,229 --> 02:31:02,731 LAUNCHED AS A PRESIDENTIAL 3636 02:31:02,731 --> 02:31:04,165 INITIATIVE AND RECEIVE THE FULL 3637 02:31:04,165 --> 02:31:05,500 SUPPORT OF THE ADMINISTRATION 3638 02:31:05,500 --> 02:31:07,168 BUT ALSO THE CONGRESS IN 3639 02:31:07,168 --> 02:31:08,203 LAUNCHING ARPA-H FOR THE PROMISE 3640 02:31:08,203 --> 02:31:11,706 OF WHAT THIS MODEL COULD BE. 3641 02:31:11,706 --> 02:31:15,143 SO OUR MISSION WHEN I WALKED IN 3642 02:31:15,143 --> 02:31:16,911 THE DOOR I'LL SAY NOTHING 3643 02:31:16,911 --> 02:31:17,479 EXISTED. 3644 02:31:17,479 --> 02:31:19,681 WE STARTED AT FIRST PRINCIPLES, 3645 02:31:19,681 --> 02:31:21,449 WHAT'S THE MISSION OF ARPA-H? 3646 02:31:21,449 --> 02:31:23,418 WE PLANTED ON THIS MISSION TO 3647 02:31:23,418 --> 02:31:23,952 ACCELERATE BETTER HEALTH 3648 02:31:23,952 --> 02:31:30,859 OUTCOMES FOR EVERYONE. 3649 02:31:30,859 --> 02:31:35,897 AND I WANT TO EMPHASIZE THAT 3650 02:31:35,897 --> 02:31:37,999 WITH THE FOCUS ON PROBLEMS FOR 3651 02:31:37,999 --> 02:31:39,934 SOLVING WE CAN ACCELERATE THE 3652 02:31:39,934 --> 02:31:41,436 TIME LINES TO BRING THE 3653 02:31:41,436 --> 02:31:42,737 SOLUTIONS FORWARD IN THE REAL 3654 02:31:42,737 --> 02:31:42,937 WORLD. 3655 02:31:42,937 --> 02:31:44,072 WE MEASURE OUR PROGRESS BY 3656 02:31:44,072 --> 02:31:45,140 BETTER HEALTH OUTCOMES. 3657 02:31:45,140 --> 02:31:47,108 SO IT'S NOT ACADEMIC 3658 02:31:47,108 --> 02:31:49,043 PUBLICATIONS, IT'S NOT FINANCIAL 3659 02:31:49,043 --> 02:31:51,513 RETURN ON INVESTMENT, IT'S 3660 02:31:51,513 --> 02:31:53,248 IMPROVING THE LIVES FOR EVERYONE 3661 02:31:53,248 --> 02:31:54,449 REALLY ALL AMERICANS. 3662 02:31:54,449 --> 02:31:56,217 WE WANT TO BE ABLE TO REACH 3663 02:31:56,217 --> 02:32:03,491 UNDER SERVED POPULATIONS OF 3664 02:32:03,491 --> 02:32:05,059 RURAL/URBAN COMMUNITIES FROM THE 3665 02:32:05,059 --> 02:32:05,326 BEGINNING. 3666 02:32:05,326 --> 02:32:07,195 A BRIEF TIME FROM THE INITIAL 3667 02:32:07,195 --> 02:32:09,330 CALL FOR THE PRESIDENT TO FUND 3668 02:32:09,330 --> 02:32:12,400 ARPA-H TO TODAY, I WAS SWORN IN 3669 02:32:12,400 --> 02:32:14,269 ABOUT JUST UNDER A YEAR AGO AND 3670 02:32:14,269 --> 02:32:15,637 WE LAUNCHED AT HOWARD UNIVERSITY 3671 02:32:15,637 --> 02:32:16,371 AROUND THAT TIME. 3672 02:32:16,371 --> 02:32:19,174 AND VERY QUICKLY STARTED TO 3673 02:32:19,174 --> 02:32:20,875 BUILD THE BUSINESS OPERATIONS 3674 02:32:20,875 --> 02:32:24,212 TEAM TO BE READY TO TAKE OUR 3675 02:32:24,212 --> 02:32:25,580 FIRST SOLICITATIONS IN MARCH OF 3676 02:32:25,580 --> 02:32:26,548 THIS YEAR. 3677 02:32:26,548 --> 02:32:28,583 I LIKE TO CALL IT MINIMAL VIABLE 3678 02:32:28,583 --> 02:32:31,019 AGENCY STATUS WHERE SOME THINGS 3679 02:32:31,019 --> 02:32:33,087 YOU'RE FAMILIAR WITH LIKE THE 3680 02:32:33,087 --> 02:32:33,888 SOLICITATION PORTAL OUR 3681 02:32:33,888 --> 02:32:35,523 CONTRACTING TEAM ARE NOW IN 3682 02:32:35,523 --> 02:32:37,625 PLACE TO MOVE VERY QUICKLY. 3683 02:32:37,625 --> 02:32:38,660 SOON THEREAFTER FROM THAT 3684 02:32:38,660 --> 02:32:41,129 ANNOUNCEMENT WE ANNOUNCED OUR 3685 02:32:41,129 --> 02:32:43,198 FIRST PROGRAM OR NITRO OUR 3686 02:32:43,198 --> 02:32:45,066 PROGRAM IN OSTEOARTHRITIS I'LL 3687 02:32:45,066 --> 02:32:47,068 WALK YOU THROUGH IN A MOMENT HOW 3688 02:32:47,068 --> 02:32:48,203 WE GOT THERE. 3689 02:32:48,203 --> 02:32:49,838 AND JUST LAST WEEK WE ANNOUNCED 3690 02:32:49,838 --> 02:32:52,207 OUR FIRST AWARD THROUGH OUR OPEN 3691 02:32:52,207 --> 02:32:54,209 AGENCY ANNOUNCEMENT WHICH IS A 3692 02:32:54,209 --> 02:32:55,176 PLACE WHERE ANYBODY CAN SUBMIT 3693 02:32:55,176 --> 02:32:57,512 AN IDEA FROM THE OUTSIDE WORLD 3694 02:32:57,512 --> 02:32:59,747 AND FROM THAT MOMENT WE 3695 02:32:59,747 --> 02:33:00,849 ANNOUNCED THE SOLICITATION IN 3696 02:33:00,849 --> 02:33:03,418 MARCH TO LAST MONTH THAT'S FIVE 3697 02:33:03,418 --> 02:33:06,221 MONTHS FROM PROPOSAL REVIEW TO 3698 02:33:06,221 --> 02:33:09,290 TRACT NEGOTIATIONS TO GETTING 3699 02:33:09,290 --> 02:33:09,924 THAT FUNDED. 3700 02:33:09,924 --> 02:33:13,194 WE ANTICIPATE THAT'S THE SLOWEST 3701 02:33:13,194 --> 02:33:15,096 AWARD WE WILL EVER HAVE BECAUSE 3702 02:33:15,096 --> 02:33:16,931 WE'RE SORT OF BUILDING THE PLANE 3703 02:33:16,931 --> 02:33:18,766 WHILE WE'RE FLYING IT. 3704 02:33:18,766 --> 02:33:21,469 WE'RE REALLY MOTIVATED BY HAVING 3705 02:33:21,469 --> 02:33:23,805 THESE TYPE OF SOLICITATIONS AND 3706 02:33:23,805 --> 02:33:25,506 AWARDS TO ALLOW US TO MOVE 3707 02:33:25,506 --> 02:33:31,179 QUICKLY TO THE POINT IN THE 3708 02:33:31,179 --> 02:33:33,681 INTRODUCTION AS WELL WE WILL NOT 3709 02:33:33,681 --> 02:33:35,516 ISSUE GRANTS BUT CONTRACTS 3710 02:33:35,516 --> 02:33:37,385 GIVING ARPA-H A SEAT AT THE 3711 02:33:37,385 --> 02:33:38,586 ABLE. 3712 02:33:38,586 --> 02:33:41,556 WE'RE LASER FOCUSSED ON SOLVING 3713 02:33:41,556 --> 02:33:43,625 THE PROBLEMS AND OUR PROGRAM 3714 02:33:43,625 --> 02:33:45,693 MANAGERS ARE ON THE HOOK TO 3715 02:33:45,693 --> 02:33:47,128 SOLVE THEM AND THEY'LL BE 3716 02:33:47,128 --> 02:33:48,296 SITTING WITH YOU HELPING YOU GET 3717 02:33:48,296 --> 02:33:54,802 ACROSS THE FINISH LINE. 3718 02:33:54,802 --> 02:33:57,672 THE WAY WE CAN DO THAT IS THE 3719 02:33:57,672 --> 02:33:59,073 CONGRESS HAS STOOD US UP IN A 3720 02:33:59,073 --> 02:34:04,679 WAY TO MOVE QUICKLY, NIMBLY AND 3721 02:34:04,679 --> 02:34:06,014 DECISIVELY. 3722 02:34:06,014 --> 02:34:07,749 WE DON'T HAVE INTRAMURAL LABS 3723 02:34:07,749 --> 02:34:10,084 LIKE NIH WE JUST DELVE OUT THE 3724 02:34:10,084 --> 02:34:16,224 FUNDS AND WE'RE INDEPENDENT FROM 3725 02:34:16,224 --> 02:34:18,660 NIH. 3726 02:34:18,660 --> 02:34:21,596 WE'RE ESTABLISHED WITHIN NIH AND 3727 02:34:21,596 --> 02:34:24,232 WE CAN SHARE EXPERTISE AND GAPS 3728 02:34:24,232 --> 02:34:26,301 IN CHALLENGES BUT ULTIMATELY WE 3729 02:34:26,301 --> 02:34:30,805 CAN MOVE OUT INDEPENDENTLY ON 3730 02:34:30,805 --> 02:34:33,341 FUNDING WITH FEEDBACK FROM THE 3731 02:34:33,341 --> 02:34:35,476 TEAMS. 3732 02:34:35,476 --> 02:34:40,915 I REPORT DIRECTLY TO SECRETARY 3733 02:34:40,915 --> 02:34:45,520 BECERRA AND TO BE ABLE TO HAVE 3734 02:34:45,520 --> 02:34:46,988 OUR OWN PATH FORWARD WHERE WITH 3735 02:34:46,988 --> 02:34:49,557 CAN PURSUE PROJECTS NOT LINKED 3736 02:34:49,557 --> 02:34:51,326 TO A SPECIFIC DISEASE OR 3737 02:34:51,326 --> 02:34:51,859 TECHNOLOGY. 3738 02:34:51,859 --> 02:34:53,094 UNIQUE TO ARPA-H WE HAVE 3739 02:34:53,094 --> 02:34:54,228 COMPLETE FREEDOM WITH THE 3740 02:34:54,228 --> 02:34:54,929 DOLLARS WHERE WE'LL SPEND THEM 3741 02:34:54,929 --> 02:34:56,731 AND WANT TO FOCUS ON WHERE WE 3742 02:34:56,731 --> 02:35:00,835 THINK WE CAN HAVE THE GREATEST 3743 02:35:00,835 --> 02:35:07,241 IMPACT AND A BOTTOM'S UP 3744 02:35:07,241 --> 02:35:10,178 APPROACH AND RATHER THAN SET A 3745 02:35:10,178 --> 02:35:12,146 TOP-DOWN AGENDA SAYING THESE ARE 3746 02:35:12,146 --> 02:35:13,781 THINGS WE'LL FUND WE HAVE 3747 02:35:13,781 --> 02:35:15,917 PROGRAM MANAGERS IDENTIFIED IN 3748 02:35:15,917 --> 02:35:17,819 THE COMMUNITY THAT BRING NOT 3749 02:35:17,819 --> 02:35:19,253 ONLY THEIR C.V. BUT BIG IDEA 3750 02:35:19,253 --> 02:35:20,221 THEY WANT TO SOLVE. 3751 02:35:20,221 --> 02:35:23,891 IN THE CASE OF NITRO WHICH ENDED 3752 02:35:23,891 --> 02:35:26,594 UP BEING OUR FIRST PROGRAM WHICH 3753 02:35:26,594 --> 02:35:32,200 WAS A COINCIDENCE WE WEREN'T 3754 02:35:32,200 --> 02:35:34,902 TARGETING THIS TO START AND A 3755 02:35:34,902 --> 02:35:36,404 SURGEON SAID I DID THE MATH AND 3756 02:35:36,404 --> 02:35:38,840 I CAN HELP THE AVERAGE SURGEON 3757 02:35:38,840 --> 02:35:41,209 CAN HELP MAYBE 1,000, 2,000 3758 02:35:41,209 --> 02:35:44,946 PATIENTS BUT I WANT TO COME TO 3759 02:35:44,946 --> 02:35:47,448 ARPA-H AND REVERSE 3760 02:35:47,448 --> 02:35:48,716 OSTEOARTHRITIS AND HAVE JOINTS 3761 02:35:48,716 --> 02:35:51,652 HEAL THEMSELVES AND I CAN HAVE A 3762 02:35:51,652 --> 02:35:52,020 GREATER IMPACT. 3763 02:35:52,020 --> 02:35:54,756 WE HIRED HIM ON WITH HIS VISION 3764 02:35:54,756 --> 02:35:56,524 AND BROUGHT HIM ON FOR A TERM 3765 02:35:56,524 --> 02:35:58,059 LIMIT OF THREE YEARS. 3766 02:35:58,059 --> 02:36:00,094 HE'S GOT THREE YEARS TO HIT THE 3767 02:36:00,094 --> 02:36:02,196 GROUND RUNG AND GET THE PROJECT 3768 02:36:02,196 --> 02:36:04,032 STARTED AND THERE'S A LOT OF 3769 02:36:04,032 --> 02:36:06,034 URGENCY ASSOCIATED WITH THAT. 3770 02:36:06,034 --> 02:36:07,535 EVERY TWO WEEKS THAT GOES BY 1% 3771 02:36:07,535 --> 02:36:13,241 OF HIS TIME IS UP. 3772 02:36:13,241 --> 02:36:17,445 WE WANT TO MAKE SURE HE'S WELL 3773 02:36:17,445 --> 02:36:18,079 RESOURCES. 3774 02:36:18,079 --> 02:36:19,247 I HOPE THAT GIVES YOU THE SPIRIT 3775 02:36:19,247 --> 02:36:24,886 OF HOW WE APPROACH THE 3776 02:36:24,886 --> 02:36:25,186 CHALLENGES. 3777 02:36:25,186 --> 02:36:28,222 THE SECOND PROGRAM IS A PROGRAM 3778 02:36:28,222 --> 02:36:29,323 MANAGER AND FINDING THE MISSION 3779 02:36:29,323 --> 02:36:30,425 AND DRIVE TO SOLVE THE SPECIFIC 3780 02:36:30,425 --> 02:36:34,495 PROBLEM IN HEALTH. 3781 02:36:34,495 --> 02:36:35,496 WE'RE HERE TO ACCELERATE THE 3782 02:36:35,496 --> 02:36:37,231 HEALTH OUTCOMES FOR THE ENTIRE 3783 02:36:37,231 --> 02:36:38,199 ECO SYSTEM. 3784 02:36:38,199 --> 02:36:40,234 WE SERVE OUR CUSTOMERS WHO ARE 3785 02:36:40,234 --> 02:36:42,170 THE GENERAL PUBLIC, HEALTH CARE 3786 02:36:42,170 --> 02:36:42,837 PROVIDERS, PATIENT GROUPS. 3787 02:36:42,837 --> 02:36:45,840 I KNOW THERE'S MANY THERE IN THE 3788 02:36:45,840 --> 02:36:50,578 ROOM TODAY THAT OUR PROGRAM 3789 02:36:50,578 --> 02:36:52,580 MANAGERS HAVE BEEN ENGAGING WITH 3790 02:36:52,580 --> 02:36:56,851 FROM ACADEMIA AND INDUSTRY AND 3791 02:36:56,851 --> 02:36:59,320 STAKEHOLDER AND THE NIH IS A 3792 02:36:59,320 --> 02:37:00,154 STAKEHOLDER AND FEDERAL PARTNERS 3793 02:37:00,154 --> 02:37:02,590 LIKE FDA AND CNS ARE REQUIRED TO 3794 02:37:02,590 --> 02:37:05,259 HELP US GET ACROSS THE FINISH 3795 02:37:05,259 --> 02:37:07,061 LINE AND REGULATION AND 3796 02:37:07,061 --> 02:37:07,995 REIMBURSEMENT ARE KEY PART OF 3797 02:37:07,995 --> 02:37:11,299 THIS AND WE WANT TO MAKE SURE 3798 02:37:11,299 --> 02:37:13,201 WE'RE ADDRESSING THIS UP FRONT 3799 02:37:13,201 --> 02:37:14,836 AND I'LL TALK ON THE BACK END 3800 02:37:14,836 --> 02:37:16,204 ABOUT THE MARKETPLACE AND 3801 02:37:16,204 --> 02:37:18,172 INVESTORS AND HOW WE'RE REALLY 3802 02:37:18,172 --> 02:37:19,874 WORKING HARD TO CREATE A 3803 02:37:19,874 --> 02:37:21,809 MARKETPLACE THAT CAN BE IN 3804 02:37:21,809 --> 02:37:23,211 RECEIPT OF ARPA-H SOLUTIONS. 3805 02:37:23,211 --> 02:37:25,880 SO THIS AA LITTLE BIT OF A 3806 02:37:25,880 --> 02:37:30,985 REFLECTION ON DARPA WHERE 3807 02:37:30,985 --> 02:37:33,621 SUCCESSES IN DARPA WERE FROM THE 3808 02:37:33,621 --> 02:37:35,056 DEFENSE DEPEND AND DOD WILL PAY 3809 02:37:35,056 --> 02:37:37,859 FOR YOUR SOLUTIONS IN THIS ECO 3810 02:37:37,859 --> 02:37:38,459 SYSTEM. 3811 02:37:38,459 --> 02:37:40,862 HHS IS NOT THE SAME AS DOD. 3812 02:37:40,862 --> 02:37:43,331 WE HAVE A FEDERATED HEALTH CARE 3813 02:37:43,331 --> 02:37:44,165 SYSTEM. 3814 02:37:44,165 --> 02:37:44,799 FINDING THE SOLUTIONS AND 3815 02:37:44,799 --> 02:37:45,666 TRANSITIONING THINGS INTO THE 3816 02:37:45,666 --> 02:37:47,535 REAL WORLD IS A MUCH BIGGER 3817 02:37:47,535 --> 02:37:49,237 CHALLENGE AND WE KNOW THAT WE 3818 02:37:49,237 --> 02:37:51,372 REALLY NEED TO ADDRESS THAT SO 3819 02:37:51,372 --> 02:37:52,140 THAT INNOVATION GETS OUT OF THE 3820 02:37:52,140 --> 02:37:54,008 LAB AND INTO THE REAL WORLD. 3821 02:37:54,008 --> 02:37:56,944 WE'RE GOING TO HAVE TO HELP 3822 02:37:56,944 --> 02:38:01,249 FACILITATE THAT AND GREECE T 3823 02:38:01,249 --> 02:38:11,759 THE -- GREASE THE SKIDS ALONG 3824 02:38:13,661 --> 02:38:14,162 THE WAY. 3825 02:38:14,162 --> 02:38:15,163 AND THE PROGRAM SHOULD BE 3826 02:38:15,163 --> 02:38:17,765 DYNAMIC SO IF WE HAVE THIS 3827 02:38:17,765 --> 02:38:19,233 CONVERSATION THREE YEARS FROM 3828 02:38:19,233 --> 02:38:21,002 NOW WE SHOULD BE TALKING ABOUT 3829 02:38:21,002 --> 02:38:22,236 COMPLETELY DIFFERENT PROGRAMS 3830 02:38:22,236 --> 02:38:24,205 BECAUSE YOU HIRED NEW PROGRAMS 3831 02:38:24,205 --> 02:38:28,809 AND LAUNCHED NEW PROGRAMS. 3832 02:38:28,809 --> 02:38:30,845 THEY COME WITH THEIR INITIAL 3833 02:38:30,845 --> 02:38:32,580 IDEA AND WITH ENGAGEMENT WITH 3834 02:38:32,580 --> 02:38:35,149 THE COMMUNITY AND OTHER STAKE 3835 02:38:35,149 --> 02:38:37,952 HOLDERS TO IDENTIFY OTHER GAPS 3836 02:38:37,952 --> 02:38:38,719 ARPA-H CAN FILL. 3837 02:38:38,719 --> 02:38:40,221 FOR US SUCCESS IS WHEN THE 3838 02:38:40,221 --> 02:38:41,389 PROJECTS MAKE IT OUT OF ARPA-H 3839 02:38:41,389 --> 02:38:42,557 AND INTO THE REAL WORLD. 3840 02:38:42,557 --> 02:38:44,559 WE'RE NOT A FOREVER FUNDER. 3841 02:38:44,559 --> 02:38:46,127 WE'RE HERE TO BE A TRANSACTION 3842 02:38:46,127 --> 02:38:48,496 TO TAKE SOMETHING COMPLETELY 3843 02:38:48,496 --> 02:38:50,097 UNCERTAIN AND DEMONSTRATE SOME 3844 02:38:50,097 --> 02:38:51,399 DEGREE OF CERTAINTY THAT 3845 02:38:51,399 --> 02:38:52,833 SOMETHING IS POSSIBLE AS WE MOVE 3846 02:38:52,833 --> 02:38:53,701 FORWARD TO DERISK IT FOR THE 3847 02:38:53,701 --> 02:38:58,472 INVESTORS. 3848 02:38:58,472 --> 02:38:59,574 ONE OF THE WAYS IS THROUGH THE 3849 02:38:59,574 --> 02:39:01,676 DESIGN OF OUR PROGRAMS. 3850 02:39:01,676 --> 02:39:05,613 EVERY PROGRAM MANAGER AT DARPA 3851 02:39:05,613 --> 02:39:13,888 HAS A COMMON LANGUAGE CALLED THE 3852 02:39:13,888 --> 02:39:15,623 HEILMEIER PROGRAM AND IT WAS 3853 02:39:15,623 --> 02:39:16,257 ANSWERED IN THE INITIAL 3854 02:39:16,257 --> 02:39:20,561 APPLICATION WHEN THE PROGRAM WAS 3855 02:39:20,561 --> 02:39:21,596 PITCHED THESE QUESTIONS SIMPLY 3856 02:39:21,596 --> 02:39:24,899 PUT WHAT ARE YOU TRYING TO DO 3857 02:39:24,899 --> 02:39:26,534 AND WHAT'S THE PROBLEM YOUR 3858 02:39:26,534 --> 02:39:29,103 TRYING TO SOLVE AND WHAT'S IT 3859 02:39:29,103 --> 02:39:30,738 DONE TODAY AND WHAT'S THE GAME 3860 02:39:30,738 --> 02:39:34,308 CHANGER YOU'LL BRING FORWARD? 3861 02:39:34,308 --> 02:39:36,210 WHAT THE RISKS? 3862 02:39:36,210 --> 02:39:38,779 HOW LONG WILL IT TAKE AND WHAT 3863 02:39:38,779 --> 02:39:41,415 ARE THE MIDTERM EXAMS FOR 3864 02:39:41,415 --> 02:39:41,649 SUCCESS? 3865 02:39:41,649 --> 02:39:43,251 WE KNOW SOME WILL BE BIG LEAPS 3866 02:39:43,251 --> 02:39:44,986 IN ADVANCES AND THAT MAY NOT 3867 02:39:44,986 --> 02:39:47,588 HAPPEN FOR FIVE TO 10 YEARS AND 3868 02:39:47,588 --> 02:39:49,090 WHAT WILL HAPPEN TO KNOW WE'RE 3869 02:39:49,090 --> 02:39:51,325 ON TRACK AND MEASURE THE 3870 02:39:51,325 --> 02:39:51,592 PROGRESS. 3871 02:39:51,592 --> 02:39:52,660 WE'RE NOT THROWING THE MONEY 3872 02:39:52,660 --> 02:39:53,961 OVER THE FENCE WE'RE THERE WITH 3873 02:39:53,961 --> 02:39:54,528 A FEW. 3874 02:39:54,528 --> 02:39:58,432 IN BLUE WE HIGHLIGHTED HOW ARE 3875 02:39:58,432 --> 02:39:59,867 WE ADDRESSING THE ALL-AMERICAN 3876 02:39:59,867 --> 02:40:01,569 PART OF OUR MANDATE. 3877 02:40:01,569 --> 02:40:03,271 IF WE SUCCEED WHAT THE HEALTH 3878 02:40:03,271 --> 02:40:04,572 OUTCOMES THAT WE'RE GOING TO 3879 02:40:04,572 --> 02:40:06,440 CHANGE AND HOW ARE WE GOING TO 3880 02:40:06,440 --> 02:40:10,044 ASSURE EQUITABLE ACCESS TO COST 3881 02:40:10,044 --> 02:40:11,312 ACCESSIBILITY AND EVEN USER 3882 02:40:11,312 --> 02:40:12,313 EXPERIENCE IS ADDRESSED AND HOW 3883 02:40:12,313 --> 02:40:13,347 ARE WE BUILDING TRUST WITH 3884 02:40:13,347 --> 02:40:19,253 COMMUNITIES AS WE GROW? 3885 02:40:19,253 --> 02:40:21,489 ON THE LEFT SIDE IS AN IMAGE 3886 02:40:21,489 --> 02:40:26,594 FROM LAST FRIDAY A SYMPOSIUM IN 3887 02:40:26,594 --> 02:40:28,229 THE DEVELOPMENT OF THE PROGRAM 3888 02:40:28,229 --> 02:40:29,330 DEEP ENGAGEMENT WITH FDA BEFORE 3889 02:40:29,330 --> 02:40:31,065 WE HAVE A PRODUCT OR TECHNOLOGY 3890 02:40:31,065 --> 02:40:31,732 OR GROUPS FUNDED. 3891 02:40:31,732 --> 02:40:33,734 WE MAPPED OUT THE END TO END 3892 02:40:33,734 --> 02:40:35,136 PATH TO SEE WHAT ARE MY BLOCKERS 3893 02:40:35,136 --> 02:40:39,573 THAT WILL STOP ME FROM BRINGING 3894 02:40:39,573 --> 02:40:42,076 THIS INTO THE REAL WORLD AND FDA 3895 02:40:42,076 --> 02:40:43,911 KNOWLEDGE THEY HAVEN'T AGREED ON 3896 02:40:43,911 --> 02:40:46,547 AN ANIMAL MODEL FOR 3897 02:40:46,547 --> 02:40:48,716 OSTEOARTHRITIS APPROPRIATE FOR 3898 02:40:48,716 --> 02:40:50,084 OUR PROGRAM. 3899 02:40:50,084 --> 02:40:51,652 EVEN BEFORE WE SELECT THE TEAM 3900 02:40:51,652 --> 02:40:56,057 IN COLLABORATION WITH FDA SOME 3901 02:40:56,057 --> 02:41:00,127 FOLKS IN THE ROOM ATTENDED THIS 3902 02:41:00,127 --> 02:41:00,361 FRIDAY. 3903 02:41:00,361 --> 02:41:02,863 WHAT'S AN ANIMAL MODEL WE CAN 3904 02:41:02,863 --> 02:41:05,933 AGREE ON SO WE'RE READY AND 3905 02:41:05,933 --> 02:41:08,536 READY FOR PRECLINICAL TRIALS FDA 3906 02:41:08,536 --> 02:41:11,138 BOUGHT IN. 3907 02:41:11,138 --> 02:41:12,239 THESE ARE THE TYPES OF THINGS WE 3908 02:41:12,239 --> 02:41:14,775 HOPE YOU WANT TO PARTNER WITH 3909 02:41:14,775 --> 02:41:16,210 ARPA-H ON AND THIS IS A BENEFIT 3910 02:41:16,210 --> 02:41:18,179 NOR ENTIRE COMMUNITY AND NOT 3911 02:41:18,179 --> 02:41:19,280 JUST ARPA-H. 3912 02:41:19,280 --> 02:41:23,918 I WILL ALSO NOTE THIS ALLOWS US 3913 02:41:23,918 --> 02:41:26,787 TO EXERCISE ONE OF OUR 3914 02:41:26,787 --> 02:41:28,255 AUTHORITIES AND REIMBURSE THEM 3915 02:41:28,255 --> 02:41:29,390 DIRECTLY FOR SERVICES AND THIS 3916 02:41:29,390 --> 02:41:31,826 IS ONE CASE TO BRING IN FDA 3917 02:41:31,826 --> 02:41:33,728 COUNTERPARTS INTO THE ROOM. 3918 02:41:33,728 --> 02:41:36,230 WE'RE ALSO REALLY INTERESTED IN 3919 02:41:36,230 --> 02:41:40,835 EXPLORING PERHAPS ACCELERATED 3920 02:41:40,835 --> 02:41:44,305 APPROVAL PATHWAYS AND 3921 02:41:44,305 --> 02:41:47,074 INCENTIVIZE PARTNERSHIPS BECAUSE 3922 02:41:47,074 --> 02:41:52,546 FDA CAN INCENTIVIZE THROUGH SOME 3923 02:41:52,546 --> 02:41:54,482 REGULATORY PRIORITIZATION AND 3924 02:41:54,482 --> 02:41:55,483 WE'RE EXPLORING WHAT THAT MIGHT 3925 02:41:55,483 --> 02:41:59,186 LOOK LIKE. 3926 02:41:59,186 --> 02:42:01,288 WALKING YOU THROUGH WHAT LOOKS 3927 02:42:01,288 --> 02:42:07,294 LIKE ONCE HAVE YOU THE 3928 02:42:07,294 --> 02:42:09,930 HEILMEIRER QUESTIONS DEFINED AND 3929 02:42:09,930 --> 02:42:14,001 WE LAUNCH THE PROGRAM LIKE NITRO 3930 02:42:14,001 --> 02:42:15,569 AND THEY SELECT THE TEAM OF 3931 02:42:15,569 --> 02:42:16,537 SOLVERS AND WE LOOK TO THE 3932 02:42:16,537 --> 02:42:17,571 COMMUNITY FOR A SOLUTION. 3933 02:42:17,571 --> 02:42:20,141 WE WON'T PRESCRIBE A SOLUTION. 3934 02:42:20,141 --> 02:42:21,842 WE WANT TO HEAR THE DIFFERENT 3935 02:42:21,842 --> 02:42:27,615 IDEAS AND WE'LL PUT SOME HEAD TO 3936 02:42:27,615 --> 02:42:28,682 HEAD AND WE'RE WILLING TO 3937 02:42:28,682 --> 02:42:32,086 EXPLORE THOSE SIDE BY SIDE. 3938 02:42:32,086 --> 02:42:33,654 IT'S THE JOB OF THE PROGRAM 3939 02:42:33,654 --> 02:42:36,023 MANAGER TO THEN LOOK AT THOSE 3940 02:42:36,023 --> 02:42:37,158 MILESTONES SET OVER THE COURSE 3941 02:42:37,158 --> 02:42:39,794 OF A THREE, FOUR, FIVE-YEAR 3942 02:42:39,794 --> 02:42:42,329 PROGRAM AND SEE WHICH PERFORMER 3943 02:42:42,329 --> 02:42:43,264 TEAMS ARE REACHING THEIR GOALS 3944 02:42:43,264 --> 02:42:45,166 AND FOR THOSE THAT AREN'T, WE 3945 02:42:45,166 --> 02:42:47,501 MAY MAKE A DECISION TO PIVOT 3946 02:42:47,501 --> 02:42:52,173 RESOURCES AND NOT FUND THE OUT 3947 02:42:52,173 --> 02:42:53,841 YEARS OF A PROJECT. 3948 02:42:53,841 --> 02:42:54,875 WHAT'S IMPORTANT FOR THE PROGRAM 3949 02:42:54,875 --> 02:42:56,544 MANAGER IS GETTING TO A SOLUTION 3950 02:42:56,544 --> 02:42:59,613 NOT FUNDING EVERY GROUP ACROSS 3951 02:42:59,613 --> 02:43:00,648 THE FINISH LINE. 3952 02:43:00,648 --> 02:43:01,782 THERE'S A LOT OF ACTIVE PROGRAM 3953 02:43:01,782 --> 02:43:03,884 MANAGEMENT SO IT'S NOT A 3954 02:43:03,884 --> 02:43:06,520 SURPRISE TO ANYBODY IF FUNDING 3955 02:43:06,520 --> 02:43:08,122 ENDS BUT IT'S AN IMPORTANT POINT 3956 02:43:08,122 --> 02:43:09,824 OF WORKING WITH ARPA-H IMPORTANT 3957 02:43:09,824 --> 02:43:10,758 FOR THOSE THAT WANT TO WORK WITH 3958 02:43:10,758 --> 02:43:13,627 US TO BE AWARE OF. 3959 02:43:13,627 --> 02:43:16,197 AND LAST BUT NOT LEAST 3960 02:43:16,197 --> 02:43:16,664 TRANSITION. 3961 02:43:16,664 --> 02:43:18,833 SO GETTING THIS INTO THE REAL 3962 02:43:18,833 --> 02:43:20,201 WORLD SO SOMEBODY ELSE CAN PICK 3963 02:43:20,201 --> 02:43:24,071 IT UP AND FUND IT TO RUN THE 3964 02:43:24,071 --> 02:43:24,805 CLINICAL TRIAL OR COMMERCIALIZE 3965 02:43:24,805 --> 02:43:26,340 IS AN IMPORTANT PART OF WHAT WE 3966 02:43:26,340 --> 02:43:26,507 DO. 3967 02:43:26,507 --> 02:43:30,911 WE DEDICATED AN ENTIRE OFFICE 3968 02:43:30,911 --> 02:43:33,180 FOR A PROJECT ACCELERATED 3969 02:43:33,180 --> 02:43:36,217 TRANSITION INNOVATION OFFICE. 3970 02:43:36,217 --> 02:43:38,519 WE KNOW HOW HARD IT IS TO GET 3971 02:43:38,519 --> 02:43:39,553 THINGS IN THE REAL WORLD AND 3972 02:43:39,553 --> 02:43:41,655 WE'RE WORKING WITH PROGRAM 3973 02:43:41,655 --> 02:43:43,090 MANAGERS TO DO A MARKET 3974 02:43:43,090 --> 02:43:43,390 ASSESSMENT. 3975 02:43:43,390 --> 02:43:44,859 IT'S OKAY IF A MARKETPLACE 3976 02:43:44,859 --> 02:43:46,293 EXISTS BUT I WANT TO KNOW THAT 3977 02:43:46,293 --> 02:43:48,529 UP FRONT AND UNDERSTAND THE 3978 02:43:48,529 --> 02:43:49,230 GAPS. 3979 02:43:49,230 --> 02:43:51,632 WE ALSO DESIGN OUR PROGRAMS WITH 3980 02:43:51,632 --> 02:43:53,467 HUMAN CENTERED DESIGN IN MIND. 3981 02:43:53,467 --> 02:43:55,569 ALL OF US HAVE HAD INTERACTION 3982 02:43:55,569 --> 02:43:58,005 WITH THE HEALTH CARE SECTOR. 3983 02:43:58,005 --> 02:43:59,340 NOT ALL HAVE BEEN GOOD. 3984 02:43:59,340 --> 02:44:00,741 IMAGINE IF WE GET INPUT BEFORE 3985 02:44:00,741 --> 02:44:02,209 WE LAUNCH PROGRAMS. 3986 02:44:02,209 --> 02:44:03,477 WHAT'S THE COMMUNITY ACTUALLY 3987 02:44:03,477 --> 02:44:07,314 REALLY WANT. 3988 02:44:07,314 --> 02:44:11,285 WHAT'S IMPORTANT FOR FOLLOW UP. 3989 02:44:11,285 --> 02:44:15,055 WE KNOW WITH MAMMOGRAM THERE'S 3990 02:44:15,055 --> 02:44:15,990 200,000 PREVENTIBLE CANCER 3991 02:44:15,990 --> 02:44:18,325 DEATHS EVERY YEAR IF THEY GET A 3992 02:44:18,325 --> 02:44:19,527 POSITIVE MAMMOGRAM THEY 3993 02:44:19,527 --> 02:44:20,227 FOLLOW-UP WITH A BIOPSY. 3994 02:44:20,227 --> 02:44:22,997 HOW DO WE CREATE A NEW DESIGN 3995 02:44:22,997 --> 02:44:24,164 THAT ALLOWS FOR THE LOOPS TO BE 3996 02:44:24,164 --> 02:44:24,398 CLOSED. 3997 02:44:24,398 --> 02:44:27,134 IT'S AT THE FRONT OF MIND FOR 3998 02:44:27,134 --> 02:44:28,469 ALL OF OUR PROGRAM MANAGERS TO 3999 02:44:28,469 --> 02:44:29,803 THE END OF A PROGRAM GETTING IT 4000 02:44:29,803 --> 02:44:37,311 OUT TO THE REAL WORLD. 4001 02:44:37,311 --> 02:44:42,950 WHILE PROGRAMS ARE BOTTOM-UP AND 4002 02:44:42,950 --> 02:44:45,953 BEFORE I CAME TO ARPA-H I WANTED 4003 02:44:45,953 --> 02:44:47,488 TO ARTICULATE FOUR AREAS OF 4004 02:44:47,488 --> 02:44:49,323 HEALTH I THOUGHT WERE RIPE FOR 4005 02:44:49,323 --> 02:44:52,560 ADDITIONAL FUNDING BY ARPA-H TO 4006 02:44:52,560 --> 02:44:56,430 CREATE THE ASYMMETRICAL BENEFITS 4007 02:44:56,430 --> 02:44:58,699 AND THEY'RE NOW OUR MISSION 4008 02:44:58,699 --> 02:44:59,934 OFFICE UNDER A MISSION OFFICE 4009 02:44:59,934 --> 02:45:00,200 DIRECTOR. 4010 02:45:00,200 --> 02:45:00,768 THE FIRST IS HEALTH SCIENCE 4011 02:45:00,768 --> 02:45:05,739 FUTURES. 4012 02:45:05,739 --> 02:45:07,341 AND TOOLS AND TECHNOLOGIES THAT 4013 02:45:07,341 --> 02:45:10,177 ARE DISEASE AGNOSTIC TO ADVANCE 4014 02:45:10,177 --> 02:45:12,613 THE STATE OF THE ART. 4015 02:45:12,613 --> 02:45:14,949 WE THINK OF THE SKUNK WORKS OF 4016 02:45:14,949 --> 02:45:17,618 LIKE WHAT'S THE NEW mRNA 4017 02:45:17,618 --> 02:45:20,054 PLATFORM WE CAN DEMONSTRATE 4018 02:45:20,054 --> 02:45:21,488 ACROSS SEVERAL DIFFERENT 4019 02:45:21,488 --> 02:45:21,989 DISEASES. 4020 02:45:21,989 --> 02:45:23,390 DR. JENKINS IS THE DIRECTOR OF 4021 02:45:23,390 --> 02:45:24,692 THIS OFFICE AND WE'RE HIRING 4022 02:45:24,692 --> 02:45:27,294 PROGRAM MANAGERS IN ALL THE 4023 02:45:27,294 --> 02:45:28,896 OFFICES I SHOULD SAY. 4024 02:45:28,896 --> 02:45:34,201 SCALABLE SOLUTIONS IS REACHING 4025 02:45:34,201 --> 02:45:35,269 EVERYONE QUICKLY WHETHER IT'S 4026 02:45:35,269 --> 02:45:36,236 MANUFACTURING OR GETTING THINGS 4027 02:45:36,236 --> 02:45:38,539 TO PEOPLE IN THEIR HOMES IN 4028 02:45:38,539 --> 02:45:40,107 RURAL SETTINGS WHERE THERE'S 4029 02:45:40,107 --> 02:45:41,942 UNDER SERVED COMMUNITIES. 4030 02:45:41,942 --> 02:45:44,612 HOW ARE THEY BRIDGING THE LAST 4031 02:45:44,612 --> 02:45:47,114 MILE GAP AND WHAT'S THE 4032 02:45:47,114 --> 02:45:48,649 INNOVATION I NEED TO SEE. 4033 02:45:48,649 --> 02:45:50,217 MAYBE SOMEBODY IN THE ROOM WOULD 4034 02:45:50,217 --> 02:45:51,585 BE INTERESTED IN PURSUING A ROLE 4035 02:45:51,585 --> 02:45:54,855 AS A SCALABLE SOLUTIONS 4036 02:45:54,855 --> 02:45:55,122 DIRECTOR. 4037 02:45:55,122 --> 02:45:58,058 WE'D LOVE TO HEAR FROM YOU. 4038 02:45:58,058 --> 02:45:59,259 AND KEEPING PEOPLE FROM BECOMING 4039 02:45:59,259 --> 02:46:00,995 PATIENTS IN THE FIRST PLACE. 4040 02:46:00,995 --> 02:46:03,697 WHAT'S THE DIAGNOSTIC DETECTION, 4041 02:46:03,697 --> 02:46:04,298 BEHAVIORAL, SOCIAL SCIENCE 4042 02:46:04,298 --> 02:46:06,100 PROGRAMS WE COULD BE FUNDING. 4043 02:46:06,100 --> 02:46:07,334 ONE OF OUR PROGRAM MANAGERS SAID 4044 02:46:07,334 --> 02:46:10,838 THIS IS THE OFFICE WHERE YOU DIE 4045 02:46:10,838 --> 02:46:11,138 HEALTHY. 4046 02:46:11,138 --> 02:46:13,307 LIVE YOUR HEALTHIEST LIFE AND 4047 02:46:13,307 --> 02:46:14,174 DIE AT THE END. 4048 02:46:14,174 --> 02:46:16,577 ALL ALONG THE WAY YOU HAVE YOUR 4049 02:46:16,577 --> 02:46:19,079 HEALTHIEST LIFE SPAN AND WE WANT 4050 02:46:19,079 --> 02:46:20,914 TO PROMOTE THE LONGEVITY IN 4051 02:46:20,914 --> 02:46:23,550 HEALTH AS LONG AS POSSIBLE AND 4052 02:46:23,550 --> 02:46:25,185 LAST BUT NOT LEAST, RESILIENT 4053 02:46:25,185 --> 02:46:25,419 SYSTEMS. 4054 02:46:25,419 --> 02:46:27,788 THE OTHER OFFICES ARE THE 4055 02:46:27,788 --> 02:46:28,922 PRODUCT INNOVATION AND RESILIENT 4056 02:46:28,922 --> 02:46:30,391 SYSTEMS IS MORE OF A SYSTEMS 4057 02:46:30,391 --> 02:46:30,591 LEVEL. 4058 02:46:30,591 --> 02:46:35,963 WHAT IS THE INTEGRATED DATA 4059 02:46:35,963 --> 02:46:37,898 COLLECTED AND WHAT IS NETWORK 4060 02:46:37,898 --> 02:46:38,899 CAPABILITY WE CAN ESTABLISH 4061 02:46:38,899 --> 02:46:42,469 THROUGH OUR ARPA-H THAT WE CAN 4062 02:46:42,469 --> 02:46:43,771 DOUBLE DOWN IN BETWEEN PANDEMICS 4063 02:46:43,771 --> 02:46:46,573 PRIOR TO A CLIMATE CRISIS TO 4064 02:46:46,573 --> 02:46:48,208 MAKE SURE THAT WE CAN RESPOND 4065 02:46:48,208 --> 02:46:50,411 MOVING FORWARD. 4066 02:46:50,411 --> 02:46:52,913 AND SO I WILL DO A LITTLE BIT OF 4067 02:46:52,913 --> 02:46:57,618 A DEEP DIVE ON THE NITRO 4068 02:46:57,618 --> 02:46:57,885 PROGRAM. 4069 02:46:57,885 --> 02:47:01,922 I'M A GENETICISTS NOT AN EXPERT 4070 02:47:01,922 --> 02:47:03,924 IN OSTEOARTHRITIS AND HOPE TO DO 4071 02:47:03,924 --> 02:47:05,759 THE PROGRAM JUSTICE WITH THE 4072 02:47:05,759 --> 02:47:09,263 GOALS WE HOPE TO PURSUE. 4073 02:47:09,263 --> 02:47:11,498 SO IN THIS FIRST PROGRAM, WE 4074 02:47:11,498 --> 02:47:13,801 WANT TO CREATE THE VISION OF THE 4075 02:47:13,801 --> 02:47:15,269 FUTURE WHERE WE CAN 4076 02:47:15,269 --> 02:47:22,076 REVOLUTIONIZE THE CARE ALGORITHM 4077 02:47:22,076 --> 02:47:24,078 FOR OSTEOARTHRITIS AND I KNOW 4078 02:47:24,078 --> 02:47:28,215 THERE'S A LOT OF PAIN AND I'M 4079 02:47:28,215 --> 02:47:30,918 FEELING SOME TODAY AND REPEAT 4080 02:47:30,918 --> 02:47:32,786 PAIN AND COMMUNITIES DON'T HAVE 4081 02:47:32,786 --> 02:47:35,122 ACCESS AND THIS IS WHAT ROSS SET 4082 02:47:35,122 --> 02:47:36,924 OUT ADDRESS. 4083 02:47:36,924 --> 02:47:38,692 IT'S A TECHNICAL PROGRAM 4084 02:47:38,692 --> 02:47:39,727 IDENTIFIED THREE TECHNICAL AREAS 4085 02:47:39,727 --> 02:47:42,129 OVER THE COURSE OF THE PROGRAM 4086 02:47:42,129 --> 02:47:43,897 WHERE HE'D LIKE TO SEE AN 4087 02:47:43,897 --> 02:47:44,998 ADVANCE OVER THE STATE OF THE 4088 02:47:44,998 --> 02:47:45,265 ART. 4089 02:47:45,265 --> 02:47:49,336 THE FIRST IS A NEEDLE-BASED 4090 02:47:49,336 --> 02:47:51,238 NON-INVASIVE BONE REGENERATION 4091 02:47:51,238 --> 02:47:54,041 PROJECT IN TA1. 4092 02:47:54,041 --> 02:48:00,214 TECHNOLOGY AREA 2 IS LOOKING AT 4093 02:48:00,214 --> 02:48:01,315 NON-INVASIVE CARTILAGE 4094 02:48:01,315 --> 02:48:11,859 REGENERATION AND TA IS ALL-G 4095 02:48:12,326 --> 02:48:20,000 ALL-GENIC -- ALLOGENEIC 4096 02:48:20,000 --> 02:48:25,939 AUTOGENOUS NON-IMMUNOGENIC 4097 02:48:25,939 --> 02:48:28,208 LOAD-BEARING AND TOTAL 4098 02:48:28,208 --> 02:48:30,677 REPLACEMENT JOINTS AND THERE'S A 4099 02:48:30,677 --> 02:48:31,311 TREMENDOUS DIFFERENCE IN THE 4100 02:48:31,311 --> 02:48:41,855 HEALTH OUTCOMES AND THIS IS WHAT 4101 02:48:45,526 --> 02:48:48,896 THEY'LL HAVE TO PURSUE TO LEAN 4102 02:48:48,896 --> 02:48:51,331 INTO STACKING THE DECK FOR A 4103 02:48:51,331 --> 02:48:51,665 BREAKTHROUGH. 4104 02:48:51,665 --> 02:48:54,668 SO THERE BE A VARIETY OF 4105 02:48:54,668 --> 02:48:55,602 APPROACH PURSUED BUT MEASURING 4106 02:48:55,602 --> 02:48:59,706 THE ELIMINATION OF THE NEED FOR 4107 02:48:59,706 --> 02:49:01,141 REPEAT SURGERY. 4108 02:49:01,141 --> 02:49:03,911 LOOKING ACROSS THE ENTIRE 4109 02:49:03,911 --> 02:49:06,046 DISEASE SPECTRUM FROM EARLY 4110 02:49:06,046 --> 02:49:08,215 DISEASE TO LATE STAGE AND 4111 02:49:08,215 --> 02:49:18,692 LOOKING AT DEPARTURES FROM 4112 02:49:25,432 --> 02:49:28,268 FORMER USES AND MAKE SURE IT'S 4113 02:49:28,268 --> 02:49:28,869 REPRESENTATIVE OF THE TRUE 4114 02:49:28,869 --> 02:49:30,270 DEMOGRAPHIC OF THE DISEASE. 4115 02:49:30,270 --> 02:49:31,738 WE KNOW IT'S GOING TO BE HARD 4116 02:49:31,738 --> 02:49:33,040 BUT SOMETHING WE'RE PASSIONATE 4117 02:49:33,040 --> 02:49:34,374 ABOUT AND COMMITTED TO PROBLEM 4118 02:49:34,374 --> 02:49:36,343 SOLVING TO GET US ACROSS THE 4119 02:49:36,343 --> 02:49:36,777 FINISH LINE. 4120 02:49:36,777 --> 02:49:38,812 AND I ENCOURAGE ALL OF YOU TO GO 4121 02:49:38,812 --> 02:49:42,249 LOOK AT THE METRICS FOR THE 4122 02:49:42,249 --> 02:49:44,651 NITRO PROGRAM. 4123 02:49:44,651 --> 02:49:47,921 THERE'S A DEEP AGENCY 4124 02:49:47,921 --> 02:49:48,822 ANNOUNCEMENT WALKING YOU THROUGH 4125 02:49:48,822 --> 02:49:49,456 THE REQUIREMENTS OF THE COURSE 4126 02:49:49,456 --> 02:49:56,930 OF THE PROGRAM. 4127 02:49:56,930 --> 02:50:00,234 AND THE WHY THE EQUITY 4128 02:50:00,234 --> 02:50:00,901 REQUIREMENTS UNDERSTANDING THE 4129 02:50:00,901 --> 02:50:02,469 KEY PERFORMANCE INDICATORS WE 4130 02:50:02,469 --> 02:50:04,838 WANT TO TRACK AS PART OF THE 4131 02:50:04,838 --> 02:50:06,206 PROGRAM AND SOME LISTENING 4132 02:50:06,206 --> 02:50:07,207 SESSIONS MAKING SURE AS WE 4133 02:50:07,207 --> 02:50:08,876 DEVELOP THE CAPABILITIES WE'RE 4134 02:50:08,876 --> 02:50:15,549 NOT PRESCRIBE ING -- PRESCRIBING 4135 02:50:15,549 --> 02:50:18,485 BUT WORKING IN PARTNERSHIP TO 4136 02:50:18,485 --> 02:50:22,489 AND THERE'S GOING TO BE A ROAD 4137 02:50:22,489 --> 02:50:23,724 MAP CREATED BY PERFORMERS 4138 02:50:23,724 --> 02:50:25,292 THEY'LL HAVE TO FOLLOW OVER THE 4139 02:50:25,292 --> 02:50:27,561 COURSE OF EFFORT MOVING FORWARD. 4140 02:50:27,561 --> 02:50:29,796 AND IN PHASE 2 I'LL SPEAK AT THE 4141 02:50:29,796 --> 02:50:32,799 END OF THIS MISSION DECK A 4142 02:50:32,799 --> 02:50:33,867 LITTLE BIT ABOUT ARPA-H WHICH WE 4143 02:50:33,867 --> 02:50:37,704 WANT TO USE NOT ONLY FOR THE 4144 02:50:37,704 --> 02:50:38,605 NITRO PROGRAM AND CLINICAL 4145 02:50:38,605 --> 02:50:40,440 TRIALS TO ACCELERATE ENROLLMENT 4146 02:50:40,440 --> 02:50:41,875 IN CLINICAL TRIALS AND TAKE 4147 02:50:41,875 --> 02:50:42,776 ADVANTAGE OF THE SCALE OF A 4148 02:50:42,776 --> 02:50:49,249 NATIONWIDE NETWORK. 4149 02:50:49,249 --> 02:50:52,219 AND BRIEFLY THE OSTEOARTHRITIS 4150 02:50:52,219 --> 02:50:54,521 MODEL SYMPOSIUM WHICH TOOK PLACE 4151 02:50:54,521 --> 02:50:56,089 JUST LAST FRIDAY AND THINKING 4152 02:50:56,089 --> 02:50:58,058 ABOUT WHAT IS THE LARGE ANIMAL 4153 02:50:58,058 --> 02:51:01,962 MODEL THAT'S GOING TO BE 4154 02:51:01,962 --> 02:51:05,299 APPROPRIATE FOR THE PROGRAM WE 4155 02:51:05,299 --> 02:51:07,100 CAN LOCK IN AND DECREASE THE 4156 02:51:07,100 --> 02:51:08,235 PRICE OF THERAPEUTICS. 4157 02:51:08,235 --> 02:51:11,038 FOR THOSE THAT PARTICIPATED I 4158 02:51:11,038 --> 02:51:11,738 WANTED TO SHARE A LITTLE BIT OF 4159 02:51:11,738 --> 02:51:13,240 THE FEEDBACK. 4160 02:51:13,240 --> 02:51:16,009 EVEN BEFORE THE SYMPOSIUM WE RAN 4161 02:51:16,009 --> 02:51:16,977 A SURVEY. 4162 02:51:16,977 --> 02:51:19,313 THIS IS THE FIRST TIME WE'VE 4163 02:51:19,313 --> 02:51:20,914 DONE THESE AT ARPA-H. 4164 02:51:20,914 --> 02:51:22,716 THERE'S A LOT OF FIRSTS AND WE 4165 02:51:22,716 --> 02:51:24,184 WANT TO BRING VALUE TO THE 4166 02:51:24,184 --> 02:51:26,119 SCIENTIFIC COMMUNITY. 4167 02:51:26,119 --> 02:51:27,921 STARTING WITH WHAT IS YOUR 4168 02:51:27,921 --> 02:51:30,590 PREFERRED ANIMAL MODEL BEFORE 4169 02:51:30,590 --> 02:51:32,893 THE EVENT AND POST-SURVEY HAS 4170 02:51:32,893 --> 02:51:40,233 YOUR LARGE ANIMAL MODEL CHANGED? 4171 02:51:40,233 --> 02:51:42,602 IT'S WIDELY SEEN IT'S NOT 4172 02:51:42,602 --> 02:51:45,439 CHANGED BUT THERE'S MOVEMENT IN 4173 02:51:45,439 --> 02:51:46,006 UNDERSTANDING WHAT WILL BE 4174 02:51:46,006 --> 02:51:47,741 REQUIRED FROM FDA. 4175 02:51:47,741 --> 02:51:52,079 I UNDERSTAND THERE'S QUITE A BIT 4176 02:51:52,079 --> 02:51:53,213 OF FOLLOW UP THAT WILL BE 4177 02:51:53,213 --> 02:51:54,414 AVAILABLE TO THE GENERAL PUBLIC 4178 02:51:54,414 --> 02:51:56,249 AS WE CONTINUE THE CONVERSATION 4179 02:51:56,249 --> 02:51:58,018 ON THE ANIMAL MODEL MOVING 4180 02:51:58,018 --> 02:52:00,520 FORWARD. 4181 02:52:00,520 --> 02:52:01,121 IMPORTANTLY, I THINK A GOOD 4182 02:52:01,121 --> 02:52:03,757 SIGNAL FOR US IS THE QUESTION DO 4183 02:52:03,757 --> 02:52:05,092 YOU HAVE A BETTER UNDERSTANDING 4184 02:52:05,092 --> 02:52:07,060 OF THE REGULATORY REQUIREMENT? 4185 02:52:07,060 --> 02:52:12,065 THE RESOUNDING, YES, IS A ROLE 4186 02:52:12,065 --> 02:52:14,468 ARPA-H CAN PLAY IN PARTNERSHIP 4187 02:52:14,468 --> 02:52:16,203 WITH OUR STAKEHOLDERS AT FDA AND 4188 02:52:16,203 --> 02:52:19,039 A FOLLOW-UP ON THE PAYER MODEL. 4189 02:52:19,039 --> 02:52:22,042 IT'S NOT ALWAYS CONNECTED WITH 4190 02:52:22,042 --> 02:52:23,243 HOW YOU GET SOMETHING REGULATED 4191 02:52:23,243 --> 02:52:24,211 AND OUT THE DOOR. 4192 02:52:24,211 --> 02:52:28,215 WE'RE HAPPY TO CONTRIBUTE IN 4193 02:52:28,215 --> 02:52:29,649 THIS WAY MOVING FORWARD. 4194 02:52:29,649 --> 02:52:32,219 JUST TO ROUND IT OUT, THE 4195 02:52:32,219 --> 02:52:33,954 JOURNEY OF A PROGRAM AT ARPA-H 4196 02:52:33,954 --> 02:52:36,223 STARTS WITH THE PROGRAM MANAGER 4197 02:52:36,223 --> 02:52:37,724 AND THE PROBLEM THEY'VE 4198 02:52:37,724 --> 02:52:38,325 IDENTIFIED. 4199 02:52:38,325 --> 02:52:40,227 THE SOLICITATION, THE 4200 02:52:40,227 --> 02:52:41,795 APPLICATIONS ARE RECEIVED AND 4201 02:52:41,795 --> 02:52:48,802 WHERE NITRO IS IN EVALUATING 4202 02:52:48,802 --> 02:52:50,370 THE FINAL PROPOSALS AND IN THE 4203 02:52:50,370 --> 02:52:51,238 NEXT MONTHS WILL MAKE A 4204 02:52:51,238 --> 02:52:52,339 SELECTION OF TEAMS TO MOVE 4205 02:52:52,339 --> 02:52:53,774 FORWARD AS A PERFORMERS TO 4206 02:52:53,774 --> 02:52:56,209 UNDERSTAND THE NITRO RAM. 4207 02:52:56,209 --> 02:53:00,947 -- PROGRAM. 4208 02:53:00,947 --> 02:53:02,482 I HOPE SOME OF YOU APPLIED AND 4209 02:53:02,482 --> 02:53:04,151 STAY TUNED FOR THE ANNOUNCEMENT. 4210 02:53:04,151 --> 02:53:14,594 THIS ISN'T A ONE AND DONE. 4211 02:53:25,439 --> 02:53:27,174 WE ACKNOWLEDGE THE CHALLENGE 4212 02:53:27,174 --> 02:53:29,443 THAT MANY AMERICANS LIVE VERY 4213 02:53:29,443 --> 02:53:30,577 FAR AWAY FROM HEALTH CARE 4214 02:53:30,577 --> 02:53:32,913 CENTERS AND WE ALSO ACKNOWLEDGE 4215 02:53:32,913 --> 02:53:34,815 THAT BIO TECH AND INNOVATION IS 4216 02:53:34,815 --> 02:53:37,384 CLUSTERED IN A FEW PARTS OF OUR 4217 02:53:37,384 --> 02:53:39,486 COUNTRY AND NOT OFTEN CO-LOCATED 4218 02:53:39,486 --> 02:53:42,389 WHERE PATIENTS REALLY ARE. 4219 02:53:42,389 --> 02:53:45,926 AND SO NUMEROUS DISEASES AS A 4220 02:53:45,926 --> 02:53:51,665 RESULT DISPROPORTIONATELY IMPACT 4221 02:53:51,665 --> 02:53:54,901 THIS AND THERE'S A NOD TO 4222 02:53:54,901 --> 02:53:57,704 HISTORY OF THE ARPA NET AT DARPA 4223 02:53:57,704 --> 02:53:59,372 WHEN THEY LAUNCH THE PROGRAM 4224 02:53:59,372 --> 02:54:01,374 THAT BECAME THE INTERNET WAS A 4225 02:54:01,374 --> 02:54:01,975 FOUR-NODE NETWORK 4226 02:54:01,975 --> 02:54:04,244 I DON'T KNOW HOW MANY NODES THE 4227 02:54:04,244 --> 02:54:05,712 INTERNET HAS TODAY BUT CERTAINLY 4228 02:54:05,712 --> 02:54:07,380 MANY MORE THAN FOUR NODES. 4229 02:54:07,380 --> 02:54:09,850 WE'RE STARTING WITH THREE NODES 4230 02:54:09,850 --> 02:54:11,451 AND THIS IS LEGISLATIVELY 4231 02:54:11,451 --> 02:54:12,219 DETERMINED CONGRESS GAVE US 4232 02:54:12,219 --> 02:54:13,153 THREE SITES. 4233 02:54:13,153 --> 02:54:15,555 WE WANT TO LEAN INTO THE THREE 4234 02:54:15,555 --> 02:54:18,024 GEOGRAPHIES AND BUILD A 50-STATE 4235 02:54:18,024 --> 02:54:20,260 HUB AND SPOKE NETWORK. 4236 02:54:20,260 --> 02:54:23,196 THREE HUBS WILL UNLOCK CERTAIN 4237 02:54:23,196 --> 02:54:24,264 KEY CAPABILITIES WE NEED TO 4238 02:54:24,264 --> 02:54:26,666 TRANSITION THINGS TO THE REAL 4239 02:54:26,666 --> 02:54:28,101 WORLD. 4240 02:54:28,101 --> 02:54:29,703 SO FIRST WE'LL HAVE A 4241 02:54:29,703 --> 02:54:33,340 STAKEHOLDER AND OPERATIONS HUB 4242 02:54:33,340 --> 02:54:36,243 IN THE WASHINGTON, D.C. REGION, 4243 02:54:36,243 --> 02:54:36,910 EXACT ADDRESS TO BE DETERMINED 4244 02:54:36,910 --> 02:54:39,412 BUT IT WILL KEEP US CLOSE TO CMS 4245 02:54:39,412 --> 02:54:43,950 TO OUR FDA PARTNERS, HRSA AND 4246 02:54:43,950 --> 02:54:46,386 OTHERS WE KNOW WILL HELP US GET 4247 02:54:46,386 --> 02:54:49,756 TECHNOLOGY TO THE REAL WORLD AND 4248 02:54:49,756 --> 02:54:51,091 OTHER TWO WE'LL ANNOUNCE NEXT 4249 02:54:51,091 --> 02:54:54,761 WEEK WHERE THE HUBS LAND. 4250 02:54:54,761 --> 02:54:55,862 A CUSTOMER EXPERIENCE HUB 4251 02:54:55,862 --> 02:54:56,930 FOCUSSED ON THE PEOPLE WE'RE 4252 02:54:56,930 --> 02:54:58,165 INTENDED TO SERVE. 4253 02:54:58,165 --> 02:55:00,033 HOW DO WE ENGAGE COMMUNITIES AND 4254 02:55:00,033 --> 02:55:01,368 ENROLL COMMUNITIES IN CLINICAL 4255 02:55:01,368 --> 02:55:02,002 TRIALS. 4256 02:55:02,002 --> 02:55:07,440 HOW DO WE PUSH OUT THE BEST 4257 02:55:07,440 --> 02:55:08,241 INNOVATION AS QUICKLY AS 4258 02:55:08,241 --> 02:55:14,915 POSSIBLE AND A PLACE FOR 4259 02:55:14,915 --> 02:55:18,718 MANAGERS TO TRY TO CREATE NEW 4260 02:55:18,718 --> 02:55:19,786 SOLUTIONS TO ARPA-H INVESTMENT 4261 02:55:19,786 --> 02:55:21,855 MOVING FORWARD AND LAST BUT NOT 4262 02:55:21,855 --> 02:55:25,926 LEAST OUR INVESTOR CLAFT 4263 02:55:25,926 --> 02:55:28,161 CATALYST HUB. 4264 02:55:28,161 --> 02:55:31,464 ARPA-H IS NOT A LONG-TERM FUNDER 4265 02:55:31,464 --> 02:55:33,733 AND WE WORK TO FUND PROJECTS 4266 02:55:33,733 --> 02:55:36,002 POST ARPA-H BUT THE MAJORITY OF 4267 02:55:36,002 --> 02:55:37,437 ARPA-H PROGRAMS WILL GO IN THE 4268 02:55:37,437 --> 02:55:38,605 PRIVATE SECTOR AND BE 4269 02:55:38,605 --> 02:55:38,972 COMMERCIALIZED. 4270 02:55:38,972 --> 02:55:40,507 SO WE WANT TO START TO CURATE 4271 02:55:40,507 --> 02:55:43,443 THE GROUP OF INVESTORS WE CAN 4272 02:55:43,443 --> 02:55:44,678 START TO UNDERSTAND WHAT DO WE 4273 02:55:44,678 --> 02:55:47,147 NEED TO DERISK FOR THEM TO PICK 4274 02:55:47,147 --> 02:55:52,219 UP FUNDING ON THE BACK END? 4275 02:55:52,219 --> 02:55:54,254 WE'RE ALSO FOCUSSING ON 4276 02:55:54,254 --> 02:55:56,223 INVESTORS NOT JUST LOOK FOR 4277 02:55:56,223 --> 02:55:57,891 FINANCIAL RETURN ON INVESTMENT 4278 02:55:57,891 --> 02:56:02,262 BUTTING IN COMMUNITIES AND 4279 02:56:02,262 --> 02:56:04,531 REGIONAL INVESTMENT AND GROWING 4280 02:56:04,531 --> 02:56:06,766 SUSTAINED LEVEL HEALTH CARE AND 4281 02:56:06,766 --> 02:56:10,770 IT'S A TOP PRIORITY FOR US AS WE 4282 02:56:10,770 --> 02:56:12,772 LAUNCH THE ARPA-H NET H. 4283 02:56:12,772 --> 02:56:14,307 I SHARED A LOT OF THIS 4284 02:56:14,307 --> 02:56:16,209 INFORMATION WITH YOU IN THE 4285 02:56:16,209 --> 02:56:17,577 PRIOR SLIDE. 4286 02:56:17,577 --> 02:56:19,145 I WANTED TO HAMMER HOME THAT WE 4287 02:56:19,145 --> 02:56:20,247 DON'T WANT TO DEVELOP SCIENCE IN 4288 02:56:20,247 --> 02:56:21,982 THE ABSENCE OF THE CUSTOMER. 4289 02:56:21,982 --> 02:56:23,783 SO THIS IS SUCH AN INTEGRAL PART 4290 02:56:23,783 --> 02:56:31,992 OF WHAT WE DO AT ARPA-H. 4291 02:56:31,992 --> 02:56:33,994 AND A CALL TO ACTION WITH THE 4292 02:56:33,994 --> 02:56:36,229 LAST SLIDE AND THEN HAPPY TO 4293 02:56:36,229 --> 02:56:38,932 TAKE QUESTIONS. 4294 02:56:38,932 --> 02:56:42,402 SUBMIT YOUR IDEA AND OUR PROGRAM 4295 02:56:42,402 --> 02:56:44,237 MANAGERS LAUNCHED PROGRAMS LIKE 4296 02:56:44,237 --> 02:56:46,640 NITRO BUT WE HAVE AN OPEN DOOR 4297 02:56:46,640 --> 02:56:50,744 FOR ANY IDEA YOU MAY WANT TO 4298 02:56:50,744 --> 02:56:54,447 PITCH US AND WE SAY IT'S THE 4299 02:56:54,447 --> 02:56:54,748 THREE-PAGER. 4300 02:56:54,748 --> 02:57:01,988 SHARE YOUR IDEA WITH US AND WE 4301 02:57:01,988 --> 02:57:02,956 WANT TO HAVE A CONVERSATION 4302 02:57:02,956 --> 02:57:04,057 AROUND IT. 4303 02:57:04,057 --> 02:57:05,859 MAYBE YOU WANT TO BECOME A 4304 02:57:05,859 --> 02:57:08,928 PROGRAM MANAGER AND MAY BE AN 4305 02:57:08,928 --> 02:57:10,630 AREA YOU'RE PASSIONATE ABOUT 4306 02:57:10,630 --> 02:57:10,997 SOLVING. 4307 02:57:10,997 --> 02:57:14,301 WE'LL PURSUE AN AREA OF SCIENCE 4308 02:57:14,301 --> 02:57:16,236 IF WE HAVE THE CHAMPION THAT 4309 02:57:16,236 --> 02:57:18,605 PROGRAM MANAGER THAT WANTS TO DO 4310 02:57:18,605 --> 02:57:25,145 THIS SIMILAR TO WHAT ROSS DID. 4311 02:57:25,145 --> 02:57:28,948 AND WE LAUNCHED A NEWSLETTER AND 4312 02:57:28,948 --> 02:57:31,217 YOU CAN SIGN UP AND HEAR THE 4313 02:57:31,217 --> 02:57:33,086 LATEST AND GREATEST. 4314 02:57:33,086 --> 02:57:36,156 TO THE NIAMS TEAM THANK YOU FOR 4315 02:57:36,156 --> 02:57:37,290 INVITING ARPA-H TO PRESENT IN 4316 02:57:37,290 --> 02:57:38,091 THE SESSION TO SHARE A LITTLE 4317 02:57:38,091 --> 02:57:41,828 BIT ABOUT THE WORK WE'RE DOING 4318 02:57:41,828 --> 02:57:42,562 ALIGNED WITH YOUR INTERESTS AND 4319 02:57:42,562 --> 02:57:43,630 I'M EXCITED TO HEAR THE 4320 02:57:43,630 --> 02:57:44,698 QUESTIONS. 4321 02:57:44,698 --> 02:57:54,874 THANK YOU. 4322 02:58:01,481 --> 02:58:02,349 >> THANK YOU. 4323 02:58:02,349 --> 02:58:05,251 IT'S THRILLING TO SEE THE 4324 02:58:05,251 --> 02:58:05,852 AMBITI 4325 02:58:05,852 --> 02:58:07,454 AMBITIOUS. 4326 02:58:07,454 --> 02:58:13,426 WE WISH YOU THE BEST. 4327 02:58:13,426 --> 02:58:15,195 WON'T BE WONDERFUL FIVE YEARS 4328 02:58:15,195 --> 02:58:16,396 FROM NOW WITH A DIFFERENT VIEW 4329 02:58:16,396 --> 02:58:18,965 OF OSTEOARTHRITIS WITH THE 4330 02:58:18,965 --> 02:58:20,700 EQUITY AND POPULATION HEALTH 4331 02:58:20,700 --> 02:58:21,234 ASPECTS. 4332 02:58:21,234 --> 02:58:23,536 THAT'S A TALL CHALLENGE BUT 4333 02:58:23,536 --> 02:58:24,971 THERE ARE THOSE IN THE ROOM WHO 4334 02:58:24,971 --> 02:58:27,006 LIVE THEIR LIFE TO ADDRESS THIS 4335 02:58:27,006 --> 02:58:30,443 PROBLEM SO IT'S EXCITING TIMES. 4336 02:58:30,443 --> 02:58:32,445 I'M HOPING TO SEE SOME HANDS. 4337 02:58:32,445 --> 02:58:41,354 MIKE. 4338 02:58:41,354 --> 02:58:46,326 >> PEDIATRIC DERMATOLOGY. 4339 02:58:46,326 --> 02:58:47,861 WHAT HAPPENS TO THE PROGRAM 4340 02:58:47,861 --> 02:58:49,496 MANAGERS AFTER THE THREE YEARS? 4341 02:58:49,496 --> 02:58:51,865 SOME OF THE PROMISING MINDS WHO 4342 02:58:51,865 --> 02:58:56,202 WOULD DO THIS STUFF MAY BALK AT 4343 02:58:56,202 --> 02:58:57,637 LEAVING THEIR JOB FOR THREE 4344 02:58:57,637 --> 02:58:59,472 YEARS AND CURIOUS ON THOUGHTS ON 4345 02:58:59,472 --> 02:59:01,241 THAT AND HOW YOU'LL CULTIVATE 4346 02:59:01,241 --> 02:59:02,008 THAT OVER TIME. 4347 02:59:02,008 --> 02:59:02,542 >> GREAT. 4348 02:59:02,542 --> 02:59:05,178 I THINK I HEARD THE QUESTION, 4349 02:59:05,178 --> 02:59:06,546 WHAT HAPPENS TO A PROGRAM 4350 02:59:06,546 --> 02:59:08,081 MANAGER AFTER THREE YEARS. 4351 02:59:08,081 --> 02:59:13,019 YOU TURN INTO A PUMPKIN AND THEN 4352 02:59:13,019 --> 02:59:13,219 WHAT? 4353 02:59:13,219 --> 02:59:14,788 BY STATUTE IT'S THREE YEARS BUT 4354 02:59:14,788 --> 02:59:19,959 IT'S RENEWABLE UP TO ANOTHER 4355 02:59:19,959 --> 02:59:27,767 THREE YEARS IF CAN AGREE TO 4356 02:59:27,767 --> 02:59:31,571 TERMS AND SIX YEARS IS IT AND 4357 02:59:31,571 --> 02:59:34,107 WE'RE LOOKING FOR DIVERSITY AND 4358 02:59:34,107 --> 02:59:35,141 DEMOGRAPHICS AND GEOGRAPHY. 4359 02:59:35,141 --> 02:59:39,179 WE'RE NOT MAKING ANYBODY MOVE SO 4360 02:59:39,179 --> 02:59:42,715 TO YOUR POINT THIS IS LEAVING 4361 02:59:42,715 --> 02:59:45,485 YOUR CAREER POTENTIALLY AND WE 4362 02:59:45,485 --> 02:59:48,254 DON'T WANT YOU TO HAVE TO MOVE 4363 02:59:48,254 --> 02:59:50,356 YOUR WHOLE FAMILY SO YOU DON'T 4364 02:59:50,356 --> 02:59:52,525 HAVE TO MOVE BUT MUST BE WILLING 4365 02:59:52,525 --> 02:59:54,461 TO TRAVEL AND WE'RE RECRUITING 4366 02:59:54,461 --> 02:59:55,295 FOLKS THAT HAVE GOVERNMENT 4367 02:59:55,295 --> 02:59:56,529 EXPERIENCE OR ACADEMIC 4368 02:59:56,529 --> 02:59:58,198 EXPERIENCE OR INDUSTRY 4369 02:59:58,198 --> 02:59:59,466 EXPERIENCE. 4370 02:59:59,466 --> 03:00:01,935 THOSE ARE ALL VALID AS WE GROW 4371 03:00:01,935 --> 03:00:02,535 THAT. 4372 03:00:02,535 --> 03:00:04,504 I CAN SPEAK -- WE HAVEN'T 4373 03:00:04,504 --> 03:00:05,371 GRADUATED ANY PROGRAM MANAGERS 4374 03:00:05,371 --> 03:00:05,638 YET. 4375 03:00:05,638 --> 03:00:09,776 WE'RE JUST STARTING BUT IN MY 4376 03:00:09,776 --> 03:00:11,945 EXPERIENCE AT DARPA THIS CAN 4377 03:00:11,945 --> 03:00:13,246 UNLOCK A LOT OF DOORS. 4378 03:00:13,246 --> 03:00:16,316 YOU BECOME AS A PROGRAM MANAGER 4379 03:00:16,316 --> 03:00:18,151 THE FACE AND VOICE OF THE 4380 03:00:18,151 --> 03:00:19,319 CHALLENGE FOR ARPA-H IN OUR 4381 03:00:19,319 --> 03:00:19,519 CASE. 4382 03:00:19,519 --> 03:00:22,422 YOU START TO BUILD NETWORKS WITH 4383 03:00:22,422 --> 03:00:23,790 YOUR COMMUNITY AND START TO TEE 4384 03:00:23,790 --> 03:00:26,326 UP WHAT DO YOU WANT TO DO NEXT? 4385 03:00:26,326 --> 03:00:27,961 WHAT'S THE BIG PROBLEM YOU WANT 4386 03:00:27,961 --> 03:00:28,895 TO SOLVE? 4387 03:00:28,895 --> 03:00:30,930 SOMETIMES PEOPLE GO BACK. 4388 03:00:30,930 --> 03:00:36,236 WE CAN DO WHAT'S CALLED AN 4389 03:00:36,236 --> 03:00:39,472 I.P.A., INTERPERSONNEL AGREEMENT 4390 03:00:39,472 --> 03:00:41,241 AND YOUR UNIVERSITY MAY GIVE US 4391 03:00:41,241 --> 03:00:44,444 TO US ON LOAN AND YOU CAN GO 4392 03:00:44,444 --> 03:00:46,379 BACK TO PICK UP WHERE YOU LEFT 4393 03:00:46,379 --> 03:00:48,248 OFF AND NOW HAVE EXPERTISE FROM 4394 03:00:48,248 --> 03:00:49,582 AN ARPA-H MODEL AND UNDERSTAND 4395 03:00:49,582 --> 03:00:51,317 THE FEDERAL GOVERNMENT MORE AND 4396 03:00:51,317 --> 03:00:53,152 WORKED WITH FDA AND CMS AND HAVE 4397 03:00:53,152 --> 03:00:54,320 A BETTER REVIEW OF THE WHOLE ECO 4398 03:00:54,320 --> 03:01:04,597 SYSTEM. 4399 03:01:04,597 --> 03:01:10,203 THAT'S IN A WAY OTHERS DON'T 4400 03:01:10,203 --> 03:01:14,607 HAVE WITH THIS EXPERIENCE AND SO 4401 03:01:14,607 --> 03:01:17,677 ARE SO MOTIVATED TO SOLVE THIS 4402 03:01:17,677 --> 03:01:19,679 PROBLEM THEY DONT LOOK AT IT AS 4403 03:01:19,679 --> 03:01:21,481 GIVING UP A POINT IN OUR CAREER 4404 03:01:21,481 --> 03:01:23,516 AND IF I LAUNCH THIS ARPA-H WILL 4405 03:01:23,516 --> 03:01:30,523 GIVE ME A BUDGET OF $100 TO 150 4406 03:01:30,523 --> 03:01:31,591 MILLION TO SOLVE A PROBLEM 4407 03:01:31,591 --> 03:01:35,395 THAT'S BEEN A BLOCKER. 4408 03:01:35,395 --> 03:01:36,796 AND IT'S A HARD JOB. 4409 03:01:36,796 --> 03:01:38,698 YOU'RE SPRINTING FOR THREE 4410 03:01:38,698 --> 03:01:39,432 YEARS, RIGHT. 4411 03:01:39,432 --> 03:01:41,167 SO YOU HAVE TO FIND THE FOLKS 4412 03:01:41,167 --> 03:01:42,368 DETERMINED TO BE THE DOERS TO 4413 03:01:42,368 --> 03:01:52,912 UNSTICK AND SOLVE THAT PROBLEM. 4414 03:01:56,916 --> 03:02:02,555 >> ONE OF THE BIG ISSUES IS THE 4415 03:02:02,555 --> 03:02:04,290 PRESUMPTION IF YOU CAN REBUILD 4416 03:02:04,290 --> 03:02:07,193 CARTILAGE YOU'LL TREAT PAIN? 4417 03:02:07,193 --> 03:02:09,529 >> THERE'S A METRIC AS I 4418 03:02:09,529 --> 03:02:13,600 UNDERSTAND THAT PAIN IS A METRIC 4419 03:02:13,600 --> 03:02:15,001 AND REDUCTION OF PAIN IS 4420 03:02:15,001 --> 03:02:16,135 SOMETHING THEY'LL BE MONITORING 4421 03:02:16,135 --> 03:02:18,271 AS ONE OF THE HEALTH OUTCOMES. 4422 03:02:18,271 --> 03:02:20,173 IT WILL BE MULTIPLE HEALTH 4423 03:02:20,173 --> 03:02:20,773 OUTCOMES MONITORED BUT THAT'S 4424 03:02:20,773 --> 03:02:31,150 CERTAINLY ONE OF THEM. 4425 03:02:48,301 --> 03:02:58,411 [OFF-MIC] 4426 03:03:02,815 --> 03:03:05,752 >> OUR INITIAL APPROPRIATION WAS 4427 03:03:05,752 --> 03:03:07,153 $1 BILLION AND A SECOND 4428 03:03:07,153 --> 03:03:08,921 APPROPRIATION FOR $1.5 BILLION. 4429 03:03:08,921 --> 03:03:10,323 WE'RE THE ONLY OPERATING 4430 03:03:10,323 --> 03:03:13,026 DIVISION I'M AWARE OF THAT HAS 4431 03:03:13,026 --> 03:03:14,594 WHAT'S CALLED THREE-YEAR MONEY. 4432 03:03:14,594 --> 03:03:15,962 WE DON'T HAVE TO SPEND IT ALL BY 4433 03:03:15,962 --> 03:03:18,097 THE END OF THE FISCAL YEAR, SO 4434 03:03:18,097 --> 03:03:19,198 NEXT WEEK. 4435 03:03:19,198 --> 03:03:20,833 WE HAVE THREE YEARS TO SPEND THE 4436 03:03:20,833 --> 03:03:21,401 MONEY. 4437 03:03:21,401 --> 03:03:24,037 THAT ALLOWS US TO MILLION AHEAD 4438 03:03:24,037 --> 03:03:24,637 ON OUR PROGRAMS. 4439 03:03:24,637 --> 03:03:27,240 WITH ROSS ASKED FOR HIS BUDGET 4440 03:03:27,240 --> 03:03:30,043 FOR HIS PROJECT, THE WAY I THINK 4441 03:03:30,043 --> 03:03:33,880 IS YES, YOU CAN DO YOUR NITRO 4442 03:03:33,880 --> 03:03:36,115 PROGRAM AND HERE'S YOUR BANK 4443 03:03:36,115 --> 03:03:36,683 ACCOUNT. 4444 03:03:36,683 --> 03:03:38,451 IT'S THEN UP TO ROSS AS WE LOOKS 4445 03:03:38,451 --> 03:03:43,589 THROUGH THE PROPROPOSALS AND HE 4446 03:03:43,589 --> 03:03:45,224 THEM EVALUATE THE PROPOSALS BUT 4447 03:03:45,224 --> 03:03:47,093 WE DO NOT MAKE DECISIONS BY 4448 03:03:47,093 --> 03:03:47,860 STUDY SECTION. 4449 03:03:47,860 --> 03:03:49,862 HE'S A SOUL DECISION MAKER. 4450 03:03:49,862 --> 03:03:53,533 HE LOOKS AT THE PROPOSALS 4451 03:03:53,533 --> 03:03:54,634 INCLUDING A TECHNICAL STATE OF 4452 03:03:54,634 --> 03:03:55,601 WORK AND BUDGET. 4453 03:03:55,601 --> 03:03:57,837 THERE'S A DEEP NEGOTIATION BACK 4454 03:03:57,837 --> 03:03:58,204 AND FORTH. 4455 03:03:58,204 --> 03:04:01,541 WE DON'T TAKE IT AT FACE VALUE. 4456 03:04:01,541 --> 03:04:04,210 IT'S NEGOTIATION AROUND THE 4457 03:04:04,210 --> 03:04:05,912 COST. 4458 03:04:05,912 --> 03:04:07,547 YEAR NOT LOOKING FOR THE LOWEST 4459 03:04:07,547 --> 03:04:09,649 BIDDER BUT COST REALISM. 4460 03:04:09,649 --> 03:04:11,517 IF WE'RE EXCITED ABOUT THE 4461 03:04:11,517 --> 03:04:12,185 REGENERATIVE BONE PROGRAM THAT 4462 03:04:12,185 --> 03:04:14,153 YOU WANT TO MOVE FORWARD WITH, 4463 03:04:14,153 --> 03:04:15,755 YOU WANT TO MAKE SURE YOU HAVE 4464 03:04:15,755 --> 03:04:19,592 THE RIGHT TEAM IN PLACE YOU HAVE 4465 03:04:19,592 --> 03:04:29,936 ALL THE BIO REACTORS AND THEY 4466 03:04:29,936 --> 03:04:32,605 TEND TO BE WELL RESOURCED 4467 03:04:32,605 --> 03:04:33,806 PROJECTS FORWARD. 4468 03:04:33,806 --> 03:04:34,741 IT'S UP TO THE PROGRAM MANAGER. 4469 03:04:34,741 --> 03:04:38,377 FOR ME AT THE AGENCY LEVEL, 4470 03:04:38,377 --> 03:04:43,649 WHAT'S IMPORTANT FOR ME IS 4471 03:04:43,649 --> 03:04:49,188 FUNDING A DIVERSITY PORTFOLIO 4472 03:04:49,188 --> 03:04:52,658 AND I NEED TO DEMONSTRATE ARPA-H 4473 03:04:52,658 --> 03:04:55,661 IS HERE TO CATALYZE THE ECO 4474 03:04:55,661 --> 03:04:57,263 SYSTEM. 4475 03:04:57,263 --> 03:04:59,332 THE ANSWERS FROM THE ARPA-H 4476 03:04:59,332 --> 03:05:01,667 NITRO AND OUR SURGICAL 4477 03:05:01,667 --> 03:05:02,034 INTERVENTIONS. 4478 03:05:02,034 --> 03:05:12,178 LAST WEEK WE ANNOUNCED A 4479 03:05:12,178 --> 03:05:12,612 MODULATORY PROGRAM. 4480 03:05:12,612 --> 03:05:15,615 WE CALL IT HIGH CONTACT PROGRAM 4481 03:05:15,615 --> 03:05:16,015 MANAGEMENT. 4482 03:05:16,015 --> 03:05:18,151 THEY'RE WELL RESOURCED PROJECTS 4483 03:05:18,151 --> 03:05:20,219 BUT IT'S NOT THROWN OVER THE 4484 03:05:20,219 --> 03:05:20,419 FENCE. 4485 03:05:20,419 --> 03:05:22,955 WE'RE THERE WITH YOU AND IF 4486 03:05:22,955 --> 03:05:25,158 THINGS AREN'T WORKING OUT WE 4487 03:05:25,158 --> 03:05:27,994 RESERVE THE RIGHT TO PIVOT THE 4488 03:05:27,994 --> 03:05:29,162 FUNDS ELSEWHERE TO MAKE MASSIVE 4489 03:05:29,162 --> 03:05:31,664 IMPACT. 4490 03:05:31,664 --> 03:05:40,373 I HOPE THAT HELPS. 4491 03:05:40,373 --> 03:05:43,676 >> I'M WITH THE NATIONAL SCLER 4492 03:05:43,676 --> 03:05:51,417 ODOR -- SCLERODERMA FOUNDATION. 4493 03:05:51,417 --> 03:05:53,719 WHAT CAN WE DO TO HELP AND 4494 03:05:53,719 --> 03:05:55,154 FACILITATE THE INTERACTION SO 4495 03:05:55,154 --> 03:05:56,422 PATIENT VOICE IS INCLUDED IN 4496 03:05:56,422 --> 03:06:00,793 THAT DECISION MAKING? 4497 03:06:00,793 --> 03:06:03,396 >> CAN YOU REPEAT THAT QUESTION 4498 03:06:03,396 --> 03:06:05,865 THAT WAS A LITTLE BIT CHOPPY FOR 4499 03:06:05,865 --> 03:06:06,098 ME. 4500 03:06:06,098 --> 03:06:07,767 >> YOU TALKED ABOUT ENGAGEMENT 4501 03:06:07,767 --> 03:06:11,838 WITH THE GENERAL PUBLIC AND 4502 03:06:11,838 --> 03:06:13,339 PATIENT COMMUNITY AND US, 4503 03:06:13,339 --> 03:06:14,373 PATIENT ADVOCACY ORGANIZATIONS. 4504 03:06:14,373 --> 03:06:16,375 WHAT CAN WE DO TO HELP AND 4505 03:06:16,375 --> 03:06:18,077 FACILITATE THOSE DISCUSSIONS AND 4506 03:06:18,077 --> 03:06:19,679 ENSURE THAT PATIENT VOICE IS 4507 03:06:19,679 --> 03:06:20,213 INCLUDED IN YOUR DECISION 4508 03:06:20,213 --> 03:06:30,356 MAKING? 4509 03:06:32,425 --> 03:06:35,962 >> AND WE HAVE ABOUT 200 PATIENT 4510 03:06:35,962 --> 03:06:37,730 GROUPS AND ONE IS LETTING PEOPLE 4511 03:06:37,730 --> 03:06:41,434 KNOW WE'RE HERE AND WHAT WE DO 4512 03:06:41,434 --> 03:06:43,202 IS DIFFERENT FROM THE REST OF 4513 03:06:43,202 --> 03:06:44,904 THE ECO FUNDING SYSTEM. 4514 03:06:44,904 --> 03:06:47,340 THAT'S BEEN AN IMPORTANT 4515 03:06:47,340 --> 03:06:49,208 LEARNING AND YOU SAY DARPA AND 4516 03:06:49,208 --> 03:06:50,776 PEOPLE GET IT BUT IN A HEALTH 4517 03:06:50,776 --> 03:06:53,246 SYSTEM THEY DON'T KNOW ARPA-H OR 4518 03:06:53,246 --> 03:06:53,679 DARPA. 4519 03:06:53,679 --> 03:06:55,648 WE HAVE TO EXPLAIN THE BUSINESS 4520 03:06:55,648 --> 03:06:55,848 MODEL. 4521 03:06:55,848 --> 03:07:00,519 WE SPEND A LOT OF TIME ENGAGING 4522 03:07:00,519 --> 03:07:01,854 WITH THE VARIETY OF PATIENT 4523 03:07:01,854 --> 03:07:04,090 GROUPS TO GET TO KNOW US AND NOW 4524 03:07:04,090 --> 03:07:05,124 THAT WE'RE LAUNCHING PROGRAMS 4525 03:07:05,124 --> 03:07:06,259 IT'S UP TO THE PROGRAM MANAGERS 4526 03:07:06,259 --> 03:07:07,994 TO START TO MAKE THOSE 4527 03:07:07,994 --> 03:07:08,294 CONNECTIONS. 4528 03:07:08,294 --> 03:07:10,363 I KNOW ROSS HAS BEEN WORKING 4529 03:07:10,363 --> 03:07:12,031 WITH THE ROOM THERE AND THE 4530 03:07:12,031 --> 03:07:13,199 FOLKS THAT ARE PRESENT BUT THE 4531 03:07:13,199 --> 03:07:15,701 OTHER WAY WE WANT TO FACILITATE 4532 03:07:15,701 --> 03:07:22,475 THIS IS THROUGH ARPA NET H AND 4533 03:07:22,475 --> 03:07:23,709 YOU'LL SEE THE DIFFERENT GROUPS 4534 03:07:23,709 --> 03:07:26,846 WHEN WE ANNOUNCE THE BESPOKE. 4535 03:07:26,846 --> 03:07:30,216 IT WILL BE THAT SNAPSHOT AT TIME 4536 03:07:30,216 --> 03:07:32,218 BUT IT'S MEANT TO BE DYNAMIC 4537 03:07:32,218 --> 03:07:37,356 WITH PROGRAM AND WHAT I DIDN'T 4538 03:07:37,356 --> 03:07:38,591 TALK ABOUT IS HOW WE'RE GOING TO 4539 03:07:38,591 --> 03:07:44,096 DO THE INTERACTIONS. 4540 03:07:44,096 --> 03:07:46,265 THAT PROJECT IS EXCLUSIVELY 4541 03:07:46,265 --> 03:07:46,966 OTHER TRANSACTION AUTHORITIES 4542 03:07:46,966 --> 03:07:48,601 WHICH MEANS SEVEN DAYS TO GET 4543 03:07:48,601 --> 03:07:49,235 UNDER CONTRACT. 4544 03:07:49,235 --> 03:07:51,337 WE WANT TO BE ABLE TO FUND 4545 03:07:51,337 --> 03:07:53,039 COMMUNITIES TO SUPPORT SOME OF 4546 03:07:53,039 --> 03:07:56,943 OUR EFFORTS AND IN ROSS'S CASE 4547 03:07:56,943 --> 03:07:58,377 WHEN HE LAUNCHES THE CLINICAL 4548 03:07:58,377 --> 03:08:00,212 TRIAL HE HAS THE BUDGET TO WORK 4549 03:08:00,212 --> 03:08:03,649 ON THE CIVIL ENGINEERING BUT 4550 03:08:03,649 --> 03:08:06,519 WE'LL REFER A BUDGET FOR ARPA 4551 03:08:06,519 --> 03:08:08,154 NET H TO DO PATIENT OUTREACH AND 4552 03:08:08,154 --> 03:08:09,488 HAVE FUNDS ASSOCIATED AND WE 4553 03:08:09,488 --> 03:08:11,357 HEARD LOUD AND CLEAR FROM 4554 03:08:11,357 --> 03:08:12,258 COMMUNITIES IT'S GREAT TO BE IN 4555 03:08:12,258 --> 03:08:13,693 THE ROOM BUT IF YOU'RE NOT 4556 03:08:13,693 --> 03:08:15,962 PAYING FOR ME TO BE HERE AND MY 4557 03:08:15,962 --> 03:08:18,331 TIME IT MAKES IT CHALLENGING. 4558 03:08:18,331 --> 03:08:21,968 WE WANT TO BE RESPONSIVE BUT 4559 03:08:21,968 --> 03:08:24,570 WE'RE OPEN TO IDEAS. 4560 03:08:24,570 --> 03:08:26,405 IF ANYONE WANTS TO REACH OUT TO 4561 03:08:26,405 --> 03:08:28,274 IDEAS OF BEST PRACTICES OR 4562 03:08:28,274 --> 03:08:29,775 WHAT'S WORKED FOR YOU AND I'M 4563 03:08:29,775 --> 03:08:33,412 HAPPY TO SHARE THIS. 4564 03:08:33,412 --> 03:08:34,780 IT'S GOING TO BE LISTENING AND 4565 03:08:34,780 --> 03:08:35,047 LEARNING. 4566 03:08:35,047 --> 03:08:41,887 >> ONE LAST ONE. 4567 03:08:41,887 --> 03:08:44,724 >> I'M WITH THE NATIONAL 4568 03:08:44,724 --> 03:08:45,324 PSORIASIS FOUNDATION. 4569 03:08:45,324 --> 03:08:46,292 WHEN WE THINK OF HEALTH OUTCOMES 4570 03:08:46,292 --> 03:08:49,161 AND HOW IT ACHIEVE THEM WE GET 4571 03:08:49,161 --> 03:08:50,529 STRUCK AT THE TRIALS AND CERTAIN 4572 03:08:50,529 --> 03:08:55,935 APPROACHES TO HEALTH CARE GIVEN 4573 03:08:55,935 --> 03:08:57,670 YOU'RE PROGRAM IS DEDICATED TO 4574 03:08:57,670 --> 03:09:01,674 THINKING OUTSIDE THE BOX, HOW 4575 03:09:01,674 --> 03:09:04,677 RECEPTIVE ARE YOU TO DIFFERENT 4576 03:09:04,677 --> 03:09:06,746 APPROACHES TO DELIVERING 4577 03:09:06,746 --> 03:09:07,513 CLINICAL TRIAL OR HEALTH CARE 4578 03:09:07,513 --> 03:09:10,316 THAT MAY IMPROVE OUTCOMES 4579 03:09:10,316 --> 03:09:11,951 OUTSIDE THE TRADITIONAL HEALTH 4580 03:09:11,951 --> 03:09:13,686 CARE SYSTEM? 4581 03:09:13,686 --> 03:09:17,490 >> I THINK YOU WERE ASKING ABOUT 4582 03:09:17,490 --> 03:09:23,896 HEALTH CARE IMPACT OUTSIDE THE 4583 03:09:23,896 --> 03:09:24,296 SUF 4584 03:09:24,296 --> 03:09:25,698 U.S. 4585 03:09:25,698 --> 03:09:29,001 >> WE KNOW CERTAIN PATIENTS ARE 4586 03:09:29,001 --> 03:09:31,537 TRADITIONALLY UNDER SERVED AND 4587 03:09:31,537 --> 03:09:33,105 THEIR HEALTH OUTCOME WILL BE 4588 03:09:33,105 --> 03:09:37,376 WORSE THAN THE AVERAGE 4589 03:09:37,376 --> 03:09:37,676 POPULATION. 4590 03:09:37,676 --> 03:09:38,411 THINKING YOUR PROGRAM ARPA-H IS 4591 03:09:38,411 --> 03:09:40,179 SUPPOSED TO THINK OUTSIDE THE 4592 03:09:40,179 --> 03:09:40,546 BOX. 4593 03:09:40,546 --> 03:09:42,748 HOW MUCH ARE YOU THINKING OF 4594 03:09:42,748 --> 03:09:44,250 DIFFERENT METHODS IN ORDER TO 4595 03:09:44,250 --> 03:09:46,419 REACH PATIENTS TO IMPROVE THEIR 4596 03:09:46,419 --> 03:09:49,855 HEALTH OUTCOMES VERSUS MORE 4597 03:09:49,855 --> 03:09:52,224 ADDITIONAL RESEARCH CLINICAL 4598 03:09:52,224 --> 03:09:53,726 TRIALS APPLICATION TO THINK 4599 03:09:53,726 --> 03:09:55,594 ABOUT IF YOU'RE FOCUSSED ON I AM 4600 03:09:55,594 --> 03:09:57,830 PROVING HEALTH OUTCOMES THE 4601 03:09:57,830 --> 03:09:59,832 EASIEST WAY IS TO GET PATIENTS 4602 03:09:59,832 --> 03:10:02,835 TO LINK UP TO EXISTING HEALTH 4603 03:10:02,835 --> 03:10:11,844 CARE OR EXISTING HEALTH CARE 4604 03:10:11,844 --> 03:10:12,244 INNOVATIONS -- 4605 03:10:12,244 --> 03:10:16,749 >> IT'S A BAD CONNECTION. 4606 03:10:16,749 --> 03:10:19,051 I APOLOGIZE IF I DIDN'T GET ALL 4607 03:10:19,051 --> 03:10:19,652 THAT. 4608 03:10:19,652 --> 03:10:24,623 HOW ARE WE GOING TO INFLUENCE 4609 03:10:24,623 --> 03:10:25,658 HEALTH CARE? 4610 03:10:25,658 --> 03:10:27,460 >> IF THERE'S ROOM FOR ARPA-H 4611 03:10:27,460 --> 03:10:28,861 WITH THESE APPROACHES OR 4612 03:10:28,861 --> 03:10:30,830 THINKING MORE ABOUT CLINICAL 4613 03:10:30,830 --> 03:10:36,235 TRIALS OR DIFFERENT TRYING TO 4614 03:10:36,235 --> 03:10:42,308 UNDERSTAND DISEASES RATHER THAN 4615 03:10:42,308 --> 03:10:43,209 DELIVERING HEALTH CARE. 4616 03:10:43,209 --> 03:10:48,247 >> THE ARPA-H MANDATE IS PRETTY 4617 03:10:48,247 --> 03:10:49,882 WIDE OPEN. 4618 03:10:49,882 --> 03:10:52,618 WE CAN FUND CROSS WHAT I THINK 4619 03:10:52,618 --> 03:10:53,619 ARE TECHNOLOGY READINESS LEVELS 4620 03:10:53,619 --> 03:10:59,959 ON THE BACK OF A NAPKIN AND WE 4621 03:10:59,959 --> 03:11:03,429 CAN FUND THE ENTIRE CONTINUUM. 4622 03:11:03,429 --> 03:11:05,297 WE'RE NOT HERE TO REFORM THE 4623 03:11:05,297 --> 03:11:06,899 HEALTH CARE SYSTEM. 4624 03:11:06,899 --> 03:11:09,201 WE'RE HERE TO DEMONSTRATE AND 4625 03:11:09,201 --> 03:11:12,271 FAVOR THE ODDS OF BREAKTHROUGHS 4626 03:11:12,271 --> 03:11:15,808 THAT CAN BE ADOPTED. 4627 03:11:15,808 --> 03:11:18,043 ARPA-H IS A NOD WE NEED TO 4628 03:11:18,043 --> 03:11:18,644 INTEGRATE IN THE HEALTH CARE 4629 03:11:18,644 --> 03:11:21,780 SYSTEM AND FIGURE OUT THE PAYER 4630 03:11:21,780 --> 03:11:22,181 MODELS. 4631 03:11:22,181 --> 03:11:24,183 WE'RE BASICALLY A TECHNOLOGY 4632 03:11:24,183 --> 03:11:25,317 ORIENTED ORGANIZATION. 4633 03:11:25,317 --> 03:11:28,120 FOUR YEARS FROM NOW WILL BE AN 4634 03:11:28,120 --> 03:11:28,921 INTERESTING MOMENT IN TIME 4635 03:11:28,921 --> 03:11:30,823 BECAUSE CONGRESS CALLED ON US TO 4636 03:11:30,823 --> 03:11:34,093 COME BACK IN FRONT OF THE 4637 03:11:34,093 --> 03:11:37,730 CONGRESS AND SAY FOUR, FIVE 4638 03:11:37,730 --> 03:11:39,031 YEARS IS PAST ARPA-H. 4639 03:11:39,031 --> 03:11:41,433 GIVE ME THE QUANTITATIVE 4640 03:11:41,433 --> 03:11:42,434 OUTCOMES HOW YOU IMPROVED HEALTH 4641 03:11:42,434 --> 03:11:43,836 CARE IN THE UNITED STATES. 4642 03:11:43,836 --> 03:11:47,239 THE IS HARD BECAUSE MOST ARPA-H 4643 03:11:47,239 --> 03:11:49,041 TIME LINES TEND TO BE 10 TO 15 4644 03:11:49,041 --> 03:11:51,410 YEAR TIME LINES WHERE YOU START 4645 03:11:51,410 --> 03:11:53,412 TO SEE THE IMPACT IN THE 4646 03:11:53,412 --> 03:11:53,679 COMMUNITY. 4647 03:11:53,679 --> 03:11:55,714 SOMETHING WE'RE THINKING ABOUT 4648 03:11:55,714 --> 03:11:58,617 AND THE IMMEDIATE STEPS WE CAN 4649 03:11:58,617 --> 03:12:03,522 DEMONSTRATE SOME OF THAT 4650 03:12:03,522 --> 03:12:04,290 MOVEMENT IN THE U.S. MOVING 4651 03:12:04,290 --> 03:12:06,425 FORWARD AND THIS IS A PASSIONATE 4652 03:12:06,425 --> 03:12:09,228 AREA FOR THE PRESIDENT AND FIRST 4653 03:12:09,228 --> 03:12:09,428 LADY. 4654 03:12:09,428 --> 03:12:10,963 THEY'VE TRYING TO LOOP US IN THE 4655 03:12:10,963 --> 03:12:12,364 CONVERSATION OF HOW DO WE CHANGE 4656 03:12:12,364 --> 03:12:17,469 THE WAY WE THINK OF HEALTH CARE 4657 03:12:17,469 --> 03:12:21,707 IN THE UNITED STATES AND CREATE 4658 03:12:21,707 --> 03:12:23,909 SPACES WE CAN INNOVATE AND TAKE 4659 03:12:23,909 --> 03:12:24,877 RISKS. 4660 03:12:24,877 --> 03:12:26,912 MAYBE IN A YEAR FROM NOW WE'LL 4661 03:12:26,912 --> 03:12:27,713 HAVE ADDITIONAL PROGRAMS THAT 4662 03:12:27,713 --> 03:12:29,281 START TO ADDRESS IT. 4663 03:12:29,281 --> 03:12:31,350 I DON'T KNOW ENOUGH TIME HAS 4664 03:12:31,350 --> 03:12:34,153 PASSED TO SAY HOW WE'RE GOING TO 4665 03:12:34,153 --> 03:12:36,222 IMPACT HEALTH CARE IN THE UNITED 4666 03:12:36,222 --> 03:12:37,923 STATES. 4667 03:12:37,923 --> 03:12:40,192 >> LET US KNOW WHEN YOU FIGURE 4668 03:12:40,192 --> 03:12:41,060 IT OUT. 4669 03:12:41,060 --> 03:12:41,527 THANK YOU, VERY MUCH. 4670 03:12:41,527 --> 03:12:48,534 THAT WAS WONDERFUL. 4671 03:12:48,534 --> 03:12:49,802 THANK YOU. 4672 03:12:49,802 --> 03:12:55,741 >> THANK YOU SO MUCH. 4673 03:12:55,741 --> 03:12:58,777 TAKE CARE, GUYS. 4674 03:12:58,777 --> 03:13:03,716 >> 4675 03:13:03,716 --> 03:13:05,484 >> THAT WAS A TERRIFIC 4676 03:13:05,484 --> 03:13:06,919 PRESENTATION TO KICK OFF OUR 4677 03:13:06,919 --> 03:13:09,121 AFTERNOON SESSIONS. 4678 03:13:09,121 --> 03:13:10,789 A COUPLE OF FEW HOUSEKEEPINGS 4679 03:13:10,789 --> 03:13:12,258 AND GUIDANCE FOR THE AFTERNOON. 4680 03:13:12,258 --> 03:13:13,726 WE'RE NOW GOING TO BE TRANSITION 4681 03:13:13,726 --> 03:13:14,927 TO POSTER SESSION WHICH I'M 4682 03:13:14,927 --> 03:13:15,261 EXCITE ABOUT. 4683 03:13:15,261 --> 03:13:16,228 IT'S ANOTHER OPPORTUNITY FOR YOU 4684 03:13:16,228 --> 03:13:18,163 ALL TO NETWORK AND ENGAGE WITH 4685 03:13:18,163 --> 03:13:20,232 EACH OTHER AND ENCOURAGE YOU TO 4686 03:13:20,232 --> 03:13:21,033 DO THAT AS MUCH AS POSSIBLE. 4687 03:13:21,033 --> 03:13:22,468 THE WAY THE POSTER SESSION'S 4688 03:13:22,468 --> 03:13:25,904 GOING TO WORK IS IF YOU HAVE AN 4689 03:13:25,904 --> 03:13:28,207 EVEN NUMBER YOU'LL BE PRESENTING 4690 03:13:28,207 --> 03:13:30,276 FOR THE FIRST HALF OF THE POSTER 4691 03:13:30,276 --> 03:13:31,377 SESSION. 4692 03:13:31,377 --> 03:13:35,948 INSTEAD OF 2:15 TO 2:35 WE'RE 4693 03:13:35,948 --> 03:13:42,421 GOING TO DO 2:20 TO 2:40 AND THE 4694 03:13:42,421 --> 03:13:46,892 ODD WILL PRESENT THE SECOND HALF 4695 03:13:46,892 --> 03:13:49,728 SO EVERYONE CAN PRESENT. 4696 03:13:49,728 --> 03:13:52,564 ENGAGE WITH ONE ANOTHER. 4697 03:13:52,564 --> 03:13:56,101 THERE'S COFFEE AND A REMINDER TO 4698 03:13:56,101 --> 03:13:58,103 FILL OUT THE RECOMMENDATION 4699 03:13:58,103 --> 03:13:59,705 FORMS THEY HELP SHAPE THE 4700 03:13:59,705 --> 03:14:00,739 MEETING THE CO-CHAIRS READ 4701 03:14:00,739 --> 03:14:01,540 THROUGH ALL OF THEM. 4702 03:14:01,540 --> 03:14:03,475 AS YOU GET IDEAS ABOUT WHAT 4703 03:14:03,475 --> 03:14:05,678 YOU'D LIKE TO HEAR OR SEE AT 4704 03:14:05,678 --> 03:14:07,579 THIS PLATFORM, RECORD IT ON THE 4705 03:14:07,579 --> 03:14:08,380 EVALUATION FORMS AND GIVE THEM 4706 03:14:08,380 --> 03:14:12,084 TO REGISTRATION ON YOUR WAY OUT. 4707 03:14:12,084 --> 03:14:13,819 ON THE TOPIC OF FEEDBACK IN THE 4708 03:14:13,819 --> 03:14:16,422 POSTER ROOMS WE'RE LOOKING FOR 4709 03:14:16,422 --> 03:14:17,856 YOUR FEEDBACK ON THE NIAMS 4710 03:14:17,856 --> 03:14:18,123 RESOURCES. 4711 03:14:18,123 --> 03:14:24,863 ANY ORGANIZATIONS RELATED TO 4712 03:14:24,863 --> 03:14:26,598 ARTHRITIS, LUPUS PLEASE GO TO 4713 03:14:26,598 --> 03:14:31,503 THE BACK TABLE WE'RE TAKE ING 4714 03:14:31,503 --> 03:14:32,538 YOUR FEEDBACK. 4715 03:14:32,538 --> 03:14:34,306 AFTER THE POSTER SESSION WE'RE 4716 03:14:34,306 --> 03:14:36,442 GOING TO BE GOING IMMEDIATELY 4717 03:14:36,442 --> 03:14:38,610 INTO THE BREAKOUT SESSION WHICH 4718 03:14:38,610 --> 03:14:40,579 MEANS THERE WON'T BE ANY 4719 03:14:40,579 --> 03:14:41,413 ANNOUNCEMENTS TO PLEASE PAY 4720 03:14:41,413 --> 03:14:44,116 ATTENTION TO YOUR AGENDA AND 4721 03:14:44,116 --> 03:14:45,484 PROMPTLY AT THE END OF THE 4722 03:14:45,484 --> 03:14:49,621 POSTER SESSION WHEN YOU HEAR THE 4723 03:14:49,621 --> 03:14:51,357 CHIME, THAT MEANS YOU GO TO YOUR 4724 03:14:51,357 --> 03:14:53,125 SELECTED BREAKOUT SESSIONS. 4725 03:14:53,125 --> 03:14:54,960 YOU SELECT THE TOPIC YOU'RE 4726 03:14:54,960 --> 03:14:56,228 INTERESTED IN AND YOU CAN MAKE 4727 03:14:56,228 --> 03:15:02,234 YOUR WAY TO THAT BREAKOUT. 4728 03:15:02,234 --> 03:15:04,103 WE HAVE A LOT OF SPEAKERS SIGNED 4729 03:15:04,103 --> 03:15:05,871 UP SO PLEASE STAY TUNED FOR 4730 03:15:05,871 --> 03:15:06,071 THEM. 4731 03:15:06,071 --> 03:15:08,240 IF YOU HAVE QUESTIONS, THERE'S 4732 03:15:08,240 --> 03:15:09,975 NIAMS STAFF WITH THE BLUE 4733 03:15:09,975 --> 03:15:11,810 RIBBONS ON AND AGAIN USE THE 4734 03:15:11,810 --> 03:15:13,145 OPPORTUNITY TO NETWORK, SHARE 4735 03:15:13,145 --> 03:15:14,613 AND LEARN FROM EACH OTHER. 4736 03:15:14,613 --> 03:15:18,317 WE CAN ALL MOVE OVER TO F1, F2 4737 03:15:18,317 --> 03:15:19,351 JUST OUTSIDE THE DOOR TO THE 4738 03:15:19,351 --> 03:15:20,119 RIGHT AND RIGHT AGAIN. 4739 03:15:20,119 --> 03:15:20,519 YOU'LL SEE A SIGN. 4740 03:15:20,519 --> 03:15:30,696 THANK YOU.